A Study to Test the Efficacy and Safety of Inhaled GB0139 in Subjects With Idiopathic Pulmonary Fibrosis (IPF)

NCT ID: NCT03832946

Last Updated: 2024-05-22

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

172 participants

Study Classification

INTERVENTIONAL

Study Start Date

2019-02-19

Study Completion Date

2023-05-17

Brief Summary

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This is a randomized, double-blind, placebo-controlled phase 2b trial in subjects with IPF (idiopathic pulmonary fibrosis) investigating the efficacy and safety of GB0139.

Detailed Description

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This study is designed to evaluate the efficacy and safety of GB0139, a galectin-3 inhibitor, administered by dry powder inhalation over 52 weeks. GB0139, given once per day, will be compared to placebo. GB0139 was previously known as TD139.

Conditions

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Idiopathic Pulmonary Fibrosis (IPF)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

All subjects eligible for the study will be randomised into one of the two treatment arms:

A. GB0139 3 mg once a day B. Placebo once a day
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
This study is a double-blind study. The blinding will be maintained throughout the study.

Study Groups

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A. GB0139 3 mg once a day

Inhalation of GB0139

Group Type EXPERIMENTAL

GB0139

Intervention Type DRUG

GB0139 is a galectin-3 inhibitor designed to modulate the fibrogenic response to tissue injury. It is administered as inhalation once a day.

B. Placebo once a day

Inhalation of Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo is administered as inhalation once a day

Interventions

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GB0139

GB0139 is a galectin-3 inhibitor designed to modulate the fibrogenic response to tissue injury. It is administered as inhalation once a day.

Intervention Type DRUG

Placebo

Placebo is administered as inhalation once a day

Intervention Type DRUG

Other Intervention Names

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TD139

Eligibility Criteria

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Inclusion Criteria

1. Male and female subjects aged ≥ 40 years of age with a diagnosis of IPF established during the previous five years according to ATS/ERS/Fleischner criteria.
2. Lung function parameters as follows:

1. Forced Vital Capacity (FVC) \> 45% of the predicted value at screening
2. Diffusion lung capacity for carbon monoxide (DLCO) (corrected for Hb) of 30% to 79% of the predicted value at screening
3. Subjects who currently are not being treated with nintedanib or pirfenidone; or cannot tolerate nintedanib or pirfenidone
4. Subjects must sign and date a written, IRB/EC approved informed consent form and any required authorization prior to initiation of any study procedures.

Exclusion Criteria

1. Currently has significant airways obstruction: Forced Expiratory Volume in 1 s (FEV1)/Forced Vital Capacity (FVC) ratio of \< 0.7 at screening.
2. Has clinical evidence of active infection, including, but not limited to, bronchitis, pneumonia, sinusitis, urinary tract infection, and cellulitis.
3. Has a history of malignancy within the last 2 years with the exception of basal cell carcinoma, chronic lymphocytic leukaemia (under observation) and prostate cancer requiring anti-androgens, localised treatment (minor surgery, radiotherapy) and/or managed by observation.
4. Has any condition other than IPF that, in the opinion of the investigator, is likely to result in the death of the subject within the next 2 years.
5. Presence of other disease that may interfere with testing procedures or in the judgement of the Investigator may interfere with trial participation or may put the patient at risk when participating in this trial.
6. Is likely to receive lung transplantation within the next 12 months.
7. Currently receiving nintedanib, pirfenidone, high dose corticosteroid, cytotoxic (e.g., chlorambucil, azathioprine, cyclophosphamide, methotrexate), vasodilator therapy for pulmonary hypertension (e.g., bosentan). A current dose of less than or equal to 15 mg/day of prednisone or its equivalent is acceptable if the dose is anticipated to remain stable during the study.
8. Prior use of GB0139 (also called TD139) or previously randomized in GALACTIC-1.
9. Prior use of nintedanib or pirfenidone within 7 days of initiation of screening.
10. Prior use of investigational drugs within 30 days (or 5 half-lives, whichever is longer) of initiation of screening.
11. Participating in another clinical trial, either interventional or observational.
12. Has a history of unstable or deteriorating cardiac or pulmonary disease (other than IPF) within the previous six months, including, but not limited to, the following:

1. Unstable angina pectoris or myocardial infarction, or percutaneous coronary intervention within the last 6 months
2. Congestive heart failure requiring hospitalization
3. Uncontrolled clinically significant arrhythmias
13. If female, the subject is pregnant or lactating or intending to become pregnant before participating in this study during the study and within (5 half- lives plus 30 days) after last dose of the study drug; or intending to donate ova during such time period.
14. Woman considered to be of childbearing potential who do not use highly effective birth control methods during the study.
15. Hypersensitivity to the active substance (TD139/GB0139) or the excipient (lactose).
Minimum Eligible Age

