Study to Evaluate the Safety and Efficacy of CTP-543 in Adults With Moderate to Severe Alopecia Areata

NCT ID: NCT03137381

Last Updated: 2022-07-19

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

149 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-08-09

Study Completion Date

2019-07-08

Brief Summary

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This study will evaluate the safety and efficacy of CTP-543 on hair loss in adults with chronic, moderate to severe alopecia areata.

Detailed Description

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This is a double-blind, randomized, placebo-controlled multi-center study consisting of 3 cohorts to assess the safety and efficacy of CTP-543. Each Cohort will be initiated sequentially in ascending dose order. Participants will be randomized to either an active dose of CTP-543 or placebo for a 24-week treatment period.

Conditions

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Alopecia Areata

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Cohort 1: CTP-543 4 mg BID

Participants will receive CTP-543 4 mg tablets, twice daily for up to 24 weeks.

Group Type EXPERIMENTAL

CTP-543

Intervention Type DRUG

Administered as tablets.

Cohort 2: CTP-543 8 mg BID

Participants will receive CTP-543 8 mg tablets, twice daily for up to 24 weeks.

Group Type EXPERIMENTAL

CTP-543

Intervention Type DRUG

Administered as tablets.

Cohort 3: CTP-543 12 mg BID

Participants will receive CTP-543 12 mg tablets, twice daily for up to 24 weeks.

Group Type EXPERIMENTAL

CTP-543

Intervention Type DRUG

Administered as tablets.

Combined Placebo

Participants will receive CTP-543 matched placebo tablets, twice daily for up to 24 weeks in Cohorts 1, 2, and 3.

Group Type PLACEBO_COMPARATOR

CTP-543 matching placebo

Intervention Type DRUG

Administered as tablets.

Interventions

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CTP-543

Administered as tablets.

Intervention Type DRUG

CTP-543 matching placebo

Administered as tablets.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Definitive diagnosis of alopecia areata with a current episode lasting at least 6 months and not exceeding 10 years at the time of Screening. Total disease duration greater than 10 years is permitted.
* At least 50% scalp hair loss, as defined by a Severity of Alopecia Tool (SALT) score ≥50, at Screening and Baseline.
* Clinical lab results within the normal range

Exclusion Criteria

* Active scalp inflammation, psoriasis, or seborrheic dermatitis requiring topical treatment to the scalp, significant trauma to the scalp, or untreated actinic keratosis on the scalp.
* Treatment with systemic immunosuppressive medications or biologics.
* Vaccination with herpes zoster vaccine or any live virus within 6 weeks of screening or during the study
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Concert Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Colleen E. Hamilton

Role: STUDY_DIRECTOR

Concert Pharmaceuticals, Inc.

Locations

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University of California, Irvine

Irvine, California, United States

Site Status

Contour Dermatology & Cosmetic Surgery Center

Rancho Mirage, California, United States

Site Status

Stanford University School of Medicine

Redwood City, California, United States

Site Status

Kaiser Permanente Northern California

San Francisco, California, United States

Site Status

Yale School of Medicine

New Haven, Connecticut, United States

Site Status

Siperstein Dermatology Group

Boynton Beach, Florida, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Minnesota Clinical Study Center

Fridley, Minnesota, United States

Site Status

Icahn School of Medicine at Mt. Sinai

New York, New York, United States

Site Status

Wake Forest University Health Sciences

Winston-Salem, North Carolina, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Northwest Dermatology

Portland, Oregon, United States

Site Status

Suzanne Bruce & Associates, PA

Houston, Texas, United States

Site Status

Countries

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United States

References

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Cassella J, Hamilton C, von Hehn J, Braman V. JAK Inhibitor CTP-543 Achieves Primary Endpoint in Phase 2 Trial in Alopecia Areata. In: Proceedings from the 2019 American Academy of Dermatology Meeting; 01-05 March 2019; Washington, DC. Abstract 11291.

Reference Type BACKGROUND

Cassella J, Hamilton C, von Hehn J, Braman V. JAK Inhibitor CTP-543 Achieves Primary Endpoint in Phase 2 Trial in Alopecia Areata. In: Proceedings from the 11th World Congress Hair Research; 24-27 April 2019; Sitges, Barcelona.

Reference Type BACKGROUND

Cassella J, Hamilton C, von Hehn J, Braman V. CTP-543, an oral JAK inhibitor, achieves primary endpoint in Phase 2 randomized, placebo-controlled, dose ranging trial in patients with moderate to severe alopecia areata. In: Proceedings from the 28th EADV Congress; 09-13 October 2019, Madrid, Spain. D3T01.1: Late breaking news.

Reference Type BACKGROUND

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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CP543.2001

Identifier Type: -

Identifier Source: org_study_id

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