The Efficacy and Safety of Inpegsomatropin Injection in Children With Idiopathic Short Stature

NCT ID: NCT06927310

Last Updated: 2025-12-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

300 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-04-28

Study Completion Date

2028-06-30

Brief Summary

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This is a multicenter, randomized, open-label, active-controlled Phase III clinical trial to evaluate the efficacy and safety of Inpegsomatropin injection,once a week,compared with recombinant human growth hormone (rhGH) in children with idiopathic short stature (ISS). It plans to enroll 300 children with ISS, who will be randomized , stratified by gender and age, and assigned to either the experimental group or the positive controlled group. Each participant will undergo a screening period (up to 12 weeks), a treatment period (52 weeks), and a post-treatment follow-up period (5 weeks). And the safety and efficacy will be evaluated.

Detailed Description

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Conditions

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Idiopathic Short Stature

Keywords

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Inpegsomatropin Injection Recombinant Human Growth Hormone Injection

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Inpegsomatropin group

Group Type EXPERIMENTAL

Inpegsomatropin Injection

Intervention Type DRUG

Inpegsomatropin injection, 280 μg/kg/week, s.c., once weekly, for 52 consecutive weeks.

rhGH group

Group Type ACTIVE_COMPARATOR

Recombinant Human Growth Hormone Injection

Intervention Type DRUG

Recombinant Human Growth Hormone Injection, 350 μg/kg/week, s.c., divided into 7 doses, i.e., 50 μg/kg/day (0.15 IU/kg/day), once daily for 52 consecutive weeks.

Interventions

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Recombinant Human Growth Hormone Injection

Recombinant Human Growth Hormone Injection, 350 μg/kg/week, s.c., divided into 7 doses, i.e., 50 μg/kg/day (0.15 IU/kg/day), once daily for 52 consecutive weeks.

Intervention Type DRUG

Inpegsomatropin Injection

Inpegsomatropin injection, 280 μg/kg/week, s.c., once weekly, for 52 consecutive weeks.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Prepubertal children: boys aged ≥3 years and \<11 years at screening with testicular volume \<4 mL; girls aged ≥3 years and \<10 years at screening with breast development at Tanner Stage I, i.e., no palpable breast glandular tissue.
* Compared to chronological age, bone age is advanced by no more than 1 year or delayed by no more than 2 years (i.e., -2 years ≤ bone age - chronological age ≤ 1 year).
* Height at screening is below -2 standard deviations (SD) from the mean for age and sex, with height reference to Appendix 1.
* Body mass index (BMI) is within the 5th to 95th percentile for age and sex of healthy children, with reference to Appendix 2.
* Peak GH level ≥10.0 ng/ml in at least one GH stimulation test.
* No prior systemic pharmacological treatment for growth promotion (continuous use ≥1 month), including but not limited to growth hormone, insulin-like growth factor 1 (IGF-1), etc.
* The legal guardian understands and signs the informed consent form. If the participants is ≥8 years old, they must also sign the informed consent form. For participants under 8 years old who are able to express their consent, their assent should be clearly documented.

Exclusion Criteria

* Individuals with closed epiphyses;
* Other types of growth and developmental abnormalities, including confirmed or highly suspected growth hormone deficiency (GHD), Noonan syndrome, Prader-Willi syndrome, Russell-Silver syndrome, Turner syndrome, small for gestational age, short stature due to SHOX gene abnormalities, growth delay due to malnutrition, growth delay due to hypothyroidism, and other short statures with a clear etiology; genetic testing results must be obtained before randomization to exclude short stature caused by definite genetic abnormalities;
* Individuals who have participated in any other clinical trial within 3 months prior to screening and have received pharmacological or non-pharmacological interventions;
* Individuals who received inhaled corticosteroids for more than 2 consecutive weeks, or oral or intravenous corticosteroids for more than 1 consecutive week, within the 3 months prior to screening;
* Individuals who are currently receiving or require long-term treatment with other therapies that may affect growth, including but not limited to methylphenidate, sex hormones, gonadotropin-releasing hormone analogs, aromatase inhibitors, anabolic agents, insulin, etc.;
* Individuals with abnormal liver or kidney function at screening (ALT \> 1.5 times the upper limit of normal, Cr \> upper limit of normal);
* Individuals diagnosed with diabetes mellitus, or with fasting blood glucose ≥6.1 mmol/L on two consecutive occasions;
* Individuals with chronic infectious diseases, such as chronic hepatitis B;
* Individuals with systemic chronic diseases, such as moderate to severe anemia, malnutrition, hypothyroidism, chronic kidney disease, cardiovascular diseases (e.g., dilated cardiomyopathy, etc.), psychiatric and psychological disorders, or those with congenital anomalies requiring clinical intervention as determined by the investigator;
* Individuals with congenital skeletal abnormalities, or those with scoliosis exceeding 15°, limping, or a history of slipped capital femoral epiphysis;
* Individuals with a history of increased intracranial pressure;
* Individuals with a history of malignancy or currently having active malignancy, including intracranial tumors;
* Individuals with severe allergic constitutions, or known allergies to growth hormone or its excipients;
* Individuals with any other disease that the investigator deems may endanger the subject's safety or compromise compliance with the study protocol.
Minimum Eligible Age

3 Years

Maximum Eligible Age

11 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Tongji Hospital

OTHER

Sponsor Role collaborator

Xiamen Amoytop Biotech Co., Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Xiaoping Luo, Ph.D

Role: PRINCIPAL_INVESTIGATOR

Tongji Hospital

Locations

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Anhui Provincial Children's Hospital

