Evaluation of the Efficacy and Safety of E2007 (Perampanel) Given as Adjunctive Therapy in Subjects With Refractory Partial Seizures

NCT ID: NCT00735397

Last Updated: 2016-03-14

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1218 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-10-31

Study Completion Date

2014-09-30

Brief Summary

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The purpose of this study was to evaluate the safety and tolerability of perampanel (up to 12 mg/day) given as adjunctive treatment in subjects with refractory partial seizures and to evaluate the maintenance of effect of perampanel for the control of refractory partial seizures.

Detailed Description

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This was an open-label extension (OLE) study for subjects who completed one of the following double-blind, placebo-controlled, Phase 3 studies: E2007-G000-304 (NCT00699972), E2007-G000-305 (NCT00699582), and E2007-G000-306 (NCT00700310). This OLE study consisted of 2 phases: an Open-label Treatment Phase (comprised of a 16-week blinded Conversion Period and a 256-week Maintenance Period) and a Follow-up Phase (4 weeks). During the Conversion Period, subjects and investigators remained blinded to the treatment received in the previous DB study. To achieve this, all subjects continued to take 6 tablets of study medication (2 mg perampanel or matching placebo) or fewer as they were instructed during the core Double-Blind (DB) study. During the open-label Maintenance Period, subjects were treated with the perampanel dose that provided the best combination of individual efficacy and tolerability.

Conditions

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Epilepsy

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Perampanel

Participants previously receiving perampanel/placebo in the double blind-study, were titrated to receive perampanel 2 mg to 12 mg, once daily in the Open-Label Extension (OLE) study up to approximately 5 years.

Group Type EXPERIMENTAL

perampanel

Intervention Type DRUG

Perampanel 2 mg to 12 mg, once daily in the Open-Label Extension (OLE) study up to approximately 5 years

Interventions

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perampanel

Perampanel 2 mg to 12 mg, once daily in the Open-Label Extension (OLE) study up to approximately 5 years

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Each participant who met the following criteria were enrolled in this study:

Exclusion Criteria

2. Provided written informed consent signed by participant or legal guardian prior to entering the study or undergoing any study procedures (If the written informed consent was provided by the legal guardian because the participant was unable to do so, a written or verbal assent from the participant was obtained).
3. Who was considered reliable and willing to be available for the study period and record seizures and report adverse events them self or have a caregiver who can record and report the events for them.
4. Females who were either of non-childbearing potential (defined as having undergone surgical sterilization, or postmenopausal \[\>age 50 and amenorrheic for 12 months\]) or of childbearing potential. Females of childbearing potential were enrolled only if they agreed to be abstinent or continue using at least 1 medically acceptable method of contraception (eg, a double-barrier method \[eg, condom + spermicide, condom + diaphragm with spermicide\], IUD, or have a vasectomised partner) throughout the study period and for 2 months after the last dose of study drug. Women using hormonal contraceptives were required to use an additional approved method of contraception (as described previously) continuously throughout the entire study period and for 2 months after the last dose of study drug. (It was not required for male subjects to use contraceptive measures based on preclinical toxicology data).
5. Continued to be treated with a stable dose of 1 or a maximum of 3 approved anti-epileptic drugs.


Participants who met the following criteria were excluded from the study:

1\. Those who, for any reason, discontinued early from the preceding double-blind study.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eisai Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Michelle Gee, PhD.

Role: STUDY_DIRECTOR

Eisai Limited

Locations

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Birmingham, Alabama, United States

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Little Rock, Arkansas, United States

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Fresno, California, United States

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San Francisco, California, United States

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Ventura, California, United States

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Denver, Colorado, United States

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Fort Collins, Colorado, United States

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Washington D.C., District of Columbia, United States

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Gulf Breeze, Florida, United States

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Jacksonville, Florida, United States

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Jacksonville, Florida, United States

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Orlando, Florida, United States

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Tallahassee, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Suwanee, Georgia, United States

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Boise, Idaho, United States

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Indianapolis, Indiana, United States

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Ames, Iowa, United States

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Lexington, Kentucky, United States

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Houma, Louisiana, United States

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Baltimore, Maryland, United States

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Bethesda, Maryland, United States

