A Study of TX000045 in Patients With Pulmonary Hypertension Secondary to Heart Failure With Preserved Ejection Fraction (the APEX Study)

NCT ID: NCT06616974

Last Updated: 2026-01-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

180 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-09-04

Study Completion Date

2026-11-20

Brief Summary

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TX000045-003 is a double-blind, randomized, parallel group, placebo-controlled, proof- of-concept (POC) study, evaluating 2 dose regimens of TX000045 over the course of a 24-week treatment period (the APEX study).

Detailed Description

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This study will enroll approximately 180 participants and eligible patients will be randomized to one of 3 treatment arms:

* Arm 1: Treatment Group 1: Placebo delivered subcutaneously (SC) every 2 weeks (Q2W) for 24 weeks
* Arm 2: Treatment Group 2: TX000045 SC at Dose A Q2W for 24 weeks
* Arm 3: Treatment Group 3: TX000045 SC at Dose B Q2W alternating with Placebo Q2W for 24 weeks

Conditions

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Pulmonary Hypertension Heart Failure With Preserved Ejection Fraction

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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TX000045 Dose B

Participants will receive alternating single doses of TX000045 Dose B and placebo subcutaneously every 2 weeks for 24 weeks from Day 1 to Day 155.

Group Type EXPERIMENTAL

TX000045- Dose B

Intervention Type DRUG

The participants will receive subcutaneous injection of Dose B of TX000045 every 4 weeks for 24 weeks where they will alternate between TX000045 and placebo every 2 weeks.

Placebo

Participants will receive a single placebo dose SC for 24 weeks from Day 1 to Day 155

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

The participants will receive a subcutaneous injection of placebo every 2 weeks for 24 weeks.

TX000045 Dose A

Participants will receive a single dose of TX000045 Dose A subcutaneously every 2 weeks for 24 weeks from Day 1 to Day 155.

Group Type EXPERIMENTAL

TX000045- Dose A

Intervention Type DRUG

The participants will receive a subcutaneous injection of Dose A of TX000045 every 2 weeks for 24 weeks.

Interventions

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TX000045- Dose A

The participants will receive a subcutaneous injection of Dose A of TX000045 every 2 weeks for 24 weeks.

Intervention Type DRUG

TX000045- Dose B

The participants will receive subcutaneous injection of Dose B of TX000045 every 4 weeks for 24 weeks where they will alternate between TX000045 and placebo every 2 weeks.

Intervention Type DRUG

Placebo

The participants will receive a subcutaneous injection of placebo every 2 weeks for 24 weeks.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Is a male or female of non-childbearing potential between the ages of 18 and 83 years.
2. Has a diagnosis of PH-HFpEF based on baseline echocardiogram and right heart catheterization (RHC).
3. Has NYHA functional class II- III heart failure.
4. Has 6MWT distance from 100 to 450m.
5. Chronic medication for heart failure or cardiovascular disease is at a stable dose prior to screening.
6. Is able to understand and provide documented consent for participation.

Exclusion Criteria

1. Diagnosis of PH in World Health Organization (WHO) Group 1, WHO Group 3, WHO Group 4, or WHO Group 5.
2. Current or recent hospitalization prior to screening.
3. Recently received vasoactive drugs, pulmonary arterial hypertension-specific therapies, or a relaxin receptor agonist.
4. Initiated a new exercise program for cardiopulmonary rehabilitation or plans to initiate such a program during the study.
5. Has a body mass index \<18 kg/meter square or \>45 kg/ meter square.
6. Was previously administered TX000045, relaxin, or a relaxin fusion protein.
7. Historical or current evidence of a clinically significant disease or disorder such as significant lung disease, cardiovascular comorbitiies, liver disease, infectious disease, or malignancy.
8. Has any of the following clinical laboratory values during screening:

1. Serum alanine aminotransferase or aspartate aminotransferase levels \> 3 x the upper limit of normal (ULN) or total bilirubin \> 3 x ULN;
2. eGFR \<30 mL/min/1.73 m2;
3. HbA1c (glycosylated hemoglobin) \>9%;
4. Platelet count \<50,000/millimeter cube;
5. Hemoglobin \<10.0g/dL;
9. History of hypersensitivity or reactions to drugs with a similar chemical structure or class to TX000045.
10. Is pregnant or breastfeeding.
11. Has a history of cancer within 5 years of screening other than basal cell carcinoma, cervical carcinoma, or squamous cell carcinomas of the skin.
12. Has a history of drug or alcohol abuse.
13. Was recently dosed in any clinical research study.
Minimum Eligible Age

