Registry for Patients With Lipodystrophy

NCT ID: NCT03553420

Last Updated: 2025-12-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Total Enrollment

5000 participants

Study Classification

OBSERVATIONAL

Study Start Date

2017-12-16

Study Completion Date

2068-01-31

Brief Summary

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Given the lack of knowledge on lipodystrophies, the medical and social responsibility for the persons affected by it calls for the monitoring of the progression over long periods of time. Sensible clinical and basic research into rare diseases such as lipodystrophy is only possible in multi-location networks with sufficient case numbers. Also, reliable information on the incidence of certain manifestation patterns, health status, etc. is of utmost importance for health care and health policy in this rare disease.

Therefore, the European Consortium of Lipodystrophies (ECLip), an association of European experts on lipodystrophy, has launched a registry (OSSE) for lipodystrophies which is committed to help to improve the research conditions by consolidating this kind of information in a registry.

Detailed Description

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As lipodystrophies are rare diseases subdivided into yet rarer sub-groups, research in this field requires international co-operation.

The European Consortium of Lipodystrophy (ECLip) consists of an association of European experts in the field of lipodystrophy. It has set up a Registry Board to implement a registry for patients with lipodystrophy using the Open Source Software OSSE (Open Source Registry System for Rare Diseases in the EU), which is a web based platform focused on a federated approach that allows to perform distributed searches which are designed to comply data protection requirements and preserve data sovereignty. To ensure data protection, medical and identifying data will be stored on two different servers both run by the Institute for Epidemiology and Medical Biometry of the University of Ulm.

Medical centers from all over the world where patients are treated with lipodystrophy are invited to join the ECLip Registry and to become ECLip Registry members. Upon registration, they can enter patient data after they have obtained local ethic committee permission and the patient in question has given written consent to this. Data entry is done at the individual locations via a web-based user interface. Identifying data are recorded directly into the identity management system. Communication between the identity management and the OSSE registry happens via a web browser.

The aim of the patient registry is to compile data on the natural history of each different sub-group of lipodystrophies, their comorbidities, treatment options used and medical and quality of life out-come for the patients. For this, the following data retrieved from regular patient visits are collected:

* Precise diagnosis including moleculargenetic results
* Clinical presentation and comorbidities
* Laboratory changes and results of diagnostic procedures
* Natural course of the disease including age at onset of disease and comorbidities
* Family history

Research within this registry can be performed by participating clinicians/researchers and third parties after a research proposal has be accepted by the responsible committee of the ECLip. The registry aims to answer the following questions

* new insights into the pathophysiology of lipodystrophy
* improve therapeutic options for the patients
* compile information material for patients, families and relevant professionals

Conditions

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Lipodystrophy Acquired Lipodystrophy Congenital

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

PROSPECTIVE

Eligibility Criteria

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Inclusion Criteria

* lipodystrophy

Exclusion Criteria

* lipodystrophy due to anti-retroviral drugs
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Sorbonne University

