A Study of the Anti-PD1 Antibody PDR001, in Combination With Dabrafenib and Trametinib in Advanced Melanoma

NCT ID: NCT02967692

Last Updated: 2025-09-18

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

568 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-02-17

Study Completion Date

2024-08-21

Brief Summary

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The purpose of this study was to evaluate safety and efficacy of the combination of an anti-PD-1 antibody (PDR001), a BRAF inhibitor (dabrafenib) and a MEK inhibitor (trametinib) in patients with BRAF V600 mutant, unresectable and metastatic melanoma.

Detailed Description

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This study was designed as a phase III, multi-center study consisting of 3 parts:

* Part 1: Safety run-in part The safety run-in part aimed to determine the recommended regimen of PDR001 in combination with dabrafenib and trametinib for previously untreated patients with BRAF V600 mutant unresectable or metastatic melanoma (stage IIIC/IV). Spartalizumab was administered at a starting dose level (DL1) of 400 mg every 4 weeks (Q4W), along with fixed doses of dabrafenib (150 mg twice daily) and trametinib (2 mg once daily). The RP3R for Part 3 was determined using the Bayesian Logistic Regression Model (BLRM) with escalation with overdose control (EWOC) criteria.
* Part 2: Biomarker cohort Part 2 was run to explore changes in the immune microenvironment and biomarker modulations upon treatment with the combination of dabrafenib, trametinib and PDR001. Part 2 started when the fourth subject in dose level 1 (DL1) of Part 1 completed approximately 4 weeks of study treatment, and fewer than 3 dose-limiting toxicities (DLTs) were observed. Participants in Part 2 received PDR001 (spartalizumab) at a dosage of 400 mg Q4W, in combination with dabrafenib (150 mg BID) and trametinib (2 mg QD).
* Part 3: Double-blind, randomized, placebo-controlled part Part 3 was comparing the efficacy and safety of spartalizumab in combination with dabrafenib and trametinib to placebo in combination with dabrafenib and trametinib. Part 3 was initiated after determining the RP3R for the combination of spartalizumab with dabrafenib and trametinib in Part 1. Subjects were randomized in a 1:1 ratio to receive either the RP3R dose of spartalizumab identified in Part 1 or placebo, along with dabrafenib (150 mg BID) and trametinib (2 mg QD).

For all parts of the study, the treatment continued until the subject experiences any of the following events: disease progression according to RECIST 1.1 as determined by the Investigator, unacceptable toxicity, initiation of a new anti-neoplastic therapy, pregnancy, withdrawal of consent, physician's decision, loss to follow-up, death, or termination of the study by the Sponsor. Safety evaluations are conducted for all subjects for up to 150 days after the last dose of spartalizumab/placebo (safety follow-up period).

Subjects who discontinued study treatment without disease progression as per RECIST 1.1 continued with tumor assessments according to the protocol until documented disease progression, withdrawal of consent, loss to follow-up, or death, regardless of the initiation of new anti-neoplastic therapy (efficacy follow-up period).

Subjects entered the survival follow-up period after completing the safety follow-up period or experiencing disease progression as per RECIST 1.1 or response criteria for immunotherapy, whichever period is longer (survival follow-up period).

Conditions

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Melanoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Part 1 and Part 2 are open- label. Part 3 is double-blind and randomized.

Study Groups

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Part 1: Safety run-in Cohort

In Part 1, participants are treated at different dose levels to determine the recommended Phase 3 regimen of spartalizumab in combination with dabrafenib and trametinib. The starting dose of spartalizumab is 400 mg Q4W in combination with the approved dose of dabrafenib (150 mg BID) and trametinib (2 mg QD).

Group Type EXPERIMENTAL

Spartalizumab

Intervention Type BIOLOGICAL

Spartalizumab powder for solution is used in Part 1 and Part 2, and as concentrate for solution for infusion for Part 3. Spartalizumab is administered via intravenous infusion over 30 minutes once every 4 weeks

Dabrafenib

Intervention Type DRUG

Dabrafenib 150 mg capsules BID is administered orally for Days 1-28 of a 28-day cycle, in fasting conditions.

Trametinib

Intervention Type DRUG

Trametinib 2 mg tablets QD is administered orally for Days 1-28 of a 28-day cycle, in fasting conditions

Part 2: Biomarker cohort

In Part 2, participants are treated with spartalizumab 400 mg Q4W in combination with the approved dose of dabrafenib (150 mg BID) and trametinib (2 mg QD).

