Study of Surgical Practices in Patients With Haemophilia A or B Treated With an Extended Half-life Recombinant Factor VIII-Fc or IX-Fc (ELOCTA®, ALPROLIX®)

NCT ID: NCT06158334

Last Updated: 2023-12-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Total Enrollment

400 participants

Study Classification

OBSERVATIONAL

Study Start Date

2022-06-01

Study Completion Date

2024-12-01

Brief Summary

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Haemophilia A and haemophilia B are inherited bleeding disorders resulting from the absence or deficiency of coagulation factors VIII and IX, respectively. The peri-operative period of people with haemophilia is commonly managed with replacement therapy.

In phase 3 studies of Elocta® (extended half-life recombinant factor VIII-Fc) and Alprolix® (extended half-life recombinant factor IX-Fc), haemostatic efficacy was demonstrated to be good or excellent, close to the haemostatic efficacy usually seen in people without haemophilia, with maintenance and stability of circulating FVIII and FIX levels compatible with the surgical procedure, while reducing the frequency of infusions and consumption of therapeutic units. In 2019, the National Protocol for Diagnosis and Care in haemophilia recommended 2 methods for managing patients with haemophilia in the peri-operative period, either discontinuous injections of standard or extended half-life factor VIII/IX or a continuous infusion of FVIII/IX.

Many countries, including France, have adopted these rFVIII/IXFc therapeuitic products and recommended their use in the surgical management of patients. However, the use of these two products in real life during surgery in haemophilic A and B patients has not been described in detail. It seems therefore relevant to better document their use in order to progressively specify their use during surgeries with varied bleeding risks.

Detailed Description

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Conditions

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Hemophilia A Hemophilia B

Keywords

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surgery Haemophilia A Haemophilia B Elocta® Alprolix®

Study Design

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Observational Model Type

COHORT

Study Time Perspective

CROSS_SECTIONAL

Study Groups

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Minor and major surgeries of patients with haemophilia A treated with Elocta®

Description of all surgical data (minor and major) on Elocta® (all dosage and treatment regimens)

Describe the respective haemostatic efficacy of Elocta® for haemopilia A during surgical procedures

Intervention Type DRUG

All surgical data will be collected: surgery, biology, administration of Elocta®, bleeding and transfusion, hemostatic efficacity, surgery complication and bleeding

Minor and major surgeries of patients with haemophilia B treated with Alprolix®

Description of all surgical data (minor and major) on Alprolix® (all dosage and treatment regimens)

Describe the respective haemostatic efficacy of Alprolix® for haemopilia B during surgical procedures

Intervention Type DRUG

All surgical data will be collected: surgery, biology, administration of Alprolix®, bleeding and transfusion, hemostatic efficacity, surgery complication and bleeding…

Interventions

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Describe the respective haemostatic efficacy of Elocta® for haemopilia A during surgical procedures

All surgical data will be collected: surgery, biology, administration of Elocta®, bleeding and transfusion, hemostatic efficacity, surgery complication and bleeding

Intervention Type DRUG

Describe the respective haemostatic efficacy of Alprolix® for haemopilia B during surgical procedures

All surgical data will be collected: surgery, biology, administration of Alprolix®, bleeding and transfusion, hemostatic efficacity, surgery complication and bleeding…

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* patient with Haemophilia A or B
* surgery performed with Elocta® or Alprolix®
* Information leaflet given to the patient who as reached the age of majority or to the parents or legal guardian for minors

Exclusion Criteria

* Any blood coagulation disorder other than Haemophilia A or B
* Patient with factor VIII or IX inhibitor
* Severe liver disease (serum ALAT/ASAT levels\> 5 x ULN)
* Severe renal disease (serum creatinine \> 2x ULN)
* Known hypersensitivity to the substances or its excipients
* patient participating in another clinical trial or having participated in another clinical trial within the previous 30 days (non-interventional studies are not a criterion for non-inclusion)
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hospices Civils de Lyon

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Centre de Référence en Hémophilie, hôpityal Louis Pradel, GHE- Hospices Civils de Lyon

Bron, , France

Site Status RECRUITING

Countries

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France

Central Contacts

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Anne LIEHNART, MD

Role: CONTACT

Phone: +33 4 72 11 88 10

Email: [email protected]

Emilie PROME COMBEL, RCA

Role: CONTACT

Phone: +33 4 72 11 66 99

Email: [email protected]

Facility Contacts

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Anne LIENHART, MD

Role: primary

Other Identifiers

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868

Identifier Type: -

Identifier Source: org_study_id