A Study to Examine the Safety and Efficacy of a New Drug in Patients With Symptoms of Overactive Bladder (OAB)

NCT ID: NCT03492281

Last Updated: 2021-03-04

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1530 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-03-26

Study Completion Date

2019-02-04

Brief Summary

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This study is designed to evaluate the safety, tolerability, and efficacy of vibegron administered once daily in patients with OAB.

Detailed Description

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Conditions

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Overactive Bladder

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Vibegron + Placebo to match Tolterodine

Group Type EXPERIMENTAL

vibegron

Intervention Type DRUG

single daily oral dose of vibegron 75 mg for 12 weeks

Tolterodine placebo

Intervention Type DRUG

placebo to match tolterodine (active comparator)

Placebo to match vibegron + Placebo to match Tolterodine

Group Type PLACEBO_COMPARATOR

Vibegron placebo

Intervention Type DRUG

placebo to match vibegron (experimental drug)

Tolterodine placebo

Intervention Type DRUG

placebo to match tolterodine (active comparator)

Tolterodine + Placebo to match vibegron

Group Type ACTIVE_COMPARATOR

Vibegron placebo

Intervention Type DRUG

placebo to match vibegron (experimental drug)

Tolterodine Tartrate ER

Intervention Type DRUG

single daily oral dose of tolterodine tartrate ER 4 mg for 12 weeks

Interventions

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vibegron

single daily oral dose of vibegron 75 mg for 12 weeks

Intervention Type DRUG

Vibegron placebo

placebo to match vibegron (experimental drug)

Intervention Type DRUG

Tolterodine Tartrate ER

single daily oral dose of tolterodine tartrate ER 4 mg for 12 weeks

Intervention Type DRUG

Tolterodine placebo

placebo to match tolterodine (active comparator)

Intervention Type DRUG

Other Intervention Names

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RVT-901 MK4618 KRP114V URO-901 Mariosea XL

Eligibility Criteria

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Inclusion Criteria

1. Has a history of OAB for at least 3 months prior to the Screening Visit.
2. Meets either the OAB Wet or OAB Dry criteria.

Exclusion Criteria

Urology Medical History

1. Patient had an average total daily urine volume \> 3000 mL in the past 6 months or during the 14-day Run-in Period.
2. Has lower urinary tract pathology that could, in the opinion of the Investigator, be responsible for urgency, frequency, or incontinence.
3. Has a history of surgery to correct stress urinary incontinence, pelvic organ prolapse, or procedural treatments for BPH within 6 months of Screening.
4. Has current history or evidence of Stage 2 or greater pelvic organ prolapse (prolapse extends beyond the hymenal ring).
5. Patient is currently using a pessary for the treatment of pelvic organ prolapse.
6. Has a known history of elevated post-void residual volume defined as greater than 150 mL.
7. Has undergone bladder training or electrostimulation within 28 days prior to Screening or plans to initiate either during the study.
8. Has an active or recurrent (\> 3 episodes per year) urinary tract infection by clinical symptoms or pre-defined laboratory criteria.
9. Has a requirement for an indwelling catheter or intermittent catheterization.
10. Has received an intradetrusor injection of botulinum toxin within 9 months prior to Screening.
11. Has uncontrolled hyperglycemia (defined as fasting blood glucose \> 150 mg/dL or 8.33 mmol/L and/or non-fasting blood glucose \> 200 mg/dL or 11.1 mmol/L) or, if in the opinion of the Investigator, is uncontrolled.
12. Has evidence of diabetes insipidus.
13. Is pregnant, breast-feeding, or is planning to conceive within the projected duration of the study.
14. Has a concurrent malignancy or history of any malignancy within 5 years prior to signing informed consent, except for adequately treated basal cell or squamous cell skin cancer or in situ cervical cancer.
15. Has uncontrolled hypertension (systolic blood pressure of ≥ 180 mmHg and/or diastolic blood pressure of ≥ 100 mmHg) or has a resting heart rate (by pulse) \> 100 beats per minute.
16. Has narrow angle glaucoma (primary open angle glaucoma is not excluded).
17. Has a history of cerebral vascular accident, transient ischemic attack, unstable angina, myocardial infarction, coronary artery interventions (e.g., coronary artery bypass grafting or percutaneous coronary interventions \[e.g., angioplasty, stent insertion\]), or neurovascular interventions (e.g., carotid artery stenting) within 6 months prior to the Screening Visit. Has a known history of liver disease.
18. Has a history of injury, surgery, or neurodegenerative diseases (e.g., multiple sclerosis, Parkinson's) that could affect the lower urinary tract or its nerve supply.
19. Has hematuria, including microscopic hematuria according to pre-defined criteria.
20. Has clinically significant electrocardiogram (ECG) abnormality.
21. Has alanine aminotransferase or aspartate aminotransferase \> 2.0 times the upper limit of normal (ULN), or bilirubin (total bilirubin) \> 1.5 x ULN (or \> 2.0 x ULN if secondary to Gilbert syndrome or pattern consistent with Gilbert syndrome).
22. Has an estimated glomerular filtration rate (eGFR) \< 30 mL/min/1.73 m2.
23. Has an allergy, intolerance, or a history of a significant clinical or laboratory adverse experience associated with any of the active or inactive components of the vibegron formulation or tolterodine formulation.
24. Is currently participating or has participated in a study with an investigational compound or device within 28 days prior to signing informed consent, or has participated in any previous study with vibegron.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Urovant Sciences GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Central Alabama Research