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Hattiesburg, Mississippi, United States

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Chesterfield, Missouri, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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Albany, New York, United States

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Buffalo, New York, United States

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Great Neck, New York, United States

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Lawrence, New York, United States

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New York, New York, United States

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Rochester, New York, United States

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Syracuse, New York, United States

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Asheville, North Carolina, United States

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Akron, Ohio, United States

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Cincinnati, Ohio, United States

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Columbus, Ohio, United States

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Toledo, Ohio, United States

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Tulsa, Oklahoma, United States

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Portland, Oregon, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Charleston, South Carolina, United States

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Memphis, Tennessee, United States

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Dallas, Texas, United States

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Dallas, Texas, United States

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Dallas, Texas, United States

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El Paso, Texas, United States

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Houston, Texas, United States

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Salt Lake City, Utah, United States

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Richmond, Virginia, United States

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Seattle, Washington, United States

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Madison, Wisconsin, United States

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Capital Federal, , Argentina

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Córdoba, , Argentina

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Córdoba, , Argentina

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La Plata, Buenos Aires, , Argentina

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Lanus Oeste, Buenos Aires, , Argentina

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Rosario, , Argentina

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Salta, , Argentina

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San Miguel de Tucumán, , Argentina

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Villa Nueva, , Argentina

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Woodville, South Australia, Australia

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Fitzroy, Victoria, Australia

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Heidelberg, Victoria, Australia

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Parkville, Victoria, Australia

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Graz, , Austria

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Innsbruck, , Austria

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Linz, , Austria

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Brussels, , Belgium

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Leuven, , Belgium

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Ottignies, , Belgium

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Pleven, , Bulgaria

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Plovdiv, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Calgary, Alberta, Canada

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London, Ontario, Canada

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Toronto, Ontario, Canada

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Greenfield Park, Quebec, Canada

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Santiago, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Valdivia, , Chile

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Beijing, , China

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Chengdu, , China

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Chongqing, , China

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Shanghai, , China

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Olomouc, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Tallinn, , Estonia

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Tartu, , Estonia

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Kuopio, , Finland

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Tampere, , Finland

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Béthune, , France

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Bron, , France

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Montpellier, , France

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Rennes, , France

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Toulouse, , France

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Berlin, , Germany

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Bernau, , Germany

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Bielefeld, , Germany

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Bonn, , Germany

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Düsseldorf, , Germany

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Erlangen, , Germany

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Göttingen, , Germany

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Kehl-Kork, , Germany

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Mainz, , Germany

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Marburg, , Germany

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München, , Germany

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Ulm, , Germany

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Westerstede, , Germany

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Thessaloniki, , Greece

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Thessaloniki, , Greece

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Hong Kong, , Hong Kong

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Kowloon, , Hong Kong

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Pokfulam, , Hong Kong

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Shatin, , Hong Kong

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Kecskemét, , Hungary

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Hyderabad, , India

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Hyderabad, , India

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Jaipur, , India

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Mangalore, , India

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Mumbai, , India

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Nagpur, , India

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Nashik, , India

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New Delhi, , India

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Pune, , India

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Pune, , India

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Visakhapatnam, , India

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Ashkelon, , Israel

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Haifa, , Israel

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Holon, , Israel

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Kfar Saba, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Florence, , Italy

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Genova, , Italy

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Milan, , Italy

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Milan, , Italy

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Napoli, , Italy

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Riga, , Latvia

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Riga, , Latvia

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Valmiera, , Latvia

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Kaunas, , Lithuania

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Klaipėda, , Lithuania

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Vilnius, , Lithuania

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Kuala Lumpur, , Malaysia

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Kuala Terengganu, , Malaysia

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Aguascalientes, , Mexico

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Mexico City, Distrito Federal, , Mexico

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Monterrey, Nuevo Leon, , Mexico

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San Luis Potosí City, , Mexico

