A Clinical Trial of Three Study Medicines (Encorafenib, Binimetinib, and Pembrolizumab) in Patients With Advanced or Metastatic Melanoma

NCT ID: NCT04657991

Last Updated: 2025-08-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

257 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-01-15

Study Completion Date

2026-03-23

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to learn about the effects of three study medicines (encorafenib, binimetinib, and pembrolizumab) given together for the treatment of melanoma that:

* is advanced or metastatic (spread to other parts of the body);
* has a certain type of abnormal gene called "BRAF"; and
* has not received prior treatment.

All participants in this study will receive pembrolizumab at the study clinic once every 3 weeks as an intravenous (IV) infusion (given directly into a vein). In addition, half of the participants will take encorafenib and binimetinib orally (by mouth) at home every day.

Participants may receive pembrolizumab for up to two years. Those participants taking encorafenib and binimetinib can continue until their melanoma is no longer responding. The study team will monitor how each participant is doing with the study treatment during regular visits at the study clinic.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This study will compare the efficacy, safety, and tolerability of encorafenib and binimetinib plus pembrolizumab (Triplet Arm) versus placebo plus pembrolizumab (Control Arm) in participants with metastatic or unresectable locally advanced BRAF V600E/K mutation-positive melanoma. The study will have an open-label safety lead-in (SLI) phase to determine the safety recommend Phase 3 dose (RP3D) and pharmacokinetics (PK) of encorafenib and binimetinib plus pembrolizumab combination therapy prior to initiation of the randomized Phase 3 part of the study. Two dose levels of encorafenib in combination with binimetinib plus pembrolizumab will be explored in parallel. A minimum of 12 evaluable participants will be enrolled per dose level. During the double-blind randomized Phase 3 part of the study, approximately 216 eligible participants will be randomized in a 1:1 ratio to the Triplet Arm (at RP3D determined in the SLI) or Control Arm (approximately 108 participants per arm). Randomization will be stratified by prior systemic adjuvant therapy and stage of disease by AJCC (ED8).

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Melanoma

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Triplet Arm

Encorafenib and Binimetinib in combination with Pembrolizumab

Group Type EXPERIMENTAL

Encorafenib

Intervention Type DRUG

Encorafenib

Binimetinib

Intervention Type DRUG

Binimetinib

Pembrolizumab

Intervention Type DRUG

Pembrolizumab

Control Arm

Pembrolizumab

Group Type ACTIVE_COMPARATOR

Pembrolizumab

Intervention Type DRUG

Pembrolizumab

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Encorafenib

Encorafenib

Intervention Type DRUG

Binimetinib

Binimetinib

Intervention Type DRUG

Pembrolizumab

Pembrolizumab

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

BRAFTOVI MEKTOVI KEYTRUDA

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Male or female participants ≥ 18 years at the time of informed consent.
* Participants who are willing and able to comply with all scheduled visits, treatment plan, laboratory tests, lifestyle considerations, and other study procedures.
* Histologically confirmed unresectable (Stage IIIB, IIIC, or IIID) or metastatic (Stage IV) cutaneous melanoma, according to the AJCC 8th edition.
* Presence of at least 1 measurable lesion as detected by radiological and/or photographic methods according to RECIST v1.1.
* ECOG performance status 0 or 1.
* Documented evidence of a BRAF V600E or V600K mutation in melanoma tumor tissue as previously determined by either PCR or NGS-based local laboratory assay (eg, US FDA-approved test, CE-marked \[European conformity\] in vitro diagnostic in EU countries, or equivalent), obtained during the course of normal clinical care, in a CLIA- or similarly certified laboratory.
* Submission of adequate tumor tissue (archival or newly obtained; block or slides to the sponsor central laboratory(ies) during the screening period and prior to enrollment (SLI)/randomization (Phase 3).
* Have not received prior first-line systemic therapy for metastatic or unresectable locally advanced melanoma.
* Adequate bone marrow function, hepatic and renal function.
* Capable of giving signed informed consent.

