Study to Assess the Efficacy and Safety of Simtuzumab (GS-6624) in Adults With Idiopathic Pulmonary Fibrosis (IPF)

NCT ID: NCT01769196

Last Updated: 2017-05-30

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

544 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-01-31

Study Completion Date

2016-02-23

Brief Summary

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The primary objectives of this study are to determine the effect of simtuzumab (GS-6624) on progression-free survival (PFS) as determined by either a categorical decline in forced vital capacity (FVC) or all-cause mortality, in all participants enrolled or in a subset of participants who are classified as lysyl oxidase-like-2 (LOXL2) high based on a prespecified level in serum at baseline.

Detailed Description

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Conditions

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Idiopathic Pulmonary Fibrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Simtuzumab

Participants will receive simtuzumab for up to 254 weeks.

Group Type EXPERIMENTAL

Simtuzumab

Intervention Type DRUG

125 mg/mL single-dose vials administered subcutaneously once a week

Simtuzumab Placebo

Participants will receive simtuzumab placebo for up to 254 weeks.

Group Type PLACEBO_COMPARATOR

Simtuzumab placebo

Intervention Type DRUG

Simtuzumab placebo single-dose vials administered subcutaneously once a week

Interventions

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Simtuzumab

125 mg/mL single-dose vials administered subcutaneously once a week

Intervention Type DRUG

Simtuzumab placebo

Simtuzumab placebo single-dose vials administered subcutaneously once a week

Intervention Type DRUG

Other Intervention Names

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GS-6624

Eligibility Criteria

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Inclusion Criteria

* Male or female subjects from 45 to 85 years of age
* Definite IPF within 3 years prior to screening
* Be able to walk at least 50 meters

Exclusion Criteria

* Significant diseases other than IPF
* Obstructive lung disease
* Aortic aneurysm greater than or equal to 3.5 cm in diameter
* Treatment with immunosuppressive, cytotoxic, or antifibrotic drugs \< 28 days prior to randomization are not permitted.

* N-acetylcysteine is permitted provided the individual has been on a stable dose for \> 4 weeks prior to screening
* Concomitant use of pirfenidone or nintedanib must be in accordance with the approved prescribing instructions in the country where the site is located
* Individuals actively listed for lung transplant are excluded. However individuals at transplant centers with long waiting times (greater than 1 year) may be permitted to enter the study after discussion with Medical Monitor.
Minimum Eligible Age

45 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Arizona Pulmonary Specialists, Ltd.

Phoenix, Arizona, United States

Site Status

Saint Joseph's Hospital and Medical Center

Phoenix, Arizona, United States

Site Status

Arizona Pulmonary Specialists, Ltd.

Scottsdale, Arizona, United States

Site Status

Mayo Clinic Arizona

Scottsdale, Arizona, United States

Site Status

The University of Arizona

Tucson, Arizona, United States

Site Status

University of California San Diego

La Jolla, California, United States

Site Status

David Geffen School of Medicine at University of California, Los Angeles

Los Angeles, California, United States

Site Status

University of California Davis Medical Center

Sacramento, California, United States

Site Status

University of California San Francisco

San Francisco, California, United States

Site Status

Sansum Clinic

Santa Barbara, California, United States

Site Status

Stanford University Medical Center

Stanford, California, United States

Site Status

National Jewish Health

Denver, Colorado, United States

Site Status

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status

Bay Area Chest Physicians

Clearwater, Florida, United States

Site Status

University of Florida

Jacksonville, Florida, United States

Site Status

Mayo Clinic Florida

Jacksonville, Florida, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Sarasota Memorial Hospital

