Long-Term PF-06651600 for the Treatment of Alopecia Areata

NCT ID: NCT04006457

Last Updated: 2025-08-14

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

1052 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-07-18

Study Completion Date

2026-01-23

Brief Summary

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This is a global Phase 3 study to evaluate the safety and effectiveness of an investigational study drug (called PF-06651600) in adults and adolescents (12 years and older) who have alopecia areata. Eligible patients from the prior studies B7931005 (NCT02974868) and B7981015 (NCT03732807) will have an opportunity to enroll as well as patients who have not previously participated in either of these studies. The study is open-label and all patients entering the study will receive active study drug.

A sub-study of approximately 60 adult patients who are participating in the B7981032 study will be conducted at select sites in the US, Australia and Canada. The sub-study will evaluate the immune response to tetanus and meningococcal vaccines in patients who have received a minimum of 6 months of 50 mg PF-06651600.

Detailed Description

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Conditions

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Alopecia Areata

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Treatment sequence 1

Participants who did not previously receive study intervention in either study B7931005 or B7981015 will receive 200 milligrams (mg) PF-06651600, given as four 50 mg tablets once daily (QD) for 1 month, followed by 50 mg PF-06651600 tablet or capsule given QD for 59 months.

Patients participating in the vaccine sub-study will receive the 2 vaccines or one of the 2 vaccines at the vaccine sub-study Day 1, which will occur at a scheduled study visit on or after the Month 9 visit and prior to or on the Month 56 visit of the main B7981032 study.

Group Type EXPERIMENTAL

PF-06651600

Intervention Type DRUG

50 mg oral tablets/capsules

Tetanus and diphtheria toxoids and acellular pertussis (Tdap) vaccine

Intervention Type BIOLOGICAL

Single intramuscular injection administered to patients participating in the vaccine sub-study

Meningococcal (groups A, C, W-135 and Y [ACWY]) oligosaccharide diphtheria CRM197 conjugate vaccine

Intervention Type BIOLOGICAL

Single intramuscular injection administered to patients participating in the vaccine sub-study

Treatment sequence 2

Participants who previously received study intervention in either study B7931005 or B7981015 will receive 50 mg PF-06651600 tablet or capsule given QD for 59 months.

Patients participating in the vaccine sub-study will receive the 2 vaccines or 1 of the 2 vaccines at the vaccine sub-study Day 1, which will occur at a scheduled study visit on or after the Month 6 visit and prior to or on the Month 56 visit of the main B7981032 study.

Group Type EXPERIMENTAL

PF-06651600

Intervention Type DRUG

50 mg oral tablets/capsules

Tetanus and diphtheria toxoids and acellular pertussis (Tdap) vaccine

Intervention Type BIOLOGICAL

Single intramuscular injection administered to patients participating in the vaccine sub-study

Meningococcal (groups A, C, W-135 and Y [ACWY]) oligosaccharide diphtheria CRM197 conjugate vaccine

Intervention Type BIOLOGICAL

Single intramuscular injection administered to patients participating in the vaccine sub-study

Interventions

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PF-06651600

50 mg oral tablets/capsules

Intervention Type DRUG

Tetanus and diphtheria toxoids and acellular pertussis (Tdap) vaccine

Single intramuscular injection administered to patients participating in the vaccine sub-study

Intervention Type BIOLOGICAL

Meningococcal (groups A, C, W-135 and Y [ACWY]) oligosaccharide diphtheria CRM197 conjugate vaccine

Single intramuscular injection administered to patients participating in the vaccine sub-study

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

For de novo participants and participants from Study B7931005 and B7981015 with \>30 days between first visit in B7981032 and last dose in the prior study:

* Clinical diagnosis of alopecia areata (AA) with no other cause of hair loss. Androgenetic alopecia coexistent with AA is allowed.
* De novo participants \>=12 to \<18 years of age: \>=50% terminal hair loss of the scalp due to AA, including alopecia totalis and alopecia universalis
* De novo participants \>=18 years of age and participants from Study B7931005 or B7981015 with \>30 days between first visit in B7981032 and last dose in the prior study: \>=25% terminal hair loss of the scalp due to AA, including alopecia totalis and alopecia universalis
* No evidence of terminal scalp hair regrowth within 6 months (de novo only)
* Current episode of terminal scalp hair loss \<=10 years (de novo only)