Birmingham, Alabama, United States

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Achieve Clinical Research

Birmingham, Alabama, United States

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Fundamental Research LLC

Gulf Shores, Alabama, United States

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Longwood Research

Huntsville, Alabama, United States

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Coastal Clinical Research Inc.

Mobile, Alabama, United States

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Clinical Research Consortium

Tempe, Arizona, United States

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Noble Clinical Research

Tucson, Arizona, United States

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Eclipse Clinical Research

Tucson, Arizona, United States

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Dream Team Clinical Research LLC

Anaheim, California, United States

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Hope Clinical Research

Canoga Park, California, United States

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Core Healthcare Group

Cerritos, California, United States

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Research Center of Fresno Inc.

Fresno, California, United States

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American Clinical Trials

Hawaiian Gardens, California, United States

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Marvel Clinical Research

Huntington Beach, California, United States

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Grossmont Center for Clinical Research

La Mesa, California, United States

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Prime-Care Clinical Research

Laguna Hills, California, United States

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Long Beach Clinical Trial Services Inc.

Long Beach, California, United States

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Long Beach Clinical Trials LLC

Long Beach, California, United States

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Downtown L.A. Research Center Inc.

Los Angeles, California, United States

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Urology Group of Southern California

Los Angeles, California, United States

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Tri Valley Urology Medical Group

Murrieta, California, United States

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Northern California Research

Sacramento, California, United States

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San Bernadino Urological Associates

San Bernardino, California, United States

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Artemis Institute for Clinical Research

San Diego, California, United States

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WR MCCCR

San Diego, California, United States

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Artemis Institute for Clinical Research

San Marcos, California, United States

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Empire Clinical Research

Upland, California, United States

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Bayview Research Group LLC

Valley Village, California, United States

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Horizons Clinical Research Center

Denver, Colorado, United States

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Lynn Institute of Denver

Denver, Colorado, United States

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Clinical Research Consulting LLC

Milford, Connecticut, United States

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Coastal Connecticut Research LLC

New London, Connecticut, United States

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Chase Medical Research, LLC

Waterbury, Connecticut, United States

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Innovative Medical Research of South Florida Inc.

Aventura, Florida, United States

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PAB Clinical Research

Brandon, Florida, United States

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Innovative Research of West FL Inc.

Clearwater, Florida, United States

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Universal Medical and Research Center LLC

Coral Gables, Florida, United States

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Top Medical Research Inc.

Cutler Bay, Florida, United States

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Avail Clinical Research

DeLand, Florida, United States

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Jesscan Medical Research

Delray Beach, Florida, United States

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Revival Research

Doral, Florida, United States

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Riverside Clinical Research

Edgewater, Florida, United States

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KO Clinical Research

Fort Lauderdale, Florida, United States

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A.G.A Clinical Trials

Hialeah, Florida, United States

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Indago Research Health Center

Hialeah, Florida, United States

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Best Quality Research, Inc.

