A Study of Baricitinib (LY3009104) in Adults With Severe or Very Severe Alopecia Areata

NCT ID: NCT03899259

Last Updated: 2025-01-31

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

546 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-07-08

Study Completion Date

2024-11-19

Brief Summary

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The reason for this study is to see if baricitinib is safe and effective in adults with severe or very severe alopecia areata (AA).

Detailed Description

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Conditions

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Alopecia Areata

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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4 Milligram (mg) Baricitinib

Participants received one 4 mg Baricitinib tablet administered orally, every day (QD) one placebo tablet administered orally QD to maintain blind.

Group Type EXPERIMENTAL

Baricitinib

Intervention Type DRUG

Administered orally

Placebo

Intervention Type DRUG

Administered orally

2 mg Baricitinib

Participants received one 2 mg Baricitinib tablet administered orally QD, and one placebo tablet administered orally QD to maintain blind.

Group Type EXPERIMENTAL

Baricitinib

Intervention Type DRUG

Administered orally

Placebo

Intervention Type DRUG

Administered orally

Placebo

Participants received two placebo tablets administered orally QD to maintain the blind.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered orally

4 mg Baricitinib Maximum Extended Enrollment (MEE)

Participants received one 4 mg Baricitinib tablet administered orally, every day (QD) one placebo tablet administered orally QD to maintain blind.

Group Type EXPERIMENTAL

Baricitinib

Intervention Type DRUG

Administered orally

Placebo

Intervention Type DRUG

Administered orally

2 mg Baricitinib MEE

Participants received one 2 mg Baricitinib tablet administered orally QD, and one placebo tablet administered orally QD to maintain blind.

Group Type EXPERIMENTAL

Baricitinib

Intervention Type DRUG

Administered orally

Placebo MEE

Participants received two placebo tablets administered orally QD to maintain the blind.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered orally

Interventions

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Baricitinib

Administered orally

Intervention Type DRUG

Placebo

Administered orally

Intervention Type DRUG

Other Intervention Names

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LY3009104

Eligibility Criteria

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Inclusion Criteria

* Are at least 18 years and ≤60 years for males (≤70 years of age for females) at the time of informed consent.
* Have severe or very severe AA, as determined by all of the following:

* Current AA episode of more than 6 months' duration and hair loss encompassing ≥50% of the scalp, as measured by SALT (AA-IGA of 3 or 4) at screening and baseline.
* No spontaneous improvement over the past 6 months.
* Current episode of severe or very severe AA of less than 8 years. Note: participants who have severe or very severe AA for ≥8 years may be enrolled if episodes of regrowth, spontaneous or under treatment, have been observed on the affected areas over the past 8 years.
* Male or nonpregnant, nonbreastfeeding female participants.

Exclusion Criteria

* Primarily "diffuse" type of AA.
* Are currently experiencing other forms of alopecia or any other concomitant conditions that would interfere with evaluations of the effect of study medication on AA.
* Previously treated with an oral Janus kinase (JAK) inhibitor and had an inadequate response (for example, absence of significant terminal hair growth after at least 12 weeks of treatment).
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role collaborator

Eli Lilly and Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM -5 PM Eastern time (UTC/GMT - 5 hours, EST)

Role: STUDY_DIRECTOR

Eli Lilly and Company

Locations

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Total Skin and Beauty Dermatology Center, PC

Birmingham, Alabama, United States

Site Status

Investigate MD

Scottsdale, Arizona, United States

Site Status

Center For Dermatology Clinical Research, Inc.

Fremont, California, United States

Site Status

Quest Dermatology Research

Northridge, California, United States

Site Status

Kaiser Permanente Hospital

San Francisco, California, United States

Site Status

New England Research Associates

Bridgeport, Connecticut, United States

Site Status

Florida Academic Centers Research and Education, LLC

Coral Gables, Florida, United States

Site Status

New Horizon Research Center

Miami, Florida, United States

Site Status

ForCare Clinical Research

Tampa, Florida, United States

Site Status

Dawes Fretzin Clinical Research Group, LLC

Indianapolis, Indiana, United States

Site Status

The South Bend Clinic Center for Research

South Bend, Indiana, United States

Site Status

Qualmedica Research, LLC

Owensboro, Kentucky, United States

Site Status

Dermatology and Skin Cancer Specialists

Rockville, Maryland, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Great Lakes Research Group, Inc.

