CAnadian CAncers With Rare Molecular Alterations (CARMA) - Basket Real-world Observational Study (BROS)

NCT ID: NCT04151342

Last Updated: 2025-12-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Total Enrollment

5500 participants

Study Classification

OBSERVATIONAL

Study Start Date

2020-01-17

Study Completion Date

2029-12-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study will collect data on Canadian cancer patients that have uncommon/rare changes in their tumours, such as alterations/rearrangements in the genetic material inside cells - known as deoxyribonucleic acid, or DNA, which acts as a map and gives directions to the cells on how to make other substances the body needs - because some of these changes have been found to respond to different drugs that help to stop the cancer. These rare changes occur in genes such as but not limited to ALK, EGFR, ROS1, BRAF, and NTRK which have targeted drugs in a family known as tyrosine kinase inhibitors (TKIs), and KRAS G12C mutation, which now has a targeted inhibitor drug therapy for patients with non small cell lung cancer (NSCLC). The goals for the study are to compare the natural history of such cancers and the treatment outcomes, including toxicities and patient-reported outcomes, for the different therapies.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Molecular heterogeneity in cancer tumours make it a complex disease to manage and treat. However, there have been significant advancements made in the detection of molecular alterations and we are able to now define distinct disease subtypes which permit targeted selection of therapies, thus optimizing treatment responses for patients and improving their survival.

With CARMA-BROS we will address the objectives that follow.

Primary Objectives:

1. To create a cohort of patients through which to better understand the natural history of disease in Canadian cancer patients with tumours that have been molecularly subtyped and identified to have rare molecular alterations.
2. To compare the natural history, stage distribution, treatment outcomes such as treatment effectiveness (composite of disease progression or death) and treatment toxicities across different patients with different molecular alterations, receiving different lines and types of therapy.

Secondary Objectives:
3. To determine the incidence, time to development, prevalence, and outcomes of patients with specific patterns of spread, such as brain metastases compared to those without, by different therapies and by molecular alterations.
4. To better understand real-world treatment patterns of rare molecular alterations in the Canadian context, across geographic or other factors, and how treatment patterns evolve over time and as new therapies become available, how patients are investigated and how targeted and other biomarkers are used as part of clinical practice in these patients.
5. To assess quality of life in patients with rare molecular alterations across different stages, lines and types of therapy.
6. To perform exploratory health economic evaluations focused on the costs and benefits of managing patients with rare molecular alterations.
7. To perform biomarker analyses, where appropriate, to improve our understanding of these rare molecular alterations.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Cancer Malignancies Multiple Malignant Solid Tumor Cancer, Therapy-Related Molecular Sequence Variation Genetic Alteration Gene Fusion Receptor Tyrosine Kinase Gene Mutation RTK Family Gene Mutation Ras (Kras or Nras) Gene Mutation

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Observational Model Type

COHORT

Study Time Perspective

OTHER

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Prospective

Living cancer patients with histologically confirmed rare molecular alterations in their tumours, such as in ALK, EGFR, ROS1, BRAF, and KRAS G12C from participating sites/cancer centres across Canada.

Cancer treatment with tyrosine kinase inhibitors (TKIs) or other molecularly targeted therapeutic agents.

Intervention Type DRUG

Observing cancer patients who have received or are currently receiving tyrosine kinase inhibitors (TKIs) or other molecularly targeted therapies for their cancer treatment.

Patient-reported outcomes (PROs)

Intervention Type OTHER

Prospectively enrolled participants will be provided with survey packets comprised of different PRO instruments at the initial/baseline visit, at 3 month follow up intervals and at the time when treatment/therapy is changed.

Retrospective

Deceased cancer patients who had histologically confirmed rare molecular alterations in their tumours, such as in ALK, EGFR, ROS1, BRAF, and KRAS G12C from participating sites/cancer centres across Canada.

Cancer treatment with tyrosine kinase inhibitors (TKIs) or other molecularly targeted therapeutic agents.

Intervention Type DRUG

Observing cancer patients who have received or are currently receiving tyrosine kinase inhibitors (TKIs) or other molecularly targeted therapies for their cancer treatment.

Comparator group

All cancer patients without rare molecular alterations in their solid tumours. This group will be established in order to determine baseline characteristics and outcomes, including treatment outcomes, of more standard treatments such as systemic chemotherapy or immunotherapy.

No interventions assigned to this group

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Cancer treatment with tyrosine kinase inhibitors (TKIs) or other molecularly targeted therapeutic agents.

Observing cancer patients who have received or are currently receiving tyrosine kinase inhibitors (TKIs) or other molecularly targeted therapies for their cancer treatment.

Intervention Type DRUG

Patient-reported outcomes (PROs)

Prospectively enrolled participants will be provided with survey packets comprised of different PRO instruments at the initial/baseline visit, at 3 month follow up intervals and at the time when treatment/therapy is changed.