Hialeah, Florida, United States

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Vital Pharm Research Inc.

Hialeah, Florida, United States

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Health Awareness, Inc.

Jupiter, Florida, United States

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San Marcus Research Clinic Inc.

Miami, Florida, United States

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LCC Medical Research Institute Inc.

Miami, Florida, United States

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Nuren Medical Research Center

Miami, Florida, United States

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AppleMed Research Group LLC

Miami, Florida, United States

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Miami Clinical Research

Miami, Florida, United States

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Advanced Medical Research Institute

Miami, Florida, United States

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Suncoast Clinical Research Inc.

New Port Richey, Florida, United States

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Bayside Clinical Research

New Port Richey, Florida, United States

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Compass Research LLC

Orlando, Florida, United States

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South Broward Research LLC

Pembroke Pines, Florida, United States

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Clinical Research Center of Florida

Pompano Beach, Florida, United States

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Meridien Research

Spring Hill, Florida, United States

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Pinellas Urology

St. Petersburg, Florida, United States

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Clinical Research of West Florida

Tampa, Florida, United States

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Bioclinica Research

The Villages, Florida, United States

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Asclepes Research Centers

Weeki Wachee, Florida, United States

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Clinical Research of Central Florida

Winter Haven, Florida, United States

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In-Quest Medical Research, LLC

Peachtree Corners, Georgia, United States

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Meridian Clinical Research LLC

Savannah, Georgia, United States

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Clinical Research Atlanta

Stockbridge, Georgia, United States

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Woodstock, Georgia, United States

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Blackfoot, Idaho, United States

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Meridian, Idaho, United States

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Evanston Premier Healthcare Research

Evanston, Illinois, United States

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Clinical Investigation Specialists Inc.

Gurnee, Illinois, United States

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Investigators Research Group LLC

Brownsburg, Indiana, United States

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MediSphere Medical Research Center

Evansville, Indiana, United States

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Heartland Research Associates LLC

Wichita, Kansas, United States

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Heartland Research Associates LLC

Wichita, Kansas, United States

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Central Kentucky Research Associates Inc.

Lexington, Kentucky, United States

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L-MARC Research Center

Louisville, Kentucky, United States

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Centex Studies Inc.

Lake Charles, Louisiana, United States

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DelRicht Research

New Orleans, Louisiana, United States

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Regional Urology LLC

Shreveport, Louisiana, United States

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Chesapeake Urology Research Associates

Hanover, Maryland, United States

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Boston Clinical Trials

Boston, Massachusetts, United States

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BTC of New Bedford

New Bedford, Massachusetts, United States

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Regeneris Medical

North Attleboro, Massachusetts, United States

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Infinity Medical Research Inc.

North Dartmouth, Massachusetts, United States

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Beacon Clinical Research

Quincy, Massachusetts, United States

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Bay State Clinical Trials Inc.

Watertown, Massachusetts, United States

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Remidica LLC

Rochester, Michigan, United States

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Saginaw Valley Medical Research

Saginaw, Michigan, United States

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CentraCare Clinic Adult & Pediatric Urology

Sartell, Minnesota, United States

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Poplar Bluff Urology

Poplar Bluff, Missouri, United States

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Montana Health Research Institute Inc.

Billings, Montana, United States

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Montana Medical Research

Missoula, Montana, United States

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Pioneer Clinical Research, LLC

Bellevue, Nebraska, United States

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Barrett Clinic P.C.

La Vista, Nebraska, United States

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Women's Clinic of Lincoln PC

Lincoln, Nebraska, United States

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Meridian Clinical Research LLC

Norfolk, Nebraska, United States

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Adult and Pediatric Urology P.C.

Omaha, Nebraska, United States

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Quality Clinical Research Inc.