Sarasota, Florida, United States

Site Status

Tampa General Hospital

Tampa, Florida, United States

Site Status

Cleveland Clinic Florida

Weston, Florida, United States

Site Status

Emory University Hospital

Atlanta, Georgia, United States

Site Status

Southeastern Lung Care

Decatur, Georgia, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

Loyola University Medical Center

Maywood, Illinois, United States

Site Status

Loess Hills Clinical Research Center

Council Bluffs, Iowa, United States

Site Status

University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

Site Status

Kentuckiana Pulmonary Associates

Louisville, Kentucky, United States

Site Status

University of Louisville

Louisville, Kentucky, United States

Site Status

Tulane University School of Medicine

New Orleans, Louisiana, United States

Site Status

University of Maryland

Baltimore, Maryland, United States

Site Status

Tufts University School of Medicine

Boston, Massachusetts, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

University of Minnesota Medical Center

Minneapolis, Minnesota, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

CardioPulmonary Associates

Chesterfield, Missouri, United States

Site Status

Saint Luke's Midwest Pulmonary Consultants

Kansas City, Missouri, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

Robert Wood Johnson Medical School

New Brunswick, New Jersey, United States

Site Status

Pulmonary and Allergy Associates, PA

Summit, New Jersey, United States

Site Status

Albany Medical College

Albany, New York, United States

Site Status

Jamaica Hospital Medical Center

Jamaica, New York, United States

Site Status

North Shore University Hospital

New Hyde Park, New York, United States

Site Status

Mount Sinai School of Medicine

New York, New York, United States

Site Status

Columbia University

New York, New York, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

University of Rochester

Rochester, New York, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

University of Cincinnati Medical Center

Cincinnati, Ohio, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

Miami Valley Hospital

Dayton, Ohio, United States

Site Status

The Oregon Clinic, PC

Portland, Oregon, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, United States

Site Status

Temple University Hospital, Temple Lung Center

Philadelphia, Pennsylvania, United States

Site Status

University of Pittsburgh Presbyterian - Montefiore

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

University of Utah

Salt Lake City, Utah, United States

Site Status

Inova Fairfax Hospital

Falls Church, Virginia, United States

Site Status

Providence Everett Medical Center

Everett, Washington, United States

Site Status

University of Washington

Seattle, Washington, United States

Site Status

Froedtert Hospital and Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Royal Prince Alfred Hospital

Camperdown, New South Wales, Australia

Site Status

Concord Repatriation General Hospital

Concord, New South Wales, Australia

Site Status

Saint Vincents Hospital

Darlinghurst, New South Wales, Australia

Site Status

Mater Adult Hospital

Brisbane, Queensland, Australia

Site Status

Prince Charles Hospital

Chermside, Queensland, Australia

Site Status

Royal Brisbane and Women's Hospital

Herston, Queensland, Australia

Site Status

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status

Sir Charles Gairdner Hospital

Nedlands, Western Australia, Australia

Site Status

Royal Perth Hospital

Perth, Western Australia, Australia

Site Status

ULB Erasme

Anderlecht, Brussels Capital, Belgium

Site Status

Universitair Ziekenhuis Leuven

Leuven, Flemish Brabant, Belgium

Site Status

Cliniques Universitaires UCL de Mont-Godinne

Yvoir, Namur, Belgium

Site Status

Kelowna Respiratory and Allergy Clinic

Kelowna, British Columbia, Canada

Site Status

Vancouver General Hospital

Vancouver, British Columbia, Canada

Site Status

University of British Columbia

Vancouver, British Columbia, Canada

Site Status

Saint Joseph's Healthcare

Hamilton, Ontario, Canada

Site Status

University Health Network

Toronto, Ontario, Canada

Site Status

Centre Hospitalier de L'Université de Montréal Hôtel-Dieu

Montreal, Quebec, Canada

Site Status

Institut Universitaire de Cardiologie et de Pneumologie de Québec

Québec, Quebec, Canada

Site Status

Fakultní nemocnice Brno

Brno, Jihormoravsky Kraj, Czechia

Site Status

Nemocnice Jihlava

Jihlava, Jihormoravsky Kraj, Czechia

Site Status

Krajská nemocnice Liberec a.s.

Liberec, Severocesky Kraj, Czechia

Site Status

Masarykova nemocnice v Ústí nad Labem o.z.