Group Type EXPERIMENTAL

Spartalizumab

Intervention Type BIOLOGICAL

Spartalizumab powder for solution is used in Part 1 and Part 2, and as concentrate for solution for infusion for Part 3. Spartalizumab is administered via intravenous infusion over 30 minutes once every 4 weeks

Dabrafenib

Intervention Type DRUG

Dabrafenib 150 mg capsules BID is administered orally for Days 1-28 of a 28-day cycle, in fasting conditions.

Trametinib

Intervention Type DRUG

Trametinib 2 mg tablets QD is administered orally for Days 1-28 of a 28-day cycle, in fasting conditions

Part 3- Arm 1: Spartalizumab in combination with dabrafenib and trametinib

In Part 3, participants are randomized to receive spartalizumab at the RP3R identified in Part 1 (400 mg Q4W) in combination with approved dose of dabrafenib (150 mg BID) and trametinib (2 mg QD)

Group Type EXPERIMENTAL

Spartalizumab

Intervention Type BIOLOGICAL

Spartalizumab powder for solution is used in Part 1 and Part 2, and as concentrate for solution for infusion for Part 3. Spartalizumab is administered via intravenous infusion over 30 minutes once every 4 weeks

Dabrafenib

Intervention Type DRUG

Dabrafenib 150 mg capsules BID is administered orally for Days 1-28 of a 28-day cycle, in fasting conditions.

Trametinib

Intervention Type DRUG

Trametinib 2 mg tablets QD is administered orally for Days 1-28 of a 28-day cycle, in fasting conditions

Part 3- Arm 2: Placebo in combination with dabrafenib and trametinib

In Part 3, participants are randomized to receive matching placebo in combination with the approved dose of dabrafenib (150 mg BID) and trametinib (2 mg QD)

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo is administered via intravenous infusion over 30 minutes once every 4 weeks

Dabrafenib

Intervention Type DRUG

Dabrafenib 150 mg capsules BID is administered orally for Days 1-28 of a 28-day cycle, in fasting conditions.

Trametinib

Intervention Type DRUG

Trametinib 2 mg tablets QD is administered orally for Days 1-28 of a 28-day cycle, in fasting conditions

Interventions

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Spartalizumab

Spartalizumab powder for solution is used in Part 1 and Part 2, and as concentrate for solution for infusion for Part 3. Spartalizumab is administered via intravenous infusion over 30 minutes once every 4 weeks

Intervention Type BIOLOGICAL

Placebo

Placebo is administered via intravenous infusion over 30 minutes once every 4 weeks

Intervention Type OTHER

Dabrafenib

Dabrafenib 150 mg capsules BID is administered orally for Days 1-28 of a 28-day cycle, in fasting conditions.

Intervention Type DRUG

Trametinib

Trametinib 2 mg tablets QD is administered orally for Days 1-28 of a 28-day cycle, in fasting conditions

Intervention Type DRUG

Other Intervention Names

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PDR001

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed, unresectable or metastatic melanoma with BRAF V600 mutation
* Aspartate transaminase (AST) \< 2.5× ULN and Alanine transaminase (ALT) \< 2.5× ULN
* Measurable disease according to RECIST 1.1
* ECOG performance status ≤ 1

Part 2: Biomarker cohort

* Histologically confirmed, unresectable or metastatic melanoma with BRAF V600 mutation
* At least two cutaneous or subcutaneous or nodal lesions for tumor sample collection
* Measurable disease according to RECIST 1.1
* ECOG performance status ≤ 2

Part 3: Double-blind, randomized, placebo-controlled part

* Histologically confirmed, unresectable or metastatic melanoma with BRAF V600 mutation
* ECOG performance status ≤ 2
* Measurable disease according to RECIST 1.1

Exclusion Criteria

Part 1: Safety run-in

* Subjects with uveal or mucosal melanoma
* Any history of CNS metastases
* Prior systemic anti-cancer treatment for unresectable or metastatic melanoma
* Neoadjuvant and/or adjuvant therapy for melanoma completed less than 6 months prior to enrollmen
* Radiation therapy within 4 weeks prior to start of study treatment
* Active autoimmune disease, and/or history of autoimmune disease(s) that required treatment

Parts 2 \& 3: Biomarker cohort \& double-blind, randomized, placebo-controlled part