Omaha, Nebraska, United States

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Excel Clinical Research

Las Vegas, Nevada, United States

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Clinical Research Consortium

Las Vegas, Nevada, United States

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Sheldon Freedman MD Ltd

Las Vegas, Nevada, United States

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Hassman Research Institute

Berlin, New Jersey, United States

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Premier Urology Group LLC

Edison, New Jersey, United States

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Urologic Research and Consulting LLC

Englewood, New Jersey, United States

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Lawrence OB-GYN Clinical Research LLC

Lawrenceville, New Jersey, United States

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Albuquerque Clinical Trials, Inc.

Albuquerque, New Mexico, United States

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AccumetRx Clinical Research - Division of Urology Group of New Mexico

Albuquerque, New Mexico, United States

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United Medical Associates

Binghamton, New York, United States

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Regional Clinical Research Inc.

Endwell, New York, United States

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AccuMed Research Associates

Garden City, New York, United States

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Drug Trials America

Hartsdale, New York, United States

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Smart Medical Research Inc.

Jackson Heights, New York, United States

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ProHealth Care AssociatesLLP

Port Jefferson, New York, United States

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Rochester Clinical Research Inc.

Rochester, New York, United States

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Upstate Clinical Research Associates LLC

Williamsville, New York, United States

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PMG Research of Cary

Cary, North Carolina, United States

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PMG Research of Charlotte LLC

Charlotte, North Carolina, United States

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PharmQuest

Greensboro, North Carolina, United States

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Peters Medical Research

High Point, North Carolina, United States

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Raleigh Medical Group PMG Research of Raleigh

Raleigh, North Carolina, United States

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Associated Urologists of North Carolina

Raleigh, North Carolina, United States

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PMG Research of Salisbury

Salisbury, North Carolina, United States

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PMG Research of Wilmington, LLC

Wilmington, North Carolina, United States

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PMG Research

Wilmington, North Carolina, United States

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Carolina Medical Trials LLC

Winston-Salem, North Carolina, United States

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PMG Research of Winston-Salem

Winston-Salem, North Carolina, United States

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Sentral Clinical Research Services

Cincinnati, Ohio, United States

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Rapid Medical Research

Cleveland, Ohio, United States

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Buckeye Health and Research

Columbus, Ohio, United States

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Aventiv Research, Inc.

Columbus, Ohio, United States

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Providence Health Partners

Dayton, Ohio, United States

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HWC Womens Research Center

Englewood, Ohio, United States

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Clinical Research Solutions

Middleburg Heights, Ohio, United States

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Family Practice Center of Wadsworth Inc. - New Venture Medical Research

Wadsworth, Ohio, United States

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Ohio Clinical Research LLC

Willoughby Hills, Ohio, United States

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Lynn Health Science Institute

Oklahoma City, Oklahoma, United States

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Leonard Maliver MD Antria, Inc.

Indiana, Pennsylvania, United States

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The Clinical Trial Center LLC

Jenkintown, Pennsylvania, United States

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Green and Seidner Family Practice Associates P.C.

Lansdale, Pennsylvania, United States

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Clinical Research of Philadelphia LLC

Philadelphia, Pennsylvania, United States

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Preferred Primary Care Physicians Inc.

Pittsburgh, Pennsylvania, United States

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Preferred Primary Care Physicians Inc.

Pittsburgh, Pennsylvania, United States

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Research Protocol Management Specialists Hills ObGyn Associates Inc

Pittsburgh, Pennsylvania, United States

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Frontier Clinical Research, LLC

Smithfield, Pennsylvania, United States

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Preferred Primary Care Physicians Inc.

Uniontown, Pennsylvania, United States

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PEAK Research LLC

Upper Saint Clair, Pennsylvania, United States

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Greater Providence Clinical Research, LLC

East Providence, Rhode Island, United States

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Omega Medical Research

Warwick, Rhode Island, United States

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Clinical Trials of South Carolina

Charleston, South Carolina, United States

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Pharmacorp Clinical Trials Inc.

Charleston, South Carolina, United States

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Piedmont Research Partners

Fort Mill, South Carolina, United States

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DeGarmo Institute of Medical Research

Greer, South Carolina, United States

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PMG Research of Charleston LLC

Moncks Corner, South Carolina, United States

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Coastal Carolina Research Center

Mt. Pleasant, South Carolina, United States

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PMG Research of Charleston LLC

Mt. Pleasant, South Carolina, United States

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Family Medicine of SayeBrook LLC

Myrtle Beach, South Carolina, United States

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Palmetto Institute of Clinical Research Inc.