Exclusion Criteria

* Other medical or psychiatric condition including recent (within the past year) or active suicidal ideation/behavior or laboratory abnormality that may increase the risk of study participation or, in the investigator's judgment, make the participant inappropriate for the study (including, but not limited to, a participant who is rapidly progressing or has clinically significant tumor related symptoms, in the judgment of the investigator).
* Mucosal or ocular melanoma.
* Diagnosis of immunodeficiency or an active autoimmune disease that required systemic treatment in the past 2 years (ie, with use of disease modifying agents, corticosteroids, or immunosuppressive drugs).
* Clinically significant multiple or severe drug allergies, intolerance to topical corticosteroids, or severe post-treatment hypersensitivity reactions (including, but not limited to, erythema multiforme major, linear IgA dermatosis, toxic epidermal necrolysis, and exfoliative dermatitis).
* Unable to swallow, retain, and absorb oral medications.
* Impairment of GI function or disease which may significantly alter the absorption of oral study intervention (eg, uncontrolled nausea, vomiting or diarrhea, malabsorption syndrome, including malabsorption syndrome secondary to prior GI surgery).
* Clinically significant cardiovascular diseases,
* History of thromboembolic or cerebrovascular events ≤ 12 weeks prior to enrollment (SLI)/randomization (Phase 3). Examples include transient ischemic attacks, cerebrovascular accidents, hemodynamically significant (ie, massive or sub-massive) deep vein thrombosis or pulmonary emboli.
* History or current evidence of RVO or current risk factors for RVO (eg, uncontrolled glaucoma or ocular hypertension, history of hyperviscosity or hypercoagulability syndromes)
* Concurrent neuromuscular disorder that is associated with the potential of elevated CK (eg, inflammatory myopathies, muscular dystrophy, amyotrophic lateral sclerosis, spinal muscular atrophy).
* Current noninfectious pneumonitis or history of noninfectious pneumonitis requiring steroids, or history of radiation pnuemonitis
* Evidence of HBV or HCV infection.
* Known history of a positive test for HIV or known AIDS.
* Any active infection requiring systemic therapeutic treatment within 2 weeks prior to enrollment (SLI)/ randomization (Phase 3).
* Participants with prior or current symptomatic brain metastasis, leptomeningeal disease or other active CNS metastases.
* Concurrent or previous other malignancy within 2 years of study entry, except curatively treated basal or squamous cell skin cancer, prostate intraepithelial neoplasm, carcinoma in-situ of the cervix, Bowen's disease and Gleason ≤ 6 prostate cancer. Participants with a history of other curatively treated cancers must be reviewed with the sponsor or designee prior to entering the study.
* Participants who previously received and subsequently discontinued encorafenib and/or binimetinib and/or anti-PD-1/-L1 due to severe toxicity.
* For participants in the SLI only: Current use or anticipated need for food or drugs that are known moderate or strong CYP3A4 inhibitors during screening and through the DLT-evaluation period
* Participant has not recovered to Grade ≤ 1 from toxic effects of prior therapy and/or complications from prior surgical intervention before enrollment (SLI)/ randomization (Phase 3).
* Receipt of protocol defined medications or treatments outside of required intervals before enrollment (SLI)/randomization (Phase 3):
* Previous administration with an investigational drug ≤ 6 months prior to enrollment (SLI)/randomization (Phase 3).
* Known sensitivity or contraindication to any component of study intervention (encorafenib, binimetinib and pembrolizumab), or their excipients.
* Pregnant, confirmed by a positive β-hCG laboratory test result, or is breastfeeding (lactating).
* Investigator site staff or Pfizer employees directly involved in the conduct of the study, site staff otherwise supervised by the investigator, and their respective family members.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role collaborator

Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

AdventHealth Orlando Infusion Center

Orlando, Florida, United States

Site Status

AdventHealth Orlando, Investigational Drug Services

Orlando, Florida, United States

Site Status

AdventHealth Orlando

Orlando, Florida, United States

Site Status

The University of Kansas Clinical Research Center

Fairway, Kansas, United States

Site Status

The University of Kansas Cancer Center - Overland Park

Overland Park, Kansas, United States

Site Status

The University of Kansas Cancer Center, Investigational Drug Services

Westwood, Kansas, United States

Site Status

The University of Kansas Cancer Center

Westwood, Kansas, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Ophthalmic Consultants of Boston Inc (OCB)

Boston, Massachusetts, United States

Site Status

University of Cincinnati Medical Center

Cincinnati, Ohio, United States

Site Status

University of Cincinnati Medical Center

West Chester, Ohio, United States

Site Status

University of Tennessee Medical Center

Knoxville, Tennessee, United States

Site Status

Sarah Cannon Research Institute

Nashville, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Nashville, Tennessee, United States

