Establishing the Safety and Efficacy of Reloxaliase in Patients With Enteric Hyperoxaluria

NCT ID: NCT03847090

Last Updated: 2022-06-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

92 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-08-26

Study Completion Date

2022-05-19

Brief Summary

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The purpose of this study is to determine the efficacy, durability and long-term safety of reloxaliase in patients with enteric hyperoxaluria.

Detailed Description

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This is a phase 3, global, multi-center, randomized, double-blind, placebo-controlled study. This study is designed to determine the short- and long-term efficacy of reloxaliase in terms of reducing urinary oxalate excretion and clinical benefits compared to placebo.

Conditions

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Enteric Hyperoxaluria

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Reloxaliase

Reloxaliase (ALLN-177) 142 mg of oxalate decarboxylase (equivalent to 3,750 units of enzyme activity) per capsule

Group Type EXPERIMENTAL

Reloxaliase

Intervention Type DRUG

Reloxaliase 2 capsules, orally, with each meal/snack, 3 to 5 times per day

placebo

placebo capsule

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo 2 capsules, orally, with each meal/snack, 3 to 5 times per day

Interventions

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Reloxaliase

Reloxaliase 2 capsules, orally, with each meal/snack, 3 to 5 times per day

Intervention Type DRUG

Placebo

Placebo 2 capsules, orally, with each meal/snack, 3 to 5 times per day

Intervention Type DRUG

Other Intervention Names

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ALLN-177 Oxalate decarboxylase Placebo capsule

Eligibility Criteria

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Inclusion Criteria

1. Provided informed consent
2. Age 18 years or older
3. Has an underlying enteric disorder associated with malabsorption with known or suspected history of hyperoxaluria (e.g., history of kidney stones or oxalate nephropathy)
4. Urinary oxalate ≥ 50 mg/24 hr
5. Has at least 1 documented kidney stone within 2 years

Exclusion Criteria

1. Acute renal failure or estimated glomerular filtration rate (eGFR) \< 30 mL/minute/1.73 m2
2. Has a known genetic, congenital, or other cause of kidney stones
3. Unable or unwilling to discontinue Vitamin C supplementation \>200mg daily
4. Cannot establish baseline kidney stone burden
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Allena Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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David Clark, MD

Role: STUDY_DIRECTOR

Allena Pharmaceuticals Inc

Locations

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University of Alabama- Department of Urology

Birmingham, Alabama, United States

Site Status

Alliance for Multispecialty Research, LLC

Mobile, Alabama, United States

Site Status

Aventiv Research Inc.

Mesa, Arizona, United States

Site Status

Arizona Kidney Disease and Hypertension Center (AKDHC)- Phoenix

Peoria, Arizona, United States

Site Status

Arizona Kidney Disease and Hypertension Center (AKDHC)- Glendale

Phoenix, Arizona, United States

Site Status

Mayo Mercy Hospital

Phoenix, Arizona, United States

Site Status

Urological Associates of Southern Arizona

Tucson, Arizona, United States

Site Status

Banner University Medical Center

Tucson, Arizona, United States

Site Status

Arkansas Urology

Little Rock, Arkansas, United States

Site Status

Applied Research Center of Arkansas

Little Rock, Arkansas, United States

Site Status

Renal Consultants Medical Group

Granada Hills, California, United States

Site Status

Amicis Research

Northridge, California, United States

Site Status

University of California, San Diego (UCSD) Health System

San Diego, California, United States

Site Status

University of California- San Francisco (UCSF)

San Francisco, California, United States

Site Status

Stanford University School of Medicine

Stanford, California, United States

Site Status

Sutter Health- Sacramento

Vacaville, California, United States

Site Status

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status

South Florida Nephrology Group PA Research Div

Coral Springs, Florida, United States

Site Status

University of Florida College of Medicine

Gainesville, Florida, United States

Site Status

Quantum Clinical Research

Hialeah, Florida, United States

Site Status

Mayo Clinic

Jacksonville, Florida, United States

Site Status

Pro-Care Research Center, Corp

Miami Gardens, Florida, United States

Site Status

Avanza Medical Research Center

Pensacola, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Idaho Catalyst Clinical Research