Bay City, Michigan, United States

Site Status

Clinical Research Institute of Michigan, LLC

Chesterfield, Michigan, United States

Site Status

Hamzavi Dermatology

Fort Gratiot, Michigan, United States

Site Status

Associated Skin Care Specialists

New Brighton, Minnesota, United States

Site Status

MediSearch Clinical Trials

Saint Joseph, Missouri, United States

Site Status

Joseph J. Schwartz, M.D.

Troy, New York, United States

Site Status

The University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Dermatology Specialists of Charlotte

Charlotte, North Carolina, United States

Site Status

M3-Emerging Medical Research

Raleigh, North Carolina, United States

Site Status

Bexley Dermatology Research

Bexley, Ohio, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

Dermatologists of Southwest Ohio

Mason, Ohio, United States

Site Status

Vital Prospects Clinical Research Institute, P.C.

Tulsa, Oklahoma, United States

Site Status

Northwest Dermatology Institute

Portland, Oregon, United States

Site Status

Oregon Dermatology and Research Center

Portland, Oregon, United States

Site Status

Velocity Clinical Research, Providence

East Greenwich, Rhode Island, United States

Site Status

Suzanne Bruce and Associates, PA

Houston, Texas, United States

Site Status

Progressive Clinical Research

San Antonio, Texas, United States

Site Status

Virginia Clinical Research, Inc.

Norfolk, Virginia, United States

Site Status

Stat Research

CABA, Buenos Aires, Argentina

Site Status

Instituto de Neumonología y Dermatología

Capital Federal, Buenos Aires, Argentina

Site Status

Centro de Investigaciones Metabólicas (CINME)

Ciudad Autónoma de Buenos Aires, Buenos Aires, Argentina

Site Status

Buenos Aires Skin

Buenos Aires, Buenos Aires F.D., Argentina

Site Status

Fundacion Respirar

Buenos Aires, Ciudad Autonoma Buenos Aires, Argentina

Site Status

Centro de Investigaciones Médicas Tucuman

SAN M. de Tucuman, Tucumán Province, Argentina

Site Status

Parra Dermatología

Mendoza, , Argentina

Site Status

Woden Dermatology

Phillip, Australian Capital Territory, Australia

Site Status

Skin & Cancer Foundation Australia

Westmead, New South Wales, Australia

Site Status

Veracity Clinical Research Pty Ltd

Woolloongabba, Queensland, Australia

Site Status

Clinical Trials SA Pty Ltd

Campbelltown, South Australia, Australia

Site Status

Skin Health Institute Inc.

Carlton, Victoria, Australia

Site Status

Sinclair Dermatology

Melbourne, Victoria, Australia

Site Status

Fremantle Dermatology

Fremantle, Western Australia, Australia

Site Status

IDERJ - Instituto de Dermatologia e Estética do Brasil

Rio de Janeiro, Rio de Janeiro, Brazil

Site Status

Irmandade da Santa Casa de Misericordia de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Centro de Pesquisa Sao Lucas

