(ARTEMIS-IPF) Randomized, Placebo-Controlled Study to Evaluate Safety and Effectiveness of Ambrisentan in IPF

NCT ID: NCT00768300

Last Updated: 2014-04-08

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

494 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-12-31

Study Completion Date

2011-02-28

Brief Summary

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The ARTEMIS-IPF study was conducted to determine if ambrisentan was effective in delaying disease progression and death in participants with idiopathic pulmonary fibrosis (IPF), to evaluate its safety, and to evaluate its effect on development of pulmonary hypertension, quality of life, and dyspnea (shortness of breath) symptoms in this participant population. Participants were randomized in a 2:1 ratio to receive ambrisentan or placebo, respectively. Participation in the study was to be up to 4 years, depending on how long it would take to enroll participants and observe study events. After randomization, visits to the clinic took place every 3 months, and laboratory procedures were performed every month.

Detailed Description

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Conditions

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Idiopathic Pulmonary Fibrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Ambrisentan

Group Type EXPERIMENTAL

Ambrisentan

Intervention Type DRUG

Ambrisentan (5mg or 10 mg tablet) was administered orally once daily.

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo to match ambrisentan was administered orally once daily.

Interventions

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Ambrisentan

Ambrisentan (5mg or 10 mg tablet) was administered orally once daily.

Intervention Type DRUG

Placebo

Placebo to match ambrisentan was administered orally once daily.

Intervention Type DRUG

Other Intervention Names

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Letairis®

Eligibility Criteria

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Inclusion Criteria

* Male or females from 40 to 80 years of age
* Diagnosis of IPF
* Honeycombing (fibrosis in the lung) on high-resolution computerised tomography (HRCT) scan of less than or equal to 5%
* Willing and able to have 2 right heart catheterizations performed
* Willing to have monthly lab tests to monitor liver function
* Able to perform the 6 minute walk test (indicated adequate physical function)
* Must have meet lung function requirements
* Normal liver function tests
* Negative serum pregnancy test
* Willing to use at least 2 reliable methods of contraception
* Able to understand and willing to sign informed consent form

Exclusion Criteria

* No restrictive lung disease (other than usual interstitial pneumonia or IPF)
* No obstructive lung disease
* No recent or active respiratory exacerbations
* No recent hospitalization for an IPF exacerbation
* No recent history of alcohol abuse
* Chronic sildenafil (or same drug class) use for pulmonary hypertension
* Chronic treatment with certain medications for IPF within 30 days of randomization
* No other serious medical conditions
Minimum Eligible Age

40 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Ganesh Raghu, MD

Role: STUDY_CHAIR

University of Washington, Div. of Pulmonary and Critical Care Medicine Chair

Locations

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University of Alabama at Birmingham Hospital

Birmingham, Alabama, United States

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Pulmonary Associates

Phoenix, Arizona, United States

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Scottsdale, Arizona, United States

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David Geffen School of Medicine at UCLA(Harbor-UCLA Medical Center)

Los Angeles, California, United States

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University of California, Davis

Sacramento, California, United States

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San Diego, California, United States

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San Francisco, California, United States

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Stanford University

Stanford, California, United States

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National Jewish Medical And Research Center

Denver, Colorado, United States

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Newark, Delaware, United States

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Bay Area Chest Physicians

Clearwater, Florida, United States

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University of Miami Miller School of Medicine

Miami, Florida, United States

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Tampa, Florida, United States

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Emory University

Atlanta, Georgia, United States

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University of Chicago

Chicago, Illinois, United States

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Council Bluffs, Iowa, United States

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Kentuckiana Pulmonary Association

Louisville, Kentucky, United States

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Louisville, Kentucky, United States

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Baltimore, Maryland, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Mayo Clinic

Rochester, Minnesota, United States

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Saint Lukes Foundation

Chesterfield, Missouri, United States

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Dartmouth Medical School

Lebanon, New Hampshire, United States

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New Brunswick, New Jersey, United States

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Piscataway, New Jersey, United States

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Pulmonary & Allergy Associates

Summit, New Jersey, United States

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Pulmonary And Critical Care Services, P.C.

Albany, New York, United States

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Winthrop University Hospital

Mineola, New York, United States

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New Hyde Park, New York, United States

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New York, New York, United States

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Columbia University Medical Center

New York, New York, United States

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Duke University Medical Center

Durham, North Carolina, United States

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Cincinnati, Ohio, United States

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The Cleveland Clinic Foundation

Cleveland, Ohio, United States

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Columbus, Ohio, United States

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The Oregon Clinic, P.C.

Portland, Oregon, United States

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University of Pennsylvania Health Systems

Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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University of Pittsburgh

Pittsburgh, Pennsylvania, United States

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The Reading Hospital and Medical Center

Reading, Pennsylvania, United States

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Medical University of South Carolina

Charleston, South Carolina, United States

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Lexington, South Carolina, United States

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Spartanburg, South Carolina, United States

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Nashville, Tennessee, United States

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Houston, Texas, United States

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McKinney, Texas, United States

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Provo, Utah, United States

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Salt Lake City, Utah, United States

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Charlottesville, Virginia, United States

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Falls Church, Virginia, United States

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Lynchburg, Virginia, United States

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Everett, Washington, United States

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Seattle, Washington, United States

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Mar del Plata, Buenos Aires, Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Mar Del Plata, Buenos Aires, , Argentina

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San Miguel de Tucumán, , Argentina

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Concord, New South Wales, Australia

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Darlinghurst, New South Wales, Australia

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Chermside, Queensland, Australia

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Woodville, South Australia, Australia

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Hobart, Tasmania, Australia

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Parkville, Victoria, Australia

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Prahran, Victoria, Australia

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Perth, Western Australia, Australia

