A Study With an Open-label Extension Phase to Evaluate the Efficacy and Safety of Perampanel (E2007) Administered as an Adjunctive Therapy in Subjects With Refractory Partial-onset Seizures

NCT ID: NCT01618695

Last Updated: 2021-07-29

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

940 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-05-15

Study Completion Date

2020-05-28

Brief Summary

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The purpose of this study is to confirm the efficacy and safety of perampanel compared to placebo in patients with refractory partial-onset seizures

Detailed Description

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Conditions

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Partial-onset Seizures

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Perampanel

Group Type EXPERIMENTAL

Perampanel

Intervention Type DRUG

Core study: 4 milligram (mg) group- Week 0 Once daily 2 milligram per day (mg/day), Week 1 to Week 18 Once daily 4 mg/day; 8 mg group- Week 0 Once daily 2 mg/day, Week 1 Once daily 4 mg/day, Week 2 Once daily 6 mg/day, Week 3 to Week 18 Once daily 8 mg/day; 12 mg group- Week 0 Once daily 2 mg/day, Week 1 Once daily 4 mg/day, Week 2 Once daily 6 mg/day, Week 3 Once daily 8 mg/day, Week 4 Once daily 10 mg/day, Week 5 to Week 18 Once daily 12 mg/day.

Extension study: 4 mg group- Week 19 to Week 22 Once daily 4 mg/day, Week 23 Once daily 6 mg/day, Week 24 Once daily 8 mg/day, Week 25 Once daily 10 mg/day, Week 26 to Week 75 or more Once daily 12 mg/day; 8 mg group- Week 19 to Week 22 Once daily 8 mg/day, Week 23 Once daily 10 mg/day, Week 24 to Week 75 or more Once daily 12 mg/day; 12 mg group- Week 19 to Week 75 or more Once daily 12 mg/day.

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Core study: Week 0 to Week 18 Once daily placebo.

Extension study:

Week 19 to Week 22 Once daily placebo, Week 23 Once daily perampanel 2 mg/day, Week 24 Once daily perampanel 4 mg/day, Week 25 Once daily perampanel 6 mg/day, Week 26 Once daily perampanel 8 mg/day, Week 27 Once daily perampanel 10 mg/day, Week 28 to Week 75 or more Once daily perampanel 12 mg/day.

Interventions

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Perampanel

Core study: 4 milligram (mg) group- Week 0 Once daily 2 milligram per day (mg/day), Week 1 to Week 18 Once daily 4 mg/day; 8 mg group- Week 0 Once daily 2 mg/day, Week 1 Once daily 4 mg/day, Week 2 Once daily 6 mg/day, Week 3 to Week 18 Once daily 8 mg/day; 12 mg group- Week 0 Once daily 2 mg/day, Week 1 Once daily 4 mg/day, Week 2 Once daily 6 mg/day, Week 3 Once daily 8 mg/day, Week 4 Once daily 10 mg/day, Week 5 to Week 18 Once daily 12 mg/day.

Extension study: 4 mg group- Week 19 to Week 22 Once daily 4 mg/day, Week 23 Once daily 6 mg/day, Week 24 Once daily 8 mg/day, Week 25 Once daily 10 mg/day, Week 26 to Week 75 or more Once daily 12 mg/day; 8 mg group- Week 19 to Week 22 Once daily 8 mg/day, Week 23 Once daily 10 mg/day, Week 24 to Week 75 or more Once daily 12 mg/day; 12 mg group- Week 19 to Week 75 or more Once daily 12 mg/day.

Intervention Type DRUG

Placebo

Core study: Week 0 to Week 18 Once daily placebo.

Extension study:

Week 19 to Week 22 Once daily placebo, Week 23 Once daily perampanel 2 mg/day, Week 24 Once daily perampanel 4 mg/day, Week 25 Once daily perampanel 6 mg/day, Week 26 Once daily perampanel 8 mg/day, Week 27 Once daily perampanel 10 mg/day, Week 28 to Week 75 or more Once daily perampanel 12 mg/day.