Exclusion Criteria

For de novo participants and participants from Study B7931005 and B7981015 with \>30 days between first visit in B7981032 and last dose in the prior study:

* Hearing loss with progression over previous 5 years, or sudden hearing loss, or middle or inner ear disease, or other auditory condition that is considered acute, fluctuating or progressive
* History of or current malignancies with the exception of adequately treated or excised non metastatic basal cell or squamous cell cancer of the skin or cervical carcinoma in situ
* History of a single episode of disseminated herpes zoster or disseminated herpes simplex, or a history of more than one episode of localized, dermatomal herpes zoster
* Infection requiring hospitalization, or parenteral antimicrobial therapy within 6 months prior to Day 1


\- Participants who have previously taken Janus kinase (JAK) inhibitors other than PF-06651600 must have received the last dose \>12 weeks prior to the screening visit
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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The University of Alabama at Birmingham Hosptial Outreach Lab

Birmingham, Alabama, United States

Site Status

The University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

The University of Alabama at Birmingham, Department of Dermatology

Birmingham, Alabama, United States

Site Status

Mosaic Dermatology

Beverly Hills, California, United States

Site Status

Univ of California, Irvine, Dermatology Clinical Research Center

Irvine, California, United States

Site Status

Dermatology Specialists Inc.

Murrieta, California, United States

Site Status

University of California, San Francisco

San Francisco, California, United States

Site Status

Kaiser Permanente Clinical Trials Unit

San Francisco, California, United States

Site Status

Southern California Dermatology, Inc.

Santa Ana, California, United States

Site Status

University of Colorado Anschutz Medical Campus

Aurora, Colorado, United States

Site Status

University of Colorado Hospital Clinical and Translational Research Center

Aurora, Colorado, United States

Site Status

University of Colorado Hospital Outpatient Pavilion

Aurora, Colorado, United States

Site Status

Yale School of Medicine, Yale Center for Clinical Investigations

New Haven, Connecticut, United States

Site Status

Medstar Georgetown University Hospital - Department of Otolaryngology

Washington D.C., District of Columbia, United States

Site Status

Medstar Georgetown University Hospital-Dept of Otolaryngology

Washington D.C., District of Columbia, United States

Site Status

MedStar Washington Hospital Center

Washington D.C., District of Columbia, United States

Site Status

Medstar Georgetown University Hospital - Department of Pediatrics

Washington D.C., District of Columbia, United States

Site Status

Siperstein Dermatology Group

Boynton Beach, Florida, United States

Site Status

Park Avenue Dermatology

Orange Park, Florida, United States

Site Status

ForCare Clinical Research

Tampa, Florida, United States

Site Status

Velocity Clinical Research - Boise

Meridian, Idaho, United States

Site Status

Northwestern Medical Group

Chicago, Illinois, United States

Site Status

Northwestern Medicine Diagnostic Testing Center

Chicago, Illinois, United States

Site Status

Northwestern Medicine

Chicago, Illinois, United States

Site Status

Northwestern Memorial Hospital Investigational Drug Service Pharmacy

Chicago, Illinois, United States

Site Status

Summit Dermatology and Aesthetic Surgery (in c/o TrialSpark, Inc)

Oakbrook Terrace, Illinois, United States

Site Status

NorthShore University HealthSystem Dermatology Clinical Trials Unit

Skokie, Illinois, United States

Site Status

Southern Illinois University School of Medicine

Springfield, Illinois, United States

Site Status

Dawes Fretzin Clinical Research Group, LLC

Indianapolis, Indiana, United States

Site Status

University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

Site Status

Medstar Georgetown University Hospital - Department of Dermatology

Chevy Chase, Maryland, United States

Site Status

Massachusetts General Hospital - Clinical Unit for Research Trials in Skin (CURTIS)

Boston, Massachusetts, United States

Site Status

University of Minnesota Clinical Research Unit (CRU)

Minneapolis, Minnesota, United States

Site Status

University of Minnesota Lillehei Clinical Research Unit (LCRU)

Minneapolis, Minnesota, United States

Site Status

University of Minnesota Medical Center, Investigational Drug Services Attn: Darlette Luke

Minneapolis, Minnesota, United States

Site Status

Skin Specialists, PC (Schlessinger MD)

Omaha, Nebraska, United States

Site Status

Schweiger Dermatology, P.C.