Site Status

Instituto Alexander Fleming

CABA, Buenos Aires, Argentina

Site Status

Clinica Viedma S. A

Viedma, Río Negro Province, Argentina

Site Status

Medizinische Universität Graz

Graz, , Austria

Site Status

Cliniques universitaires Saint-Luc

Brussels, , Belgium

Site Status

Instituto de Oncologia do Paraná - IOP Matriz Mateus Leme

Curitiba, Paraná, Brazil

Site Status

Instituto de Oncologia do Paraná - IOP Oncoville

Curitiba, Paraná, Brazil

Site Status

Instituto Nacional de Câncer José Alencar Gomes da Silva - INCA

Rio de Janeiro, Rio de Janeiro, Brazil

Site Status

Hospital de Clínicas de Passo Fundo

Passo Fundo, Rio Grande do Sul, Brazil

Site Status

Hospital de Clinicas de Porto Alegre

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Fundação Pio XII - Hospital de Câncer de Barretos

Barretos, São Paulo, Brazil

Site Status

Hospital Sírio-Libanês - Unidade Bela Vista

São Paulo, , Brazil

Site Status

Complex Oncology Center - Plovdiv EOOD

Plovdiv, , Bulgaria

Site Status

Medical Center Nadezhda Clinical EOOD

Sofia, , Bulgaria

Site Status

Acibadem City Clinic Multiprofile Hospital for Active Treatment Tokuda EAD

Sofia, , Bulgaria

Site Status

Umhato Ead

Sofia, , Bulgaria

Site Status

CIUSSS du Saguenay-Lac-Saint-Jean

Chicoutimi, Quebec, Canada

Site Status

Olomouc University Hospital

Olomouc, Olomoucký kraj, Czechia

Site Status

Fakultni nemocnice Ostrava

Ostrava-Poruba, , Czechia

Site Status

Fakultni nemocnice Bulovka

Praha 8-Liben, , Czechia

Site Status

Tampereen yliopistollinen sairaala

Tampere, Pirkanmaa, Finland

Site Status

Helsinki University Hospital - Comprehensive Cancer Center (HYKS - Syöpäkeskus)

Helsinki, , Finland

Site Status

CHU d'Amiens - Hôpital Nord

Amiens, , France

Site Status

CHU Grenoble Alpes

La Tronche, , France

Site Status

Hôpital Lyon Sud

Pierre-Bénite, , France

Site Status

CHU de Poitiers

Poitiers, , France

Site Status

Universitaetsklinikum Tuebingen

Tübingen, Baden-Wurttemberg, Germany

Site Status

Klinik und Poliklinik für Dermatologie und Allergologie

München, Bavaria, Germany

Site Status

Universitätsklinikum Bonn

Bonn, North Rhine-Westphalia, Germany

Site Status

Johannes Wesling Klinikum Minden

Minden, North Rhine-Westphalia, Germany

Site Status

Universitätsmedizin Johannes Gutenberg Universität Mainz

Mainz, Rhineland-Palatinate, Germany

Site Status

Universitaetsklinikum Carl Gustav Carus, Technischen Universitaet Dresden

Dresden, Saxony, Germany

Site Status

Universitätsklinikum Leipzig

Leipzig, Saxony, Germany

Site Status

Universitaetsklinikum Schleswig-Holstein Campus Kiel

Kiel, Schleswig-Holstein, Germany

Site Status

Universitätsklinikum Schleswig-Holstein

Lübeck, Schleswig-Holstein, Germany

Site Status

SRH Wald-Klinikum Gera

Gera, Thuringia, Germany

Site Status

Charité Universitaetsmedizin Berlin - Campus Mitte

Berlin, , Germany

Site Status

HELIOS Klinikum Erfurt

Erfurt, , Germany

Site Status

Universitätsklinikum Essen (AöR)

Essen, , Germany

Site Status

Universitaetsklinikum Halle - Universitaetsklinik und Poliklinik fuer Dermatologie und Venerologie

Halle, , Germany

Site Status

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Universitätsklinikum Heidelberg

Heidelberg, , Germany

Site Status

University Hospital Muenster

Münster, , Germany

Site Status

Fachklinik Hornheide

Münster, , Germany

Site Status

Klinikum Nürnberg Nord

Nuremberg, , Germany

Site Status

Universitätsklinikum Regensburg

Regensburg, , Germany

Site Status

General Hospital of Athens "Laiko"