Intervention Type OTHER

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Patients ≥ 18 years at cancer diagnosis
* Diagnosed with malignant tumour(s) with molecular testing completed that identified rare molecular alterations
* Accessible/available molecular testing reports/documentation to confirm type(s) of molecular alteration(s) (resulting from the conduct of polymerase chain reaction \[PCR\] based next generation sequencing \[NGS\], immunohistochemistry \[IHC\], fluorescence in situ hybridization \[FISH\], liquid biopsy)
* Canadian resident received follow-up for cancer care in Canada or is currently receiving/planning follow-up for cancer care to occur in Canada at time of enrollment

Exclusion Criteria

* Previous refusal of the deceased patient, when living, to enroll in this study or patient approached for this study is unable to provide informed consent
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Takeda Canada, Inc.

INDUSTRY

Sponsor Role collaborator

Applied Health Research Centre

OTHER

Sponsor Role collaborator

Programs for Assessment of Technology in Health Research Institute

OTHER

Sponsor Role collaborator

AstraZeneca

INDUSTRY

Sponsor Role collaborator

Amgen

INDUSTRY

Sponsor Role collaborator

Bayer

INDUSTRY

Sponsor Role collaborator

Nuvation Bio Inc.

INDUSTRY

Sponsor Role collaborator

IQVIA Solutions Canada Inc.

UNKNOWN

Sponsor Role collaborator

University Health Network, Toronto

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Geoffrey Liu, MD, MSc

Role: PRINCIPAL_INVESTIGATOR

Princess Margaret Cancer Centre

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Tom Baker Cancer Centre - University of Calgary - Alberta Health Services

Calgary, Alberta, Canada

Site Status RECRUITING

Cross Cancer Institute, University of Alberta - Alberta Health Services

Edmonton, Alberta, Canada

Site Status NOT_YET_RECRUITING

BC Cancer

Vancouver, British Columbia, Canada

Site Status RECRUITING

CancerCare Manitoba/University of Manitoba

Winnipeg, Manitoba, Canada

Site Status RECRUITING

Dr. Everett Chalmers Regional Hospital

Fredericton, New Brunswick, Canada

Site Status RECRUITING

Dr. H. Bliss Murphy Cancer Centre

St. John's, Newfoundland and Labrador, Canada

Site Status NOT_YET_RECRUITING

Queen Elizabeth II (QEII) Health Sciences Centre

Halifax, Nova Scotia, Canada

Site Status RECRUITING

William Osler Health System - Brampton Civic Hospital

Brampton, Ontario, Canada

Site Status RECRUITING

Health Sciences North

Greater Sudbury, Ontario, Canada

Site Status RECRUITING

Hamilton Health Sciences - Juravinski Cancer Centre

Hamilton, Ontario, Canada

Site Status RECRUITING

Kingston Health Sciences Centre (KHSC)

Kingston, Ontario, Canada

Site Status RECRUITING

Lawson Health Research Institute - London Health Sciences Centre

London, Ontario, Canada

Site Status RECRUITING

Ottawa Hospital Cancer Centre

Ottawa, Ontario, Canada

Site Status RECRUITING

Thunder Bay Regional Health Sciences Centre

Thunder Bay, Ontario, Canada

Site Status NOT_YET_RECRUITING

Princess Margaret Cancer Centre (PMCC) - University Health Network (UHN)

Toronto, Ontario, Canada

Site Status RECRUITING

Mount Sinai Hospital

Toronto, Ontario, Canada

Site Status RECRUITING

Sunnybrook Research Institute - Sunnybrook Health Sciences Centre

Toronto, Ontario, Canada

Site Status RECRUITING

Centre hospitalier de l'Université de Montréal (CHUM)

Montreal, Quebec, Canada

Site Status RECRUITING

Hôpital du Sacré-Coeur-de-Montréal (HSCM)

Montreal, Quebec, Canada

Site Status RECRUITING

Jewish General Hospital

Montreal, Quebec, Canada

Site Status RECRUITING

McGill University Health Centre

Montreal, Quebec, Canada

Site Status NOT_YET_RECRUITING

St. Mary's Hospital Center

Montreal, Quebec, Canada

Site Status NOT_YET_RECRUITING

Centre hospitalier de l'université de Québec - Université Laval

Québec, Quebec, Canada

Site Status NOT_YET_RECRUITING

Institut Universitaire de Cardiologie et de Pneumologie de Québec

Québec, Quebec, Canada

Site Status NOT_YET_RECRUITING

Centre hospitalier universitaire de Sherbrooke (CHUS)

Sherbrooke, Quebec, Canada

Site Status RECRUITING

Allan Blair Cancer Centre

Regina, Saskatchewan, Canada

Site Status NOT_YET_RECRUITING

Saskatoon Cancer Centre

Saskatoon, Saskatchewan, Canada

Site Status NOT_YET_RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

Canada

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Faisal Al-Agha, BSc

Role: CONTACT

416-946-4501

Roula Raptis, MSc

Role: CONTACT

416-864-6060 ext. 47106

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Faisal Al-Agha, BSc

Role: primary

416-946-4501 ext. 3428

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Roula Raptis, MSc

Role: primary

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

18-5902

Identifier Type: OTHER

Identifier Source: secondary_id

1632

Identifier Type: OTHER

Identifier Source: secondary_id

CARMA-BROS

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.