Verona, New Jersey, United States

Site Status

NYU School of Medicine, The Ronald O. Perelman Department of Dermatology

New York, New York, United States

Site Status

Pura Dermatology (in c/o TrialSpark, Inc)

New York, New York, United States

Site Status

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status

UNC CTRC

Chapel Hill, North Carolina, United States

Site Status

UNC Dermatology and Skin Cancer Center

Chapel Hill, North Carolina, United States

Site Status

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Vital Prospects Clinical Research Institute, P.C.

Tulsa, Oklahoma, United States

Site Status

Oregon Medical Research Center

Portland, Oregon, United States

Site Status

The University of Texas Health Science Center at Houston

Bellaire, Texas, United States

Site Status

Tamjidi Skin Institute (in c/o TrialSpark, Inc)

Vienna, Virginia, United States

Site Status

CINME Centro de Investigaciones Metabolicas

CABA, Buenos Aires, Argentina

Site Status

Psoriahue Medicina Interdisciplinaria

CABA, , Argentina

Site Status

Premier Specialists Pty Ltd

Kogarah, New South Wales, Australia

Site Status

St George Dermatology & Skin Cancer Centre

Kogarah, New South Wales, Australia

Site Status

The Skin Centre

Benowa, Queensland, Australia

Site Status

Veracity Clinical Research Pty Ltd

Woolloongabba, Queensland, Australia

Site Status

Skin Health Institute

Carlton, Victoria, Australia

Site Status

Sinclair Dermatology

East Melbourne, Victoria, Australia

Site Status

Royal Melbourne Hospital

Parkville, Victoria, Australia

Site Status

Wiseman Dermatology Research Inc.

Winnipeg, Manitoba, Canada

Site Status

Eastern Canada Cutaneous Research Associates Ltd.

Halifax, Nova Scotia, Canada

Site Status

Sudbury Skin Clinique

Greater Sudbury, Ontario, Canada

Site Status

Guenther Research Inc

London, Ontario, Canada

Site Status

Lynderm Research Inc.

Markham, Ontario, Canada

Site Status

The Centre for Clinical Trials

Oakville, Ontario, Canada

Site Status

SKiN Centre for Dermatology

Peterborough, Ontario, Canada

Site Status

York Dermatology Clinic and Research Centre

Richmond Hill, Ontario, Canada

Site Status

Research Toronto

Toronto, Ontario, Canada

Site Status

Innovaderm Research Inc.

Montreal, Quebec, Canada

Site Status

Centre de Recherche Dermatologique du Quebec metropolitain (CRDQ)

Québec, Quebec, Canada

Site Status

Centro Medico Skin Med

Santiago, LAS Condes, Chile

Site Status

Centro Internacional de Estudios Clinicos - CIEC

Santiago, Recoleta, Chile

Site Status

Clinica Dermacross S.A.

Santiago, Vitacura, Chile

Site Status

Medical Skin Center

Viña del Mar, , Chile

Site Status

Beijing Friendship Hospital, Capital Medical University

Beijing, Beijing Municipality, China

Site Status

Peking University Third Hospital

Beijing, Beijing Municipality, China

Site Status

The First Affiliated Hospital, Sun Yat-sen University

Guangzhou, Guangdong, China

Site Status

The University of Hong Kong - Shenzhen Hospital

Shenzhen, Guangdong, China

Site Status

Union Hospital, Tongji Medical College, Huazhong University of Science and Technology

Wuhan, Hubei, China

Site Status

The First Affiliated Hospital with Nanjing Medical University

Nanjing, Jiangsu, China

Site Status

Ruijin Hospital Affiliated to Shanghai Jiaotong University School of Medicine

Shanghai, Shanghai Municipality, China

Site Status

The First Affiliated Hospital of College of Medicine, Zhejiang University

Hangzhou, Zhejiang, China

Site Status

Fundacion Centro de Investigacion Clinica CIC

Medellín, Antioquia, Colombia

Site Status

Fundacion Hospitalaria San Vicente de Paul

Medellín, Antioquia, Colombia

Site Status

Centro de Investigacion en Reumatologia y Especialidades Medicas S.A.S, CIREEM S.A.S

Bogota D.C., , Colombia

Site Status

DERMAMEDICA s.r.o.

Náchod, , Czechia

Site Status

Fakultni nemocnice Olomouc

Olomouc, , Czechia

Site Status

Clintrial s.r.o.

