A Study to Evaluate the Durability of Response of CTP-543 in Adult Patients With Moderate to Severe Alopecia Areata

NCT ID: NCT04784533

Last Updated: 2024-10-09

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

317 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-02-26

Study Completion Date

2023-05-16

Brief Summary

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This study is designed to evaluate the regrowth of hair with CTP-543 and subsequent durability of that regrowth following dose reduction in adult patients with moderate to severe alopecia areata.

Detailed Description

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Conditions

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Alopecia Areata

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Part A: Period 1 - CTP-543 8 mg BID

Participants received CTP-543 8 milligrams (mg) tablets, orally, twice daily (BID) for up to 24 weeks.

Group Type EXPERIMENTAL

CTP-543

Intervention Type DRUG

Oral dosing

Part A: Period 1 - CTP-543 12 mg BID

Participants received CTP-543 12 mg tablets, orally, BID for up to 24 weeks.

Group Type EXPERIMENTAL

CTP-543

Intervention Type DRUG

Oral dosing

Part A: Period 2 - CTP-543 8 mg BID to 4 mg BID

Participants who received CTP-543 8 mg during Period 1 of Part A and achieved an absolute severity of alopecia tool (SALT) score of ≤20 at Week 24, received CTP-543 4 mg tablets, orally, BID, for up to 24 weeks.

Group Type EXPERIMENTAL

CTP-543

Intervention Type DRUG

Oral dosing

Part A: Period 2 - CTP-543 12 mg BID to 8 mg BID

Participants who received CTP-543 12 mg during Period 1 of Part A and achieved an absolute SALT score of ≤20 at Week 24, received CTP-543 8 mg tablets, orally, BID, for up to 24 weeks.

Group Type EXPERIMENTAL

CTP-543

Intervention Type DRUG

Oral dosing

Part A: Period 2 - CTP-543 8 mg BID to Placebo

Participants who received CTP-543 8 mg during Period 1 of Part A and achieved an absolute SALT score of ≤20 at Week 24, received CTP-543 matched placebo tablets, orally, BID, for up to 24 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Oral dosing

Part A: Period 2 - CTP-543 12 mg BID to Placebo

Participants who received CTP-543 12 mg during Period 1 of Part A and achieved an absolute SALT score of ≤20 at Week 24, received CTP-543 matched placebo tablets, orally, BID, for up to 24 weeks.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Oral dosing

Part B: CTP-543 8 mg BID to 4 mg BID to 8 mg BID

Participants who received CTP-543 8 mg during Period 1, followed by CTP-543 4 mg during Period 2 of Part A and met the criteria for loss of regrowth maintenance (LOM) (absolute SALT score of \> 20), received re-treatment with CTP-543 8 mg tablets, orally, BID, for up to 24 weeks.

Group Type EXPERIMENTAL

CTP-543

Intervention Type DRUG

Oral dosing

Part B: CTP-543 12 mg BID to 8 mg BID to 12 mg BID

Participants who received CTP-543 12 mg during Period 1, followed by CTP-543 8 mg during Period 2 of Part A and met the criteria for LOM (absolute SALT score of \> 20), received re-treatment with CTP-543 12 mg tablets, orally, BID, for up to 24 weeks.

Group Type EXPERIMENTAL

CTP-543

Intervention Type DRUG

Oral dosing

Part B: CTP-543 8 mg BID to Placebo to 8 mg BID

Participants who received CTP-543 8 mg during Period 1, followed by CTP-543 matched placebo during Period 2 of Part A and met the criteria for LOM (absolute SALT score of \> 20), received re-treatment with CTP-543 8 mg tablets, orally, BID, for up to 24 weeks.

Group Type EXPERIMENTAL

CTP-543

Intervention Type DRUG

Oral dosing

Part B: CTP-543 12 mg BID to Placebo to 12 mg BID

Participants who received CTP-543 12 mg during Period 1, followed by CTP-543 matched placebo during Period 2 of Part A and met the criteria for LOM (absolute SALT score of \> 20), received re-treatment with CTP-543 12 mg tablets, orally, BID, for up to 24 weeks.