Campinas, São Paulo, Brazil

Site Status

Hospital de Clínicas Da Universidade Estadual de Campinas

Campinas, São Paulo, Brazil

Site Status

Faculdade de Medicina do ABC

Santo André, São Paulo, Brazil

Site Status

IBPClin - Instituto Brasil de Pesquisa Clínica

Rio de Janeiro, , Brazil

Site Status

IPITEC

São Paulo, , Brazil

Site Status

Servidor Público Estadual - IAMSPE - centro de estudos urológicos

São Paulo, , Brazil

Site Status

Beijing Chao-Yang Hospital, Capital Medical University

Beijing, Beijing Municipality, China

Site Status

Beijing Friendship Hospital Affiliate of Capital University

Beijing, Beijing Municipality, China

Site Status

Peking University Third Hospital

Beijing, Beijing Municipality, China

Site Status

Chinese PLA General Hospital

Beijing, Beijing Municipality, China

Site Status

Guangdong Province Dermatology Hospital

Guangzhou, Guangdong, China

Site Status

Xiangya Hospital Central South University

Changsha, Hunan, China

Site Status

Jiangsu Province Hospital

Nanjing, Jiangsu, China

Site Status

Affiliated Hospital of Jiangsu University

Zhenjiang, Jiangsu, China

Site Status

The Second Affiliated Hospital of Xi'an Jiaotong University

Xi'an, Shaanxi, China

Site Status

HuaShan Hospital Affiliated To Fudan University

Shanghai, Shanghai Municipality, China

Site Status

Shanghai Skin Disease Hospital

Shanghai, Shanghai Municipality, China

Site Status

First Affiliated Hospital of Shanxi Medical University

Taiyuan, Shanxi, China

Site Status

Tianjin Medical University General Hospital

Tianjin, Tianjin Municipality, China

Site Status

Zhejiang Provincial People's Hospital

Hangzhou, Zhejiang, China

Site Status

The Second Affiliated Hospital of Zhejiang University School of Medicine

Hangzhou, Zhejiang, China

Site Status

Rabin Medical Center

Petah Tikva, Central District, Israel

Site Status

Sheba Medical Center

Ramat Gan, Central District, Israel

Site Status

Hadassah Medical Center

Jerusalem, Jerusalem, Israel

Site Status

Emek Medical Center

Afula, Northern District, Israel

Site Status

Rambam Medical Center

Haifa, Northern District, Israel

Site Status

Soroka Medical Center

Beersheba, Southern District, Israel

Site Status

Sourasky Medical Center

Tel Aviv, Tell Abīb, Israel

Site Status

Yokohama Rosai Hospital

Yokohama, Kanagawa, Japan

Site Status

Hamamatsu University Hospital

Hamamatsu, Shizuoka, Japan

Site Status

Juntendo University Hospital

Bunkyo-ku, Tokyo, Japan

Site Status

Juntendo Tokyo Koto Geriatric Medical Center

Koto-ku, Tokyo, Japan

Site Status

Kyorin University Hospital

Mitaka, Tokyo, Japan

Site Status

Tokyo Medical Univ. Hospital

Shinjuku-ku, Tokyo, Japan

Site Status

Yamaguchi University Hospital

Ube, Yamaguchi, Japan

Site Status

Osaka City University Hospital

Osaka, , Japan

Site Status

Clinical Research Puerto Rico

San Juan, , Puerto Rico

Site Status

Dankook University Hospital

Cheonan, Chungcheongnam-do, South Korea

Site Status

Soonchunhyang University Bucheon Hospital

Bucheon-si, Gyeonggi-do, South Korea

Site Status

Ajou University Hospital

Suwon, Gyeonggi-do, South Korea

Site Status

Boramae Medical Center

Dongjak-gu, Seoul-teukbyeolsi [Seoul], South Korea

Site Status

Kyunghee University Hospital at Gangdong

Seoul, Seoul-teukbyeolsi [Seoul], South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Chung Shan Medical University Hospital

Taichung, Taichung, Taiwan

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Chang Gung Medical Foundation-Linkou Branch

Taoyuan District, , Taiwan

Site Status

Countries

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United States Argentina Australia Brazil China Israel Japan Puerto Rico South Korea Taiwan

References

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King B, Mostaghimi A, Shimomura Y, Piraccini BM, Blume-Peytavi U, Sontag A, Dutronc Y, Denning K, Kolodsick J, Lu X, Srivastava A, Sinclair R. Safety of Baricitinib in Adults with Severe Alopecia Areata from Two Phase III Trials Over a Median of 2.3 Years and Up to 4 Years of Treatment. Am J Clin Dermatol. 2025 Jul;26(4):611-622. doi: 10.1007/s40257-025-00932-0. Epub 2025 Apr 11.