18 Years

Maximum Eligible Age

83 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Tectonic Therapeutic

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Robert Rogers, MD

Role: STUDY_DIRECTOR

Tectonic Therapeutic

Locations

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Phoenix

Phoenix, Arizona, United States

Site Status RECRUITING

Scottsdale

Scottsdale, Arizona, United States

Site Status RECRUITING

San Francisco

San Francisco, California, United States

Site Status RECRUITING

Santa Rosa

Santa Rosa, California, United States

Site Status RECRUITING

Aurora

Aurora, Colorado, United States

Site Status RECRUITING

Jacksonville

Jacksonville, Florida, United States

Site Status RECRUITING

Tampa

Tampa, Florida, United States

Site Status RECRUITING

Augusta

Augusta, Georgia, United States

Site Status RECRUITING

McDonough

McDonough, Georgia, United States

Site Status RECRUITING

Boise

Boise, Idaho, United States

Site Status RECRUITING

Chicago

Chicago, Illinois, United States

Site Status RECRUITING

Indianapolis

Indianapolis, Indiana, United States

Site Status RECRUITING

USA

Louisville, Kentucky, United States

Site Status RECRUITING

Baltimore

Baltimore, Maryland, United States

Site Status RECRUITING

Boston

Boston, Massachusetts, United States

Site Status RECRUITING

Minneapolis

Minneapolis, Minnesota, United States

Site Status RECRUITING

St Louis

St Louis, Missouri, United States

Site Status RECRUITING

Omaha

Omaha, Nebraska, United States

Site Status RECRUITING

New York

New York, New York, United States

Site Status RECRUITING

New York

New York, New York, United States

Site Status RECRUITING

Durham

Durham, North Carolina, United States

Site Status RECRUITING

Toledo

Toledo, Ohio, United States

Site Status RECRUITING

Philadelphia

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

York

York, Pennsylvania, United States

Site Status RECRUITING

Rock Hill

Rock Hill, South Carolina, United States

Site Status RECRUITING

Port Arthur

Port Arthur, Texas, United States

Site Status RECRUITING

Waco

Waco, Texas, United States

Site Status RECRUITING

Salt Lake City

Salt Lake City, Utah, United States

Site Status RECRUITING

United States

Norfolk, Virginia, United States

Site Status RECRUITING

Richmond

Richmond, Virginia, United States

Site Status RECRUITING

Yerevan

Yerevan, , Armenia

Site Status RECRUITING

Yerevan

Yerevan, , Armenia

Site Status RECRUITING

Yerevan

Yerevan, , Armenia

Site Status RECRUITING

Camperdown

Camperdown, New South Wales, Australia

Site Status RECRUITING

Macquarie

Macquarie, New South Wales, Australia

Site Status RECRUITING

New Lambton

New Lambton, New South Wales, Australia

Site Status RECRUITING

Sydney

Sydney, New South Wales, Australia

Site Status RECRUITING

Wollongong

Wollongong, New South Wales, Australia

Site Status RECRUITING

Auchenflower

Auchenflower, Queensland, Australia

Site Status RECRUITING

Chermside

Chermside, Queensland, Australia

Site Status RECRUITING

Hobart

Hobart, Tasmania, Australia

Site Status RECRUITING

Malvern

Malvern, Victoria, Australia

Site Status RECRUITING

Camperdown

Camperdown, , Australia

Site Status RECRUITING

New Lambton

New Lambton, , Australia

Site Status RECRUITING

Austria

Vienna, , Austria

Site Status NOT_YET_RECRUITING

Brussel

Brussels, , Belgium

Site Status RECRUITING

Genk

Genk, , Belgium

Site Status RECRUITING

Pleven

Pleven, , Bulgaria

Site Status RECRUITING

Plovdiv

Plovdiv, , Bulgaria

Site Status RECRUITING

Sofia

Sofia, , Bulgaria

Site Status RECRUITING

Sofia

Sofia, , Bulgaria

Site Status RECRUITING

Tbilisi

Tbilisi, Tb, Georgia

Site Status RECRUITING

Tbilisi

Tbilisi, , Georgia

Site Status RECRUITING

Tbilisi

Tbilisi, , Georgia

Site Status RECRUITING

Tbilisi

Tbilisi, , Georgia

Site Status RECRUITING

Mainz

Mainz, , Germany

Site Status RECRUITING

Riga

Riga, , Latvia

Site Status RECRUITING

Chisinau

Chisinau, , Moldova

Site Status RECRUITING

Christchurch

Christchurch, , New Zealand

Site Status RECRUITING

Dunedin

Dunedin, , New Zealand

Site Status RECRUITING

Białystok

Bialystok, , Poland

Site Status RECRUITING

Krakow

Krakow, , Poland

Site Status RECRUITING

Łodź

Lodz, , Poland

Site Status RECRUITING

Lublin

Lublin, , Poland

Site Status RECRUITING

Warsaw

Warsaw, , Poland

Site Status RECRUITING

Wrocław

Wroclaw, , Poland

Site Status RECRUITING

Almada

Almada, , Portugal

Site Status RECRUITING

Lisboa

Lisbon, , Portugal

Site Status NOT_YET_RECRUITING

Porto

Porto, , Portugal

Site Status RECRUITING

Bucuresti

Bucharest, , Romania

Site Status RECRUITING

Craiova

Craiova, , Romania

Site Status RECRUITING

Targu Mures

Târgu Mureş, , Romania

Site Status RECRUITING

Nis, Belgrade

Belgrade, Nis, Serbia

Site Status RECRUITING

Belgrade

Belgrade, , Serbia

Site Status RECRUITING

Serbia

Belgrade, , Serbia

Site Status RECRUITING

Sremska Kamenica

Kamenitz, , Serbia

Site Status RECRUITING

Kragujevac

Kragujevac, , Serbia

Site Status RECRUITING

Barcelona

Barcelona, , Spain

Site Status RECRUITING

Madrid

Madrid, , Spain

Site Status RECRUITING

Madrid

Madrid, , Spain

Site Status RECRUITING

Santiago de Compostela ( Coruña )

Santiago de Compostela, , Spain

Site Status RECRUITING

Toledo

Toledo, , Spain

Site Status NOT_YET_RECRUITING

Valencia

Valencia, , Spain

Site Status RECRUITING

Valencia

Valencia, , Spain

Site Status RECRUITING

Ukraine

Kyiv, , Ukraine

Site Status RECRUITING

Countries

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United States Armenia Australia Austria Belgium Bulgaria Georgia Germany Latvia Moldova New Zealand Poland Portugal Romania Serbia Spain Ukraine

Central Contacts

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Clinical Trials

Role: CONTACT

+1 339 337 4053

Other Identifiers

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TX000045-003

Identifier Type: -

Identifier Source: org_study_id

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