A Study Extension Period of PEG-somatropin (Pegylated-somatropin) in the Treatment of Children With Idiopathic Short Stature

NCT ID: NCT03255694

Last Updated: 2025-08-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

360 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-05-12

Study Completion Date

2030-06-30

Brief Summary

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After the first stage (52 weeks) of Phase II clinical trial, Pegylated recombinant human growth hormone (PEG-rhGH) injection of appropriate dose in compliance with ISS clinical treatment strategy is used to treat children with ISS (Idiopathic Short Stature). The long-term efficacy and safety of the investigational product are evaluated, which can provide more scientific and reliable medication guidance information for clinical diagnosis and treatment.

Detailed Description

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Conditions

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Dwarfism

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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PEG-somatropin

After the first stage (52 weeks) of Phase II clinical trial, the initial medication dose of this extension period is 0.2 mg/kg weight/week of PEG-rhGH for the high dose group, low dose group and negative control group, and it is adjusted in accordance with yearly height velocity (HV) and IGF-1 SDS of each visit. The maximum dose shall not exceed 0.4 mg/kg weight/week.

Group Type EXPERIMENTAL

PEG-somatropin

Intervention Type DRUG

After the first stage (52 weeks) of Phase II clinical trial, the initial medication dose of this extension period is 0.2 mg/kg weight/week of PEG-rhGH for high dose group, low dose group and negative control group, and it is adjusted in accordance with yearly height velocity (HV) and IGF-1 SDS of each visit. The maximum dose shall not exceed 0.4 mg/kg weight/week.

Interventions

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PEG-somatropin

After the first stage (52 weeks) of Phase II clinical trial, the initial medication dose of this extension period is 0.2 mg/kg weight/week of PEG-rhGH for high dose group, low dose group and negative control group, and it is adjusted in accordance with yearly height velocity (HV) and IGF-1 SDS of each visit. The maximum dose shall not exceed 0.4 mg/kg weight/week.

Intervention Type DRUG

Other Intervention Names

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Polyethylene Glycol Recombinant Human Somatropin Injection

Eligibility Criteria

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Inclusion Criteria

* All subjects who have completed the first stage (52 weeks) of Phase II clinical trial (including negative controls) with completed follow-up records may be enrolled in the extension period study.
* Before the extension period study, the investigator shall fully inform the subjects and their guardians of all the information about the extension period study, including detailed follow-up procedure, treatment plan, laboratory examination items during follow-ups and possible benefits and risks. The extension period study shall only be initiated after the subjects and their guardians are well informed, and agree to cooperate and complete the treatment, follow-ups and examinations during the study, and sign the written informed consent.

Exclusion Criteria

* Subjects who have taken the following medications within 2 months before entering the extension period study:

1. Aromatase inhibitors (which include but are not limited to Lelrozol and Anastrozole), with continuous medication ≥1 month;
2. Gonadotropin releasing hormone analogues (which include but are not limited to Triptorelin, Leuprorelin and Goserelin),, with continuous medication ≥1 month;
3. Sex steroids (which include but are not limited to any type of estrogen, progestin and androgen) , with continuous medication ≥1 month;
4. Protein anabolic drugs (which include but are not limited to Oxandrolone, Danazol and Strombafort), with continuous medication ≥1 month;
5. Glucocorticoids via oral/intravenous administration for more than 1 month..
Minimum Eligible Age

4 Years

Maximum Eligible Age

9 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Tongji Hospital

OTHER

Sponsor Role collaborator

The First Hospital of Jilin University

OTHER

Sponsor Role collaborator

Affiliated Hospital of Jiangnan University

OTHER

Sponsor Role collaborator

The First Affiliated Hospital with Nanjing Medical University

OTHER

Sponsor Role collaborator

Shanghai Children's Hospital

OTHER

Sponsor Role collaborator

The Children's Hospital of Zhejiang University School of Medicine

OTHER

Sponsor Role collaborator

Children's Hospital of Fudan University

OTHER

Sponsor Role collaborator

Jiangxi Province Children's Hospital

OTHER

Sponsor Role collaborator

Hunan Children's Hospital

OTHER_GOV

Sponsor Role collaborator

Beijing Children's Hospital

OTHER

Sponsor Role collaborator

Children's Hospital of Soochow University

OTHER

Sponsor Role collaborator

Wuxi Women's & Children's Hospital

OTHER

Sponsor Role collaborator

Changchun GeneScience Pharmaceutical Co., Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Xiaoping Luo

Role: PRINCIPAL_INVESTIGATOR

Department of Pediatrics of Tongji Hospital of Tongji Medical College, Huazhong University of Science and Technology

Locations

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Beijing Children's Hospital, Capital Medical University, National Center for Children's Health

Beijing, Beijing Municipality, China

Site Status

Department of Pediatrics of Tongji Hospital of Tongji Medical College, Huazhong University of Science and Technology, Wuhan

Wuhan, Hubei, China

Site Status

Hunan Children's Hospital

Changsha, Hunan, China

Site Status

Children's Hospital of Soochow University

Naning, Jiangsu, China

Site Status

The First Affiated Hospital of Nanjing Medical Universit

Nanjing, Jiangsu, China

Site Status

Affiliated Hospital of Jiangnan University

Wuxi, Jiangsu, China

Site Status

Wuxi Children's Hospital

Wuxi, Jiangsu, China

Site Status

Jiangxi Provincial Children's Hospital

Nanchang, Jiangxi, China

Site Status

The First Hospital of Jilin University

Changchun, Jilin, China

Site Status

The Children's Hospital of Zhejiang University School of Medicine

Hangzhou, Zhejiang, China

Site Status

Shanghai Children's Hospital of Fudan University

Shanghai, , China

Site Status

Shanghai Children's Hospital

Shanghai, , China

Site Status

Countries

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China

Other Identifiers

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GenSci 033 CT-Extension Period

Identifier Type: -

Identifier Source: org_study_id

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