A Study to Evaluate Efficacy and Safety of Perampanel Administered as an Adjunctive Therapy in Pediatric Participants With Childhood Epilepsy

NCT ID: NCT04015141

Last Updated: 2025-10-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

100 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-05-31

Study Completion Date

2027-12-23

Brief Summary

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The purpose of the study is to evaluate the efficacy of perampanel as measured by the 50 percent (%) responder rate during the maintenance period of the core study for seizure frequency in participants with pediatric epileptic syndrome (Cohort 1) and partial-onset seizures (POS) (Cohort 2).

Detailed Description

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This study will consist of a Core Study, Extension Phase A and Extension Phase B.

1. Core Study will consist of the following 2 phases: Pretreatment (4 weeks screening or baseline period) and Treatment Period. The Treatment Period (23 weeks) of Core study include Titration period (10 weeks) and Maintenance period (13 weeks).
2. Extension Phase A will consist of a Treatment Period (33 weeks) and a Follow-up Period (4 weeks). All participants who will complete the Core Study will be eligible to participate in Extension Phase A of the study.
3. Extension Phase B will only be for participants who reside in countries where perampanel (oral tablets or oral suspension) is not commercially available or an extended access program (EAP) is not yet implemented, participants have completed Extension Phase A, and who, in the opinion of the investigator, will continue to benefit from treatment with perampanel.

Conditions

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Pediatric Epileptic Syndrome Partial-onset Seizures

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Perampanel

Participants aged 1 month to less than 18 years with pediatric epileptic syndrome (Cohort 1) or aged 1 month to less than 2 years with POS (Cohort 2) will receive perampanel oral suspension or perampanel tablets, once daily up to 56 weeks.

Group Type EXPERIMENTAL

Perampanel Oral Suspension

Intervention Type DRUG

Perampanel oral suspension.

Perampanel Tablet

Intervention Type DRUG

Perampanel tablet.

Interventions

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Perampanel Oral Suspension

Perampanel oral suspension.

Intervention Type DRUG

Perampanel Tablet

Perampanel tablet.

Intervention Type DRUG

Other Intervention Names

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E2007 Fycompa E2007 Fycompa

Eligibility Criteria

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Inclusion Criteria

* Male or female participants. Cohort 1: age 1 month to less than 18 years; Cohort 2: age 1 month to less than 2 years at the time of informed consent/assent. Participants below the age of 1 year must have been at least 36 weeks of gestational age at birth.
* Have a diagnosis of epilepsy with a pediatric epileptic syndrome (Cohort 1) or epilepsy with POS with or without secondary generalization (Cohort 2).
* Have had equal or greater than 4 seizures over the 4-week interval prior to enrollment visit.
* Absence of any progressive cause of epilepsy that has been confirmed clinically or based on brain imaging (example, magnetic resonance imaging \[MRI\] scan or computed tomography \[CT\] or ultrasound \[for less than 1 year old\]).
* Currently maintained on stable doses of 1 to a maximum of 4 approved antiepileptic drugs (AEDs). A prescription medical marijuana (including products containing cannabidiol) is counted as 1 of the maximum of 4 allowed AEDs; however, it cannot be the only concomitant AED if this product is not an approved AED in the country where the study site is located. Doses must be stable for at least 4 weeks (at least 2 weeks for participant less than \[\<\] 6 months old) before Visit 1/Baseline or screening; only 1 enzyme-inducing antiepileptic drug (EIAED) (defined as carbamazepine, phenytoin, oxcarbazepine, or eslicarbazepine) out of the maximum of 4 AEDs is allowed.

Exclusion Criteria

* Current or history of pseudo-seizures (psychogenic nonepileptic seizures) within approximately 5 years before screening visit.
* Have a history of status epilepticus that required hospitalization within 6 months before screening visit.
* Have an unstable psychiatric diagnosis that may confound participant's ability to participate in the study or that may prevent completion of the protocol specified tests (example, significant suicide risk, including suicidal behavior and ideation within 6 months before screening visit 1, current psychotic disorder, acute mania).
* Any suicidal ideation with intent with or without a plan within 6 months before enrollment visit (answering "Yes" to questions 4 or 5 on the Suicidal Ideation section of the C-SSRS) in participants aged 6 and above or based on the opinion of the Investigator for participants less than 6 years.
* Are scheduled or confirmed or both to have epilepsy surgery within 6 months after screening visit; however, those who have previously documented "failed" epilepsy surgery will be allowed.
* Have a progressive central nervous system (CNS) disease, including degenerative CNS diseases and progressive tumors.
* Benzodiazepines for any indications other than epilepsy (example, anxiety/sleep disorders) prohibited from 1 month before Visit 1/Baseline or screening and during the study. Benzodiazepines for seizure control and as rescue medication are allowed.
* A vagal nerve stimulator (VNS), responsive neurostimulator (RNS), or deep brain stimulator (DBS) implanted less than 5 months before screening visit or changes in parameter less than 4 weeks before screening visit (or thereafter during the study).
* Use of perampanel within 30 days before screening visit, or perampanel was discontinued due to adverse reactions (perampanel-related) or lack of efficacy in case of previous exposure.
* Weight less than 4.0 kilogram (kg) at Visit 1 (Baseline or screening).
Minimum Eligible Age

