A Study to Evaluate the Real-world Effectiveness and Usage of Alprolix in Patients With Haemophilia B in France

NCT ID: NCT03655340

Last Updated: 2024-09-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

91 participants

Study Classification

OBSERVATIONAL

Study Start Date

2018-09-12

Study Completion Date

2022-03-16

Brief Summary

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Alprolix (rFIXFc) is a recombinant extended half-life coagulation factor product. The purpose of this non-interventional study is to describe the real-world usage and effectiveness of Alprolix in the on-demand and prophylactic treatment of haemophilia B.

Detailed Description

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Conditions

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Haemophilia B

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Prophylactic patients

Alprolix will be prescribed according to local practice and administered by patients with haemophilia B for prophylactic treatment

Alprolix

Intervention Type DRUG

Extended half-life factor IX product

On demand patients

Alprolix will be prescribed according to local practice and administered by patients with haemophilia B for on-demand treatment

Alprolix

Intervention Type DRUG

Extended half-life factor IX product

Interventions

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Alprolix

Extended half-life factor IX product

Intervention Type DRUG

Other Intervention Names

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Eftrenonacog alfa, rFIXFc

Eligibility Criteria

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Inclusion Criteria

* Have a diagnosis of haemophilia B and been treated previously with factor IX Product
* Have started Alprolix treatment prior to enrolment visit, or at enrolment prescribed treatment with Alprolix, regardless of participation in the study
* Signed and dated informed consent provided by the patient, or the patient's legally acceptable representative for patients under the legal age, before any study-related activities are undertaken. Assent should be obtained from paediatric patients according to local regulations

Exclusion Criteria

* Participation in an investigational medicinal product trial at enrolment visit
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Swedish Orphan Biovitrum

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Elena Santagostino, MD

Role: STUDY_DIRECTOR

Swedish Orphan Biovitrum

Locations

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Swedish Orphan Biovitrum Research Site (CHU de Bordeaux)

Bordeaux, , France

Site Status

Swedish Orphan Biovitrum Research Site

Brest, , France

Site Status

Swedish Orphan Biovitrum Research Site

Caen, , France

Site Status

Swedish Orphan Biovitrum Research Site

Chambéry, , France

Site Status

Swedish Orphan Biovitrum Research Site

Clermont-Ferrand, , France

Site Status

Swedish Orphan Biovitrum Research Site

Dijon, , France

Site Status

Swedish Orphan Biovitrum Research Site

La Réunion, , France

Site Status

Swedish Orphan Biovitrum Research Site

Lille, , France

Site Status

Swedish Orphan Biovitrum Research Site

Marseille, , France

Site Status

Swedish Orphan Biovitrum Research Site

Montpellier, , France

Site Status

Swedish Orphan Biovitrum Research Site

Nantes, , France

Site Status

Swedish Orphan Biovitrum Research Site

Nîmes, , France

Site Status

Swedish Orphan Biovitrum research site

Paris, , France

Site Status

Swedish Orphan Biovitrum research site

Poitiers, , France

Site Status

Swedish Orphan Biovitrum research site

Rennes, , France

Site Status

Swedish Orphan Biovitrum Research Site

Rouen, , France

Site Status

Swedish Orphan Biovitrum research site

Strasbourg, , France

Site Status

Swedish Orphan Biovitrum Research Site

Toulouse, , France

Site Status

Countries

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France

References

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Chambost H, Repesse Y, Genre-Volot F, Desprez D, Castet SM, Vanderbecken S, Zidi M, Gandossi C, Nuesch E, Palmborg H, Santagostino E; B-SURE Study Group. Real-world usage and effectiveness of recombinant factor IX Fc in haemophilia B from the B-SURE study in France. Ther Adv Hematol. 2025 Jan 26;16:20406207241311535. doi: 10.1177/20406207241311535. eCollection 2025.

Reference Type DERIVED
PMID: 39872008 (View on PubMed)

Other Identifiers

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Sobi.Alprolix-001

Identifier Type: -

Identifier Source: org_study_id

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