Handheld Ultrasound (HHUS) for Home Use in Hemophilia

NCT ID: NCT04131920

Last Updated: 2022-06-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

10 participants

Study Classification

OBSERVATIONAL

Study Start Date

2019-10-01

Study Completion Date

2022-06-22

Brief Summary

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This is a study in 3 phases that will assess the feasibility and utility of handheld home ultrasound (HHUS) in a patient's home to assess whether a painful episode in the elbow, knee or ankle is a bleed or not.

Detailed Description

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This is a study in 3 phases that will assess the feasibility and utility of handheld home ultrasound (HHUS) in a patient's home to assess whether a painful episode in the elbow, knee or ankle is a bleed or not.

Phase 1 will assess whether 10 subjects with severe hemophilia A can be trained to use HHUS in clinic to identify basic joint structures of the elbow, knee and ankle. It will then assess whether these subjects can identify these structures at home and transmit the images life via tele-ultrasound.

Phase 2 will assess whether the determination of "bleed" vs. "non-bleed" made at home via HHUS can be confirmed/validated with a standard high resolution ultrasound machine in clinic.

Phase 3 will then utilize HHUS during the EmiMSKUS study over 3 years to more objectively identify patient reported bleeding during the study.

Conditions

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Joint Bleed Hemophilia A

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Phase 1 and 2

10 male patients with severe Hemophilia A from the Washington Center for Bleeding Disorders

handheld ultrasound: Philips Lumify integrated tele-ultrasound powered by Reacts collaborative platform

Intervention Type DEVICE

Patients receive training by the physical therapist to operate a handheld ultrasound (HHUS) including proper probe placement. Subjects will be tested on their knowledge at the HTC to demonstrate proficiency, and will then repeat the testing at home via tele-ultrasound.

Phase 3

20 subjects who are also participating in the EmiMSKUS study

handheld ultrasound: Philips Lumify integrated tele-ultrasound powered by Reacts collaborative platform

Intervention Type DEVICE

Patients receive training by the physical therapist to operate a handheld ultrasound (HHUS) including proper probe placement. Subjects will be tested on their knowledge at the HTC to demonstrate proficiency, and will then repeat the testing at home via tele-ultrasound.

Interventions

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handheld ultrasound: Philips Lumify integrated tele-ultrasound powered by Reacts collaborative platform

Patients receive training by the physical therapist to operate a handheld ultrasound (HHUS) including proper probe placement. Subjects will be tested on their knowledge at the HTC to demonstrate proficiency, and will then repeat the testing at home via tele-ultrasound.

Intervention Type DEVICE

Eligibility Criteria

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Inclusion Criteria

* Severe hemophilia A
* Male
* Over 18 years of age
* Able to read, write and understand English
* Willing to come to the center for an 8 hour training session
* Lives in proximity of the HTC and is willing to come in for acute joint episodes in phase 2
* Willing and able to follow study procedures
* Willing and able to keep HHUS at a safe place
* Have the dexterity to operate a HHUS unit

Exclusion Criteria

* Unable to follow study instructions
* Physically or mentally unable to operate a HHUS unit
Minimum Eligible Age

18 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Genentech, Inc.

INDUSTRY

Sponsor Role collaborator

Washington Institute for Coagulation

OTHER

Sponsor Role lead

Responsible Party

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Rebecca Kruse-Jarres, MD, MPH

Executive/Medical Director, Washington Center for Bleeding Disorders

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Rebecca Kruse-Jarres, MD, MPH

Role: PRINCIPAL_INVESTIGATOR

Washington Institute for Coagulation

Locations

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Washington Center for Bleeding Disorders at Washington Institute for Coagulation

Seattle, Washington, United States

Site Status

Countries

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United States

References

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Forsyth AL, Giangrande P, Hay CR, Kenet G, Kessler CM, Knobl PN, Llinas A, Santagostino E, Young G. Difficult clinical challenges in haemophilia: international experiential perspectives. Haemophilia. 2012 Jul;18 Suppl 5:39-45. doi: 10.1111/j.1365-2516.2012.02887.x.