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Graz, , Austria

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Innsbruck, , Austria

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Linz, , Austria

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Vienna, , Austria

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Anderlecht, , Belgium

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Brussels, , Belgium

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Leuven, , Belgium

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Yvoir, , Belgium

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São Paulo, São Paulo, Brazil

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Belo Horizonte, , Brazil

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Florianópolis, , Brazil

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Goiânia, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Rio de Janeiro, , Brazil

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Santo André, , Brazil

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Calgary, Alberta, Canada

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Edmondton, Alberta, Canada

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Vancouver, British Columbia, Canada

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Vancouver, British Columbia, Canada

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St. John's, Newfoundland and Labrador, Canada

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Montreal, Quebec, Canada

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Sainte-Foy, Quebec, Canada

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Toronto, , Canada

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Santiago, , Chile

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Talcahuano, , Chile

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Valparaíso, , Chile

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Bogotá, , Colombia

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Floridablanca, , Colombia

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Brno, , Czechia

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Hradec Králové, , Czechia

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Jihlava, , Czechia

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Liberec, , Czechia

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Olomouc, , Czechia

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Pilsen, , Czechia

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Lille, , France

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Marseille, , France

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Montpellier, , France

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Nice, , France

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Paris, , France

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Paris, , France

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Pessac, , France

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Rennes, , France

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Tours, , France

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Berlin, , Germany

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Berlin, , Germany

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Coswig, , Germany

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Donaustauf, , Germany

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Essen, , Germany

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Freiburg im Breisgau, , Germany

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Greifswald, , Germany

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Heidelberg, , Germany

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Löwenstein, , Germany

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München, , Germany

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Dublin, , Ireland

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Ashkelon, , Israel

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Beersheba, , Israel

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Haifa, , Israel

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Haifa, , Israel

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Jerusalem, , Israel

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Jerusalem, , Israel

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Petah Tikva, , Israel

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Rehovot, , Israel

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Tel Aviv, , Israel

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Tel Litwinsky, , Israel

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Catania, , Italy

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Forlì, , Italy

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Milan, , Italy

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Milan, , Italy

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Modena, , Italy

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Napoli, , Italy

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Padua, , Italy

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Palermo, , Italy

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Roma, , Italy

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Siena, , Italy

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Torino, , Italy

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Guadalajara, Jalisco, Mexico

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Monterrey, Nuevo León, Mexico

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Huixquilucan Edo. de Mexico, , Mexico

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Mexico City, DF, , Mexico

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Monterrey, , Mexico

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Zapopan, Jalisco, , Mexico

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Almelo, , Netherlands

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Callao, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Bydgoszcz, , Poland

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Lodz, , Poland

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Cadiz, Andalusia, Spain

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Hospital Virgen del Rocio

Seville, Andalusia, Spain

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Complejo Asistencial Universitario de León

León, Castilla, Spain

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Pontevedra, Galicia, Spain

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Pozuelo de Alarcón, Madrid, Communidad de, Spain

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Oviedo, Principality of Asturias, Spain

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Badalona, , Spain

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Barcelona, , Spain

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Madrid, , Spain

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Basel, , Switzerland

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Bern, , Switzerland

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Lausanne, , Switzerland

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Sheffield, South Yorkshire, United Kingdom

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Chertsey, Surrey, United Kingdom

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Cambridge, , United Kingdom

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Chelmsford, , United Kingdom

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Edinburgh, , United Kingdom

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Glasgow, , United Kingdom

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Liverpool, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Mancesheter, , United Kingdom

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Countries

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United States Argentina Australia Austria Belgium Brazil Canada Chile Colombia Czechia France Germany Ireland Israel Italy Mexico Netherlands Peru Poland Spain Switzerland United Kingdom

References

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Raghu G, Behr J, Brown KK, Egan JJ, Kawut SM, Flaherty KR, Martinez FJ, Nathan SD, Wells AU, Collard HR, Costabel U, Richeldi L, de Andrade J, Khalil N, Morrison LD, Lederer DJ, Shao L, Li X, Pedersen PS, Montgomery AB, Chien JW, O'Riordan TG; ARTEMIS-IPF Investigators*. Treatment of idiopathic pulmonary fibrosis with ambrisentan: a parallel, randomized trial. Ann Intern Med. 2013 May 7;158(9):641-9. doi: 10.7326/0003-4819-158-9-201305070-00003.

Reference Type RESULT
PMID: 23648946 (View on PubMed)

Raghu G, Lynch D, Godwin JD, Webb R, Colby TV, Leslie KO, Behr J, Brown KK, Egan JJ, Flaherty KR, Martinez FJ, Wells AU, Shao L, Zhou H, Pedersen PS, Sood R, Montgomery AB, O'Riordan TG. Diagnosis of idiopathic pulmonary fibrosis with high-resolution CT in patients with little or no radiological evidence of honeycombing: secondary analysis of a randomised, controlled trial. Lancet Respir Med. 2014 Apr;2(4):277-84. doi: 10.1016/S2213-2600(14)70011-6. Epub 2014 Feb 18.

Reference Type DERIVED
PMID: 24717624 (View on PubMed)

Chien JW, Richards TJ, Gibson KF, Zhang Y, Lindell KO, Shao L, Lyman SK, Adamkewicz JI, Smith V, Kaminski N, O'Riordan T. Serum lysyl oxidase-like 2 levels and idiopathic pulmonary fibrosis disease progression. Eur Respir J. 2014 May;43(5):1430-8. doi: 10.1183/09031936.00141013. Epub 2013 Oct 31.

Reference Type DERIVED
PMID: 24177001 (View on PubMed)

Other Identifiers

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GS-US-231-0101

Identifier Type: -

Identifier Source: org_study_id

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