Athens, Attikí, Greece

Site Status

Laiko Hospital

Athens, Attikí, Greece

Site Status

Pécsi Tudományegyetem Klinikai Központ

Pécs, Baranya, Hungary

Site Status

Jász-Nagykun-Szolnok Megyei Hetényi Géza Kórház

Szolnok, Jász-Nagykun-Szolnok, Hungary

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

Orszagos Onkologiai Intezet

Budapest, , Hungary

Site Status

Debreceni Egyetem Klinikai Kozpont

Debrecen, , Hungary

Site Status

Szent-Gyorgyi Albert Klinikai Kozpont

Szeged, , Hungary

Site Status

Soroka University Medical Center

Beersheba, , Israel

Site Status

Hadassah Medical Organization, Hadassah Medical Center, Ein-Karem

Jerusalem, , Israel

Site Status

Azienda Sanitaria Universitaria Friuli Centrale

Udine, Friuli Venezia Giulia, Italy

Site Status

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, MI, Italy

Site Status

Istituto Dermopatico dell'Immacolata (IDI-IRCCS)

Roma, RM, Italy

Site Status

A.O.U.S. Policlinico "Le Scotte"

Siena, SI, Italy

Site Status

Istituto di Candiolo IRCCS - Fondazione del Piemonte per l'Oncologia

Candiolo, Torino, Italy

Site Status

Istituto Tumori Giovanni Paolo II

Bari, , Italy

Site Status

IRCCS Ospedale Policlinico San Martino

Genova, , Italy

Site Status

Istituto Europeo di Oncologia IRCCS

Milan, , Italy

Site Status

Istituto Nazionale Tumori IRCCS "Fondazione G. Pascale"

Napoli, , Italy

Site Status

Istituto Oncologico Veneto IOV - IRCCS

Padua, , Italy

Site Status

AO di Perugia - Ospedale S. Maria della Misericordia, S.C Oncologia Medica

Perugia, , Italy

Site Status

Istituto Nazionale Tumori Regina Elena

Roma, , Italy

Site Status

Preparaciones Oncológicas S.C.

León, Guanajuato, Mexico

Site Status

ONCARE Viaducto Nápoles

Benito Juárez, Mexico City, Mexico

Site Status

I Can Oncology Center S.A. de C.V.

Monterrey, Nuevo León, Mexico

Site Status

BRCR Global Mexico - CDMX

Mexico City, , Mexico

Site Status

El Cielo Medical Center RSB, S.C

Puebla City, , Mexico

Site Status

Palmerston North Hospital

Palmerston North, Manawatu, New Zealand

Site Status

Oslo universitetssykehus, Radiumhospitalet

Oslo, , Norway

Site Status

Jagiellońskie Centrum Innowacji Sp. z o .o.

Krakow, , Poland

Site Status

Szpital Kliniczny im. Heliodora Święcickiego UM w Poznaniu

Poznan, , Poland

Site Status

Narodowy Instytut Onkologii im. Marii Skłodowskiej-Curie - Państwowy Instytut Badawczy

Warsaw, , Poland

Site Status

Private Medical Institution "Euromedservice"

Pushkin, Sankt-Peterburg, Russia

Site Status

Ars Medika Center, LLC

Kaliningrad, , Russia

Site Status

BIH of Omsk Region "Clinical Oncological Dispensary"

Omsk, , Russia

Site Status

Eurocityclinic LLC

Saint Petersburg, , Russia

Site Status

Onkologicky ustav sv. Alzbety, s.r.o.

Bratislava, , Slovakia

Site Status

Narodny onkologicky ustav

Bratislava, , Slovakia

Site Status

Vychodoslovensky onkologicky ustav, a.s.

Košice, , Slovakia

Site Status

Nemocnica na okraji mesta, n.o.

Partizánske, , Slovakia

Site Status

POKO Poprad, s.r.o.

Poprad, , Slovakia

Site Status

WCR Office

Johannesburg, Gauteng, South Africa

Site Status

Wits Clinical Research

Johannesburg, Gauteng, South Africa

Site Status

Sandton Oncology Medical Group (Pty) Ltd

Johannesburg, Gauteng, South Africa

Site Status

Drs Alberts, Bouwer and Jordaan Inc.

