A Study to Learn About the Study Medicine Called PF-07868489 in Healthy Adult People and in People With Pulmonary Arterial Hypertension

NCT ID: NCT06137742

Last Updated: 2025-12-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

90 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-11-17

Study Completion Date

2027-02-13

Brief Summary

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The purpose of the study is to learn how the study medicine called PF-07868489 is tolerated and acts in healthy adult people and people with pulmonary arterial hypertension (PAH).

Part A:

An investigator- and participant-blind, sponsor-open, placebo-controlled, single ascending dose study to assess the safety, tolerability, and pharmacokinetics (PK) of PF-07868489 in healthy adult participants.

Part B:

A 24-week, randomized, double blind, placebo-controlled study to assess the safety, tolerability, PK, and pharmacodynamics (PD) of PF-07868489 in adult participants with PAH.

Detailed Description

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Conditions

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Pulmonary Arterial Hypertension

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Part A is a sequential study. Part B is a parallel group study.
Primary Study Purpose

BASIC_SCIENCE

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Part A is an investigator- and participant-blind, sponsor-open, placebo-controlled, single ascending dose.

Part B is a 24-week, randomized, double blind, placebo-controlled study.

Study Groups

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PF-07868489

single subcutaneous injection (Part A); 6 subcutaneous injections at regular intervals (Part B)

Group Type EXPERIMENTAL

PF-07868489

Intervention Type DRUG

Experimental Treatment

Placebo

single subcutaneous injection (Part A); 6 subcutaneous injections at regular intervals (Part B)

Group Type PLACEBO_COMPARATOR

Placebo for PF-07868489

Intervention Type DRUG

Placebo

Interventions

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PF-07868489

Experimental Treatment

Intervention Type DRUG

Placebo for PF-07868489

Placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* overtly healthy
* Body mass index (BMI) of 16 to 32 kg/m2; and a total body weight \>50 kg.


* diagnosis of pulmonary arterial hypertension (PAH)
* stable dose of standard of care PAH vasodilators
* BMI 16 to 40 kg/m2; and a total body weight \>45 kg.
* 6MWD ≥ 150 and ≤ 450.
* Pre-randomization RHC documenting a minimum of PVR ≥ 400 dyn ∙sec/cm5.

Exclusion Criteria

* clinically significant hematological, renal, endocrine, pulmonary, gastrointestinal, cardiovascular, hepatic, psychiatric, neurological, infections or allergic disease.
* smoking more than 10 cigarettes (or equivalent) per day or smoking history ≥10 pack-years.


* Any medical or psychiatric condition or laboratory abnormality.
* Stopped receiving pulmonary hypertension chronic general supportive therapy 90 days prior to Day 1.
* Pulmonary capillary wedge pressure \> 15 mmHg on right heart catheterization (RHC) conducted during Screening.
* History of severe allergic or anaphylactic reaction or hypersensitivity to recombinant proteins or excipients in investigational product.
* Major surgery within 8 weeks prior to randomization.
* Participants who smoke more than 10 cigarettes (or equivalent) per day or has a smoking history ≥10 pack-years.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Anaheim Clinical Trials, LLC

Anaheim, California, United States

Site Status ACTIVE_NOT_RECRUITING

UCI Health - Costa Mesa

Costa Mesa, California, United States

Site Status NOT_YET_RECRUITING

UCI Health Center for Innovative Health Therapies (CIHT)

