A Phase 2a Proof-of-Concept Trial of Bempikibart (ADX-914) for the Treatment of Severe Alopecia Areata (SIGNAL-AA)

NCT ID: NCT06018428

Last Updated: 2025-10-31

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

75 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-09-12

Study Completion Date

2026-09-30

Brief Summary

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Part A is a randomized, double-blind, placebo-controlled, multi-center Proof-of-Concept (POC) Trial in subjects with severe Alopecia Areata. All participants in Part A have completed participation.

Part B is a multicenter, open-label study to assess the efficacy, safety, and tolerability of bempikibart (ADX-914) in participants with severe Alopecia Areata.

Detailed Description

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Part A is a Phase IIa, Randomized, Double-blind, Placebo-controlled, multi-center Proof-of-Concept (POC) study in adult subjects with severe Alopecia Areata (AA). Bempikibart (ADX-914) or matching placebo is administered subcutaneously in the clinic setting every 2 weeks for 24 weeks, with follow-up for 12 weeks. Subjects will be randomized 3:1 to drug vs placebo. All participants in Part A have completed participation.

Part B is a multicenter, open-label study comprised of a screening period of up to 4 weeks, a treatment period of 36 weeks, and a follow-up period of 16 weeks, for a total study duration of up to 56 weeks.

Open Label Extension Cohort is a multicenter, open-label extension to assess the long-term efficacy, safety, and tolerability of bempikibart (ADX-914) in participants with severe AA who experienced hair regrowth as participants in Part A of the study. Participants enrolled in the Open Label Extension Cohort will receive bempikibart (ADX-914) for a duration of 6 months followed by a 16-week follow-up period.

Conditions

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Alopecia Areata

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Part A was double blind-randomized. Part B and OLE are open label.

Study Groups

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Experimental: bempikibart (ADX-914)

200mg dose of bempikibart (ADX-914) administered via injection under the skin

Group Type EXPERIMENTAL

bempikibart (ADX-914)

Intervention Type DRUG

Subcutaneous administration of bempikibart (ADX-914)

Interventions

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bempikibart (ADX-914)

Subcutaneous administration of bempikibart (ADX-914)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Adult men and women, aged 18 to 75 years, inclusive, at the time of informed consent.
2. Clinical diagnosis of severe to very severe alopecia areata, defined as the presence of ≥50% total scalp hair loss at screening and baseline as measured by the SALT score.

Exclusion Criteria

1. History of or diagnosis at screening of any another form of alopecia based on assessment by investigator.
2. History (lifetime) or presence of hair transplants.
3. History (lifetime) or presence of micropigmentation of the scalp (Note: Microblading of the eyebrows is permitted).
4. Use of systemic, topical, or device-based therapy for AA.
5. History of, recent, or current clinically serious viral, bacterial, fungal, or parasitic infection or mycobacterial infection or at risk of serious infection.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Q32 Bio Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Scottsdale, Arizona

Scottsdale, Arizona, United States

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Fayetteville, Arkansas

Fayetteville, Arkansas, United States

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Hot Springs, Arkansas

Hot Springs, Arkansas, United States

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Encinitas, California

Encinitas, California, United States

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Fountain Valley, California

Fountain Valley, California, United States

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Lomita, California

Lomita, California, United States

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New Haven, Connecticut

New Haven, Connecticut, United States

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Miami, Florida

Miami, Florida, United States

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Tampa, Florida

Tampa, Florida, United States

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Clarksville, Indiana

Clarksville, Indiana, United States

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Bowling Green, Kentucky

Bowling Green, Kentucky, United States

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Burlington, Massachusetts

Burlington, Massachusetts, United States

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Troy, Michigan

Troy, Michigan, United States

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Warren, Michigan

Warren, Michigan, United States

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New York, New York

New York, New York, United States

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New York, New York

New York, New York, United States

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Wilmington, North Carolina

Wilmington, North Carolina, United States

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Bexley, Ohio

Bexley, Ohio, United States

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Canton, Ohio, United States

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Mason, Ohio

Mason, Ohio, United States

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Mayfield Heights, Ohio

Mayfield Heights, Ohio, United States

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Portland, Oregon

Portland, Oregon, United States

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Austin, Texas

Austin, Texas, United States

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Frisco, Texas

Frisco, Texas, United States

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Houston, Texas

Houston, Texas, United States

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San Antonio, Texas

San Antonio, Texas, United States

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Jordan, Utah

Jordan, Utah, United States

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Spokane, Washington

Spokane, Washington, United States

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Calgary, Alberta, Canada

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Winnipeg, Manitoba, Canada

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Oakville, Ontario, Canada

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Peterborough, Ontario, Canada

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Waterloo, Ontario, Canada

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Countries

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United States Canada

Other Identifiers

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SIGNAL-AA

Identifier Type: OTHER

Identifier Source: secondary_id

ADX-914-203

Identifier Type: -

Identifier Source: org_study_id

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