A Study of PEG-somatropin Injection to Treat Children of Turner Syndrome

NCT ID: NCT03189160

Last Updated: 2017-12-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2

Total Enrollment

180 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-03-31

Brief Summary

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This study aims to explore the optimal dose of pegylated recombinant human growth hormone (PEG-rhGH) injection to treat children of Turner syndrome (TS), preliminarily evaluate its safety and efficacy and provide scientific and reliable evidence for the medication dosage in Phase 3 clinical trial.

Detailed Description

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Conditions

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Turner Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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PEG-rhGH low dose

PEG-rhGH Injection (27IU/4.5mg/0.5ml/bottle) 0.1 mg/kg/w by subcutaneous injection for 52 weeks.

Group Type EXPERIMENTAL

PEG-rhGH low dose

Intervention Type BIOLOGICAL

PEG-rhGH Injection 0.1 mg/kg/w by subcutaneous injection for 52 weeks.

PEG-rhGH high dose

Intervention Type BIOLOGICAL

PEG-rhGH Injection 0.2 mg/kg/w by subcutaneous injection for 52 weeks.

Non-treatment control group

Intervention Type OTHER

PEG-rhGH high dose

PEG-rhGH Injection (27IU/4.5mg/0.5ml/bottle) 0.2 mg/kg/w by subcutaneous injection for 52 weeks.

Group Type EXPERIMENTAL

PEG-rhGH low dose

Intervention Type BIOLOGICAL

PEG-rhGH Injection 0.1 mg/kg/w by subcutaneous injection for 52 weeks.

PEG-rhGH high dose

Intervention Type BIOLOGICAL

PEG-rhGH Injection 0.2 mg/kg/w by subcutaneous injection for 52 weeks.

Non-treatment control group

Intervention Type OTHER

Non-treatment control group

Group Type NO_INTERVENTION

No interventions assigned to this group

Interventions

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PEG-rhGH low dose

PEG-rhGH Injection 0.1 mg/kg/w by subcutaneous injection for 52 weeks.

Intervention Type BIOLOGICAL

PEG-rhGH high dose

PEG-rhGH Injection 0.2 mg/kg/w by subcutaneous injection for 52 weeks.

Intervention Type BIOLOGICAL

Non-treatment control group

Intervention Type OTHER

Other Intervention Names

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Polyethylene Glycol Recombinant Human Somatropin Injection Polyethylene Glycol Recombinant Human Somatropin Injection

Eligibility Criteria

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Inclusion Criteria

* Female
* Bone age \<12 years
* Karyotype: 45, X; 45, X / 46, XXqi; 45, X / 46, XXr; 45, X / 46, XX; 46, XXqi; 46, XXpi; 45, X / 47, XXX; 46, XXp-; 45, X / 46, XXp-; 46, XXq-; 45X / 46, XXq-; 45, X / 46, XX / 47, XXX, etc. (count 50 or more cells);
* Facial appearance and abnormalities: Patients with at least one of the following signs, which include but are not limited to facial pigmented nevus, short neck, webbed neck, low posterior hairline, low-set ears, micrognathia, high-voulted arch, shield-like chest, cubitus valgus, genu valgum, short 4th and 5th metacarpals, nail dysplasia, scoliosis, ptosis and strabismus, cardiovascular abnormalities (such as aortic stenosis, bicuspid aortic valve and hypertension), reproductive abnormalities (such as primary gonadal dysfunction), renal abnormalities, thyroid hypofunction, middle ear lesion, etc.
* Short stature: height below -2.5SD of the mean height of the same age and gender.
* Pre-pubertal (Tanner Stage I ) patients
* No history of growth hormone treatment
* The subject and his/her guardian sign the informed consent (if the subject is incapable to sign the informed consent, his/her legal guardian shall sign the name of the subject instead)

Exclusion Criteria

* Subjects with abnormal liver and kidney functions (ALT \> upper limit of normal value; Cr \> upper limit of normal value)
* Subjects positive for anti-HBc, HbsAg or HbeAg in Hepatitis B virus tests;
* Subjects with highly allergic constitution or allergy to proteins or investigational product or its excipient
* Subjects with systemic chronic disease and immune deficiency
* Patients diagnosed with tumor
* For patients whose tumor markers exceeding normal range in combination with other information, considering as potential high risks of tumor, they may be excluded from the treatment.
* Patients with mental disease
* Subjects with impaired glucose regulation (IGR) (including impaired fasting glucose (IFG) and/or impaired glucose tolerance (IGT) ) or diabetes
* Subjects who took part in other clinical trials within 3 months
* Subjects who received medicines which may interfere GH secretion or GH function, or other hormones within 3 months (such as sex steroids, glucocorticoids, etc.)
* Other conditions which are unsuitable for this study in the opinion of the investigator.
Minimum Eligible Age

2 Years

Maximum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Beijing Children's Hospital

OTHER

Sponsor Role collaborator

The First Affiliated Hospital with Nanjing Medical University

OTHER

Sponsor Role collaborator

Shanghai Children's Hospital

OTHER

Sponsor Role collaborator

Children's Hospital of Fudan University

OTHER

Sponsor Role collaborator

Xinhua Hospital, Shanghai Jiao Tong University School of Medicine

OTHER

Sponsor Role collaborator

The First Hospital of Jilin University

OTHER

Sponsor Role collaborator

Jiangxi Province Children's Hospital

OTHER

Sponsor Role collaborator

Affiliated Hospital of Jiangnan University

OTHER

Sponsor Role collaborator

The Children's Hospital of Zhejiang University School of Medicine

OTHER

Sponsor Role collaborator

Changchun GeneScience Pharmaceutical Co., Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Chunxiu Gong, PhD

Role: PRINCIPAL_INVESTIGATOR

Beijing Children's Hospital

Locations

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The First Affiliated Hospital with Nanjing Medical University

Nanjing, Jiangsu, China

Site Status RECRUITING

Affiliated Hospital of Jiangnan University

Wuxi, Jiangsu, China

Site Status RECRUITING

Jiangxi Provincial Children's Hospital

Nanchang, Jiangxi, China

Site Status RECRUITING

First Hospital of Jilin University

Changchun, Jilin, China

Site Status RECRUITING

The Children's Hospital of Zhejiang University School of Medicine

Hangzhou, Zhejiang, China

Site Status RECRUITING

Beijing Children's Hospital,Capital Medical University

Beijing, , China

Site Status RECRUITING

Children's Hospital of Fudan University

Shanghai, , China

Site Status RECRUITING

Shanghai Children's Hospital

Shanghai, , China

Site Status RECRUITING

Xinhua Hospital of Shanghai Jiao Tong University School of Medicine

Shanghai, , China

Site Status RECRUITING

Countries

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China

Central Contacts

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Xiaohua Feng

Role: CONTACT

Phone: 0431-85170552

Email: [email protected]

Facility Contacts

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Yuhua Hu

Role: primary

Zhuangjian Xu

Role: primary

Yu Yang

Role: primary

Hongwei Du

Role: primary

Junfeng Fu

Role: primary

Chunxiu Gong, PhD

Role: primary

Feihong Luo

Role: primary

Pin Li

Role: primary

Jun Ye

Role: primary

Other Identifiers

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GenSci 032 CT

Identifier Type: -

Identifier Source: org_study_id