Garadacimab Safety, Pharmacokinetics, and Pharmacodynamics in Idiopathic Pulmonary Fibrosis

NCT ID: NCT05130970

Last Updated: 2024-12-13

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

81 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-02-03

Study Completion Date

2024-01-02

Brief Summary

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This is a prospective, phase 2a, multicenter, randomized, double-blind, placebo-controlled, parallel-group study to assess the safety, pharmacokinetics (PK), and pharmacodynamics (PD) of garadacimab in subjects with idiopathic pulmonary fibrosis (IPF).

Detailed Description

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Conditions

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Idiopathic Pulmonary Fibrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Garadacimab

Administered IV and SC

Group Type EXPERIMENTAL

Garadacimab

Intervention Type DRUG

Participants received garadacimab intravenous (IV) loading dose followed by 3 subcutaneous (SC) doses.

Placebo

Administered IV and SC

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Participants received a matching placebo IV loading dose, followed by 3 SC doses.

Interventions

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Garadacimab

Participants received garadacimab intravenous (IV) loading dose followed by 3 subcutaneous (SC) doses.

Intervention Type DRUG

Placebo

Participants received a matching placebo IV loading dose, followed by 3 SC doses.

Intervention Type DRUG

Other Intervention Names

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Factor XIIa antagonist monoclonal antibody CSL312

Eligibility Criteria

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Inclusion Criteria

* Male or female patients ≥ 40 years of age
* Documented diagnosis of IPF

Exclusion Criteria

* History of clinically significant cardiovascular disease, including myocardial infarction, unstable ischemic heart disease, congestive heart failure, or angina during the 6 months before screening
* Sinoatrial or atrioventricular block, uncontrolled hypertension
* Active bleeding or current clinically significant coagulopathy
Minimum Eligible Age

40 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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CSL Behring

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

CSL Behring

Locations

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The University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Pulmonary Associates Clinical Trials AZ

Phoenix, Arizona, United States

Site Status

National Institute of Clinical Research

Huntington Beach, California, United States

Site Status

University of Southern California - Center for Advanced Lung Disease

Los Angeles, California, United States

Site Status

University of California Irvine

Orange, California, United States

Site Status

Meris Clinical Research

Brandon, Florida, United States

Site Status

Reliant Medical Research

Miami, Florida, United States

Site Status

US Associates in Research LLC

Miami, Florida, United States

Site Status

Lakes Research

Miami Lakes, Florida, United States

Site Status

Renstar Medical Research

Ocala, Florida, United States

Site Status

Central Florida Pulmonary Group, PA

Orlando, Florida, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Jadestone Clinical Research

Silver Spring, Maryland, United States

Site Status

Hannibal Clinic

Hannibal, Missouri, United States

Site Status

Weill Cornell Medical Center

New York, New York, United States

Site Status

Superior Clinical Research

Smithfield, North Carolina, United States

Site Status

Southeastern Research Center

Winston-Salem, North Carolina, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, United States

Site Status

Temple University TMS

Philadelphia, Pennsylvania, United States

Site Status

Clinical Trial Center of Middle Tennesse

Franklin, Tennessee, United States

Site Status

Elite Medical Research

Dallas, Texas, United States

Site Status

Southwest Family Medicine Associates

Dallas, Texas, United States

Site Status

Baylor Scott and White Health - Advanced Lung Disease Specialists

Dallas, Texas, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

Royal Adelaide Hospital

Adelaide, , Australia

Site Status

Medizinische Univerität Graz

Graz, , Austria

Site Status

Kepler Universitätsklinikum

Linz, , Austria

Site Status

Universitair Ziekenhuis (UZ) Leuven

Leuven, , Belgium

Site Status

Centre Hospitalier Universitaire Sart Tilman

Liège, , Belgium

Site Status

St. Joseph's Healthcare Hamilton

Hamilton, Ontario, Canada

Site Status

Dr. Syed Anees Medicine Professional Corporation

Windsor, Ontario, Canada

Site Status

Odense Universitetshospital - Lungemedicinsk Forskningsenhed

Odense, , Denmark

Site Status

Fachkrankenhaus Coswig GmbH

Coswig, , Germany

Site Status

Universitaetsklinikum Essen - Ruhrlandklinik (Westdeutsches Lungenzentrum)

Essen, , Germany

Site Status

Medizinische Hochschule Hannover - Klinik für Pneumologie

Hanover, , Germany

Site Status

Petrus Krankenhaus Wuppertal

Wuppertal, , Germany

Site Status

Azienda Ospedaliera Universitaria Ospedali Riuniti Foggia

Foggia, , Italy

Site Status

Centrum Medycyny Oddechowej Bialymstoku

Bialystok, , Poland

Site Status

Twoja Przychodnia Centrum Medyczne Nowa Sol

Nowa Sól, , Poland

Site Status

Centrum Badań Klinicznych NZOZ

Wroclaw, , Poland

Site Status

Giromed Institute, SLP

Barcelona, , Spain

Site Status

Hospital Universitario Puerta del Mar (HUPM)

Cadiz, , Spain

Site Status

The Churchill Hospital - Oxford University Hospitals NHS Trust

Oxford, MD, United Kingdom

Site Status

Queen Elizabeth Hospital

Birmingham, , United Kingdom

Site Status

Altnagelvin Area Hospital

Londonderry, , United Kingdom

Site Status

Manchester Univ NHS - Wythenshawe Hospital

Manchester, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Canada Denmark Germany Italy Poland Spain United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2021 003162 12

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CSL312_2002

Identifier Type: -

Identifier Source: org_study_id