Hefei, Anhui, China

Site Status RECRUITING

The Second Affiliated Hospital of Anhui Medical University

Hefei, Anhui, China

Site Status RECRUITING

Capital Institute of Pediatrics, Beijing (SHOUER)

Beijing, Beijing Municipality, China

Site Status RECRUITING

Children's Hospital of Chongqing Medical University

Chongqing, Chongqing Municipality, China

Site Status RECRUITING

The First Affiliated Hospital of Xiamen University

Xiamen, Fujian, China

Site Status RECRUITING

Gansu Provincial Maternity and Child Care Hospital

Lanzhou, Gansu, China

Site Status RECRUITING

Guangzhou Women and Children's Medical Center

Guangzhou, Guangdong, China

Site Status RECRUITING

Sun Yat-sen Memorial Hospital, Sun Yat-sen University

Guangzhou, Guangdong, China

Site Status RECRUITING

The Third Affiliated Hospital, Sun Yat-sen University

Guangzhou, Guangdong, China

Site Status RECRUITING

Henan Children's Hospital Zhengzhou Children's Hospital

Zhengzhou, Henan, China

Site Status RECRUITING

Wuhan Children's Hospital

Wuhan, Hubei, China

Site Status RECRUITING

Hunan Children's Hospital

Changsha, Hunan, China

Site Status RECRUITING

Children's Hospital Affiliated to Soochow University

Suzhou, Jiangsu, China

Site Status RECRUITING

Jiangxi Provincial Children's Hospital

Nanchang, Jiangxi, China

Site Status RECRUITING

Children's Hospital of Shanghai

Shanghai, Shanghai Municipality, China

Site Status RECRUITING

Chengdu Women's and Children's Central Hospital

Chengdu, Sichuan, China

Site Status RECRUITING

West China Second University Hospital, Sichuan University

Chengdu, Sichuan, China

Site Status RECRUITING

The Affiliated Women's and Children's Hospital of Ningbo University

Ningbo, Zhejiang, China

Site Status RECRUITING

The Second Affiliated Hospital and Yuying Children's Hospital of Wenzhou Medical University

Wenzhou, Zhejiang, China

Site Status RECRUITING

Sanya Central Hospital

Hainan, , China

Site Status RECRUITING

Hangzhou First People's Hospital

Hangzhou, , China

Site Status RECRUITING

Zhejiang Provincial People's Hospital

Hangzhou, , China

Site Status RECRUITING

The First Affiliated Hospital of Henan University of Science and Technology

Henan, , China

Site Status RECRUITING

Jiaxing First Hospital

Jiaxing, , China

Site Status RECRUITING

Affiliated Hospital of Jining Medical University

Jining, , China

Site Status RECRUITING

Kunming Children's Hospital

Kunming, , China

Site Status RECRUITING

Nanjing Children's Hospital

Nanjing, , China

Site Status RECRUITING

Qingdao Women and Children's Hospital

Qingdao, , China

Site Status RECRUITING

Ruijin Hospital, Shanghai Jiao Tong University School of Medicine

Shanghai, , China

Site Status RECRUITING

Shanghai Children's Medical Center

Shanghai, , China

Site Status RECRUITING

Xinhua Hospital, Shanghai Jiao Tong University School of Medicine

Shanghai, , China

Site Status RECRUITING

The First Hospital of Hebei Medical University

Shijiazhuang, , China

Site Status RECRUITING

Renmin Hospital of Wuhan University

Wuhan, , China

Site Status RECRUITING

The Second Affiliated Hospital of Xi'an Jiaotong University

Xi'an, , China

Site Status RECRUITING

Xiangyang Central Hospital

Xiangyang, , China

Site Status RECRUITING

The First Affiliated Hospital of Xinjiang Medical University

Xinjiang, , China

Site Status RECRUITING

Yuncheng Central Hospital

Yuncheng, , China

Site Status RECRUITING

Zhuzhou Central Hospital

Zhuzhou, , China

Site Status RECRUITING

Countries

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China

Central Contacts

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Xiaoping Luo, Ph.D

Role: CONTACT

Phone: 15671671188

Email: [email protected]

Facility Contacts

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Yuqing Chen

Role: primary

Deyun Liu

Role: primary

Fuying Song

Role: primary

Min Zhu

Role: primary

Qun Lian

Role: primary

Bo Sun

Role: primary

Wen Zhang

Role: primary

Liyang Liang

Role: primary

Shunye Zhu

Role: primary

Haiyan Wei

Role: primary

Hui Yao

Role: primary

Yan Zhong

Role: primary

Haiying Wu

Role: primary

Yu Yang

Role: primary

Pin Li

Role: primary

Xinran Cheng

Role: primary

Fan Yang

Role: primary

Shuxia Ding

Role: primary

Xiaoou Shan

Role: primary

Hua Zhang

Role: primary

Chunming Jiang

Role: primary

Xiaoming Luo

Role: primary

Dan Lou

Role: primary

Shunfeng Mao

Role: primary

Meiyun Xin

Role: primary

Na Tao

Role: primary

Wei Gu

Role: primary

Tang Li

Role: primary

Wenli Lu

Role: primary

Xiumin Wang

Role: primary

Yu Ding

Role: backup

Huiwen Zhang

Role: primary

Huijuan Ma

Role: primary

Jingping Ye

Role: primary

Yanfeng Xiao

Role: primary

Rui Pan

Role: primary

Miregul Mamat

Role: primary

Sufang Chang

Role: primary

Xianglan Wen

Role: primary

Other Identifiers

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PEGPESEN-4-2-001

Identifier Type: -

Identifier Source: org_study_id