Trial Outcomes & Findings for Open-Label Extension Study of Ubenimex in Patients With Pulmonary Arterial Hypertension (WHO Group 1) (NCT NCT02736149)

NCT ID: NCT02736149

Last Updated: 2023-01-18

Results Overview

Number of Patients with TEAEs collected for all patients and recorded on the Adverse Event Case Report Form

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

51 participants

Primary outcome timeframe

At least 24 weeks of open-label treatment with ubenimex followed by 4 weeks follow-up

Results posted on

2023-01-18

Participant Flow

Participant milestones

Participant milestones
Measure
Ubenimex
ubenimex capsules 150 mg three times a day (TID), administered orally, minimum of 24 weeks for all patients. The maximum anticipated time an individual patient will participate will vary because treatment will continue until the last patient enrolled has received at least 24 weeks of open-label treatment.
Overall Study
STARTED
51
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
51

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Open-Label Extension Study of Ubenimex in Patients With Pulmonary Arterial Hypertension (WHO Group 1)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Ubenimex
n=51 Participants
ubenimex capsules 150 mg three times a day (TID), administered orally, minimum of 24 weeks for all patients. The maximum anticipated time an individual patient will participate will vary because treatment will continue until the last patient enrolled has received at least 24 weeks of open-label treatment.
Age, Continuous
51.8 years
n=5 Participants
Sex: Female, Male
Female
41 Participants
n=5 Participants
Sex: Female, Male
Male
10 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=5 Participants
Race (NIH/OMB)
White
46 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
3 Participants
n=5 Participants
Mean pulmonary artery pressure
45.43 millimetre of mercury (mmHg)
STANDARD_DEVIATION 9.95 • n=5 Participants

PRIMARY outcome

Timeframe: At least 24 weeks of open-label treatment with ubenimex followed by 4 weeks follow-up

Number of Patients with TEAEs collected for all patients and recorded on the Adverse Event Case Report Form

Outcome measures

Outcome measures
Measure
Ubenimex
n=51 Participants
Ubenimex capsules 150 mg three times a day (TID), administered orally, minimum of 24 weeks for all patients. The maximum anticipated time an individual patient will participate will vary because treatment will continue until the last patient enrolled has received at least 24 weeks of open-label treatment.
Treatment-emergent Adverse Events (TEAEs)
44 Participants

Adverse Events

Ubenimex

Serious events: 12 serious events
Other events: 42 other events
Deaths: 1 deaths

Serious adverse events

Serious adverse events
Measure
Ubenimex
n=51 participants at risk
ubenimex capsules 150 mg TID, administered orally, minimum of 24 weeks for all patients. The maximum anticipated time an individual patient will participate will vary because treatment will continue until the last patient enrolled has received at least 24 weeks of open-label treatment.
Cardiac disorders
Right ventricular failure
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Vascular disorders
Syncope
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
General disorders
Device occlusion
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Renal and urinary disorders
Nephrolithiasis
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Gastrointestinal disorders
Ascites
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Respiratory, thoracic and mediastinal disorders
Dyspnoea
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Metabolism and nutrition disorders
Dehydration
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
General disorders
Ulcer
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Gastrointestinal disorders
Bowel obstruction
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Gastrointestinal disorders
Abdominal pain
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Respiratory, thoracic and mediastinal disorders
Respiratory failure
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Surgical and medical procedures
Wound drainage /
2.0%
1/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up

Other adverse events

Other adverse events
Measure
Ubenimex
n=51 participants at risk
ubenimex capsules 150 mg TID, administered orally, minimum of 24 weeks for all patients. The maximum anticipated time an individual patient will participate will vary because treatment will continue until the last patient enrolled has received at least 24 weeks of open-label treatment.
Gastrointestinal disorders
Nausea
13.7%
7/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Gastrointestinal disorders
Diarrhea
11.8%
6/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Metabolism and nutrition disorders
oedema peripheral
17.6%
9/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Respiratory, thoracic and mediastinal disorders
Dyspnoea
15.7%
8/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Respiratory, thoracic and mediastinal disorders
Upper respiratory tract infection
11.8%
6/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up
Nervous system disorders
headache
11.8%
6/51 • Up to 24 weeks of treatment from baseline with 4 weeks of follow-up

Additional Information

Senior VP, Clinical Development

Eiger BioPharmaceuticals, Inc.

Phone: 1-650-272-6138

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place