Open-Label Extension Study of Ubenimex in Patients With Pulmonary Arterial Hypertension (WHO Group 1)

NCT ID: NCT02736149

Last Updated: 2023-01-18

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

51 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-12-31

Study Completion Date

2018-08-31

Brief Summary

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Ubenimex is being developed for the treatment of pulmonary arterial hypertension (PAH) (World Health Organization \[WHO\] Group 1) to improve exercise capacity and delay clinical worsening.

This study is a Phase 2, open-label, extension study to evaluate long-term safety and efficacy of ubenimex in patients with PAH (WHO Group 1) who complete Study EIG-UBX-001.

Detailed Description

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This study is a Phase 2, open-label, multicenter, extension study to evaluate long-term safety and efficacy of ubenimex in patients with PAH (WHO Group 1) who complete Study EIG-UBX-001 (Study EIG-UBX-001 is a Phase 2, randomized, double-blind, placebo-controlled clinical trial) and meet the eligibility criteria for Study EIG-UBX-002. The primary objective for this study is:

\- to obtain long-term safety and tolerability data for ubenimex (150 mg administered three times daily \[TID\]) in patients with PAH (WHO Group 1).

Conditions

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Pulmonary Arterial Hypertension

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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ubenimex

ubenimex capsules 150 mg three times a day (TID), administered orally, minimum of 24 weeks for all patients.

The maximum anticipated time an individual patient will participate will vary because treatment will continue until the last patient enrolled has received at least 24 weeks of open-label treatment.

Group Type EXPERIMENTAL

ubenimex

Intervention Type DRUG

Interventions

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ubenimex

Intervention Type DRUG

Other Intervention Names

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UBX

Eligibility Criteria

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Inclusion Criteria

* Patients must have completed Study EIG-UBX-001 through Week 24.
* In the opinion of the Principal Investigator, has been generally compliant with study requirements during Study EIG-UBX-001.
* Agrees to use a medically acceptable method of contraception throughout the entire study period.
* Willing and able to comply with scheduled visits, treatment plans, and laboratory tests and other study procedures.

Exclusion Criteria

* Is pregnant or lactating.
* Concurrent regular use of another leukotriene pathway inhibitor.
* Any reason that, in the opinion of the investigator, precludes the patient from participating in the study.

1. Any condition that is unstable or that could jeopardize the safety of the patient and his/her compliance in the study
2. A serious uncontrolled medical disorder/condition that in the opinion of the investigator would impair the ability of the patient to receive protocol therapy
* An ongoing, drug-related, serious adverse event (SAE).
* Significant/chronic renal insufficiency.
* Transaminases (alanine transaminase, aspartate transaminase) levels \>3 × upper limit of normal (ULN) and/or bilirubin level \>2 × ULN.
* Absolute neutrophil count \<1500 mm3.
* Hemoglobin concentration \<9 g/dL at Screening.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Eiger BioPharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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California Heart Center Foundation, An Affiliate of Cedars-Sinai Heart Institute, Cedars-Sinai Medical Care Foundation

Beverly Hills, California, United States

Site Status

UCSD Medical Center

La Jolla, California, United States

Site Status

Stanford University Medical Center

Palo Alto, California, United States

Site Status

Harbor - UCLA Medical Center

Torrance, California, United States

Site Status

University of Colorado Denver

Aurora, Colorado, United States

Site Status

Cleveland Clinic, Florida

Weston, Florida, United States

Site Status

Kentuckiana Pulmonary Associates

Louisville, Kentucky, United States

Site Status

Chest Medicine Associates

South Portland, Maine, United States

Site Status

Johns Hopkins University, Pulmonary and Critical Care Medicine

Baltimore, Maryland, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

Boston University School of Medicine

Boston, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

Mayo Clinic College of Medicine

Rochester, Minnesota, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Weill Cornell Medicine

New York, New York, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Cleveland Clinic Respiratory Institute

Cleveland, Ohio, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Allegheny General Hospital

Pittsburgh, Pennsylvania, United States

Site Status

University of Pennsylvania Medical Center

Pittsburgh, Pennsylvania, United States

Site Status

Alpert Medical School of Brown University Rhode Island Hospital

Providence, Rhode Island, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

Houston Methodist Hospital

Houston, Texas, United States

Site Status

University Texas Health Science Center

San Antonio, Texas, United States

Site Status

London Health Sciences Centre

London, Ontario, Canada

Site Status

University of Ottawa Heart Institute

Ottawa, Ontario, Canada

Site Status

Countries

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United States Canada

References

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Tian W, Jiang X, Tamosiuniene R, Sung YK, Qian J, Dhillon G, Gera L, Farkas L, Rabinovitch M, Zamanian RT, Inayathullah M, Fridlib M, Rajadas J, Peters-Golden M, Voelkel NF, Nicolls MR. Blocking macrophage leukotriene b4 prevents endothelial injury and reverses pulmonary hypertension. Sci Transl Med. 2013 Aug 28;5(200):200ra117. doi: 10.1126/scitranslmed.3006674.

Reference Type BACKGROUND
PMID: 23986401 (View on PubMed)

Qian J, Tian W, Jiang X, Tamosiuniene R, Sung YK, Shuffle EM, Tu AB, Valenzuela A, Jiang S, Zamanian RT, Fiorentino DF, Voelkel NF, Peters-Golden M, Stenmark KR, Chung L, Rabinovitch M, Nicolls MR. Leukotriene B4 Activates Pulmonary Artery Adventitial Fibroblasts in Pulmonary Hypertension. Hypertension. 2015 Dec;66(6):1227-1239. doi: 10.1161/HYPERTENSIONAHA.115.06370. Epub 2015 Oct 5.

Reference Type BACKGROUND
PMID: 26558820 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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EIG-UBX-002

Identifier Type: -

Identifier Source: org_study_id

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