Pelzer, South Carolina, United States

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Hillcrest Clinical Research LLC

Simpsonville, South Carolina, United States

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Palmetto Clinical Research

Summerville, South Carolina, United States

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PMG Research of Bristol LLC

Bristol, Tennessee, United States

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WR - ClinSearch LLC

Chattanooga, Tennessee, United States

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The Jackson Clinic

Jackson, Tennessee, United States

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MultiSpecialty Clinical Research, Inc.

Johnson City, Tennessee, United States

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Volunteer Research Group - NOCCR

Knoxville, Tennessee, United States

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Adams Patterson Gynecology and Obstetrics

Memphis, Tennessee, United States

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Clinical Research Associates Inc.

Nashville, Tennessee, United States

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DiscoveResearch Inc.

Bryan, Texas, United States

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WR Global Medical Research

DeSoto, Texas, United States

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Advances in Health

Houston, Texas, United States

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Centex Studies Inc.

Houston, Texas, United States

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Discovery MM Services Inc.

Houston, Texas, United States

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BI Research Center

Houston, Texas, United States

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Pioneer Research Solutions

Houston, Texas, United States

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Protenium Clinical Research

Hurst, Texas, United States

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Discovery MM Services Inc.

Katy, Texas, United States

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Discovery MM Services Inc.

Missouri City, Texas, United States

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Village Health Partners ACRC Trials

Plano, Texas, United States

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Clinical Trials of Texas Inc.

San Antonio, Texas, United States

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Bandera Family Health Care

San Antonio, Texas, United States

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Clinova Clinical Trials

Spring, Texas, United States

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Progressive Clinical Research

Bountiful, Utah, United States

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Wasatch Clinical Research LLC

Salt Lake City, Utah, United States

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Advanced Clinical Research

West Jordan, Utah, United States

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Millennium Clinical Trials

Arlington, Virginia, United States

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Health Research of Hampton Roads Inc.

Newport News, Virginia, United States

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Seattle Urology Research

Burien, Washington, United States

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Seattle Women's: Health, Research, Gynecology

Seattle, Washington, United States

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North Spokane Womens Health

Spokane, Washington, United States

Site Status

Central Alberta Research Clinic

Red Deer, Alberta, Canada

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Silverado Research Inc.

Victoria, British Columbia, Canada

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PrimeHealth Clinical Research

Toronto, Ontario, Canada

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Manna Research (Quebec)

Lévis, Quebec, Canada

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Recherche GCP Research

Montreal, Quebec, Canada

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Manna Research (Montreal)

Montreal, Quebec, Canada

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Diex Research Sherbrooke Inc.

Sherbrooke, Quebec, Canada

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Obudai Egeszsegugyi Centrum Kft.

Budapest, , Hungary

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Szarka Ödön Egyesitett Egeszsegügyi es Szocialis Intezmeny

Csongrád, , Hungary

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Szent Anna Private Surgery

Debrecen, , Hungary

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Mediroyal Prevention Center

Kecskemét, , Hungary

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Uro-clin Ltd

Pécs, , Hungary

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Daugavpils Regional Hospital

Daugavpils, , Latvia

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Uro Ltd.

Riga, , Latvia

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Pauls Stradins Clinical University Hospital

Riga, , Latvia

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Public Institution Republican Klaipda Hospital

Klaipėda, , Lithuania

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Vilnius

Vilnius, , Lithuania

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Vilnius city Clinical hospital

Vilnius, , Lithuania

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Poradnia Urologiczna EuroMediCare Szpital Specjalistyczny z Przychodnia

Wroclaw, Woj. Dolnoslaskie, Poland

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ETG Lodz

Lodz, Woj. Lodzkie, Poland

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NZOZ NOVITA Specjalistyczne Gabinety Lekarskie

Lublin, Woj. Lubelskie, Poland

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Nzoz Heureka

Piaseczno, Woj. Mazowieckie, Poland

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Klimed Marek Klimkiewicz

Bialystok, Woj. Podlaskie, Poland

Site Status

NZOZ Centrum Urologiczne sp. z o.o.