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Heeze, , Netherlands

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Zwolle, , Netherlands

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Ermita, , Philippines

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Makati City, , Philippines

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Bialystok, , Poland

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Gdansk, , Poland

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Gdansk, , Poland

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Katowice, , Poland

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Lublin, , Poland

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Warsaw, , Poland

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Coimbra, , Portugal

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Lisbon, , Portugal

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Porto, , Portugal

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Bucharest, , Romania

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Bucharest, , Romania

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Kazan', , Russia

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Nizhny Novgorod, , Russia

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Omsk, , Russia

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Samara, , Russia

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Smolensk, , Russia

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Tyumen, , Russia

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Yaroslavl, , Russia

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Yekaterinburg, , Russia

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Belgrade, , Serbia

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Niš, , Serbia

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Novi Sad, , Serbia

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Johannesburg, Gauteng, South Africa

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Cape Town, Western Cape, South Africa

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Cape Town, , South Africa

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Busan, , South Korea

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Daegu, , South Korea

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Pusan, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Granada, Andalusia, Spain

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Barakaldo, Basque Country, Spain

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Badalona, Catalonia, Spain

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Barcelona, Catalonia, Spain

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Barcelona, Catalonia, Spain

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Alcorcón, Madrid, Communidad de, Spain

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Madrid, Madrid, Communidad de, Spain

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Valencia, Valencia, Spain

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Gothenburg, , Sweden

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Linköping, , Sweden

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Kaohsiung City, , Taiwan

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Taichung, , Taiwan

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Tainan City, , Taiwan

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Taoyuan District, , Taiwan

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Chiang Mai, , Thailand

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Muang, , Thailand

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Donetsk, , Ukraine

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Donetsk, , Ukraine

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Kharkiv, , Ukraine

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Kharkiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Lviv, , Ukraine

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Uzhhorod, , Ukraine

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Liverpool, , United Kingdom

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London, , United Kingdom

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Middlesbrough, , United Kingdom

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Stoke-on-Trent, , United Kingdom

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Countries

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United States Argentina Australia Austria Belgium Bulgaria Canada Chile China Czechia Estonia Finland France Germany Greece Hong Kong Hungary India Israel Italy Latvia Lithuania Malaysia Mexico Netherlands Philippines Poland Portugal Romania Russia Serbia South Africa South Korea Spain Sweden Taiwan Thailand Ukraine United Kingdom

References

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Maguire M. Response to "Perampanel and pregnancy: Could experience be a gloomy lantern that does not even illuminate its bearer?". Epilepsy Behav. 2022 Apr;129:108654. doi: 10.1016/j.yebeh.2022.108654. Epub 2022 Mar 16. No abstract available.

Reference Type DERIVED
PMID: 35305920 (View on PubMed)

Krauss GL, Perucca E, Kwan P, Ben-Menachem E, Wang XF, Shih JJ, Patten A, Yang H, Williams B, Laurenza A. Final safety, tolerability, and seizure outcomes in patients with focal epilepsy treated with adjunctive perampanel for up to 4 years in an open-label extension of phase III randomized trials: Study 307. Epilepsia. 2018 Apr;59(4):866-876. doi: 10.1111/epi.14044. Epub 2018 Mar 25.

Reference Type DERIVED
PMID: 29574701 (View on PubMed)

Rosenfeld W, Conry J, Lagae L, Rozentals G, Yang H, Fain R, Williams B, Kumar D, Zhu J, Laurenza A. Efficacy and safety of perampanel in adolescent patients with drug-resistant partial seizures in three double-blind, placebo-controlled, phase III randomized clinical studies and a combined extension study. Eur J Paediatr Neurol. 2015 Jul;19(4):435-45. doi: 10.1016/j.ejpn.2015.02.008. Epub 2015 Mar 5.

Reference Type DERIVED
PMID: 25823975 (View on PubMed)

Krauss GL, Perucca E, Ben-Menachem E, Kwan P, Shih JJ, Clement JF, Wang X, Bagul M, Gee M, Zhu J, Squillacote D. Long-term safety of perampanel and seizure outcomes in refractory partial-onset seizures and secondarily generalized seizures: results from phase III extension study 307. Epilepsia. 2014 Jul;55(7):1058-68. doi: 10.1111/epi.12643. Epub 2014 May 27.

Reference Type DERIVED
PMID: 24867391 (View on PubMed)

Other Identifiers

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E2007-G000-307

Identifier Type: -

Identifier Source: org_study_id

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