Case and Use Scenario Study to Gain Knowledge on the User Needs for a Medical Device for Hemophilia a Monitoring

NCT ID: NCT06369740

Last Updated: 2024-10-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

74 participants

Study Classification

OBSERVATIONAL

Study Start Date

2024-08-22

Study Completion Date

2024-08-25

Brief Summary

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This observational study consists of two parts.

In part one, case scenario focus groups with hemophilia A patients and healthcare providers (HCPs) will be held. This parts aims to identify potential use scenarios of a point of care (POC) in vitro medical for patients with hemophilia A. The main questions it aims to answer are:

* How is coagulation lab testing for patients with hemophilia A currently organized?
* What is the interest and what are desired alternatives of a POC in-vitro diagnostic medical device for patients with hemophilia A?

Part two of the study consists of a use scenario study in which patients with hemophilia A and HCPs will evaluate two types of non-functional mock-ups of a POC in vitro medical device. The main goal of this part is to evaluate the usability of the current prototypes of the POC device.

Detailed Description

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Conditions

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Hemophilia a

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

CROSS_SECTIONAL

Study Groups

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Hemophilia A patients - case scenario focus groups

60 patients with hemophilia A aged 12 years and older that partake in the case scenario focus groups

Case scenarios - questionnaire

Intervention Type OTHER

Participants fill in a questionnaire on the current care of hemophilia A and envisioned use scenarios of a point-of-care diagnostic device for hemophilia A.

Case scenarios - Focus groups

Intervention Type OTHER

Participants partake in focus groups on the current care for hemophilia A, the envisioned use scenarios of point-of-care diagnostic device for hemophilia A and desired features of such a diagnostic device.

Healthcare providers - case scenario focus groups

30 healthcare providers with experience in the field of hemophilia A that partake in the case scenario focus groups

Case scenarios - questionnaire

Intervention Type OTHER

Participants fill in a questionnaire on the current care of hemophilia A and envisioned use scenarios of a point-of-care diagnostic device for hemophilia A.

Case scenarios - Focus groups

Intervention Type OTHER

Participants partake in focus groups on the current care for hemophilia A, the envisioned use scenarios of point-of-care diagnostic device for hemophilia A and desired features of such a diagnostic device.

Hemophilia A patients - use scenarios

6 patients with hemophilia A aged 12 years and older that partake in the use scenarios usability evaluation

Use scenarios - Usability test

Intervention Type OTHER

Participants are asked to perform basic tasks with the mock-ups with minimal instructions, they will also be given a graphic of the user interface (GUI).

Use scenarios - interview

Intervention Type OTHER

The participants will be interviewed and asked for their opinions and experiences with the mock-ups.

Healthcare providers - use scenarios

6 healthcare providers with experience in the field of hemophilia A that partake in the use scenarios usability evaluation

Use scenarios - Usability test

Intervention Type OTHER

Participants are asked to perform basic tasks with the mock-ups with minimal instructions, they will also be given a graphic of the user interface (GUI).

Use scenarios - interview

Intervention Type OTHER

The participants will be interviewed and asked for their opinions and experiences with the mock-ups.

Interventions

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Case scenarios - questionnaire

Participants fill in a questionnaire on the current care of hemophilia A and envisioned use scenarios of a point-of-care diagnostic device for hemophilia A.

Intervention Type OTHER

Case scenarios - Focus groups

Participants partake in focus groups on the current care for hemophilia A, the envisioned use scenarios of point-of-care diagnostic device for hemophilia A and desired features of such a diagnostic device.

Intervention Type OTHER

Use scenarios - Usability test

Participants are asked to perform basic tasks with the mock-ups with minimal instructions, they will also be given a graphic of the user interface (GUI).

Intervention Type OTHER

Use scenarios - interview

The participants will be interviewed and asked for their opinions and experiences with the mock-ups.

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

Patients:

* With Hemophilia A diagnosis
* All Hemophilia A severity categories are eligible (mild, moderate, or severe)
* Aged 12 years and older
* For children aged 12 through 17 their parent must provide permission by signing the informed consent form
* Consider English their primary language (capable of communicating in English verbally and in writing)
* Capable of giving informed consent or assent

Family member(s) of patients:

* Related to a patient with Hemophilia A (mild, moderate, or severe)
* Aged 18 years and older
* Consider English their primary language (capable of communicating in English verbally and in writing)
* Capable of giving informed consent or assent

Healthcare professionals:

* Healthcare workers specialized in hemophilia care. (e.g. hematologists, nurse practitioners, physician assistants, nurses, and pharmacists)
* Capable of giving informed consent

Exclusion Criteria

Patients:

* Without a diagnosis of Hemophilia A
* With acquired Hemophilia A
* Younger than 12 years of age
* Unable to communicate in English
* Incapable of giving consent or assent for themselves

Specifically for the case scenario focus group

* Unwilling to consent to voice recording
* Participating in the use scenario part of the study

Specifically for the use scenario part of the study

* Unwilling to consent to video recording
* Participating in the case scenario part of the study

Family members:

* No relation to a patient with Hemophilia A (mild, moderate, or severe)
* Related to a patient with acquired Hemophilia A
* Younger than 18 years of age
* Unable to communicate in English
* Incapable of giving consent or assent for themselves

Specifically for the case scenario focus group

* Unwilling to consent to voice recording
* Participating in the use scenario part of the study

Specifically for the use scenario part of the study

* Unwilling to consent to video recording
* Participating in the case scenario part of the study

Healthcare professionals:

* Without any prior hematological experience
* Not licensed as hematologists, nurse practitioners, physician assistants, nurses or pharmacists
* Unable to communicate in English
* Incapable of giving their consent to participate

Specifically for the case scenario part of the study • Unwilling to consent to voice recording

Specifically for the use scenario part of the study

• Unwilling to consent to video recording
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Indiana Hemophilia & Thrombosis Center

UNKNOWN

Sponsor Role collaborator

Enzyre B.V.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Indiana Hemophilia & Thrombosis Center

Indianapolis, Indiana, United States

Site Status

Countries

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United States

Other Identifiers

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ENZ20-2024-INDIANAPOLIS

Identifier Type: -

Identifier Source: org_study_id

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