A Study to Assess FLX-787 in Subjects With Motor Neuron Disease Experiencing Muscle Cramps.

NCT ID: NCT03196375

Last Updated: 2018-08-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

54 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-07-28

Study Completion Date

2018-07-27

Brief Summary

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The COMMEND Study will assess the safety and effectiveness of FLX-787 in men and women with Motor Neuron Disease \[including Amyotrophic Lateral Sclerosis (ALS), Primary Lateral Sclerosis (PLS) or Progressive Muscular Atrophy (PMA)\] experiencing muscle cramps. Participants will be asked to take two study products during the course of the study. One of these study products will be a placebo.

Approximately 120 participants in approximately 30 study centers across the United States are expected to take part. Participants will be in the study for approximately 3 months and visit the study clinic 3 times.

Detailed Description

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Conditions

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Motor Neuron Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Experimental

Group Type EXPERIMENTAL

FLX-787-ODT (orally disintegrating tablet)

Intervention Type DRUG

FLX-787-ODT taken three times daily for 28 days

Placebo Comparator

Group Type PLACEBO_COMPARATOR

Placebo ODT

Intervention Type DRUG

Placebo ODT taken three times daily for 28 days

Interventions

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FLX-787-ODT (orally disintegrating tablet)

FLX-787-ODT taken three times daily for 28 days

Intervention Type DRUG

Placebo ODT

Placebo ODT taken three times daily for 28 days

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Documented diagnosis of Motor Neuron Disease (MND) \[including Amyotrophic Lateral Sclerosis (ALS), Primary Lateral Sclerosis (PLS) or Progressive Muscular Atrophy (PMA)\]
* Expected survival \> 6 months
* Weekly muscle cramping (defined as: a sustained muscle contraction that's most often painful and lasts seconds to minutes)

Exclusion Criteria

* Presence of major gastrointestinal disorders, such as inflammatory bowel disease, diverticulitis, active peptic ulcer disease, or significant gastroesophageal reflux disease (i.e., not well-controlled on antacids or proton pump inhibitors), or oral or esophageal lesions/ulcers
* Presence of laryngospasm or significant swallowing problems
* Presence of percutaneous endoscopic gastrostomy, esophagogastroduodenoscopy, or G-tube
* Unable or unwilling to discontinue medications for cramps and/or opiates
* Inability to tolerate a spicy sensation in the mouth or stomach
* Actively using illicit drugs or history of chronic substance abuse within the past year prior to screening, including abuse of alcohol
* Intention to change the current level of tobacco use or use of nicotine-containing products (i.e., new smokers or those actively trying to quit may not enrolled)
* Participated in a clinical study (except natural history studies without administration of an investigational product) within 30 days prior to screening
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Flex Pharma, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bjorn Oskarsson, MD

Role: PRINCIPAL_INVESTIGATOR

Mayo Clinic Jacksonville Florida

Locations

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Honor Health Research Institute

Scottsdale, Arizona, United States

Site Status

Mayo Clinic

Scottsdale, Arizona, United States

Site Status

California Pacific Medical Center

Sacramento, California, United States

Site Status

University of California - Davis

Sacramento, California, United States

Site Status

University of California San Francisco

San Francisco, California, United States

Site Status

University of Colorado

Aurora, Colorado, United States

Site Status

Hospital for Special Care

New Britain, Connecticut, United States

Site Status

GW Medical Faculty Associates Inc.

Washington D.C., District of Columbia, United States

Site Status

Mayo Clinic

Jacksonville, Florida, United States

Site Status

University of South Florida Health

Tampa, Florida, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

Indiana University Neuroscience Center

Indianapolis, Indiana, United States

Site Status

University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Johns Hopkins Hospital

Baltimore, Maryland, United States

Site Status

Lahey Hospital and Medical Center

Burlington, Massachusetts, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Saint Louis University

St Louis, Missouri, United States

Site Status

Hospital for Special Surgery

New York, New York, United States

Site Status

Guilford Neurologic Associates

Greensboro, North Carolina, United States

Site Status

Wake Forest University

Winston-Salem, North Carolina, United States

Site Status

Providence Brain and Spine Institute

Portland, Oregon, United States

Site Status

Oregon Health Sciences University

Portland, Oregon, United States

Site Status

Penn State Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Temple University

Philadelphia, Pennsylvania, United States

Site Status

University of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Austin Neuromuscular Center

Austin, Texas, United States

Site Status

Baylor Scott and White Health

Round Rock, Texas, United States

Site Status

UT Health San Antonio

San Antonio, Texas, United States

Site Status

The University of Utah

Salt Lake City, Utah, United States

Site Status

University of Vermont Medical Center

Burlington, Vermont, United States

Site Status

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status

Saint Luke's Rehabilitation Institute

Spokane, Washington, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Countries

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United States

Other Identifiers

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FLX-787-203

Identifier Type: -

Identifier Source: org_study_id

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