Pembrolizumab With Talimogene Laherparepvec or Placebo in Unresected Melanoma

NCT ID: NCT02263508

Last Updated: 2022-11-14

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

713 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-12-08

Study Completion Date

2021-03-11

Brief Summary

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The primary objectives of the Phase 1b part of the study are to evaluate the safety, as assessed by incidence of dose limiting toxicity (DLT), of talimogene laherparepvec in combination with pembrolizumab in adults with previously untreated, unresectable, stage IIIB to IVM1c melanoma.

The primary objective of Phase 3 are to evaluate the efficacy of talimogene laherparepvec with pembrolizumab versus placebo with pembrolizumab, as assessed by progression-free survival (PFS) (response evaluation by blinded independent central review using modified Response Evaluation Criteria in Solid Tumors \[RECIST\] 1.1) and overall survival (OS).

Detailed Description

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Conditions

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Melanoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Phase 1b was an open-label, single-arm study. Phase 3 was a randomized, double-blind, placebo-controlled study design.
Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Phase 1b: Talimogene Laherparepvec + Pembrolizumab

Participants received talimogene laherparepvec at an initial dose of up to 4 mL 10⁶ plaque-forming units (PFU)/mL by intralesional injection. Subsequent doses of talimogene laherparepvec at up to 4 mL of 10⁸ PFU/mL began 3 weeks after the first dose and were administered every 2 weeks until disappearance of injectable lesions, complete response (CR), confirmed disease progression (PD) per modified Immune-related Response Criteria (irRC), intolerance of study treatment, 24 months from the date of the first dose of pembrolizumab, or end of study, whichever occurred first. Participants also received 200 mg pembrolizumab administered intravenously every 2 weeks starting at the time of the third dose of talimogene laherparepvec (week 6) until confirmed PD per modified irRC, treatment intolerance, 24 months from the first dose, or end of study, whichever occurred first.

Group Type EXPERIMENTAL

Talimogene Laherparepvec

Intervention Type DRUG

Talimogene laherparepvec administered by intratumoral injection

Pembrolizumab

Intervention Type DRUG

Administered at a dose of 200 mg as an intravenous infusion over approximately 30 minutes.

Phase 3 : Placebo + Pembrolizumab

Participants received up to 4 mL placebo to talimogene laherparepvec by intralesional injection on day 1 of week 0. Subsequent doses of placebo (up to 4 mL) began 3 weeks after the first dose and were administered every 2 weeks until the fifth injection (week 9), and then synchronously with pembrolizumab thereafter every 3 weeks until disappearance of injectable lesions, complete response per modified Immune-related Response Criteria simulating Response Evaluation Criteria in Solid Tumors (irRC-RECIST) (iCR), confirmed iPD per modified irRC-RECIST, intolerance of study treatment, 24 months from the date of the first dose of placebo, or end of study, whichever occurred first. Participants also received 200 mg pembrolizumab administered intravenously every 3 weeks starting on day 1 of week 0, until confirmed iPD per modified irRC-RECIST, treatment intolerance, 24 months from the first dose, or end of study, whichever occurred first.

Group Type PLACEBO_COMPARATOR

Pembrolizumab

Intervention Type DRUG

Administered at a dose of 200 mg as an intravenous infusion over approximately 30 minutes.

Placebo

Intervention Type DRUG

Administered by intratumoral injection

Phase 3: Talimogene Laherparepvec + Pembrolizumab

Participants received talimogene laherparepvec at an initial dose of up to 4 mL 10⁶ PFU/mL by intralesional injection on day 1. Subsequent doses of talimogene laherparepvec at 10⁸ PFU/mL (up to 4 mL) began 3 weeks after the first dose and were administered every 2 weeks until the fifth injection of talimogene laherparepvec (week 9), and then synchronously with pembrolizumab thereafter every 3 weeks until disappearance of injectable lesions, iCR, confirmed iPD per modified irRC-RECIST, intolerance of study treatment, 24 months from the date of the first dose of talimogene laherparepvec, or end of study, whichever occurred first. Participants also received 200 mg pembrolizumab administered intravenously every 3 weeks starting on day 1 of week 0, until confirmed iPD per modified irRC-RECIST, treatment intolerance, 24 months from the first dose, or end of study, whichever occurred first.

Group Type EXPERIMENTAL

Talimogene Laherparepvec

Intervention Type DRUG

Talimogene laherparepvec administered by intratumoral injection

Pembrolizumab

Intervention Type DRUG

Administered at a dose of 200 mg as an intravenous infusion over approximately 30 minutes.

Interventions

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Talimogene Laherparepvec

Talimogene laherparepvec administered by intratumoral injection

Intervention Type DRUG

Pembrolizumab

Administered at a dose of 200 mg as an intravenous infusion over approximately 30 minutes.