* Subjects with uveal or mucosal melanoma
* Prior systemic anti-cancer treatment for unresectable or metastatic melanoma
* Neoadjuvant and/or adjuvant therapy for melanoma completed less than 6 months prior to enrollment
* Radiation therapy within 4 weeks prior to start of study treatment
* Clinically active cerebral melanoma metastasis.
* Active autoimmune disease, and/or history of autoimmune disease(s) that required treatment

Other protocol-defined Inclusion/Exclusion may apply.
Minimum Eligible Age

18 Years

Maximum Eligible Age

100 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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California Cancer Associates for Research and Excellence

Encinitas, California, United States

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UC Irvine Medical Center

Orange, California, United States

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California Pacific Medical Center

San Francisco, California, United States

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Stanford Cancer Center

Stanford, California, United States

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University of Kansas Cancer Center

Westwood, Kansas, United States

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Johns Hopkins U

Lutherville, Maryland, United States

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Nebraska Cancer Specialists

Omaha, Nebraska, United States

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NYU Laura and Isaac Perlmutter Cancer Center

New York, New York, United States

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University of Pittsburgh Med Center

Pittsburgh, Pennsylvania, United States

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University of Tennessee Medical Ctr

Knoxville, Tennessee, United States

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Univ of TX MD Anderson Cancer Cntr

Houston, Texas, United States

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Utah Cancer Specialists

Salt Lake City, Utah, United States

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CABA, Buenos Aires, Argentina

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CABA, Buenos Aires, Argentina

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Rosario, Santa Fe Province, Argentina

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Caba, , Argentina

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Gateshead, New South Wales, Australia

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North Sydney, New South Wales, Australia

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Greenslopes, Queensland, Australia

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Melbourne, Victoria, Australia

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Nedlands, Western Australia, Australia

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Innsbruck, Tyrol, Austria

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Graz, , Austria

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Linz, , Austria

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Salzburg, , Austria

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Sankt Pölten, , Austria

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Brussels, , Belgium

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Brussels, , Belgium

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Curitiba, Paraná, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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São Paulo, São Paulo, Brazil

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Rio de Janeiro, , Brazil

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Plovdiv, , Bulgaria

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Sofia, , Bulgaria

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Vancouver, British Columbia, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Montreal, Quebec, Canada

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Sherbrooke, Quebec, Canada

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Temuco, Región de la Araucanía, Chile

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Santiago, , Chile

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Santiago, , Chile

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Brno, Czech Republic, Czechia

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Zlín, Czech Republic, Czechia

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Hradec Králové, CZE, Czechia

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Ostrava, Poruba, Czechia

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Olomouc, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Aarhus N, , Denmark

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Limoges, Haute Vienne, France

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Amiens, , France

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Besançon, , France

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Bobigny, , France

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Bordeaux, , France

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Boulogne-Billancourt, , France

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Caen, , France

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Dijon, , France

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Grenoble, , France

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Le Mans, , France

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Lille, , France

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Lorient, , France

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Vandœuvre-lès-Nancy, , France

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Villejuif, , France

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Mannheim, Baden-Wurttemberg, Germany

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Regensburg, Bavaria, Germany

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Leipzig, Saxony, Germany

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Halle, Saxony-Anhalt, Germany

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Berlin, , Germany

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Berlin, , Germany

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Bonn, , Germany

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Chemnitz, , Germany

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Dresden, , Germany

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Düsseldorf, , Germany

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Erfurt, , Germany

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Essen, , Germany

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Freiburg im Breisgau, , Germany

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Gera, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Heidelberg, , Germany

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Homburg, , Germany

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Kiel, , Germany

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Mainz, , Germany

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Marburg, , Germany

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Minden, , Germany

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München, , Germany

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Münster, , Germany

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Stade, , Germany

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Tübingen, , Germany

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Athens, , Greece

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Athens, , Greece

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Budapest, , Hungary

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Debrecen, , Hungary

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Szeged, , Hungary

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Haifa, , Israel

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Jerusalem, , Israel

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Ramat Gan, , Israel

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Bari, BA, Italy

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Bergamo, BG, Italy

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Bologna, BO, Italy

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Brescia, BS, Italy

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Meldola, FC, Italy

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Genova, GE, Italy

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Monza, MB, Italy

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Milan, MI, Italy

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Milan, MI, Italy

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Modena, MO, Italy

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Padua, PD, Italy

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Roma, RM, Italy

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Siena, SI, Italy

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Candiolo, TO, Italy

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Torino, TO, Italy

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Verona, VR, Italy

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Napoli, , Italy

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Kyushu University Hospital

Fukuoka, Fukuoka, Japan

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Kyoto University Hospital

Sakyo Ku, Kyoto, Japan

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Osaka International Cancer Institute

