Home Monitoring in Hemophilia a

NCT ID: NCT06702579

Last Updated: 2024-11-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Total Enrollment

30 participants

Study Classification

OBSERVATIONAL

Study Start Date

2024-10-30

Study Completion Date

2025-11-01

Brief Summary

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Rationale: A novel point-of-care device capable of measuring factor VIII (FVIII) activity and thrombin generation (TG) is currently under development. Utilization of this device in a home situation could potentially transform hemophilia care and improve patients' autonomy.

Objective: To explore the potential consequences of home monitoring of hemostatic parameters in patients with hemophilia A

Study design: Cross-sectional observational study consisting of semi-structured interviews and focus groups

Study population: Approximately 10 patients treated with vitamin K antagonists engaging in self-monitoring of coagulation at home and approximately 20 patients with hemophilia A.

Main study parameters/endpoints: The main outcome of this study is to assess series of interrelated themes related to the unmet needs of hemophilia patients and the envisioned potential consequences of home monitoring on these unmet needs.

Secondary outcomes include: identifying key features of a home monitoring platform to be used in hemophilia care, describing the experienced consequences of implementing home self-monitoring in anticoagulation treatment, assessing the current experiences of patients with self-monitoring, and providing an overview of the burdens and unmet needs experienced by patients with hemophilia with current hemophilia care.

Nature and extent of the burden and risks associated with participation, benefit and group relatedness: The risk associated with participation in this study is negligible. Minor patients will be included in this study only if informed consent is given by both the patient and his/her caregiver (in patients between 12-16 years old). Gathering the insights of caregivers of minor patients on the current care for hemophilia and potential consequences of home self-monitoring is vital, as their experiences and needs might differ significantly from older patients. Participating in this study does not entail direct benefits. However, patients who participate can contribute to the development of future monitoring systems, which have the potential to alleviate the current burden of their disease and treatment.

Detailed Description

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Conditions

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Hemophilia a Anticoagulant Therapy Monitoring Point of Care Testing Qualitative Research

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

CROSS_SECTIONAL

Study Groups

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Patients receiving anticoagulation therapy

Adult patients on anticoagulation therapy who perform INR self-testing at home.

No interventions assigned to this group

Hemophilia A

Patients over 12 years old with congenital hemophilia A receiving prophylactic therapy.

No interventions assigned to this group

Healthcare professionals

Hematologists, hemophilia nurses, pharmacists or other healthcare providers currently involved in the care for patients with hemophilia.

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

* Aged \> 16 years
* Patient using vitamin K antagonist for any indication
* Registered at the "Trombosezorg dichterbij"
* Self-testing INR at home for \> 3 months
* A history of monitoring INR at a care facility (not self-testing)
* Signed informed consent form
* Able to speak and understand Dutch or English without a translator


* Diagnosis of congenital hemophilia A, with or without inhibitors
* Receiving prophylactic treatment
* Patients aged ≥ 12 years or caregivers of patients aged \< 12 years old
* Signed informed consent form

* Hematologist, hemophilia nurse, pharmacist or healthcare provider currently involved in the care for patients with hemophilia
* At least \> 3 years clinical experience in hemophilia care
* Signed informed consent form
* Able to speak and understand Dutch or English without a translator

Exclusion Criteria

• Unwilling to consent with the study or with audio recording

* No diagnosis of congenital hemophilia A
* Unwilling to consent with the study or with audio recording
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Radboud University Medical Center

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Radboudumc

Nijmegen, Gelderland, Netherlands

Site Status RECRUITING

Countries

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Netherlands

Facility Contacts

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Aernoud Bavinck, MD

Role: primary

+31 24 361 1111

Other Identifiers

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HEMSTOL85

Identifier Type: -

Identifier Source: org_study_id

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