Idaho Falls, Idaho, United States

Site Status

Idaho Urologic Institute

Meridian, Idaho, United States

Site Status

IU Health Physicians

Carmel, Indiana, United States

Site Status

Indiana University (IU) Nephrology

Indianapolis, Indiana, United States

Site Status

University of Iowa

Iowa City, Iowa, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

University of Kentucky

Lexington, Kentucky, United States

Site Status

Regional Urology

Shreveport, Louisiana, United States

Site Status

Chesapeake Urology Associates, LLC d/b/a/ Chesapeake Urology Research Associates

Glen Burnie, Maryland, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

Mayo Clinic- Department of Nephrology Hyperoxaluria Center

Rochester, Minnesota, United States

Site Status

University of Missouri Healthcare

Columbia, Missouri, United States

Site Status

Montana Medical Research, Inc

Missoula, Montana, United States

Site Status

Sheldon J. Freedman, MD

Las Vegas, Nevada, United States

Site Status

New York Presbyterian/Queens

Flushing, New York, United States

Site Status

Long Island Gastrointestinal Research Group

Great Neck, New York, United States

Site Status

New York University School of Medicine- Langone Medical Center

New York, New York, United States

Site Status

University of Rochester

Rochester, New York, United States

Site Status

University of North Carolina (UNC) - Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Associated Urologists of North Carolina

Raleigh, North Carolina, United States

Site Status

University of Cincinnati (UC) - Department of Nephrologyv

Cincinnati, Ohio, United States

Site Status

Ohio State University (OSU)-Renal Division

Columbus, Ohio, United States

Site Status

Clinical Research Solutions- Middleburg Heights

Middleburg Heights, Ohio, United States

Site Status

Genito-Urinary Surgeons

Toledo, Ohio, United States

Site Status

Oregon Health and Science University (OHSU)

Portland, Oregon, United States

Site Status

Northeast Clinical Research Center

Bethlehem, Pennsylvania, United States

Site Status

Lifespan Physician Group Minimally Invasive Urology Institute

Providence, Rhode Island, United States

Site Status

Carolina Urologic Research Center

Myrtle Beach, South Carolina, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Accelemed Research Institute

Austin, Texas, United States

Site Status

Renal Disease Research Institute

Dallas, Texas, United States

Site Status

Houston Metro Urology

Houston, Texas, United States

Site Status

University of Texas Health Science Center at San Antonio

San Antonio, Texas, United States

Site Status

Urology San Antonio Research

San Antonio, Texas, United States

Site Status

Baylor Scott and White Research Institute- Temple

Temple, Texas, United States

Site Status

Virginia Urology

Richmond, Virginia, United States

Site Status

Urology of Virginia

Virginia Beach, Virginia, United States

Site Status

University of Wisconsin - Division of Nephrology

Madison, Wisconsin, United States

Site Status

Medizinische Universitat Wien, Innere Medizin III

Vienna, , Austria

Site Status

UVC Brugmann University Hospital- Centre Hospitalier Universitaire

Brussels, , Belgium

Site Status

Universite Libre de Bruxelles -Hospital Erasme

Brussels, , Belgium

Site Status

University Hospital Gent

Ghent, , Belgium

Site Status

Hospital das Clinicas de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital das Clinicas da UFMG

Belo Horizonte, , Brazil

Site Status

Faculdade de Medicina do ABC

Santo André, , Brazil

Site Status

Pesquisare Saude

Santo André, , Brazil

Site Status

University of Alberta- Division of Urology

Edmonton, Alberta, Canada

Site Status

Silverado Research Inc

Victoria, British Columbia, Canada

Site Status

Centre de Recherche Du Centre Hospitalier de l'Universite de Montreal

Montreal, Quebec, Canada

Site Status

Alpha Recherche Clinique

Québec, Quebec, Canada

Site Status

Polyclinic Solme

Zagreb, , Croatia

Site Status

Hopital Beaujon_AP_HP

Clichy, , France

Site Status

AP-HM Hospital de la Conception

Marseille, , France

Site Status

Hospital Tenon-AP-HP

Paris, , France

Site Status

CHRU de Nancy-Hopitaux de Brabois

Vandœuvre-lès-Nancy, , France

Site Status

Charite Universitaetsmedizin- Berlin

Berlin, , Germany

Site Status

Klinikum der Universitaet- Muenche

München, , Germany

Site Status

Azienda USL Toscana Centro-Ospedale Santa Maria Nuova

Florence, , Italy

Site Status

IRCCS Azienda Ospedaliera Universitaria San Martino IST

Genova, , Italy

Site Status

Fondazione Policlinico Universitario A.Gemelli IRCCS - Universita Cattolica del Sacro Cuore