Orange, California, United States

Site Status NOT_YET_RECRUITING

University of California, Irvine Medical Center

Orange, California, United States

Site Status NOT_YET_RECRUITING

UC Davis Health Medical Center

Sacramento, California, United States

Site Status NOT_YET_RECRUITING

University of California Davis Health

Sacramento, California, United States

Site Status NOT_YET_RECRUITING

UCSF Health St. Mary's Hospital

San Francisco, California, United States

Site Status RECRUITING

UCSF Helen Diller Medical Center at Parnassus Heights

San Francisco, California, United States

Site Status RECRUITING

University of Colorado Anschutz Medical Campus

Aurora, Colorado, United States

Site Status NOT_YET_RECRUITING

Norton Hospital

Louisville, Kentucky, United States

Site Status NOT_YET_RECRUITING

Norton Pulmonary Specialists

Louisville, Kentucky, United States

Site Status NOT_YET_RECRUITING

Icahn school of medicine at Mount Sinai

New York, New York, United States

Site Status RECRUITING

Eastowne 100 Medical Office Building

Chapel Hill, North Carolina, United States

Site Status RECRUITING

Eastowne Medical Office Building - Clinical Research Unit

Chapel Hill, North Carolina, United States

Site Status RECRUITING

UNC Health - Eastowne Medical Office

Chapel Hill, North Carolina, United States

Site Status RECRUITING

UNC Hospitals

Chapel Hill, North Carolina, United States

Site Status RECRUITING

Investigational Drug Services Pharmacy

Morrisville, North Carolina, United States

Site Status RECRUITING

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status NOT_YET_RECRUITING

Center for Advanced Lung Care

Providence, Rhode Island, United States

Site Status NOT_YET_RECRUITING

Medical University of South Carolina - Nexus

Charleston, South Carolina, United States

Site Status RECRUITING

Medical University of South Carolina - Radiology

Charleston, South Carolina, United States

Site Status RECRUITING

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status RECRUITING

Royal Prince Alfred Hospital

Camperdown, New South Wales, Australia

Site Status RECRUITING

Wesley Research Institute

Auchenflower, Queensland, Australia

Site Status RECRUITING

Université Libre de Bruxelles - Hôpital Erasme

Brussels, Bruxelles-capitale, Région de, Belgium

Site Status RECRUITING

UZ Leuven

Leuven, Vlaams-brabant, Belgium

Site Status RECRUITING

London Health Sciences Centre - Verspeeten Family Cancer Centre

London, Ontario, Canada

Site Status NOT_YET_RECRUITING

London Health Sciences Centre - University Hospital

London, Ontario, Canada

Site Status NOT_YET_RECRUITING

Guangdong Provincial People's Hospital

Guangzhou, Guangdong, China

Site Status RECRUITING

The Second Xiangya Hospital of Central South University

Changsha, Hunan, China

Site Status RECRUITING

Zhongda Hospital Southeast University

Nanjing, Jiangsu, China

Site Status RECRUITING

Shanghai Pulmonary Hospital

Shanghai, Shanghai Municipality, China

Site Status RECRUITING

Vseobecna fakultni nemocnice v Praze

Prague, , Czechia

Site Status RECRUITING

Institut Klinicke a Experimentalni Mediciny

Prague, , Czechia

Site Status NOT_YET_RECRUITING

CHRU de Brest

Brest, Finistère, France

Site Status RECRUITING

Centre Hospitalier Universitaire de Saint Étienne - Hôpital Nord

Saint Priest En Jarez, Pays de la Loire Region, France

Site Status RECRUITING

Chu Grenoble Alpes

La Tronche, , France

Site Status NOT_YET_RECRUITING

Thoraxklinik-Heidelberg gGmbH

Heidelberg, Baden-Wurttemberg, Germany

Site Status RECRUITING

Universitätsklinikum Regensburg

Regensburg, Bavaria, Germany

Site Status RECRUITING

UKGM Gießen/Marburg

Giessen, Hesse, Germany

Site Status RECRUITING

Universitätsmedizin Greifswald

Greifswald, Mecklenburg-Vorpommern, Germany

Site Status RECRUITING

Universitaetsklinikum Carl Gustav Carus, Technischen Universitaet Dresden

Dresden, Saxony, Germany

Site Status RECRUITING

University General Hospital "ATTIKON" - General Hospital of West Attica "H AGIA VARVARA"

Chaïdári, Attikí, Greece

Site Status NOT_YET_RECRUITING

Fondazione IRCCS San Gerardo dei Tintori

Monza, Monza E Brianza, Italy

Site Status NOT_YET_RECRUITING

ISMETT Istituto Mediterraneo per i Trapianti e Terapie ad Alta Specializzazione

Palermo, , Italy

Site Status NOT_YET_RECRUITING

Fondazione IRCCS Policlinico San Matteo

Pavia, , Italy

Site Status RECRUITING

Kobe University Hospital

Kobe, Hyōgo, Japan

Site Status RECRUITING

St. Marianna University Hospital

Kawasaki, Kanagawa, Japan

Site Status RECRUITING

Tohoku University Hospital

Sendai, Miyagi, Japan

Site Status RECRUITING

Yokohama City University Hospital

Kanagawa, , Japan

Site Status NOT_YET_RECRUITING

National Hospital Organization Okayama Medical Center

Okayama, , Japan

Site Status RECRUITING

Gachon University Gil Medical Center

Namdong-gu, Incheon-gwangyeoksi [incheon], South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, Seoul-teukbyeolsi [seoul], South Korea

Site Status RECRUITING

Severance Hospital, Yonsei University Health System

Seoul, Seoul-teukbyeolsi [seoul], South Korea

Site Status RECRUITING

Samsung Medical Center

Seoul, Seoul-teukbyeolsi [seoul], South Korea

Site Status RECRUITING

Hospital Universitario Marqués de Valdecilla

Santander, Cantabria, Spain

Site Status NOT_YET_RECRUITING

Hospital Universitario La Paz

Madrid, Madrid, Comunidad de, Spain

Site Status RECRUITING

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status RECRUITING

Hammersmith Hospital

London, London, CITY of, United Kingdom

Site Status RECRUITING

Golden Jubilee National Hospital

Clydebank, , United Kingdom

Site Status NOT_YET_RECRUITING

Royal Free Hospital

London, , United Kingdom

Site Status NOT_YET_RECRUITING

Royal Brompton Hospital

London, , United Kingdom

Site Status NOT_YET_RECRUITING

Countries

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United States Australia Belgium Canada China Czechia France Germany Greece Italy Japan South Korea Spain United Kingdom

Central Contacts

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Pfizer CT.gov Call Center

Role: CONTACT

1-800-718-1021

Related Links

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https://pmiform.com/clinical-trial-info-request?StudyID=C5001001

To obtain contact information for a study center near you, click here.

Other Identifiers

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2024-514064-17-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

C5001001

Identifier Type: -

Identifier Source: org_study_id