Effect of Pyridostigmine (Mestinon) on Muscle Strength in Myasthenia Gravis

NCT ID: NCT03510546

Last Updated: 2018-04-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

UNKNOWN

Clinical Phase

PHASE4

Total Enrollment

44 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-04-09

Study Completion Date

2021-08-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

A randomized, placebo-controlled, double-blinded cross-over study evaluating and quantifying the effect of pyridostigmine on muscle strength and symptoms in Myasthenia Gravis (MG)

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

The study aims to evaluate and quantify the effect of pyridostigmine on symptoms and muscle strength in newly-diagnosed patients and patients on stable medication.

Pyridostigmine treatment is initiated in the vast majority of MG patients. No studies have quantified the effect in a randomized trial, and no studies have examined the potential difference in effect in newly diagnosed patients as compared to patients on stable, antimyasthenic medications.

The study will investigate the effect in two groups

1. Newly diagnosed, treatment-naive patients.
2. MG patients on stable antimyasthenic medication.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Myasthenia Gravis

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Active

De-novo: Each capsule contains 60 mg. pyridostigmine. 1 capsule is administered twice within 4 hours.

Chronic: Each capsule contains 60 mg. pyridostigmine. Number of administered capsules per dosage depend on the patient's usual dosage. Study drug is administered twice within 4 hours.

Patients are examined/rated before 1st dose, 1 hour after 1st dose, 1 hour after 2nd dose (Visit 1). After cross-over (Visit 2), patients will be rated open-label at 1 month (Visit 3) and 3 months (Visit 4).

Group Type EXPERIMENTAL

Pyridostigmine

Intervention Type DRUG

Study dose as per protocol.

Placebo

Same as "Active", however capsules contain placebo.

Group Type PLACEBO_COMPARATOR

Placebo oral capsule

Intervention Type DRUG

Study dose as per protocol.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Pyridostigmine

Study dose as per protocol.

Intervention Type DRUG

Placebo oral capsule

Study dose as per protocol.

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* MG verified by a) anti-body, or b) single-fiber EMG and/or decrement on ENG.

Exclusion Criteria

* Anti-MuSK
* Known cardio-pulmonary disease
* Known neuropathy
* Known myopathy
* Known malignant disease
* Pregnancy or breastfeeding
* Mechanic ileus, urinary tract obstruction, peritonitis

De-novo MG Eligibility Criteria

* MG diagnosis \< 2 months, no prior antimyasthenic medications

Chronic MG Eligibility Criteria

* MG diagnosis \> 1 year, and stable pyridostigmine dosis
Minimum Eligible Age

18 Years

Maximum Eligible Age

90 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Aarhus University Hospital

OTHER

Sponsor Role collaborator

University of Aarhus

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Jan Lykke Scheel Thomsen

MD, PhD Fellow

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Jan LS Thomsen, MD

Role: PRINCIPAL_INVESTIGATOR

University of Aarhus

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Department of Neurology Aarhus University Hospital

Aarhus, Central Jutland, Denmark

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

Denmark

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Jan LS Thomsen, MD

Role: CONTACT

+45 7846 6647

Henning Andersen, MD PhD DMSc

Role: CONTACT

+45 7846 6647

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Jan LS Thomsen, MD

Role: primary

+45 7846 6647

Henning Andersen, MD PhD DMSc

Role: backup

+45 7846 6647

References

Explore related publications, articles, or registry entries linked to this study.

Barnett C, Katzberg H, Nabavi M, Bril V. The quantitative myasthenia gravis score: comparison with clinical, electrophysiological, and laboratory markers. J Clin Neuromuscul Dis. 2012 Jun;13(4):201-5. doi: 10.1097/CND.0b013e31824619d5.

Reference Type BACKGROUND
PMID: 22622164 (View on PubMed)

Burns TM, Conaway M, Sanders DB; MG Composite and MG-QOL15 Study Group. The MG Composite: A valid and reliable outcome measure for myasthenia gravis. Neurology. 2010 May 4;74(18):1434-40. doi: 10.1212/WNL.0b013e3181dc1b1e.

Reference Type BACKGROUND
PMID: 20439845 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

Mestinon2018

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

A Pilot Study of Pyridostigmine in Pompe Disease
NCT02357225 TERMINATED EARLY_PHASE1