Intervention Type DRUG

Placebo

Administered by intratumoral injection

Intervention Type DRUG

Other Intervention Names

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IMLYGIC® OncoVEX^GM-CSF T-VEC MK-3475 Keytruda®

Eligibility Criteria

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Inclusion Criteria

* Age ≥ 18 years with histologically confirmed diagnosis of melanoma and stage IIIB to IVM1c for whom surgery is not recommended.
* Subjects must have measurable disease and be a candidate for intralesional therapy administration into cutaneous, subcutaneous, or nodal lesions.
* Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
* Adequate hematologic, hepatic, renal, and coagulation function.
* Subjects with serine/threonine protein kinase B-Raf V600 (BRAFV600) wild-type tumors must not have received any prior systemic anticancer treatment consisting of chemotherapy, immunotherapy, or targeted therapy given in a non-adjuvant setting for unresectable stage IIIB to IVM1c melanoma.
* Subjects with B-Raf V600 (BRAFV600) mutated tumors who have received prior BRAF inhibitor therapy either alone or in combination with mitogen-activated protein kinase kinase (MEK) inhibitor as their only prior systemic therapy are eligible.
* Subjects who received prior adjuvant therapy for melanoma will not be excluded (including, but not limited to, interferon, ipilimumab, limb infusion/perfusion, or use of investigational agents in the adjuvant setting) with the exception that prior adjuvant therapy with inhibitors of programmed cell death-1 (PD-1) or programmed cell death ligand 1 (PD-L1) is not allowed. However, if the subject received adjuvant therapy, the subject must have completed therapy at least 28 days prior to enrollment.
* Subjects must have a tumor sample that is adequate for PD-L1 assessment prior to randomization.

Exclusion Criteria

* Subjects must not have clinically active cerebral metastases.
* Subjects must not have primary uveal or mucosal melanoma, history or evidence of melanoma associated with immunodeficiency states or history of other malignancy within the past 3 years.
* Subjects may not have been previously treated with talimogene laherparepvec, any other oncolytic virus, pembrolizumab, or any other inhibitor of PD-1, PD-L1, or PD-L2.
* Subjects must not have history or evidence of symptomatic autoimmune pneumonitis, glomerulonephritis, vasculitis, other symptomatic autoimmune disease, documented history of autoimmune disease or syndrome requiring systemic treatment in the past 2 years (ie, with use of disease modifying agents, steroids or immunosuppressive agents) except vitiligo or resolved childhood asthma/atopy, or evidence of clinically significant immunosuppression.
* Subjects must not have active herpetic skin lesions or prior complications of herpetic infection and must not require intermittent or chronic treatment with an antiherpetic drug (eg, acyclovir), other than intermittent topical use.
Minimum Eligible Age

18 Years

Maximum Eligible Age

95 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role collaborator

Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Birmingham, Alabama, United States

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Mobile, Alabama, United States

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Beverly Hills, California, United States

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Duarte, California, United States

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Encinitas, California, United States

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La Jolla, California, United States

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Los Angeles, California, United States

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Los Angeles, California, United States

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Riverside, California, United States

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San Francisco, California, United States

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San Francisco, California, United States

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Santa Monica, California, United States

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Miami, Florida, United States

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Miami Beach, Florida, United States

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Orlando, Florida, United States

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Atlanta, Georgia, United States

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Chicago, Illinois, United States

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Chicago, Illinois, United States

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Louisville, Kentucky, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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Detroit, Michigan, United States

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Fridley, Minnesota, United States

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St Louis, Missouri, United States

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Hackensack, New Jersey, United States

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Buffalo, New York, United States

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New York, New York, United States

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New York, New York, United States

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New York, New York, United States

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Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Germantown, Tennessee, United States

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Knoxville, Tennessee, United States

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Nashville, Tennessee, United States

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Dallas, Texas, United States

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Murray, Utah, United States

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Salt Lake City, Utah, United States

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Seattle, Washington, United States

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North Sydney, New South Wales, Australia

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Waratah, New South Wales, Australia

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Wollongong, New South Wales, Australia

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Southport, Queensland, Australia

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Woolloongabba, Queensland, Australia

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Woodville South, South Australia, Australia

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Geelong, Victoria, Australia

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Heidelberg, Victoria, Australia

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Melbourne, Victoria, Australia

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Prahran, Victoria, Australia

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Murdoch, Western Australia, Australia

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Graz, , Austria

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Innsbruck, , Austria

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Salzburg, , Austria

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Vienna, , Austria

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Brussels, , Belgium

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Liège, , Belgium

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Edmonton, Alberta, Canada

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Kingston, Ontario, Canada

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London, Ontario, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Brno, , Czechia

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Olomouc, , Czechia

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Ostrava-Poruba, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Helsinki, , Finland

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Bordeaux, , France

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Grenoble, , France

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Lille, , France

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Lyon, , France

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Marseille, , France

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Nantes, , France

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Paris, , France

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Pierre-Bénite, , France

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Toulouse, , France

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Vandœuvre-lès-Nancy, , France