Pretoria, Gauteng, South Africa

Site Status

ICO-Badalona Hospital Germans Trias i Pujol

Badalona, Barcelona, Spain

Site Status

Hospital Universitario Marqués de Valdecilla

Santander, Cantabria, Spain

Site Status

Hospital Universitario Puerta de Hierro Majadahonda

Majadahonda, Madrid, Spain

Site Status

Hospital Clinico Universitario Virgen de la Arrixaca

El Palmar, Murcia, Spain

Site Status

CHUAC-Hospital Teresa Herrera

A Coruña, , Spain

Site Status

Hospital Universitari Vall D'Hebron, Servicio de Oncología Médica

Barcelona, , Spain

Site Status

Hospital Clinic Barcelona

Barcelona, , Spain

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofía

Córdoba, , Spain

Site Status

Complejo Hospitalario de Jaen

Jaén, , Spain

Site Status

Hospital Universitario Arnau de Vilanova

Lleida, , Spain

Site Status

Hospital Universitario Ramón y Cajal

Madrid, , Spain

Site Status

Hospital Regional Universitario de Malaga - Hospital Civil

Málaga, , Spain

Site Status

Hospital Universitario Virgen Macarena

Seville, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Fundacion Instituto Valenciano de Oncologia

Valencia, , Spain

Site Status

Hospital Universitario Miguel Servet

Zaragoza, , Spain

Site Status

UniversitätsSpital Zürich

Zürich Flughafen, , Switzerland

Site Status

Istanbul University Cerrahpasa Medical Faculty Hospital

Istanbul, İ̇stanbul, Turkey (Türkiye)

Site Status

TC Saglik Bakanligi Goztepe Prof. Dr. Suleyman Yalcin Sehir Hastanesi

Istanbul, İ̇stanbul, Turkey (Türkiye)

Site Status

Memorial Ankara Hastanesi

Ankara, , Turkey (Türkiye)

Site Status

CNI KRC "Regional Cardiology Centre"

Kharkiv, , Ukraine

Site Status

National Cancer Institute

Kyiv, , Ukraine

Site Status

Communal Noncommercial Enterprise of Lviv Regional Council "Lviv Oncological Regional Therapeutical

Lviv, , Ukraine

Site Status

Derzhavna ustanova Instytut zahalnoi ta nevidkladnoi khirurhii im.V.T.Zaitseva Natsionalnoi akademii

M. Kharkiv, , Ukraine

Site Status

St. Bartholomew's Hospital, Barts Health NHS Trust

London, , United Kingdom

Site Status

The South West Wales Cancer Institute, Swansea Bay University Health Board

Swansea, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Austria Belgium Brazil Bulgaria Canada Czechia Finland France Germany Greece Hungary Israel Italy Mexico New Zealand Norway Poland Russia Slovakia South Africa Spain Switzerland Turkey (Türkiye) Ukraine United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Schadendorf D, Dummer R, Robert C, Ribas A, Sullivan RJ, Panella T, McKean M, Santos ES, Brill K, Polli A, Pietro AD, Ascierto PA. STARBOARD: encorafenib + binimetinib + pembrolizumab for first-line metastatic/unresectable BRAF V600-mutant melanoma. Future Oncol. 2022 Jun;18(17):2041-2051. doi: 10.2217/fon-2021-1486. Epub 2022 Mar 11.

Reference Type DERIVED
PMID: 35272485 (View on PubMed)

Zimmer L, Livingstone E, Krackhardt A, Schultz ES, Goppner D, Assaf C, Trebing D, Stelter K, Windemuth-Kieselbach C, Ugurel S, Schadendorf D. Encorafenib, binimetinib plus pembrolizumab triplet therapy in patients with advanced BRAFV600 mutant melanoma: safety and tolerability results from the phase I IMMU-TARGET trial. Eur J Cancer. 2021 Nov;158:72-84. doi: 10.1016/j.ejca.2021.09.011. Epub 2021 Oct 13.

Reference Type DERIVED
PMID: 34655839 (View on PubMed)

Related Links

Access external resources that provide additional context or updates about the study.

https://pmiform.com/clinical-trial-info-request?StudyID=C4221016

To obtain contact information for a study center near you, click here.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

KEYNOTE-B80

Identifier Type: OTHER

Identifier Source: secondary_id

2024-512038-13-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

STARBOARD

Identifier Type: OTHER

Identifier Source: secondary_id

C4221016

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.