ATI-501 Oral Suspension Compared to Placebo in Subjects With Alopecia Areata, Alopecia Universalis or Alopecia Totalis

NCT ID: NCT03594227

Last Updated: 2020-09-16

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

87 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-06-11

Study Completion Date

2019-06-18

Brief Summary

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This Phase 2, multicenter, randomized study will evaluate the safety, tolerability and efficacy of ATI-501 for the treatment of Alopecia Areata (AA), Alopecia Universalis (AU) or Alopecia Totalis (AT) in adult subjects.

Detailed Description

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This Phase 2, multicenter, randomized study will evaluate the safety, tolerability and efficacy of ATI-501 for the treatment of Alopecia Areata (AA), Alopecia Universalis (AU) or Alopecia Totalis (AT) in adult subjects. Subjects will be required to have a clinical diagnosis of stable AA, AU, or AT. A total of approximately 80 subjects will be randomized.

Conditions

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Alopecia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

OTHER

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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400mg BID (Low dose)

ATI-501 low dose - oral administration

Group Type ACTIVE_COMPARATOR

ATI-501 400mg BID (Low dose)

Intervention Type DRUG

ATI-501 400mg BID oral low dose for oral administration

600mg BID (Mid dose)

ATI-501 mid dose - oral administration

Group Type ACTIVE_COMPARATOR

ATI-501 600mg BID (Mid dose)

Intervention Type DRUG

ATI-501 600mg BID oral mid dose for oral administration

800mg BID (High dose)

ATI-501 high dose - oral administration

Group Type ACTIVE_COMPARATOR

ATI-501 800mg BID (High dose)

Intervention Type DRUG

ATI-501 800mg BID high dose for oral administration

Placebo

Placebo - oral administration

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo - oral administration

Interventions

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ATI-501 400mg BID (Low dose)

ATI-501 400mg BID oral low dose for oral administration

Intervention Type DRUG

ATI-501 600mg BID (Mid dose)

ATI-501 600mg BID oral mid dose for oral administration

Intervention Type DRUG

ATI-501 800mg BID (High dose)

ATI-501 800mg BID high dose for oral administration

Intervention Type DRUG

Placebo

Placebo - oral administration

Intervention Type DRUG

Other Intervention Names

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Active comparator: Low dose Comparator : Mid dose Comparator: high dose - oral administration

Eligibility Criteria

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Inclusion Criteria

Subjects must meet the following criteria to be eligible for participation in the study:

1. Able to comprehend and willing to sign an Informed Consent Form (ICF).
2. Male or non-pregnant, non-nursing female ≥ 18 years old at the time of informed consent.
3. Have a clinical diagnosis of stable Alopecia Areata (AA), Alopecia Universalis (AU), or Alopecia Totalis (AT).
4. If the subject is a woman of childbearing potential (WOCBP), she must have:

* Negative urine and serum pregnancy tests at Screening (Visit 1); and
* A negative urine pregnancy test at Baseline (Visit 2); and
* Agree to not be planning a pregnancy during the study duration and use a highly effective method of contraception for the duration of the study and 30 days after the last dose of study medication. (Refer to Section 8.4.2).
5. Be in good general health and free of any known disease state or physical condition which, in the investigator's opinion, might impair evaluation of the subject or which might expose the subject to an unacceptable risk by study participation.
6. Be willing to maintain the same hair style and hair dyeing throughout the study period.
7. Subjects taking hormonal replacement therapies must be on stable doses for 6 months prior to enrollment and remain on a maintenance dose throughout the study.
8. Subjects taking thyroid replacement medication must be on stable doses for 6 months prior to enrollment and remain on a maintenance dose throughout the study.
9. Sexually active male subjects whose partner is a WOCBP must agree to use a barrier method of contraception from the first dose of study medication to at least 30 days after the last dose of study medication.

Exclusion Criteria

Subjects are excluded from this study if any 1 or more of the following criteria is met:

1. Females who are nursing, pregnant, or planning to become pregnant for the duration of the study and up to 30 days after the last dose of study medication.
2. Diffuse AA or a history of an atypical pattern of AA.
3. Concomitant hair loss disorder (by history or physical exam) such as androgenetic alopecia (AGA) or scarring alopecia.
4. Active skin disease on the scalp or a history of skin disease on the scalp that in the opinion of the investigator would interfere with study assessments of efficacy or safety.
5. Active scalp trauma or other condition affecting the scalp that, in the investigator's opinion, may affect the course of AA, AU or AT or interfere with the study conduct or evaluations.
6. The presence of a permanent or difficult to remove hairpiece or wig that will, in the opinion of the investigator, interfere with study assessments if not removed at each visit.
7. History of, or current, severe, progressive or uncontrolled autoimmune, metabolic, hepatic, endocrine, renal, gastrointestinal, pulmonary, cardiovascular, genitourinary, or hematological disease, neurologic or cerebral disorders, or coagulation disorders that, as determined by the Investigator, would preclude participation in and completion of study assessments.
8. History of, current or suspected systemic or cutaneous malignancy and /or lymphoproliferative disease, other than subjects with a history of adequately treated and well healed and completely cleared non-melanoma skin cancers (e.g. basal or squamous cell carcinoma) treated successfully at least 1 year prior to study entry with no evidence of disease.
9. Evidence of active or latent bacterial (including tuberculosis) or viral infections at the time of enrollment, or history of incompletely treated or untreated tuberculosis. Subjects who have completed therapy for latent tuberculosis may participate.
10. History of serious local infection (e.g., cellulitis, abscess) or systemic infection including but not limited to a history of treated infection (e.g., pneumonia, septicemia) within 3 months prior to Baseline. Subjects on an antibiotic for a nonserious, acute local infection must complete the course prior to enrollment into the study.
11. Positive for HIV, Hepatitis B or C. Subjects with serologic evidence of Hepatitis B vaccination (HepB surface Ab without the presence of Hep B surface Ag will be allowed to participate).
12. History of recurrent herpes zoster (more than one episode) or disseminated herpes zoster (a single episode) or disseminated herpes simplex (single episode) or cytomegalovirus (CMV) that resolved less than 2 months before study enrollment. Subjects with a history of frequent outbreaks of Herpes Simplex Virus (defined as 4 or more outbreaks a year).
13. Subjects who have received any of the following treatments for the timeframes specified below:

* Disease Modifying Anti-Rheumatic Drugs (DMARDS), Biologics or immunosuppressants, including but not limited to: anakinra, adalimumab, azathioprine, corticosteroids, cyclosporine, etanercept, infliximab, methotrexate, TNF inhibitors, ustekinumab within 1 month or 5 half-lives (whichever is greater) of Baseline (Visit 2).
* Plaquenil within 2 months of Baseline (Visit 2).
* Janus kinase (JAK) inhibitors (oral or topical) within 6 months of Baseline (Visit 2).
* Intralesional steroids or platelet rich plasma injections in the scalp within 1 month of Baseline (Visit 2).
* Topical treatments on the scalp with anthralin, bimatoprost, corticosteroids, diphencyprone, diphenylcyclopropenone (DPCP), squaric acid dibutylester (SADBE), minoxidil, pimecrolimus, or tacrolimus within 1 month of Baseline (Visit 2).
* Phototherapy (narrow band Ultraviolet B \[NB UVB\] or broadband therapy) within 4 weeks of Baseline (Visit 2).
14. Participation in an investigational drug or device trial in which administration of an investigational drug or device occurred within 30 days or 5 half-lives (whichever is longer) of Baseline (Visit 2).
15. Any condition possibly affecting oral drug absorption, e.g., gastrectomy, clinically significant diabetic gastroenteropathy, or certain types of bariatric surgery such as gastric bypass. Procedures such as gastric banding are not exclusionary.
16. Unwillingness to refrain from weaves, hair extensions, or shaving of the scalp for at least two weeks prior to a study visit, at the discretion of the investigator, based on the ability to assess hair growth.
17. Vaccination with a live or attenuated vaccine within 6 weeks prior to Baseline (Visit 2) or planned vaccination with these vaccines at any time during treatment or within 6 weeks following discontinuation of study medication.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Aclaris Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Susan Moran, RN

Role: STUDY_CHAIR

Aclaris Therapeutics

Locations

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Aclaris Investigator Site

Hot Springs, Arkansas, United States

Site Status

Aclaris Investigator Site

Rogers, Arkansas, United States

Site Status

Aclaris Investigator Site

Denver, Colorado, United States

Site Status

Aclaris Investigator Site

Boynton Beach, Florida, United States

Site Status

Aclaris Investigator Site

Miami, Florida, United States

Site Status

Aclaris Investigator Site

Sanford, Florida, United States

Site Status

Aclaris Investigator Site

Snellville, Georgia, United States

Site Status

Aclaris Investigator Site

Clinton Township, Michigan, United States

Site Status

Aclaris Investigator Site

Detroit, Michigan, United States

Site Status

Aclaris Investigator Site

Fridley, Minnesota, United States

Site Status

Aclaris Investigator Site

Minneapolis, Minnesota, United States

Site Status

Aclaris Investigator Site

Saint Joseph, Missouri, United States

Site Status

Aclaris Investigator Site

Omaha, Nebraska, United States

Site Status

Aclaris Investigator Site

Las Vegas, Nevada, United States

Site Status

Aclaris Investigator Site

New York, New York, United States

Site Status

Aclaris Investigator Site

Rochester, New York, United States

Site Status

Aclaris Investigator Site

Portland, Oregon, United States

Site Status

Aclaris Investigator Site

Greenville, South Carolina, United States

Site Status

Aclaris Investigator Site

Knoxville, Tennessee, United States

Site Status

Aclaris Investigator Site

Nashville, Tennessee, United States

Site Status

Aclaris Investigational Site

Austin, Texas, United States

Site Status

Aclaris Investigator Site

Houston, Texas, United States

Site Status

Aclaris Investigator Site

San Antonio, Texas, United States

Site Status

Aclaris Investigator Site

Lynchburg, Virginia, United States

Site Status

Aclaris Investigator Site

Norfolk, Virginia, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Document Type: Informed Consent Form

View Document

Other Identifiers

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ATI-501-AUAT-201

Identifier Type: -

Identifier Source: org_study_id

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