Mysłowice, Woj. Slaskie, Poland

Site Status

Countries

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United States Canada Hungary Latvia Lithuania Poland

References

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Staskin D, Frankel J, Gregg SG, Varano S, Owens-Grillo J. Plain language summary of safety and symptom improvement with vibegron in people with overactive bladder: results from the EMPOWUR study. J Comp Eff Res. 2023 Sep;12(9):CER. doi: 10.57264/cer-2023-0043. Epub 2023 Aug 10.

Reference Type DERIVED
PMID: 37586057 (View on PubMed)

Frankel J, Staskin D, Varano S, Newman DK, Gregg SG, Owens-Grillo J. Plain language summary: does treatment with vibegron result in improvements in overactive bladder (OAB) symptoms that are meaningful to people with OAB? J Comp Eff Res. 2023 Sep;12(9):CER. doi: 10.57264/cer-2023-0049. Epub 2023 Aug 10.

Reference Type DERIVED
PMID: 37586052 (View on PubMed)

Stoniute A, Madhuvrata P, Still M, Barron-Millar E, Nabi G, Omar MI. Oral anticholinergic drugs versus placebo or no treatment for managing overactive bladder syndrome in adults. Cochrane Database Syst Rev. 2023 May 9;5(5):CD003781. doi: 10.1002/14651858.CD003781.pub3.

Reference Type DERIVED
PMID: 37160401 (View on PubMed)

Newman DK, Thomas E, Greene H, Haag-Molkenteller C, Varano S. Efficacy and Safety of Vibegron for the Treatment of Overactive Bladder in Women: A Subgroup Analysis From the Double-Blind, Randomized, Controlled EMPOWUR Trial. Urogynecology (Phila). 2023 Jan 1;29(1):48-57. doi: 10.1097/SPV.0000000000001258. Epub 2022 Oct 21.

Reference Type DERIVED
PMID: 36384907 (View on PubMed)

Staskin D, Frankel J, Varano S, Kennelly M, Newman DK, Rosenberg MT, Shortino DD, Jankowich RA, Mudd PN Jr. Vibegron for the Treatment of Patients with Dry and Wet Overactive Bladder: A Subgroup Analysis from the EMPOWUR Trial. Int J Clin Pract. 2022 Apr 13;2022:6475014. doi: 10.1155/2022/6475014. eCollection 2022.

Reference Type DERIVED
PMID: 35685566 (View on PubMed)

Frankel J, Staskin D, Varano S, Kennelly M, Newman DK, Rosenberg MT, Jankowich RA, Shortino D, Mudd PN Jr, Girman CJ. Interpretation of the Meaningfulness of Symptom Reduction with Vibegron in Patients with Overactive Bladder: Analyses from EMPOWUR. Adv Ther. 2022 Feb;39(2):959-970. doi: 10.1007/s12325-021-01972-8. Epub 2021 Dec 18.

Reference Type DERIVED
PMID: 34921665 (View on PubMed)

Varano S, Staskin D, Frankel J, Shortino D, Jankowich R, Mudd PN Jr. Efficacy and Safety of Once-Daily Vibegron for Treatment of Overactive Bladder in Patients Aged >/=65 and >/=75 Years: Subpopulation Analysis from the EMPOWUR Randomized, International, Phase III Study. Drugs Aging. 2021 Feb;38(2):137-146. doi: 10.1007/s40266-020-00829-z. Epub 2021 Jan 20.

Reference Type DERIVED
PMID: 33469832 (View on PubMed)

Frankel J, Varano S, Staskin D, Shortino D, Jankowich R, Mudd PN Jr. Vibegron improves quality-of-life measures in patients with overactive bladder: Patient-reported outcomes from the EMPOWUR study. Int J Clin Pract. 2021 May;75(5):e13937. doi: 10.1111/ijcp.13937. Epub 2021 Jan 22.

Reference Type DERIVED
PMID: 33332699 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2017-003293-14

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

RVT-901-3003

Identifier Type: -

Identifier Source: org_study_id

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