40 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Syneos Health

OTHER

Sponsor Role collaborator

bioRASI, LLC

INDUSTRY

Sponsor Role collaborator

Galecto Biotech AB

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Toby Maher, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Keck Medicine of USC

Locations

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SEC Clinical Research

Andalusia, Alabama, United States

Site Status

Jasper Summit Research, LLC Pulmonary & Sleep Associates

Jasper, Alabama, United States

Site Status

Palmtree Clinical Research Inc

Palm Springs, California, United States

Site Status

Paradigm Research

Redding, California, United States

Site Status

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status

Health Shands Hospital

Gainesville, Florida, United States

Site Status

Harmony Medical Research Institute, Inc

Hialeah, Florida, United States

Site Status

Advanced Research for Health Improvement

Naples, Florida, United States

Site Status

Broward Research Centre

Pembroke Pines, Florida, United States

Site Status

Avanza Medical Research Centre

Pensacola, Florida, United States

Site Status

Coastal Pulmonary Critical Care PLC

St. Petersburg, Florida, United States

Site Status

Tampa General Hospital/Uni Florida

Tampa, Florida, United States

Site Status

Piedmont Healthcare Pulmonary and Critical Care Research

Atlanta, Georgia, United States

Site Status

The Emory Clinic

Atlanta, Georgia, United States

Site Status

DC Research Works

Marietta, Georgia, United States

Site Status

Northwestern Memorial Hospital

Chicago, Illinois, United States

Site Status

LaPorte County Institute for Clinical Research

Michigan City, Indiana, United States

Site Status

University of Kansas Medical Centre

Kansas City, Kansas, United States

Site Status

University of Louisville Hospital

Louisville, Kentucky, United States

Site Status

University of Maryland

Baltimore, Maryland, United States

Site Status

Harvard Medical School - Brigham and Womens Hospital (BWH)

Boston, Massachusetts, United States

Site Status

The Lung Research Center LLC

Chesterfield, Missouri, United States

Site Status

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

Pulmonlx LLC

Greensboro, North Carolina, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

The Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

University of Texas Health Centre at Houston

Houston, Texas, United States

Site Status

University of Texas Health Sciences Center at Houston

Houston, Texas, United States

Site Status

Diagnostics Research Group

San Antonio, Texas, United States

Site Status

University of Utah Health Scieces Center

Salt Lake City, Utah, United States

Site Status

TPMG Clinical Research

Williamsburg, Virginia, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Lung Research QLD

Chermside, Queensland, Australia

Site Status

Flinders Medical Centre

Adelaide, South Australia, Australia

Site Status

Respiratory Clinical Trials

Kent Town, South Australia, Australia

Site Status

Institute for Respiratory Health Sir Charles Gairdner Hospital

Nedlands, Western Australia, Australia

Site Status

TrialsWest

Spearwood, Western Australia, Australia

Site Status

Cliniques Universitaires St-Luc

Louvain-la-Neuve, Wallon Region, Belgium

Site Status

UZ Antwerp

Antwerp, , Belgium

Site Status

CUB Hopital Erasme

Brussels, , Belgium

Site Status

UZ Leuven- Campus Gasthuisberg

Brussels, , Belgium

Site Status

CHU UCL Namur site Godinne

Namur, , Belgium

Site Status

Firestone Institute for Respiratory Health

Hamilton, Ontario, Canada

Site Status

Dr Anees Medicine Professional Corporation

Windsor, Ontario, Canada

Site Status

Dr Dhar Medical Practice

Windsor, Ontario, Canada

Site Status

Toronto General Hosp Research Inst

Toronto, , Canada

Site Status

Groupe Hospitalier Hopitaux Universitaires Paris-Seine-Saint-Denis-Hopital Avicenne

Bobigny, , France

Site Status

CHRU Lille - Hopital Calmette

Lille, , France

Site Status

Hopital Nord de Marseille

Marseille, , France

Site Status

APHP - Hopital Europen Georges-Pompidou

Paris, , France

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Hopital Bichat

Paris, , France

Site Status

Centre Hospitalier Universitaire de Rennes Hopital Pontchaillou

Rennes, , France

Site Status

CHU de la Réunion Site SUD (Terre Sainte)