Rome, , Italy

Site Status

Invesclinic MX

Irapuato, Gto, C.P, Mexico

Site Status

ICARO Investigaciones en Medicina SA de CV/Hospital Christus Muguerza

Chihuahua City, , Mexico

Site Status

Clinstile, S.A. de C.V- Col. Roma Norte Delegacion

Cuauhtémoc, , Mexico

Site Status

Centro specializado en Diabetes, Obesidad y Prevencion de Enfermedades Cardiovasculares

Mexico City, , Mexico

Site Status

Hospital Fernando da Fonseca

Amadora, , Portugal

Site Status

Centro Hospitalar Universitario de Sao Joao

Porto, , Portugal

Site Status

Sana Medical Center

Bucharest, , Romania

Site Status

Institutul Clinic Fundeni

Bucharest, , Romania

Site Status

Spitalul Clinic Universitar de Urgenta Bucuresti

Bucharest, , Romania

Site Status

ClinTrial/County Hospital Caracal

Caracal, , Romania

Site Status

Centru de Diagnostic si Tratament Affidea- Medicina Interna

Constanța, , Romania

Site Status

Clinic of Urology LLC

Penza, , Russia

Site Status

LLC Medsi St Petersburg

Saint Petersburg, , Russia

Site Status

S.M Kirov Military Medical Academy

Saint Petersburg, , Russia

Site Status

Medical Center "Reavita Med StP" LLC

Saint Petersburg, , Russia

Site Status

City Hospital #15

Saint Petersburg, , Russia

Site Status

Saratov State Medical University, n.a. V.I. Razumosky

Saratov, , Russia

Site Status

Fundacio Puigvert

Barcelona, , Spain

Site Status

Hospital Universitari de Girona

Girona, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Inselspital, Universitaetsspital Bern Inselspital Bern University Hospital

Bern, , Switzerland

Site Status

Centre Hospitalier Universitaire Vaudois (CHUV) Lausanne Nephrology Department

Lausanne, , Switzerland

Site Status

University Hospital of Wales

Cardiff, , United Kingdom

Site Status

Darent Valley Hospital

Dartford, , United Kingdom

Site Status

The Royal Free Hospital

London, , United Kingdom

Site Status

South Tyneside District Hospital - South Shields

South Shields, , United Kingdom

Site Status

Wrexham Maelor Hospital

Wrexham, , United Kingdom

Site Status

Countries

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United States Austria Belgium Brazil Canada Croatia France Germany Italy Mexico Portugal Romania Russia Spain Switzerland United Kingdom

References

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Langman CB, Grujic D, Pease RM, Easter L, Nezzer J, Margolin A, Brettman L. A Double-Blind, Placebo Controlled, Randomized Phase 1 Cross-Over Study with ALLN-177, an Orally Administered Oxalate Degrading Enzyme. Am J Nephrol. 2016;44(2):150-8. doi: 10.1159/000448766. Epub 2016 Aug 17.

Reference Type BACKGROUND
PMID: 27529510 (View on PubMed)

Lingeman JE, Pareek G, Easter L, Pease R, Grujic D, Brettman L, Langman CB. ALLN-177, oral enzyme therapy for hyperoxaluria. Int Urol Nephrol. 2019 Apr;51(4):601-608. doi: 10.1007/s11255-019-02098-1. Epub 2019 Feb 19.

Reference Type BACKGROUND
PMID: 30783888 (View on PubMed)

Related Links

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https://www.ncbi.nlm.nih.gov/pubmed/27529510

A Double-Blind, Placebo Controlled, Randomized Phase 1 Cross-Over Study with ALLN-177, an Orally Administered Oxalate Degrading Enzyme

https://www.ncbi.nlm.nih.gov/pubmed/30783888

ALLN-177, oral enzyme therapy for hyperoxaluria

Other Identifiers

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2018-000921-29

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

ALLN-177-302

Identifier Type: -

Identifier Source: org_study_id

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