A Study of PEG-somatropin in the Treatment of Children With Idiopathic Short Stature

NCT ID: NCT03221088

Last Updated: 2017-07-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2

Total Enrollment

360 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-06-30

Brief Summary

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This study aims to explore the optimal dose of pegylated recombinant human growth hormone (PEG-rhGH) injection to treat children with idiopathic short stature (ISS), evaluate its safety and efficacy, and provide scientific and reliable evidence for the medication dosage in Phase III clinical study.

Detailed Description

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Conditions

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Dwarfism

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Jintrolong® low dose group

PEG-rhGH Injection (27IU/4.5mg/0.5ml/bottle) 0.1 mg/kg/w by subcutaneous injection for 52 weeks.

Group Type EXPERIMENTAL

Jintrolong® low dose group

Intervention Type DRUG

PEG-somatropin 0.1mg/kg/wk by weekly subcutaneous injection for 52 weeks.

Jintrolong® high dose group

Intervention Type DRUG

PEG-somatropin 0.2 mg/kg/wk by weekly subcutaneous injection for 52 weeks.

Jintrolong® high dose group

PEG-rhGH Injection (27IU/4.5mg/0.5ml/bottle) 0.2 mg/kg/w by subcutaneous injection for 52 weeks.

Group Type EXPERIMENTAL

Jintrolong® low dose group

Intervention Type DRUG

PEG-somatropin 0.1mg/kg/wk by weekly subcutaneous injection for 52 weeks.

Jintrolong® high dose group

Intervention Type DRUG

PEG-somatropin 0.2 mg/kg/wk by weekly subcutaneous injection for 52 weeks.

Negative control group

Untreated Control Group

Group Type NO_INTERVENTION

No interventions assigned to this group

Interventions

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Jintrolong® low dose group

PEG-somatropin 0.1mg/kg/wk by weekly subcutaneous injection for 52 weeks.

Intervention Type DRUG

Jintrolong® high dose group

PEG-somatropin 0.2 mg/kg/wk by weekly subcutaneous injection for 52 weeks.

Intervention Type DRUG

Other Intervention Names

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PEG-somatropin PEG-somatropin

Eligibility Criteria

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Inclusion Criteria

* Boys are between 4 and 9 years of age and girls are between 4 and 8 years of age.
* Height \<-2 SD for chronological age.
* Growth velocity\<5.0 cm/yr.
* GH peak concentration ≥10.0 ng/mL in two different stimulation tests.
* The difference of bone age (BA) and chronological age (CA) is within -2 to +2.
* IGF-1 concentration is between -2 SDS to +2 SDS.
* Prepubertal Status(Tanner Stage I).
* Birth weight within the normal range.
* Growth hormone treatment-naive.
* Subjects are willing and able to cooperate to complete scheduled visits, treatment plans and laboratory tests and other procedures, to sign informed consent.

Exclusion Criteria

* Subjects with abnormal liver and kidney functions (ALT \> upper limit of normal value; Cr \> upper limit of normal value).
* Subjects are positive for anti-HBc, HbsAg or HbeAg in Hepatitis B virus tests.
* Subjects with known highly allergic constitution or allergy to investigational product or its excipient.
* Subjects with systemic chronic disease and immune deficiency.
* Patients diagnosed with tumor.
* Patients with mental disease.
* Patients with other types of abnormal growth and development.

1. Growth hormone deficiency (GHD) (confirmed by GH stimulation test);
2. Turner syndrome (confirmed by karyotype test of girls);
3. Noonan syndrome (hypertelorism, pectus carinatum, hypophrenia, frequently with skin disease and congenital heart disease, missense mutation of the protein tyrosine phosphatase, non-receptor type 11 (PTPN11) gene on chromosome 12 for half of the patients, for both male and female patients);
4. Laron sydrome (confirmed by IGF-1 generation test);
5. Small for gestational age ( the birth height or weight is below the tenth percentile or 2 SD, with catch-up growth uncompleted at 2 years old).
* Growth disorders caused by malnutrition or hypothyroidism (thyroid function test).
* Congenital skeletal abnormalities or scoliosis, claudication.
* Subjects with impaired glucose regulation (IGR) (including impaired fasting glucose (IFG) and/or impaired glucose tolerance (IGT) ) or diabetes).
* Subjects with abnormal electrolyte, blood gas analysis (vein), creatine kinase.
* Subjects who took part in other clinical trials within 3 months.
* Subjects who received medications which may interfere GH secretion or GH function, or other hormones within 3 months (such as sex steroids, glucocorticoids, etc.).
* For patients with potential high tumor risks such as tumor markers exceed normal range and some other relative information, they may be excluded from the treatment.
* Other conditions which is inappropriate for this study in the opinion of the investigator.
Minimum Eligible Age

4 Years

Maximum Eligible Age

9 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Tongji Hospital

OTHER

Sponsor Role collaborator

The First Hospital of Jilin University

OTHER

Sponsor Role collaborator

Affiliated Hospital of Jiangnan University

OTHER

Sponsor Role collaborator

The First Affiliated Hospital with Nanjing Medical University

OTHER

Sponsor Role collaborator

Shanghai Children's Hospital

OTHER

Sponsor Role collaborator

The Children's Hospital of Zhejiang University School of Medicine

OTHER

Sponsor Role collaborator

Children's Hospital of Fudan University

OTHER

Sponsor Role collaborator

Changchun GeneScience Pharmaceutical Co., Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Xiaoping Luo

Role: PRINCIPAL_INVESTIGATOR

Department of Pediatrics of Tongji Hospital of Tongji Medical College, Huazhong University of Science and Technology

Locations

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Tongji Hospital of Tongji Medical College of Huazhong University of Science and Technology

Wuhan, Hubei, China

Site Status RECRUITING

The First Affiated Hospital of Nanjing Medical University

Nanjing, Jiangsu, China

Site Status RECRUITING

Affiliated Hospital of Jiangnan University

Wuxi, Jiangsu, China

Site Status RECRUITING

The First Hospital of Jilin University

Changchun, Jilin, China

Site Status RECRUITING

The Children's Hospital of Zhejiang University School of Medicine

Hangzhou, Zhejiang, China

Site Status RECRUITING

Shanghai Children's Hospital of Fudan University

Shanghai, , China

Site Status RECRUITING

Shanghai Children's Hospital

Shanghai, , China

Site Status RECRUITING

Countries

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China

Central Contacts

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Yanlin Chen

Role: CONTACT

+86-60871786-8197

Facility Contacts

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Xiaoping Luo, PhD

Role: primary

Yuhua Hu, MD

Role: primary

Zhuangjian Xu, MD

Role: primary

Hongwei Du, MD

Role: primary

Junfen Fu, MD

Role: primary

Feihong Luo, MD

Role: primary

Pin Li, MD

Role: primary

Other Identifiers

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GenSci 033 CT-one year

Identifier Type: -

Identifier Source: org_study_id

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