OTHER

Sponsor Role collaborator

University Hospital, Lille

OTHER

Sponsor Role collaborator

University of Cambridge

OTHER

Sponsor Role collaborator

Endocrinology Research Centre, Moscow

OTHER_GOV

Sponsor Role collaborator

University of Leipzig

OTHER

Sponsor Role collaborator

University of Amsterdam

OTHER

Sponsor Role collaborator

Dokuz Eylul University

OTHER

Sponsor Role collaborator

IRCCS Azienda Ospedaliero-Universitaria di Bologna

OTHER

Sponsor Role collaborator

University of Rome Tor Vergata

OTHER

Sponsor Role collaborator

University of Pisa

OTHER

Sponsor Role collaborator

University of Santiago de Compostela

OTHER

Sponsor Role collaborator

Università degli Studi del Piemonte Orientale Amedeo Avogadro

OTHER

Sponsor Role collaborator

University Hospital Muenster

OTHER

Sponsor Role collaborator

Szeged University

OTHER

Sponsor Role collaborator

Centro Hospitalar do Porto

OTHER

Sponsor Role collaborator

University Medical Centre Ljubljana

OTHER

Sponsor Role collaborator

Medical University of Vienna

OTHER

Sponsor Role collaborator

National and Kapodistrian University of Athens

OTHER

Sponsor Role collaborator

Stoffwechselzentrum St. Gallen

UNKNOWN

Sponsor Role collaborator

National Taiwan University Hospital

OTHER

Sponsor Role collaborator

Marmara University

OTHER

Sponsor Role collaborator

University of Palermo

OTHER

Sponsor Role collaborator

Attikon Hospital

OTHER

Sponsor Role collaborator

Kinderkrankenhaus auf der Bult

OTHER

Sponsor Role collaborator

Hopital Universitaire Robert-Debre

OTHER

Sponsor Role collaborator

University of Milan

OTHER

Sponsor Role collaborator

C.I. Parhon National Institute of Endocrinology

OTHER

Sponsor Role collaborator

University of Ulm

OTHER

Sponsor Role lead

Responsible Party

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Julia von Schnurbein

Prinicipal Investigator

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Martin Wabitsch, Prof. Dr.

Role: STUDY_CHAIR

University of Ulm

David Araujo-Vilar, Prof. Dr.

Role: PRINCIPAL_INVESTIGATOR

Santiago de Compostela University

Julia von Schnurbein, Dr.

Role: PRINCIPAL_INVESTIGATOR

University of Ulm

Gabriele Nagel, Prof.

Role: PRINCIPAL_INVESTIGATOR

University of Ulm

Camille Vatier, Dr.

Role: PRINCIPAL_INVESTIGATOR

Pierre et Marie Curie School of Medicine (Paris)

Marie-Christine Vantyghem, Prof.

Role: PRINCIPAL_INVESTIGATOR

Lille University

Giovanni Ceccarini, Dr.

Role: PRINCIPAL_INVESTIGATOR

Endocrine Unit, University Hospital of Pisa

David Savage, Prof.

Role: PRINCIPAL_INVESTIGATOR

University of Cambridge Metabolic Research Laboratories

Locations

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Medical University of Vienna

Vienna, , Austria

Site Status RECRUITING

Lille University

Lille, , France

Site Status RECRUITING

AP-HP Nord Université de Paris, Hôpital Universitaire Robert-Debré

Paris, , France

Site Status RECRUITING

Pierre et Marie Curie School of Medicine, Sorbonne University

Paris, , France

Site Status RECRUITING

Kinder-und Jugendkrankenhaus AUF DER BULT

Hanover, , Germany

Site Status RECRUITING

Department of Internal Medicine (Endocrinology and Nephrology), University of Leipzig

Leipzig, , Germany

Site Status RECRUITING

Med. Klinik B für Gastroenterologie und Hepatologie, Universitätsklinikum Münster

Münster, , Germany

Site Status RECRUITING

Dept for Pediatrics and Adolescent Medicine, University of Ulm: Interdisciplinary obesity clinic

Ulm, , Germany

Site Status RECRUITING

National and Kapodistrian University of Athens

Athens, , Greece

Site Status RECRUITING

Second Department of Internal Medicine, Medical School, National and Kapodistrian University of Athens, Attikon University Hospital

Athens, , Greece

Site Status RECRUITING

University of Szeged, Department of Internal Medicine

Szeged, , Hungary

Site Status RECRUITING

Endocrinology Unit, Department of Clinical and Medical science, S. Orsola-Malpighi Hospital , University of Bologna

Bologna, , Italy

Site Status RECRUITING

Policlinic University Hospital of Milan

Milan, , Italy

Site Status RECRUITING

Universita del piemonte Orientale

Novara, , Italy

Site Status RECRUITING

Palermo University

Palermo, , Italy

Site Status RECRUITING

Endocrine Unit of University Hospital of Pisa

Pisa, , Italy

Site Status RECRUITING

Tor Vergata University - Policlinico of Tor Vergata

Roma, , Italy

Site Status RECRUITING

Academic Medical Center, University of Amsterdam

Amsterdam, , Netherlands

Site Status RECRUITING

Abel Salazar Biomedical Sciences Institute - University of Porto

Porto, , Portugal

Site Status RECRUITING

C. I. Parhon National Institute of Endocrinology, Bucharest, Romania

Bucharest, , Romania

Site Status RECRUITING

Endocrinology Research Centre

Moscow, , Russia

Site Status RECRUITING

University Medical Center Ljubljana - Clinical Institute of Medical Genetics

Ljubljana, , Slovenia

Site Status RECRUITING

Santiago de Compostela University

Santiago de Compostela, , Spain

Site Status RECRUITING

Stoffwechselzentrum friendlydocs

Sankt Gallen, , Switzerland

Site Status RECRUITING

National Taiwan University Hospital

Taipei, , Taiwan

Site Status RECRUITING

Marmara University, Pediatric Endocrinology and Diabetes

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

Dokuz Eylul University School of Medicine

Izmir, , Turkey (Türkiye)

