ARTEMIS-PH - Study of Ambrisentan in Subjects With Pulmonary Hypertension Associated With Idiopathic Pulmonary Fibrosis

NCT ID: NCT00879229

Last Updated: 2014-05-15

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

40 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-07-31

Study Completion Date

2011-02-28

Brief Summary

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Ambrisentan is an endothelin receptor antagonist used for the treatment of pulmonary hypertension (PH). Based on research suggesting a role for endothelin-1 in the pathogenesis of idiopathic pulmonary fibrosis (IPF) and the poor prognosis for patients with IPF who are also diagnosed with PH, this study was designed to evaluate the effectiveness and safety of ambrisentan in that patient population.

Detailed Description

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Conditions

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Idiopathic Pulmonary Fibrosis Pulmonary Hypertension

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Ambrisentan

Participants were randomized to receive ambrisentan treatment at an initial dose of 5 mg for 4 weeks, followed by ambrisentan at the target dose of 10 mg for an additional 52 weeks

Group Type EXPERIMENTAL

Ambrisentan

Intervention Type DRUG

Ambrisentan (5 mg or 10 mg tablet) administered orally once daily.

Placebo

Participants were randomized to receive placebo to match ambrisentan for 48 weeks, then transition to ambrisentan treatment at the initial dose of 5 mg for 4 weeks, followed by ambrisentan at the target dose of 10 mg for an additional 4 weeks.

Group Type PLACEBO_COMPARATOR

Ambrisentan

Intervention Type DRUG

Ambrisentan (5 mg or 10 mg tablet) administered orally once daily.

Placebo

Intervention Type DRUG

Placebo to match ambrisentan administered orally once daily.

Interventions

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Ambrisentan

Ambrisentan (5 mg or 10 mg tablet) administered orally once daily.

Intervention Type DRUG

Placebo

Placebo to match ambrisentan administered orally once daily.

Intervention Type DRUG

Other Intervention Names

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Letairis

Eligibility Criteria

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Inclusion Criteria

* Weight ≥ 40 kg at screening
* Diagnosis of IPF based on modified American Thoracic Society-European Respiratory Society guidelines
* Diagnosis of PH based on the following hemodynamic requirements: mean pulmonary artery pressure (mPAP ≥ 25 mm Hg; pulmonary vascular resistance \> 240 dyne.sec/cm\^5; pulmonary capillary wedge pressure or left ventricular end-diastolic pressure ≤ 15 mm Hg
* Forced vital capacity (FVC) ≥ 40%
* Able to walk at least 50 meters during two 6-minute walk tests
* If receiving calcium channel blockers, low-dose oral corticosteroids, immunosuppressive, cytoxic, or antifibrotic drugs dose must have been stable.

Exclusion Criteria

* Diagnosis of PH primarily due to an etiology other than IPF
* Surgical lung biopsy diagnosis other than Usual Interstitial Pneumonia
* Other known cause of interstitial lung disease
* Evidence of significant obstructive lung disease
* Recent hospitalization for an acute exacerbation of IPF
* Recent active pulmonary or upper respiratory tract infection
* Left ventricular ejection fraction \< 40%
* Serum creatinine ≥ 2.5 mg/dL
* Required hemodialysis, peritoneal dialysis, or hemofiltration
* Female subject who was pregnant or breastfeeding
* Recent treatment for PH with an endothelin receptor antagonist (ERA), phosphodiesterase type 5 inhibitor, or prostacyclin derivative
* Recent treatment with high dose oral corticosteroids
* Recent treatment (within 4 weeks prior to screening) with imatinib mesylate (Gleevec)
* Alanine aminotransferase or aspartate aminotransferase lab value that was greater than 1.5 x the upper limit of the normal range
* Discontinued other ERA treatment for any adverse reaction other than those associated with liver function test abnormalities
Minimum Eligible Age

35 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Hunter Gillies, M.D.

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Mayo Clinic Arizona

Scottsdale, Arizona, United States

Site Status

University of California Davis

Davis, California, United States

Site Status

David Geffen School of Medicine UCLA

Los Angeles, California, United States

Site Status

University of California San Diego Medical Center

San Diego, California, United States

Site Status

University of California at San Francisco

San Francisco, California, United States

Site Status

Stanford University

Stanford, California, United States

Site Status

University of Colorado Heatlh Sciences Center

Aurora, Colorado, United States

Site Status

Bay Area Chest Physicians

Clearwater, Florida, United States

Site Status

University of Florida

Gainesville, Florida, United States

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University of Miami Medical Center

Miami, Florida, United States

Site Status

Suncoast Lung Center

Sarasota, Florida, United States

Site Status

Sarasota Memorial Hospital

Sarasota, Florida, United States

Site Status

Cleveland Clinic Florida

Weston, Florida, United States

Site Status

Atlanta Institute for Medical Research

Decatur, Georgia, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

Kentuckiana Pulmonary Association

Louisville, Kentucky, United States

Site Status

Maine Medical Center

Portland, Maine, United States

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Johns Hopkins University School of Medicine