Ústí nad Labem, Severocesky Kraj, Czechia

Site Status

Fakultní Nemocnice Ostrava

Ostrava - Poruba, Severomoravsky Kraj, Czechia

Site Status

Fakultní nemocnice Plzen

Pilsen, Zapadocesky Kraj, Czechia

Site Status

Thomayerova nemocnice

Prague 4 - Krc, , Czechia

Site Status

Hôpitaux Universitaires de Strasbourg

Strasbourg, Alsace, France

Site Status

Centre Hospitalier Universitaire Grenoble Hopital Michalon

Grenoble, Auvergne-Rhône-Alpes, France

Site Status

Centre Hospitalier Universitaire de Rennes, Hôpital Pontchaillou

Rennes, Brittany Region, France

Site Status

Centre Hospitalier Régional et Universitaire - Hôpital Bretonneau

Tours, Centre-Val de Loire, France

Site Status

Hôpital Albert Calmette

Lille, Hauts-de-France, France

Site Status

Hôpital Arnaud de Villeneuve

Montpellier, Languedoc-roussillon, France

Site Status

Hôpital Larrey, CHU de Toulouse, Service de Pneumologie

Toulouse, Midi-pyrenees, France

Site Status

Centre Hospitalier Universitaire de Nice-Hôpital Pasteur

Nice, Poitou-charentes, France

Site Status

Centre Hospitalier Universitaire Hôpital Nord

Marseille, Provence-Alpes-Côte d'Azur Region, France

Site Status

Hôpital Louis Pradel

Bron, Rhone-aples, France

Site Status

Centre Hospitalier Universitaire Hôpital Avicenne

Bobigny, Île-de-France Region, France

Site Status

Hôpital Bichat-Claude Bernard

Paris, Île-de-France Region, France

Site Status

HEGP

Paris, Île-de-France Region, France

Site Status

Universität Freiburg, Klinikum, Abt für Pneumologie

Freiburg im Breisgau, Baden-Wurttemberg, Germany

Site Status

Thoraxklinik am Universitätsklinikum Heidelberg

Heidelberg, Baden-Wurttemberg, Germany

Site Status

Ruhrlandklinik

Mannheim, Baden-Wurttemberg, Germany

Site Status

Klinikum Großhadern der Ludwig-Maximilians-Universität München

München, Bavaria, Germany

Site Status

Philipps-Universität und Universitätsklinikum Gießen und Marburg GmbH

Giessen, Hesse, Germany

Site Status

Lungenfachklinik Immenhausen

Immenhausen, Hesse, Germany

Site Status

Medizinische Hochschule Hannover

Hanover, Lower Saxony, Germany

Site Status

Fachkrankenhaus Coswig

Coswig, Saxony, Germany

Site Status

Universitätsklinikum Leipzig

Leipzig, Saxony, Germany

Site Status

Helios Klinikum Emil von Behring, Lungenklinik Heckeshorn

Berlin, , Germany

Site Status

Soroka University Medical Center

Beersheba, Beersheba, Israel

Site Status

Chaim Sheba Medical Center

Tel Litwinsky, Tel Aviv, Israel

Site Status

Hadassah-Hebrew University Medical Center

Jerusalem, , Israel

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Meir Medical Center

Kfar Saba, , Israel

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Rabin Medical Center

Petach Tikvah, , Israel

Site Status

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

Ospedale "G.B.Morgagni - L. Pierantoni"

Forlì, Forli-cesena, Italy

Site Status

Azienda Ospedaliera San Gerardo di Monza

Monza, Monza E Brianza, Italy

Site Status

Policlinico Universitario di Catania

Catania, , Italy

Site Status

San Giuseppe Hospital, Dept. of Internal Medicine

Milan, , Italy

Site Status

Azienda Ospedaliero-Universitaria Policlinico di Modena

Modena, , Italy

Site Status

Università degli studi Federico II di Napoli

Napoli, , Italy

Site Status

Istituto Mediterraneo Trapianti e Terapia Alta Specializzazione (ISMETT)

Palermo, , Italy

Site Status

Fondazione PTV - Policlinico Tor Vergata

Roma, , Italy

Site Status

Azienda Ospedaliera Universitaria Senese Policlinico Le Scotte

Siena, , Italy

Site Status

10 Wojskowy Szpital Kliniczny z Poliklinika SP ZOZ w Bydgoszczy

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, Poland

Site Status

Instytut Gruzlicy i Chorób Pluc

Warsaw, Masovian Voivodeship, Poland

Site Status

Uniwersyteckie Centrum Kliniczne

Gdansk, Pomeranian Voivodeship, Poland

Site Status

Samodzielny Publiczny Szpital Kliniczny nr 3 w Zabrzu Slaskiego Uniwersytetu Medycznego w Katowicach

Zabrze, Silesian Voivodeship, Poland

Site Status

Samodzielny Publiczny ZOZ, Uniwersytecki Szpital Kliniczny nr 1 im. Norberta Barlickiego