Reference Type DERIVED
PMID: 40214720 (View on PubMed)

Craiglow B, Lee YW, Vano-Galvan S, Egeberg A, Dutronc Y, Durand F, Pierce E, Yu G, Chen YF, Mostaghimi A. Improvement in Measures of Quality of Life and Symptoms of Anxiety and Depression in Patients with Severe Alopecia Areata Achieving Sustained Scalp Hair Regrowth with Baricitinib. Dermatol Ther (Heidelb). 2024 Jul;14(7):1959-1968. doi: 10.1007/s13555-024-01208-x. Epub 2024 Jun 21.

Reference Type DERIVED
PMID: 38904749 (View on PubMed)

Senna MM, Kwon O, Piraccini BM, Sinclair R, Ball S, Ding Y, Chen YF, Dutronc Y, King B. Clinical Benefits of Baricitinib Therapy According to Scalp Hair Regrowth in Patients with Severe Alopecia Areata. Dermatol Ther (Heidelb). 2023 Dec;13(12):3209-3220. doi: 10.1007/s13555-023-01063-2. Epub 2023 Nov 22.

Reference Type DERIVED
PMID: 37991697 (View on PubMed)

Ko JM, Mayo TT, Bergfeld WF, Dutronc Y, Yu G, Ball SG, Somani N, Craiglow BG. Clinical Outcomes for Uptitration of Baricitinib Therapy in Patients With Severe Alopecia Areata: A Pooled Analysis of the BRAVE-AA1 and BRAVE-AA2 Trials. JAMA Dermatol. 2023 Sep 1;159(9):970-976. doi: 10.1001/jamadermatol.2023.2581.

Reference Type DERIVED
PMID: 37556146 (View on PubMed)

Piraccini BM, Ohyama M, Craiglow B, Bewley A, Ding Y, Chen YF, Dutronc Y, Pierce E, Durand F, Mostaghimi A. Scalp hair regrowth is associated with improvements in health-related quality of life and psychological symptoms in patients with severe alopecia areata: results from two randomized controlled trials. J Dermatolog Treat. 2023 Dec;34(1):2227299. doi: 10.1080/09546634.2023.2227299.

Reference Type DERIVED
PMID: 37381691 (View on PubMed)

Kwon O, Senna MM, Sinclair R, Ito T, Dutronc Y, Lin CY, Yu G, Chiasserini C, McCollam J, Wu WS, King B. Efficacy and Safety of Baricitinib in Patients with Severe Alopecia Areata over 52 Weeks of Continuous Therapy in Two Phase III Trials (BRAVE-AA1 and BRAVE-AA2). Am J Clin Dermatol. 2023 May;24(3):443-451. doi: 10.1007/s40257-023-00764-w. Epub 2023 Mar 1.

Reference Type DERIVED
PMID: 36855020 (View on PubMed)

King B, Mostaghimi A, Shimomura Y, Zlotogorski A, Choi GS, Blume-Peytavi U, Passeron T, Holzwarth K, Dutronc Y, McCollam J, Yang FE, Stanley S, Wu WS, Sinclair R. Integrated safety analysis of baricitinib in adults with severe alopecia areata from two randomized clinical trials. Br J Dermatol. 2023 Feb 10;188(2):218-227. doi: 10.1093/bjd/ljac059.

Reference Type DERIVED
PMID: 36763878 (View on PubMed)

King B, Ohyama M, Kwon O, Zlotogorski A, Ko J, Mesinkovska NA, Hordinsky M, Dutronc Y, Wu WS, McCollam J, Chiasserini C, Yu G, Stanley S, Holzwarth K, DeLozier AM, Sinclair R; BRAVE-AA Investigators. Two Phase 3 Trials of Baricitinib for Alopecia Areata. N Engl J Med. 2022 May 5;386(18):1687-1699. doi: 10.1056/NEJMoa2110343. Epub 2022 Mar 26.

Reference Type DERIVED
PMID: 35334197 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://trials.lillytrialguide.com/en-US/trial/10fuouLYVPNjWekNxnfJoE

A Study of Baricitinib (LY3009104) in Adults With Severe or Very Severe Alopecia Areata

Other Identifiers

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I4V-MC-JAIR

Identifier Type: OTHER

Identifier Source: secondary_id

16978

Identifier Type: -

Identifier Source: org_study_id

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