Group Type EXPERIMENTAL

CTP-543

Intervention Type DRUG

Oral dosing

Interventions

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CTP-543

Oral dosing

Intervention Type DRUG

Placebo

Oral dosing

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Definitive diagnosis of alopecia areata with a current episode of scalp hair loss lasting at least 6 months and not exceeding 10 years at the time of Screening. Total disease duration greater than 10 years is permitted.
* At least 50% scalp hair loss, as defined by a severity of alopecia tool (SALT) score ≥50, at Screening and Baseline.
* Willing to comply with the study visits and requirements of the study protocol.

Exclusion Criteria

* Treatment with other medications or agents within 1 month of Baseline or during the study that may affect hair regrowth or immune response.
* Active scalp inflammation, psoriasis, or seborrheic dermatitis requiring topical treatment to the scalp, significant trauma to the scalp, or other scalp condition that may interfere with the SALT assessment, or untreated actinic keratosis anywhere on the body at Screening and/or Baseline.
* Treatment with systemic immunosuppressive medications within 3 months of Screening or during the study, or biologics within 6 months of Screening or during the study.
* Females who are nursing, pregnant, or planning to become pregnant while in the study, and for 30 days after last dose of study drug.
* Clinically significant medical condition, psychiatric disease, or social condition, as determined by the Investigator, that may unfavorably alter the risk-benefit of study participation, adversely affect study compliance, or confound interpretation of study results.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Concert Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Total Skin and Beauty Dermatology Center, PC

Birmingham, Alabama, United States

Site Status

Center for Dermatology and Plastic Surgery/CCT Research

Scottsdale, Arizona, United States

Site Status

Kern Research, Inc.

Bakersfield, California, United States

Site Status

Hope Clinical Research

Canoga Park, California, United States

Site Status

California Dermatology & Clinical Research Institute

Encinitas, California, United States

Site Status

University of California, Irvine

Irvine, California, United States

Site Status

Quest Dermatology Research

Northridge, California, United States

Site Status

Kaiser Permanente

Oakland, California, United States

Site Status

Palmtree Clinical Research, Inc.

Palm Springs, California, United States

Site Status

Kaiser Permanente

San Francisco, California, United States

Site Status

Colorado Center for Dermatology and Skin Surgery

Centennial, Colorado, United States

Site Status

Colorado Medical Research Center, Inc.

Denver, Colorado, United States

Site Status

Yale University Church Street Research Unit

New Haven, Connecticut, United States

Site Status

Skin Care Research, LLC

Boca Raton, Florida, United States

Site Status

Skin Care Research, LLC

Hollywood, Florida, United States

Site Status

DeNova Research

Chicago, Illinois, United States

Site Status

The Indiana Clinical Trials Center, PC

Plainfield, Indiana, United States

Site Status

DS Research

Louisville, Kentucky, United States

Site Status

Michigan Center for Research Company, LLC

Clarkston, Michigan, United States

Site Status

University of Minnesota Department of Dermatology

Minneapolis, Minnesota, United States

Site Status

Minnesota Clinical Study Center

New Brighton, Minnesota, United States

Site Status

Skin Specialists, PC

Omaha, Nebraska, United States

Site Status

Skin Laser and Surgery Specialists of New Jersey

Hackensack, New Jersey, United States

Site Status

Darst Dermatology

Charlotte, North Carolina, United States

Site Status

Dermatology Specialists of Charlotte

Charlotte, North Carolina, United States

Site Status

North Carolina Dermatology Associates, PLLC

Raleigh, North Carolina, United States

Site Status

Bexley Dermatology Research

Bexley, Ohio, United States

Site Status

Remington Davis

Columbus, Ohio, United States

Site Status

Vital Prospects Clinical Research Institute, PC

Tulsa, Oklahoma, United States

Site Status

Northwest Dermatology

Portland, Oregon, United States

Site Status

Dermatology Associates of Plymouth Meeting

Plymouth Meeting, Pennsylvania, United States

Site Status

PEAK Research, LLC

Upper Saint Clair, Pennsylvania, United States

Site Status

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status

Clinical Research Center of the Carolinas

Charleston, South Carolina, United States

Site Status

Dermatology Treatment and Research Center, PA

Dallas, Texas, United States

Site Status

Austin Institute for Clinical Research

Houston, Texas, United States

Site Status

Austin Institute for Clinical Research, Inc.

Pflugerville, Texas, United States

Site Status

Springville Dermatology/CCT Research

Springville, Utah, United States

Site Status

West End Dermatology Associates

Richmond, Virginia, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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CP543.2004

Identifier Type: -

Identifier Source: org_study_id

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