Prague, , Czechia

Site Status

Sanatorium profesora Arenbergera

Prague, , Czechia

Site Status

Fachklinik Bad Bentheim

Bad Bentheim, , Germany

Site Status

Emovis GmbH

Berlin, , Germany

Site Status

Universitaetsklinikum Erlangen

Erlangen, , Germany

Site Status

University Hospital Frankfurt

Frankfurt am Main, , Germany

Site Status

University Hospital Schleswig-Holstein

Lübeck, , Germany

Site Status

University Hospital Muenster

Münster, , Germany

Site Status

Nagoya City University Hospital

Nagoya, Aichi-ken, Japan

Site Status

Tohoku University Hospital

Sendai, Miyagi, Japan

Site Status

Hamamatsu University Hospital

Hamamatsu, Shizuoka, Japan

Site Status

Juntendo Tokyo Koto Geriatric Medical Center

Koto-ku, Tokyo, Japan

Site Status

Kyorin University Hospital

Mitaka-shi, Tokyo, Japan

Site Status

Osaka Metropolitan University Hospital

Osaka, , Japan

Site Status

Tokyo Medical University Hospital

Tokyo, , Japan

Site Status

Sociedad de Metabolismo y Corazon S.C.

Veracruz, , Mexico

Site Status

Hospital D Maria

Veracruz, , Mexico

Site Status

Twoja Przychodnia SCM

Szczecin, West Pomeranian Voivodeship, Poland

Site Status

McBk S.C.

Grodzisk Mazowiecki, , Poland

Site Status

Centermed Krakow Sp.z o.o.

Krakow, , Poland

Site Status

Dermoklinika Centrum Medyczne s.c. M.Kierstan, J. Narbutt, A. Lesiak

Lodz, , Poland

Site Status

Dermedic Jacek Zdybski

Ostrowiec Świętokrzyski, , Poland

Site Status

RCMed Oddzial Warszawa

Warsaw, , Poland

Site Status

Magdalena Opadczuk Carpe Diem Centrum Medycyny Estetycznej

Warsaw, , Poland

Site Status

ETG Warszawa

Warsaw, , Poland

Site Status

Royalderm Agnieszka Nawrocka

Warsaw, , Poland

Site Status

EMC Instytut Medyczny S.A. Przychodnia przy ul. Lowieckiej we Wroclawiu

Wroclaw, , Poland

Site Status

Cityclinic Przychodnia Lekarsko Psychologiczna Matusiak Spółka Partnerska

Wroclaw, , Poland

Site Status

Centrum Medyczne OPOROW

Wroclaw, , Poland

Site Status

State Budgetary Healthcare Institution "Chelyabinsk Regional Clinical Dermatovenerologic Dispensary"

Chelyabinsk, , Russia

Site Status

University Clinic of Kirov SMU

Kirov, , Russia

Site Status

FSBEI HE Russian University of Medicine of the MoH of Russia

Moscow, , Russia

Site Status

Federal State Autonomous Institution "National Medical Research Centre of Children's' Health"

Moscow, , Russia

Site Status

State Budgetary Institution of the Rostov Region "Dermatovenerologic Dispensary"

Rostov-on-Don, , Russia

Site Status

Limited Liability Company "Centre Vitiligo" ("Centre Vitiligo" LLC)

Saint Petersburg, , Russia

Site Status

Limited Liability Company "Pierre Volkenshtein Skin Diseases Clinic"

Saint Petersburg, , Russia

Site Status

Saint Petersburg State Budgetary Healthcare Institution "Dermatovenerologic Dispensary No. 10 -

Saint Petersburg, , Russia

Site Status

State Autonomous Healthcare Institution of the Yaroslavl Region "Clinical Emergency Hospital

Yaroslavl, , Russia

Site Status

Pusan National University Hospital

Busan, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Hospital Universitari Germans Trias i Pujol

Badalona, Barcelona, Spain

Site Status

Hospital del Mar

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

Hospital Universitario Infanta Leonor

Madrid, , Spain

Site Status

Hospital Universitario La Paz: Servicio de Farmacia

Madrid, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitario y Politecnico La Fe

Valencia, , Spain

Site Status

Chung-Shan Medical University Hospital

Taichung, R.o.c., Taiwan

Site Status

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, , Taiwan

Site Status

Chang Gung Medical Foundation Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, , Taiwan