Intervention Type DRUG

Other Intervention Names

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E2007

Eligibility Criteria

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Inclusion Criteria

1. Male or female and greater than or equal to 12 years of age;
2. Have a diagnosis of epilepsy with partial seizures with or without secondarily generalized seizures
3. Participants with computed tomography (CT) or magnetic resonance imaging (MRI) diagnosis within the last 10 years (for adults) and 5 years (for adolescents) prior to visit 1 that ruled out progressive central nervous system (CNS) disorders, example, neurodegenerative disorders, brain tumors. For participants without existing CT or MRI results, CT or MRI was performed at or after Visit 1 but results evaluation was performed by Visit 2
4. Participants who had been treated for at least 12 weeks but confirmed to be uncontrolled with more than one standard antiepileptic drug (AED) for 2 years before enrollment
5. During the 6-week Prerandomization Phase participants must have had greater than or equal to 5 partial seizures per 6-week
6. Are currently being treated with stable doses and administrations of 1, 2, or a maximum of 3 approved AEDs. Only 1 inducer AED (defined as carbamazepine, phenytoin or oxcarbazepine only) out of the maximum of 3 AEDs is allowed

Exclusion Criteria

1. Presence of nonmotor simple partial seizures only;
2. Presence of primary generalized epilepsies or seizures, such as absences and/or myoclonic epilepsies;
3. Presence or previous history of Lennox-Gastaut syndrome;
4. A history of status epilepticus within 1 year prior to screening
5. Seizure clusters where individual seizures cannot be counted
6. A history of psychogenic seizures within 5 years prior to screening
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eisai Co., Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Facility #1

Bedford Park, , Australia

Site Status

Facility #1

Camperdown, , Australia

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Clayton, , Australia

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Fitzroy, , Australia

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Heidelberg, , Australia

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Melbourne, , Australia

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Randwick, , Australia

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Beijing, Beijing Municipality, China

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Chongqing, Chongqing Municipality, China

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Xiamen, Fujian, China

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Guangzhou, Guangdong, China

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Guangzhou, Guangdong, China

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Harbin, Heilongjiang, China

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Changchun, Jilin, China

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Xi'an, Shaanxi, China

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Xi'an, Shaanxi, China

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Xi'an, Shaanxi, China

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Taiyuan, Shan'xi, China

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Jinan, Shandong, China

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Jinan, Shandong, China

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Qingdao, Shandong, China

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Shanghai, Shanghai Municipality, China

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Shanghai, Shanghai Municipality, China

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Shanghai, Shanghai Municipality, China

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Chengdu, Sichuan, China

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Chengdu, Sichuan, China

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Tianjin, Tianjin Municipality, China