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Berlin, , Germany

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Dresden, , Germany

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Erlangen, , Germany

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Essen, , Germany

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Hanover, , Germany

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Heidelberg, , Germany

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Kiel, , Germany

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Leipzig, , Germany

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Mainz, , Germany

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Mannheim, , Germany

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München, , Germany

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Regensburg, , Germany

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Tübingen, , Germany

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Würzburg, , Germany

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Athens, , Greece

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Athens, , Greece

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Heraklion - Crete, , Greece

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Ioannina, , Greece

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Thessaloniki, , Greece

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Budapest, , Hungary

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Pécs, , Hungary

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Szeged, , Hungary

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Bergamo, , Italy

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Brescia, , Italy

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Meldola FC, , Italy

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Milan, , Italy

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Milan, , Italy

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Siena, , Italy

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Amsterdam, , Netherlands

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Amsterdam, , Netherlands

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Groningen, , Netherlands

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Nijmegen, , Netherlands

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Bielsko-Biala, , Poland

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Bydgoszcz, , Poland

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Gdansk, , Poland

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Konin, , Poland

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Krakow, , Poland

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Poznan, , Poland

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Poznan, , Poland

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Szczecin, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Almada, , Portugal

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Lisbon, , Portugal

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Lisbon, , Portugal

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Porto, , Portugal

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Moscow, , Russia

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Saint Petersburg, , Russia

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Groenkloof, Gauteng, South Africa

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Johannesburg, Gauteng, South Africa

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Parktown, Gauteng, South Africa

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Kraaifontein, , South Africa

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Pretoria, , South Africa

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Pretoria, , South Africa

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Seoul, , South Korea

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Seoul, , South Korea

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Donostia / San Sebastian, Basque Country, Spain

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Badalona, Catalonia, Spain

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Barcelona, Catalonia, Spain

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Pamplona, Navarre, Spain

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Valencia, Valencia, Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Bellinzona, , Switzerland

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Bern, , Switzerland

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Geneva, , Switzerland

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Lausanne, , Switzerland

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Zurich, , Switzerland

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Birmingham, , United Kingdom

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Guildford, , United Kingdom

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Leeds, , United Kingdom

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Leicester, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Oxford, , United Kingdom

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Preston, , United Kingdom

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Southampton, , United Kingdom

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Countries

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United States Australia Austria Belgium Canada Czechia Finland France Germany Greece Hungary Italy Netherlands Poland Portugal Russia South Africa South Korea Spain Switzerland United Kingdom

References

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Ribas A, Dummer R, Puzanov I, VanderWalde A, Andtbacka RHI, Michielin O, Olszanski AJ, Malvehy J, Cebon J, Fernandez E, Kirkwood JM, Gajewski TF, Chen L, Gorski KS, Anderson AA, Diede SJ, Lassman ME, Gansert J, Hodi FS, Long GV. Oncolytic Virotherapy Promotes Intratumoral T Cell Infiltration and Improves Anti-PD-1 Immunotherapy. Cell. 2017 Sep 7;170(6):1109-1119.e10. doi: 10.1016/j.cell.2017.08.027.

Reference Type BACKGROUND
PMID: 28886381 (View on PubMed)

Dummer R, Hoeller C, Gruter IP, Michielin O. Combining talimogene laherparepvec with immunotherapies in melanoma and other solid tumors. Cancer Immunol Immunother. 2017 Jun;66(6):683-695. doi: 10.1007/s00262-017-1967-1. Epub 2017 Feb 25.

Reference Type BACKGROUND
PMID: 28238174 (View on PubMed)

Chesney JA, Ribas A, Long GV, Kirkwood JM, Dummer R, Puzanov I, Hoeller C, Gajewski TF, Gutzmer R, Rutkowski P, Demidov L, Arenberger P, Shin SJ, Ferrucci PF, Haydon A, Hyngstrom J, van Thienen JV, Haferkamp S, Guilera JM, Rapoport BL, VanderWalde A, Diede SJ, Anderson JR, Treichel S, Chan EL, Bhatta S, Gansert J, Hodi FS, Gogas H. Randomized, Double-Blind, Placebo-Controlled, Global Phase III Trial of Talimogene Laherparepvec Combined With Pembrolizumab for Advanced Melanoma. J Clin Oncol. 2023 Jan 20;41(3):528-540. doi: 10.1200/JCO.22.00343. Epub 2022 Aug 23.

Reference Type BACKGROUND
PMID: 35998300 (View on PubMed)

Watanabe D, Goshima F. Oncolytic Virotherapy by HSV. Adv Exp Med Biol. 2018;1045:63-84. doi: 10.1007/978-981-10-7230-7_4.

Reference Type DERIVED
PMID: 29896663 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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2014-000185-22

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

KEYNOTE-034

Identifier Type: OTHER

Identifier Source: secondary_id

20110265

Identifier Type: -

Identifier Source: org_study_id

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