Study To Compare On-Demand Treatment To A Prophylaxis Regimen Of BeneFIX In Subjects With Moderately Severe to Severe Hemophilia B

NCT ID: NCT01335061

Last Updated: 2015-06-08

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

25 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-09-30

Study Completion Date

2014-04-30

Brief Summary

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The purpose of this study will be to determine if a once-weekly prophylaxis regimen of BeneFIX in subjects with moderately severe to severe Hemophilia B is safe and effective.

Detailed Description

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Conditions

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Hemophilia B

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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BeneFIX

Group Type OTHER

Nonacog alfa

Intervention Type BIOLOGICAL

Period 1: During on-demand period, dosing at the discretion of investigator.

Nonacog alfa

Intervention Type BIOLOGICAL

Period 2: During the prophylaxis period, 100 IU/kg once weekly

Interventions

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Nonacog alfa

Period 1: During on-demand period, dosing at the discretion of investigator.

Intervention Type BIOLOGICAL

Nonacog alfa

Period 2: During the prophylaxis period, 100 IU/kg once weekly

Intervention Type BIOLOGICAL

Other Intervention Names

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BeneFIX BeneFIX

Eligibility Criteria

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Inclusion Criteria

* Documented history of moderately-severe to severe hemophilia B (FIX activity \</=2%).
* Male subjects, aged 12 years to 65 years.
* Subjects with at least 100 exposure days (EDs) to factor IX products.
* Subjects with a minimum of 12 bleeding episodes, 6 of which must be joint bleeds, in the 12-month period before the Screening visit.

Exclusion Criteria

* Subjects who have received FIX as a primary or secondary prophylaxis regimen within the last 12 months prior to the Screening visit.
* Subjects who have had major surgery or an orthopedic surgical procedure within the past 3 months prior to Screening visit.
* Subjects for which major surgery or orthopedic surgery is planned within the duration of study participation.
* Subjects with a past history of, or current FIX inhibitor, defined as \>ULN (upper limit of normal) of the reporting laboratory.
* Subjects with a known hypersensitivity to any FIX product or hamster protein.
Minimum Eligible Age

12 Years

Maximum Eligible Age

65 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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UMBAL Sveti Georgi, Klinika po hematologia

Plovdiv, , Bulgaria

Site Status

The Ottawa Hospital

Ottawa, Ontario, Canada

Site Status

University Hospital Center Zagreb

Zagreb, , Croatia

Site Status

National Blood Centre

Kuala Lumpur, Kuala Lumpur, Malaysia

Site Status

Hospital Tengku Ampuan Afzan

Kuantan, Pahang, Malaysia

Site Status

Instituto Biomedico de Investigacion A.C.

Aguascalientes, Aguascalientes, Mexico

Site Status

Hospital y Clinica OCA

Monterrey, Nuevo León, Mexico

Site Status

Nzoz Triclinium

Warsaw, , Poland

Site Status

Klinika Hematologii, Nowotworow Krwi i Transplantacji Szpiku

Wroclaw, , Poland

Site Status

Singapore General Hospital

Singapore, , Singapore

Site Status

Eulji University Hospital

Daejeon, , South Korea

Site Status

Istanbul Universitesi Cerrahpasa Tip Fakultesi Ic Hastaliklari Anabilim Dali Hematoloji Bilim Dali

Fatih, Istanbul, Turkey (Türkiye)

Site Status

Hacettepe Universitesi Tip Fakultesi Ic Hastaliklari Anabilim Dali Hematoloji Bolumu

Ankara, , Turkey (Türkiye)

Site Status

Ege Universitesi Tip Fakultesi

Bornova/Izmir, , Turkey (Türkiye)

Site Status

Gaziantep Universitesi Tip Fakultesi Sahinbey Arastirma ve Uygulama Hastanesi Hematoloji Poliklinigi

Gaziantep, , Turkey (Türkiye)

Site Status

Erciyes Universitesi Tip Fakultesi

Kayseri, , Turkey (Türkiye)

Site Status

Erciyes Universitesi Tip Fakultesi Hastaneleri M. Kemal Dedeman Onkoloji Hastanesi

Kayseri̇, Erciyes, , Turkey (Türkiye)

Site Status

Countries

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Bulgaria Canada Croatia Malaysia Mexico Poland Singapore South Korea Turkey (Türkiye)

References

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Wojciechowski J, Gaitonde P, Hughes JH, Ravva P. Population Modeling of Factor IX Activity Following Administration of Fidanacogene Elaparvovec Gene Therapy in Participants with Hemophilia B. Clin Pharmacokinet. 2025 Oct;64(10):1531-1548. doi: 10.1007/s40262-025-01535-y. Epub 2025 Aug 1.

Reference Type DERIVED
PMID: 40750723 (View on PubMed)

Tortella BJ, Carr ME, Rendo P, Korth-Bradley J, Smith LM, Kavakli K. Once-weekly prophylaxis regimen of nonacog alfa in patients with hemophilia B: an analysis of timing of bleeding event onset. Blood Coagul Fibrinolysis. 2021 Apr 1;32(3):180-185. doi: 10.1097/MBC.0000000000001012.

Reference Type DERIVED
PMID: 33631774 (View on PubMed)

Related Links

Other Identifiers

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3090A1-3306

Identifier Type: OTHER

Identifier Source: secondary_id

2011-000520-15

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

B1821010

Identifier Type: -

Identifier Source: org_study_id

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