Reference Type BACKGROUND
PMID: 22757683 (View on PubMed)

Manco-Johnson MJ, Abshire TC, Shapiro AD, Riske B, Hacker MR, Kilcoyne R, Ingram JD, Manco-Johnson ML, Funk S, Jacobson L, Valentino LA, Hoots WK, Buchanan GR, DiMichele D, Recht M, Brown D, Leissinger C, Bleak S, Cohen A, Mathew P, Matsunaga A, Medeiros D, Nugent D, Thomas GA, Thompson AA, McRedmond K, Soucie JM, Austin H, Evatt BL. Prophylaxis versus episodic treatment to prevent joint disease in boys with severe hemophilia. N Engl J Med. 2007 Aug 9;357(6):535-44. doi: 10.1056/NEJMoa067659.

Reference Type BACKGROUND
PMID: 17687129 (View on PubMed)

Konkle BA, Ebbesen LS, Erhardtsen E, Bianco RP, Lissitchkov T, Rusen L, Serban MA. Randomized, prospective clinical trial of recombinant factor VIIa for secondary prophylaxis in hemophilia patients with inhibitors. J Thromb Haemost. 2007 Sep;5(9):1904-13. doi: 10.1111/j.1538-7836.2007.02663.x.

Reference Type BACKGROUND
PMID: 17723130 (View on PubMed)

Leissinger C, Gringeri A, Antmen B, Berntorp E, Biasoli C, Carpenter S, Cortesi P, Jo H, Kavakli K, Lassila R, Morfini M, Negrier C, Rocino A, Schramm W, Serban M, Uscatescu MV, Windyga J, Zulfikar B, Mantovani L. Anti-inhibitor coagulant complex prophylaxis in hemophilia with inhibitors. N Engl J Med. 2011 Nov 3;365(18):1684-92. doi: 10.1056/NEJMoa1104435.

Reference Type BACKGROUND
PMID: 22047559 (View on PubMed)

Oldenburg J, Mahlangu JN, Kim B, Schmitt C, Callaghan MU, Young G, Santagostino E, Kruse-Jarres R, Negrier C, Kessler C, Valente N, Asikanius E, Levy GG, Windyga J, Shima M. Emicizumab Prophylaxis in Hemophilia A with Inhibitors. N Engl J Med. 2017 Aug 31;377(9):809-818. doi: 10.1056/NEJMoa1703068. Epub 2017 Jul 10.

Reference Type BACKGROUND
PMID: 28691557 (View on PubMed)

Mahlangu et al. Emicizumab prophylaxis administered once-weekly or every two weeks provides effective bleed prevention in persons with haemophilia A without inhibitors - Results from the phase III HAVEN 3 study . Oral presented at the World Federation of Hemophilia Meeting in Glasgow, May 21, 2018.

Reference Type BACKGROUND

Ceponis A, Wong-Sefidan I, Glass CS, von Drygalski A. Rapid musculoskeletal ultrasound for painful episodes in adult haemophilia patients. Haemophilia. 2013 Sep;19(5):790-8. doi: 10.1111/hae.12175. Epub 2013 May 15.

Reference Type BACKGROUND
PMID: 23672827 (View on PubMed)

Zhou JY, Rappazzo KC, Volland L, Barnes RFW, Brackman M, Steiner B, Kruse-Jarres R, Quon DV, Bailey C, Chang EY, von Drygalski A. Pocket handheld ultrasound for evaluation of the bleeding haemophilic joint: A novel and reliable way to recognize joint effusions. Haemophilia. 2018 Mar;24(2):e77-e80. doi: 10.1111/hae.13429. Epub 2018 Feb 12. No abstract available.

Reference Type BACKGROUND
PMID: 29436079 (View on PubMed)

Other Identifiers

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ML41066

Identifier Type: -

Identifier Source: org_study_id

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