1 Month

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eisai Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Phoenix Childrens Hospital

Phoenix, Arizona, United States

Site Status WITHDRAWN

Center For Neurosciences

Tucson, Arizona, United States

Site Status WITHDRAWN

David Geffen School of Medicine at UCLA

Los Angeles, California, United States

Site Status RECRUITING

Childrens Hospital Colorado

Aurora, Colorado, United States

Site Status ACTIVE_NOT_RECRUITING

Nemours Foundation Alfred Dupont Children's Hospital

Wilmington, Delaware, United States

Site Status WITHDRAWN

Nicklaus Children's Hospital

Miami, Florida, United States

Site Status TERMINATED

Pediatric Neurology PA

Orlando, Florida, United States

Site Status WITHDRAWN

Pediatric Epilepsy and Neurology Specialists

Tampa, Florida, United States

Site Status RECRUITING

PANDA Neurology

Atlanta, Georgia, United States

Site Status WITHDRAWN

Meridian Clinical Research-(Savannah Georgia)

Savannah, Georgia, United States

Site Status COMPLETED

Children's Hospital of Michigan

Detroit, Michigan, United States

Site Status COMPLETED

Northeast Regional Epilepsy Group

Hackensack, New Jersey, United States

Site Status COMPLETED

Columbia University Medical Center

New York, New York, United States

Site Status WITHDRAWN

Wake Forest Baptist Medical Center - PPDS

Winston-Salem, North Carolina, United States

Site Status ACTIVE_NOT_RECRUITING

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status COMPLETED

Dayton Children's Hospital

Dayton, Ohio, United States

Site Status COMPLETED

Doernbecher Children's Hospital

Portland, Oregon, United States

Site Status WITHDRAWN

Child Neurology Consultants of Austin

Austin, Texas, United States

Site Status COMPLETED

Road Runner Research Ltd

San Antonio, Texas, United States

Site Status RECRUITING

Children's Specialty Group

Norfolk, Virginia, United States

Site Status COMPLETED

Children's Hospital of Richmond at VCU - CHoR-PIN

Richmond, Virginia, United States

Site Status COMPLETED

Seattle Children's Hospital

Seattle, Washington, United States

Site Status RECRUITING

Centre Neurologique William Lennox

Ottignies, Brabant Wallon, Belgium

Site Status COMPLETED

Cliniques Universitaires Saint-Luc

Brussels, Brussels Capital, Belgium

Site Status WITHDRAWN

H�pital Universitaire des Enfants Reine Fabiola

Brussels, Brussels Capital, Belgium

Site Status RECRUITING

UZ Brussel

Brussels, Brussels Capital, Belgium

Site Status COMPLETED

UZ Gent

Ghent, Oost-Vlaanderen, Belgium

Site Status COMPLETED

H�pital Erasme

Anderlecht, , Belgium

Site Status WITHDRAWN

Fakultni nemocnice Brno

Brno, , Czechia

Site Status COMPLETED

Fakultni nemocnice Ostrava

Ostrava, , Czechia

Site Status WITHDRAWN

Fakultni nemocnice Plzen

Pilsen, , Czechia

Site Status WITHDRAWN

Aarhus Universitetshospital

Aarhus N, Central Jutland, Denmark

Site Status WITHDRAWN

Regionshospitalet Randers

Randers, , Denmark

Site Status WITHDRAWN

Hopitaux de La Timone

Marseille, Bouches-du-Rhone, France

Site Status COMPLETED

H�pital Pellegrin-Enfants

Bordeaux, , France

Site Status COMPLETED

Hopital Necker

Paris, , France

Site Status RECRUITING

Hopitaux de Paris CHU Hopital Robert Debre - Inserm U676

Paris, , France

Site Status RECRUITING

CHRU Rennes

Rennes, , France

Site Status ACTIVE_NOT_RECRUITING

Centre Hospitalier Universitaire de Toulouse

Toulouse, , France

Site Status RECRUITING

Universit�tsklinikum Freiburg

Freiburg im Breisgau, , Germany

Site Status COMPLETED

Universit�tsklinikum Jena

Jena, , Germany

Site Status COMPLETED

Dr. Von Haunersches Kinderspital

Munich, , Germany

Site Status COMPLETED

Kleinwachau S�chsisches Epilepsiezentrum Radeberg Gemeinn�tzige Gmbh

Radeberg, , Germany

Site Status COMPLETED

Centro Medico Teknon � Grupo Quironsalud

Barcelona, , Spain

Site Status WITHDRAWN

Hospital Clinico San Carlos

Madrid, , Spain

Site Status COMPLETED

Hospital General Universitario Gregorio Mara�on

Madrid, , Spain

Site Status RECRUITING

Complejo Hospitalario de Navarra

Pamplona, , Spain

Site Status RECRUITING

CHUS � H. Clinico U. de Santiago

Santiago de Compostela, , Spain

Site Status RECRUITING

Hospital Universitario Virgen del Rocio - PPDS

Seville, , Spain

Site Status RECRUITING

Countries

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United States Belgium Czechia Denmark France Germany Spain

Central Contacts

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Eisai Medical Information

Role: CONTACT

+1-888-274-2378

Other Identifiers

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2018-004456-38

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

E2007-G000-236

Identifier Type: -

Identifier Source: org_study_id

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