Site Status

Taipei Medical University-Shuang Ho Hospital, Ministry of Health and Welfare

New Taipei City, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Chang Gung Medical Foundation Linkou Chang Gung Memorial Hospital

Taoyuan, , Taiwan

Site Status

University Hospital Southampton NHS Foundation Trust

Southampton, Hampshire, United Kingdom

Site Status

University Hospital Southampton NHS Foundation Trust

Southampton, Hampshire, United Kingdom

Site Status

University Hospitals Sussex NHS Foundation Trust (UHSussex)

Brighton, , United Kingdom

Site Status

NHS Greater Glasgow and Clyde, Queen Elizabeth University Hospital

Glasgow, , United Kingdom

Site Status

Guy's and St Thomas Hospitals NHS Foundation Trust, St Thomas Hospital

London, , United Kingdom

Site Status

Guy's and St Thomas' Hospitals NHS Foundation Trust, St Thomas' Hospital

London, , United Kingdom

Site Status

Guy's and St Thomas' Hospitals NHS Foundation Trust, Guy's Hospital

London, , United Kingdom

Site Status

Countries

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United States Argentina Australia Canada Chile China Colombia Czechia Germany Japan Mexico Poland Russia South Korea Spain Taiwan United Kingdom

References

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King B, Mirmirani P, Lo Sicco K, Ramot Y, Sinclair R, Asfour L, Ezzedine K, Paul C, Ohyama M, Edwards RA, Bonfanti G, Kerkmann U, Wajsbrot D, Ishowo-Adejumo R, Zwillich SH, Lejeune A. Patterns of clinical response in patients with alopecia areata treated with ritlecitinib in the ALLEGRO clinical development programme. J Eur Acad Dermatol Venereol. 2025 Jun;39(6):1163-1173. doi: 10.1111/jdv.20547. Epub 2025 Feb 17.

Reference Type DERIVED
PMID: 39962358 (View on PubMed)

Tziotzios C, Sinclair R, Lesiak A, Mehlis S, Kinoshita-Ise M, Tsianakas A, Luo X, Law EH, Ishowo-Adejumo R, Wolk R, Sadrarhami M, Lejeune A. Long-term safety and efficacy of ritlecitinib in adults and adolescents with alopecia areata and at least 25% scalp hair loss: Results from the ALLEGRO-LT phase 3, open-label study. J Eur Acad Dermatol Venereol. 2025 Jun;39(6):1152-1162. doi: 10.1111/jdv.20526. Epub 2025 Jan 23.

Reference Type DERIVED
PMID: 39846397 (View on PubMed)

Piliang M, Soung J, King B, Shapiro J, Rudnicka L, Farrant P, Magnolo N, Piraccini BM, Luo X, Wolk R, Woodworth D, Schaefer G, Lejeune A. Efficacy and safety of the oral Janus kinase 3/tyrosine kinase expressed in hepatocellular carcinoma family kinase inhibitor ritlecitinib over 24 months: integrated analysis of the ALLEGRO phase IIb/III and long-term phase III clinical studies in alopecia areata. Br J Dermatol. 2025 Jan 24;192(2):215-227. doi: 10.1093/bjd/ljae365.

Reference Type DERIVED
PMID: 39432738 (View on PubMed)

King B, Soung J, Tziotzios C, Rudnicka L, Joly P, Gooderham M, Sinclair R, Mesinkovska NA, Paul C, Gong Y, Anway SD, Tran H, Wolk R, Zwillich SH, Lejeune A. Integrated Safety Analysis of Ritlecitinib, an Oral JAK3/TEC Family Kinase Inhibitor, for the Treatment of Alopecia Areata from the ALLEGRO Clinical Trial Program. Am J Clin Dermatol. 2024 Mar;25(2):299-314. doi: 10.1007/s40257-024-00846-3. Epub 2024 Jan 23.

Reference Type DERIVED
PMID: 38263353 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan: Main study

View Document

Document Type: Statistical Analysis Plan: sub study SAP

View Document

Related Links

Access external resources that provide additional context or updates about the study.

https://pmiform.com/clinical-trial-info-request?StudyID=B7981032

To obtain contact information for a study center near you, click here.

Other Identifiers

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2023-509801-59-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

B7981032

Identifier Type: -

Identifier Source: org_study_id

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