Osaka, Osaka, Japan

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Tokyo Metropolitan Komagome Hospital

Bunkyo Ku, Tokyo, Japan

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National Cancer Hospital

Chuo Ku, Tokyo, Japan

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León, Guanajuato, Mexico

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Guadalajara, Jalisco, Mexico

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Mexico City, Mexico City, Mexico

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Leiden, South Holland, Netherlands

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Amersfroort, , Netherlands

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Oslo, , Norway

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Gdansk, , Poland

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Warsaw, , Poland

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Lisbon, , Portugal

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Porto, , Portugal

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Chelyabinsk, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Nizhny Novgorod, , Russia

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Omsk, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Samara, , Russia

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Málaga, Andalusia, Spain

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Seville, Andalusia, Spain

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Jerez de la Frontera, Cadiz, Spain

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Badalona, Catalonia, Spain

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Barcelona, Catalonia, Spain

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A Coruña, Galicia, Spain

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Oviedo, Principality of Asturias, Spain

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Valencia, Valencia, Spain

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Las Palmas de Gran Canaria, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Gothenburg, , Sweden

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Lund, , Sweden

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Stockholm, , Sweden

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Aarau, Canton of Aargau, Switzerland

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Zurich, , Switzerland

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Songkhla, Hat Yai, Thailand

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Bangkok, , Thailand

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Truro, Cornwall, United Kingdom

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Guildford, Surrey, United Kingdom

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Sutton, Surrey, United Kingdom

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Leicester, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Middlesbrough, , United Kingdom

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Preston, , United Kingdom

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Rickmansworth Road, , United Kingdom

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Countries

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United States Argentina Australia Austria Belgium Brazil Bulgaria Canada Chile Czechia Denmark France Germany Greece Hungary Israel Italy Japan Mexico Netherlands Norway Poland Portugal Russia Spain Sweden Switzerland Thailand United Kingdom

References

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Tawbi HA, Robert C, Brase JC, Gusenleitner D, Gasal E, Garrett J, Savchenko A, Gorgun G, Flaherty KT, Ribas A, Dummer R, Schadendorf D, Long GV, Nathan PD, Ascierto PA. Spartalizumab or placebo in combination with dabrafenib and trametinib in patients with BRAF V600-mutant melanoma: exploratory biomarker analyses from a randomized phase 3 trial (COMBI-i). J Immunother Cancer. 2022 Jun;10(6):e004226. doi: 10.1136/jitc-2021-004226.

Reference Type DERIVED
PMID: 35728875 (View on PubMed)

Dummer R, Long GV, Robert C, Tawbi HA, Flaherty KT, Ascierto PA, Nathan PD, Rutkowski P, Leonov O, Dutriaux C, Mandala M, Lorigan P, Ferrucci PF, Grob JJ, Meyer N, Gogas H, Stroyakovskiy D, Arance A, Brase JC, Green S, Haas T, Masood A, Gasal E, Ribas A, Schadendorf D. Randomized Phase III Trial Evaluating Spartalizumab Plus Dabrafenib and Trametinib for BRAF V600-Mutant Unresectable or Metastatic Melanoma. J Clin Oncol. 2022 May 1;40(13):1428-1438. doi: 10.1200/JCO.21.01601. Epub 2022 Jan 14.

Reference Type DERIVED
PMID: 35030011 (View on PubMed)

Dummer R, Lebbe C, Atkinson V, Mandala M, Nathan PD, Arance A, Richtig E, Yamazaki N, Robert C, Schadendorf D, Tawbi HA, Ascierto PA, Ribas A, Flaherty KT, Pakhle N, Campbell CD, Gusenleitner D, Masood A, Brase JC, Gasal E, Long GV. Combined PD-1, BRAF and MEK inhibition in advanced BRAF-mutant melanoma: safety run-in and biomarker cohorts of COMBI-i. Nat Med. 2020 Oct;26(10):1557-1563. doi: 10.1038/s41591-020-1082-2. Epub 2020 Oct 5.

Reference Type DERIVED
PMID: 33020648 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-002794-35

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CPDR001F2301

Identifier Type: -

Identifier Source: org_study_id

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