Baltimore, Maryland, United States

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Tufts Medical Center

Boston, Massachusetts, United States

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Brigham and Women's Hospital

Boston, Massachusetts, United States

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Boston University Medical Center

Boston, Massachusetts, United States

Site Status

Beth Israel Deacones Medical Center

Boston, Massachusetts, United States

Site Status

University of Michigan Health Systems

Ann Arbor, Michigan, United States

Site Status

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Creighton University Center for Allergy & Asthma

Omaha, Nebraska, United States

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Dartmouth Medical School

Lebanon, New Hampshire, United States

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Albany Medical Center

Albany, New York, United States

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Winthrop University Hospital

Mineola, New York, United States

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North Shore Health System

New Hyde Park, New York, United States

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Mount Sinai School of Medicine

New York, New York, United States

Site Status

Columbia University

New York, New York, United States

Site Status

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

The Lindner Center for Research & Education at The Christ Hospital

Cincinnati, Ohio, United States

Site Status

University Hospitals of Cleveland Case Western

Cleveland, Ohio, United States

Site Status

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Temple University School of Medicine

Philadelphia, Pennsylvania, United States

Site Status

Alleghany General Hospital

Pittsburgh, Pennsylvania, United States

Site Status

University of Pittsburgh Cancer Institute

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

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University of Texas Southwestern

Dallas, Texas, United States

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Baylor College of Medicine

Houston, Texas, United States

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University of Utah

Salt Lake City, Utah, United States

Site Status

Inova Heart Institiute and Vascular Institute

Falls Church, Virginia, United States

Site Status

Virginia Commonwealth University Health System

Richmond, Virginia, United States

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Providence Everett Medical Center

Everett, Washington, United States

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St. Vincents Hospital

Sydney, New South Wales, Australia

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The Prince Charles Hospital

Chermside, Queensland, Australia

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Royal Perth Hospital

Perth, Western Australia, Australia

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Medizinische Universität Graz

Graz, , Austria

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Universitatsklinikum Innsbruck

Innsbruck, , Austria

Site Status

Medizinische Universität Wien

Vienna, , Austria

Site Status

Peter Loughheed Center- Calgary General Hospital

Calgary, Alberta, Canada

Site Status

University of British Columbia

Vancouver, British Columbia, Canada

Site Status

London Health Sciences Centre

London, Ontario, Canada

Site Status

Toronto General Hospital

Toronto, Ontario, Canada

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Centre Hospitalier De L'Universite de Montreal

Montreal, Quebec, Canada

Site Status

Sir Mortimer B. Davis Jewish General Center

Montreal, Quebec, Canada

Site Status

Centre de Pneumologie de L'Hospital Laval

Sainte-Foy, Quebec, Canada

Site Status

Evangelische Lungenklinik Berlin

Berlin, , Germany

Site Status

Charite-Universitatsmedizin Berlin

Berlin, , Germany

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Krankenhaus Donaustauf der LVA

Donaustauf, , Germany

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Universitatsklinikum Freiburg

Freiburg im Breisgau, , Germany

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Universitat Greifswald

Greifswald, , Germany

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Medizinische Hochschule Hannover

Hanover, , Germany

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Thorax Klinik

Heidelberg, , Germany

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LMU Klinikum der Universitat

München, , Germany

Site Status

Azienda Ospedaliero Universitaria

Catania, , Italy

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Presidio Ospedaliero G.B. Morgagni

Forlì, , Italy

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Ospedale S.Giuseppe Fatebenefratelli

Milan, , Italy

Site Status

Unita Funzionale di Pneumologia e Fisiopatologia Respiratoria

Milan, , Italy

Site Status

Azienda Ospedaliera di Padova

Padua, , Italy

Site Status

Instituto Mediterraneo per i Trapianti e Terapie ad Alta Specializzazione

Palermo, , Italy

Site Status

Policlinico Universitario Tor Vergata

Rome, , Italy

Site Status

Azienda Ospedaliera Universitaria Senese

Siena, , Italy

Site Status

Centro delle Interstiziopatie Polmonari e Malattie Rare del Polmone

Torino, , Italy

Site Status

Papworth Hospital NHS Foundation Trust

Cambridge, , United Kingdom

Site Status

University Hospital Aintree

Liverpool, , United Kingdom

Site Status

University College Hosptial

London, , United Kingdom

Site Status

Royal Hallamshire Hospital

Sheffield, , United Kingdom

Site Status

Countries

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United States Australia Austria Canada Germany Italy United Kingdom

References

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Ruocco G, Cekorja B, Rottoli P, Refini RM, Pellegrini M, Di Tommaso C, Del Castillo G, Franci B, Nuti R, Palazzuoli A. Role of BNP and echo measurement for pulmonary hypertension recognition in patients with interstitial lung disease: An algorithm application model. Respir Med. 2015 Mar;109(3):406-15. doi: 10.1016/j.rmed.2014.12.011. Epub 2015 Jan 3.

Reference Type DERIVED
PMID: 25613108 (View on PubMed)

Other Identifiers

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GS-US-300-0128

Identifier Type: -

Identifier Source: org_study_id

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