Safety and Efficacy of Momelotinib in Subjects With Polycythemia Vera or Essential Thrombocythemia

NCT ID: NCT01998828

Last Updated: 2020-04-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

39 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-02-19

Study Completion Date

2015-05-07

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This open-label study is to determine the safety and efficacy of momelotinib in participants with either polycythemia vera (PV) or essential thrombocythemia (ET) who have not yet received treatment with a Janus kinase (JAK) inhibitor.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Polycythemia Vera Essential Thrombocythemia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Momelotinib 100 mg PV

Participants with polycythemia vera will receive 100 mg of momelotinib.

Group Type EXPERIMENTAL

Momelotinib

Intervention Type DRUG

Momelotinib tablet administered orally once daily

Momelotinib 200 mg PV

Participants with polycythemia vera will receive 200 mg of momelotinib.

Group Type EXPERIMENTAL

Momelotinib

Intervention Type DRUG

Momelotinib tablet administered orally once daily

Momelotinib 100 mg ET

Participants with essential thrombocythemia will receive 100 mg of momelotinib.

Group Type EXPERIMENTAL

Momelotinib

Intervention Type DRUG

Momelotinib tablet administered orally once daily

Momelotinib 200 mg ET

Participants with essential thrombocythemia will receive 200 mg of momelotinib.

Group Type EXPERIMENTAL

Momelotinib

Intervention Type DRUG

Momelotinib tablet administered orally once daily

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Momelotinib

Momelotinib tablet administered orally once daily

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

GS-0387 CYT387

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Diagnosis of either PV or ET as defined by the 2008 World Health Organization (WHO) Diagnostic Criteria
* Requires treatment for PV or ET, in the opinion of the study investigator
* Intolerant of, resistant to, or refuses current or available treatment for PV or ET
* Direct bilirubin ≤ 2.0 x upper limit of the normal range (ULN)
* Aspartate transaminase (AST) and alanine transaminase (ALT) ≤ 3 x ULN
* Calculated creatinine clearance (CrCl) of ≥ 45 mL/min
* Life expectancy \> 24 weeks
* Male subjects and female subjects of childbearing potential who engage in heterosexual intercourse must agree to use protocol specified method(s) of contraception
* Females who are nursing must agree to discontinue nursing before the first dose of study drug
* Able to comprehend and willing to sign informed consent form

Exclusion Criteria

* Prior splenectomy
* Uncontrolled intercurrent illness, per protocol
* Known positive status for human immunodeficiency virus (HIV)
* Chronic active or acute viral hepatitis A, B, or C infection, or hepatitis B or C carrier
* Myeloproliferative neoplasm-directed therapy, other than aspirin, hydroxyurea, anagrelide, and/or phlebotomy, within 21 days prior to the first dose of study drug
* Anagrelide within 7 days prior to the first dose of study drug
* Presence of peripheral neuropathy ≥ Grade 2
* Unwilling or unable to take oral medication
* Prior use of a JAK1 or JAK2 inhibitor
* Use of strong CYP3A4 inducers within 1 week prior to the first dose of study drug
* QTc interval \> 450 msec, unless attributed to bundle branch block
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Sierra Oncology LLC - a GSK company

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Peter Lee, MD, PhD

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Scottsdale, Arizona, United States

Site Status

Whittier, California, United States

Site Status

Tupelo, Mississippi, United States

Site Status

St Louis, Missouri, United States

Site Status

Houston, Texas, United States

Site Status

Frankston, Victoria, Australia

Site Status

Parkville, Victoria, Australia

Site Status

Vancouver, British Columbia, Canada

Site Status

Toronto, Ontario, Canada

Site Status

Montreal, Quebec, Canada

Site Status

La Tronche, , France

Site Status

Nantes, , France

Site Status

Paris, , France

Site Status

Dresden, , Germany

Site Status

Minden, , Germany

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Canada France Germany

References

Explore related publications, articles, or registry entries linked to this study.

Verstovsek S, Courby S, Griesshammer M, Mesa RA, Brachmann CB, Kawashima J, Maltzman JD, Shao L, Xin Y, Huang D, Bajel A. A phase 2 study of momelotinib, a potent JAK1 and JAK2 inhibitor, in patients with polycythemia vera or essential thrombocythemia. Leuk Res. 2017 Sep;60:11-17. doi: 10.1016/j.leukres.2017.05.002. Epub 2017 May 30.

Reference Type DERIVED
PMID: 28622623 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2013-004105-11

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GS-US-354-0101

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.