Site Status RECRUITING

University of Cambridge Metabolic Research Laboratories

Cambridge, , United Kingdom

Site Status RECRUITING

Countries

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Austria France Germany Greece Hungary Italy Netherlands Portugal Romania Russia Slovenia Spain Switzerland Taiwan Turkey (Türkiye) United Kingdom

Central Contacts

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Julia von Schnurbein, Dr.

Role: CONTACT

0049 731 500 ext. 57401

Martin Wabitsch, Prof. Dr.

Role: CONTACT

0049 731 500 ext. 57401

Facility Contacts

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Thomas Scherer, M.D.

Role: primary

Marianna Beghini, M.D.

Role: backup

Marie-Christine Vantyghem, Prof.

Role: primary

Elise Bismuth, Dr.

Role: primary

Camille Vatier, Dr.

Role: primary

Corinne Vigouroux, Prof. Dr.

Role: backup

Jantje Weiskorn, Dr.

Role: primary

Konstanze Miehle, Dr.

Role: primary

Hartmut Schmidt, Prof.

Role: primary

Elena Vorona, Dr. med.

Role: backup

Martin Wabitsch, Prof. Dr.

Role: primary

0049 731 500 ext. 57401

Julia von Schnurbein, Dr. med.

Role: backup

0049 731 500 ext. 57401

Alexandraki, Prof.

Role: primary

Spyroglou, Prof.

Role: backup

Vaia Lambadiari, Prof.

Role: primary

Eva Csajbok, Dr.

Role: primary

Alessandra Gambineri, Ass. Prof.

Role: primary

Giovanna Lattanzi

Role: backup

Giulia Rodari, Dr.

Role: primary

Flavia Prodam, Dr

Role: primary

Gianluca Aimaretti, Prof

Role: backup

Silvio Buscemi, Prof.

Role: primary

Giovanni Ceccarini, Prof. Dr.

Role: primary

Ferruccio Santini, Prof. Dr.

Role: backup

+39 050 544 ext. 723

Giusepe Novelli, Prof

Role: primary

Maria Rosaria D'Apice, Dr

Role: backup

Kleinendorst Lotte, Dr.

Role: primary

Marjoleine Broekema, Dr.

Role: backup

Ermelinda Santos Silva, Prof. Dra

Role: primary

Iuliana Gherlan

Role: primary

Marina Shestakova, MD

Role: primary

Karin Writzl, Dr.

Role: primary

003861522 ext. 6031

David Araujo-Vilar, Prof. Dr.

Role: primary

Antía Fernández Pombo

Role: backup

Katrin Heldt, MD

Role: primary

Ni-Chung Lee, Dr.

Role: primary

Belma Haliloglu, Prof.

Role: primary

Baris Akinci

Role: primary

David Savage, Prof.

Role: primary

Claire Adams

Role: backup

References

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von Schnurbein J, Adams C, Akinci B, Ceccarini G, D'Apice MR, Gambineri A, Hennekam RCM, Jeru I, Lattanzi G, Miehle K, Nagel G, Novelli G, Santini F, Santos Silva E, Savage DB, Sbraccia P, Schaaf J, Sorkina E, Tanteles G, Vantyghem MC, Vatier C, Vigouroux C, Vorona E, Araujo-Vilar D, Wabitsch M. European lipodystrophy registry: background and structure. Orphanet J Rare Dis. 2020 Jan 15;15(1):17. doi: 10.1186/s13023-020-1295-y.

Reference Type BACKGROUND
PMID: 31941540 (View on PubMed)

Other Identifiers

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ECLip Registry

Identifier Type: -

Identifier Source: org_study_id

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