Lódz, Łódź Voivodeship, Poland

Site Status

Soon Chun Hyang University Hospital Bucheon

Bucheon-si, Gyeonggi-do, South Korea

Site Status

Gachon University Gil Medical Center

Incheon, Gyeonggi-do, South Korea

Site Status

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, South Korea

Site Status

Samsung Medical Center

Seoul, Gyeonggi-do, South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Korea University Anam Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Hospital Quirón Madrid

Pozuelo de Alarcón, Madrid, Spain

Site Status

Hospital Universitario Central de Asturias

Oviedo, Principality of Asturias, Spain

Site Status

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status

Hospital Universitario Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario La Princesa

Madrid, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Kantonsspital St. Gallen

Sankt Gallen, Canton of St. Gallen, Switzerland

Site Status

Centre Hospitalier Universitaire Vaudois Lausanne (CHUV)

Lausanne, Canton of Vaud, Switzerland

Site Status

Universitätsspital Basel

Basel, , Switzerland

Site Status

Birmingham Heartlands Hospital

Birmingham, England, United Kingdom

Site Status

Southmead Hospital

Bristol, England, United Kingdom

Site Status

Papworth Hospital

Cambridge, England, United Kingdom

Site Status

Castle Hill Hospital

Cottingham, England, United Kingdom

Site Status

Royal Devon and Exeter Hospital

Exeter, England, United Kingdom

Site Status

Saint James's University Hospital

Leeds, England, United Kingdom

Site Status

Glenfield Hospital

Leicester, England, United Kingdom

Site Status

Aintree University Hospitals NHS Foundation Trust

Liverpool, England, United Kingdom

Site Status

Royal Brompton Hospital

London, England, United Kingdom

Site Status

University Hospital of South Manchester NHS Foundation Trust

Manchester, England, United Kingdom

Site Status

Nottingham City Hospital

Nottingham, England, United Kingdom

Site Status

Churchill Hospital

Oxford, England, United Kingdom

Site Status

Northern General Hospital

Sheffield, England, United Kingdom

Site Status

Southampton General Hospital

Southampton, England, United Kingdom

Site Status

Royal Infirmary of Edinburgh

Edinburgh, Scotland, United Kingdom

Site Status

Glasgow Royal Infirmary

Glasgow, Scotland, United Kingdom

Site Status

Countries

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United States Australia Belgium Canada Czechia France Germany Israel Italy Poland South Korea Spain Switzerland United Kingdom

References

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Raghu G, Brown KK, Collard HR, Cottin V, Gibson KF, Kaner RJ, Lederer DJ, Martinez FJ, Noble PW, Song JW, Wells AU, Whelan TP, Wuyts W, Moreau E, Patterson SD, Smith V, Bayly S, Chien JW, Gong Q, Zhang JJ, O'Riordan TG. Efficacy of simtuzumab versus placebo in patients with idiopathic pulmonary fibrosis: a randomised, double-blind, controlled, phase 2 trial. Lancet Respir Med. 2017 Jan;5(1):22-32. doi: 10.1016/S2213-2600(16)30421-0. Epub 2016 Dec 7.

Reference Type BACKGROUND
PMID: 27939076 (View on PubMed)

Humphries SM, O'Riordan TG, Zhang JJ, Bayly S, Sood R, Hayden A, Lynch DA; Relationship Baseline Fibrosis Score to Lung Function in A Clinical Trial Population with Idiopathic Pulmonary Fibrosis. ATS International Conference, 2016 May 13-18, San Francisco CA.

Reference Type RESULT

Raghu G, Brown K, Collard H, Lederer D, Martinez F, Noble P, Song JW, Wells A, Whelan T, Moreau E, Patterson S, Bayly S, Chien J, Zhang J, O'Riordan T; Simtuzumab in Idiopathic Pulmonary Fibrosis: Results of a Randomized Clinical Trial. ERS Congress, 2016 September 3-7, London, UK.

Reference Type RESULT

Raghu G, Brown KK, Collard HR, Lederer DJ, Martinez FJ, Noble PW, Song JW, Wells AU, Whalen TP, Lambert L, Chien JW, Zhang JJ, O'Riordan TG; Simtuzumab in Idiopathic Pulmonary Fibrosis (IPF): Baseline Demographic and Lung Function Data from a Clinical Trial. ATS International Conference, 2016 May 13-18, San Francisco CA.

Reference Type RESULT

Other Identifiers

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2012-001571-36

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GS-US-322-0207

Identifier Type: -

Identifier Source: org_study_id

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