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Kunming, Yunnan, China

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Facility #1

Wenzhou, Zhejiang, China

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Eisai Trial Site #1

Nagoya, Aichi-ken, Japan

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Eisai Trial Site #2

Nagoya, Aichi-ken, Japan

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Eisai Trial Site #3

Nagoya, Aichi-ken, Japan

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Eisai Trial Site #1

Tōon, Ehime, Japan

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Eisai Trial Site #1

Yoshida-gun, Fukui, Japan

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Eisai Trial Site #1

Kitakyushu, Fukuoka, Japan

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Eisai Trial Site #1

Koga, Fukuoka, Japan

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Eisai Trial Site #1

Kurume, Fukuoka, Japan

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Eisai Trial Site #1

Sapporo, Hokkaido, Japan

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Eisai Trial Site #2

Sapporo, Hokkaido, Japan

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Eisai Trial Site #1

Itami, Hyōgo, Japan

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Eisai Trial Site #1

Tsuchiura, Ibaraki, Japan

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Eisai Trial Site #1

Kanazawa, Ishikawa-ken, Japan

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Eisai Trial Site #1

Zentsujichó, Kagawa-ken, Japan

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Eisai Trial Site #1

Fujisawa, Kanagawa, Japan

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Eisai Trial Site #1

Kawasaki, Kanagawa, Japan

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Eisai Trial Site #1

Gōshi, Kumamoto, Japan

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Eisai Trial Site #1

Tamana, Kumamoto, Japan

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Eisai Trial Site #1

Iwanuma, Miyagi, Japan

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Eisai Trial Site #1

Sendai, Miyagi, Japan

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Eisai Trial Site #1

Miyakonojō, Miyazaki, Japan

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Eisai Trial Site #1

Ōmura, Nagasaki, Japan

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Eisai Trial Site #1

Beppu, Oita Prefecture, Japan

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Eisai Trial Site #1

Kurashiki, Okayama-ken, Japan

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Eisai Trial Site #1

Izumi, Osaka, Japan

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Eisai Trial Site #1

Sakai, Osaka, Japan

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Eisai Trial Site #2

Sakai, Osaka, Japan

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Eisai Trial Site #1

Sayama, Osaka, Japan

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Eisai Trial Site #1

Takatsuki, Osaka, Japan

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Eisai Trial Site #1

Asaka, Saitama, Japan

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Eisai Trial Site #1

Higashimurayama, Saitama, Japan

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Eisai Trial Site #1

Moriyama, Shiga, Japan

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Eisai Trial Site #1

Matsue, Shimane, Japan

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Eisai Trial Site #1

Hamamatsu, Shizuoka, Japan

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Eisai Trial Site #1

Komatsushimachō, Tokushima, Japan

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Eisai Trial Site #1

Kodaira, Tokyo, Japan

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Eisai Trial Site #1

Kokubunji, Tokyo, Japan

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Eisai Trial Site #1

Ube, Yamaguchi, Japan

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Eisai Trial Site #1

Akita, , Japan

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Eisai Trial Site #1

Aomori, , Japan

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Eisai Trial Site #1

Fukui, , Japan

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Eisai Trial Site #1

Fukuoka, , Japan

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Eisai Trial Site #2

Fukuoka, , Japan

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Eisai Trial Site #1

Gifu, , Japan

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Eisai Trial Site #1

Hiroshima, , Japan

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Eisai Trial Site #2

Hiroshima, , Japan

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Eisai Trial Site #1

Kagoshima, , Japan

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Eisai Trial Site #2

Kagoshima, , Japan

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Eisai Trial Site #1

Kumamoto, , Japan

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Eisai Trial Site #1

Kyoto, , Japan

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Eisai Trial Site #1

Miyazaki, , Japan

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Eisai Trial Site #1

Nara, , Japan

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Eisai Trial Site #1

Niigata, , Japan

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Eisai Trial Site #1

Okayama, , Japan

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Eisai Trial Site #1

Saitama, , Japan

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Eisai Trial Site #2

Saitama, , Japan

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Eisai Trial Site #1

Shizuoka, , Japan

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Eisai Trial Site #2

Shizuoka, , Japan

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Eisai Trial Site #1

Toyama, , Japan

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Eisai Trial Site #1

Yamagata, , Japan

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Facility #1

Kuala Lumpur, , Malaysia

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Perak, , Malaysia

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Pulau Pinang, , Malaysia

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Terengganu, , Malaysia

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Busan, , South Korea

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Busan, , South Korea

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Daegu, , South Korea

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Daejeon, , South Korea

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Gwangju, , South Korea

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Incheon, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Taichung, , Taiwan

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Tainan City, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taoyuan District, , Taiwan

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Facility #1

Rajathevee, , Thailand

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Facility #1

Tha Muang, , Thailand

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Facility #2

Tha Muang, , Thailand

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Facility #3

Tha Muang, , Thailand

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Facility #4

Tha Muang, , Thailand

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Countries

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Australia China Japan Malaysia South Korea Taiwan Thailand

References

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Bresnahan R, Hill RA, Wang J. Perampanel add-on for drug-resistant focal epilepsy. Cochrane Database Syst Rev. 2023 Apr 14;4(4):CD010961. doi: 10.1002/14651858.CD010961.pub2.

Reference Type DERIVED
PMID: 37059702 (View on PubMed)

Nishida T, Lee SK, Inoue Y, Saeki K, Ishikawa K, Kaneko S. Adjunctive perampanel in partial-onset seizures: Asia-Pacific, randomized phase III study. Acta Neurol Scand. 2018 Apr;137(4):392-399. doi: 10.1111/ane.12883. Epub 2017 Dec 17.

Reference Type DERIVED
PMID: 29250772 (View on PubMed)

Other Identifiers

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E2007-J000-335

Identifier Type: -

Identifier Source: org_study_id

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