Saint-Pierre, , France

Site Status

CHU de la Réunion- Site Félix Guyon

Saint-Pierre, , France

Site Status

Hopitaux Universitaires de Strasborg Service de Pneumologie Nouvel Hopital Civil

Strasbourg, , France

Site Status

Centre Hospitalier Rgional et Universitaire - Hopital Bretonneau

Tours, , France

Site Status

Chapidze Emergency Cardiology Center

Tbilisi, , Georgia

Site Status

The First Medical Center

Tbilisi, , Georgia

Site Status

Thoraxklinik-Heidelberg gGmbH

Heidelberg, Baden-Wurttemberg, Germany

Site Status

Lungenfachklinik Immenhausen Department for Clinical Studies

Immenhausen, Hesse, Germany

Site Status

ZMS Zentrum für medizinische Studien GmbH

Warendorf, Rhine-Westphalia, Germany

Site Status

Klifeck GmbH Praxis Med. Gerald Eckhardt

Delitzsch, Saxony, Germany

Site Status

Studienzentrum Dr.med Falk Brunner FA fuer Innere Medizin und Pneumologie

Leipzig, Saxony, Germany

Site Status

CIMS Studienzentrum Bamberg GmbH

Bamberg, , Germany

Site Status

Krankenhaus Donaustauf

Donaustauf, , Germany

Site Status

Ruhrlandklinik Essen

Essen, , Germany

Site Status

Universitaetsklinikum Leipzig Klinik und Poliklinik für Onkologie, Gastroenterologie, Hepatologie, P

Leipzig, , Germany

Site Status

POIS Leipzig GbR

Leipzig, , Germany

Site Status

Klinikum Grossadern der Ludwig-Maximilians-Universitaet Muenchen

Munich, , Germany

Site Status

Trinity Centre for Health Sciences

Dublin, , Ireland

Site Status

Hadassah Medical Center

Jerusalem, , Israel

Site Status

Meir Medical Center

Kefar Sava, , Israel

Site Status

Pulmonary Institute Rabin Medical Center

Petah Tikva, , Israel

Site Status

Sheba Medical Center

Ramat Gan, , Israel

Site Status

Kaplan Medical Center

Rehovot, , Israel

Site Status

University-Hospital Policlinico Vittorio Emanuele

Catania, , Italy

Site Status

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, , Italy

Site Status

Ospedale San Giuseppe Clinica Malattie dell Apparato Respiratorio

Milan, , Italy

Site Status

University Hospital of Mondena-AOU - Policlinico di Modena

Modena, , Italy

Site Status

A.O. Dei Colli OSPEDALE MONALDI

Napoli, , Italy

Site Status

Ospedale GB Morgagni

Padua, , Italy

Site Status

Istituto Mediterraneo Trapianti e Terapia Alta Specializzazione (ISMETT)

Palermo, , Italy

Site Status

Azienda Ospedaliera Universitaria Senese

Siena, , Italy

Site Status

AOU Città della Salute e della Scienza, PO Molinette

Turin, , Italy

Site Status

Oddział Kliniczny Pulmonologii i Alergologii Szpitala Uniwersyteckiego w Krakowie

Krakow, Lesser Poland Voivodeship, Poland

Site Status

Instytut Gruzlicy i Chorob Pluc, I Klinika Chorob Pluc

Warsaw, Masovian Voivodeship, Poland

Site Status

Klinika Alergologii Pneumonologii

Gdansk, Pomeranian Voivodeship, Poland

Site Status

Szpital Kliniczny Przemienienia Pańskiego Uniwersytetu Medycznego im. Karola Marcinkowskiego w Poznaniu

Poznan, , Poland

Site Status

Uniwersytecki Szpital Kliniczny Nr 1 im. Norberta Barlickiego Uniwersytetu Medycznego w Lodzi

Lodz, Łódź Voivodeship, Poland

Site Status

Regional Clinical Hospital No. 3

Chelyabinsk, , Russia

Site Status

Kazan SMU, Republican Clinical Hospital of MOH, Republic of Tatarstan

Kazan', , Russia

Site Status

OLLA-MED

Moscow, , Russia

Site Status

Pulmonology Scientific Research Institute

Moscow, , Russia

Site Status

Evdokimov Moscow State University of Medicine and Dentistry

Moscow, , Russia

Site Status

Pavlov First Saint Petersburg State Medical University

Saint Petersburg, , Russia

Site Status

Soloviev Clinical Emergency Hospital

Yaroslavl, , Russia

Site Status

LLC "Medical Association Novaya Bolnitsa"

Yekaterinburg, , Russia

Site Status

Hospital Univ. Marques de Valdecilla

Santander, Cantabria, Spain

Site Status

Hospital Universitario Lucas Augusti

Lugo, Galicia, Spain

Site Status

Hospital Universitario Quiron Madrid

Pozuelo de Alarcón, Madrid, Spain

Site Status

Hospital Universitario Central de Asturias

Oviedo, Principality of Asturias, Spain

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Policlinica Barcelona

Barcelona, , Spain

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Hospital Clinic de Barcelona

Barcelona, , Spain

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Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

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Hopital de Bellvitge

Barcelona, , Spain

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Hospital Vall d'Hebron

Barcelona, , Spain

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Hospital Clinico San Carlos

Madrid, , Spain

Site Status

Hospital General de Valencia

Valencia, , Spain

Site Status

Chernivtsi Regional Clinical Hospital

Chernivtsi, , Ukraine

Site Status

National Institute of Phthisiology and Pulmonology n.a. F.G.Yanovsky

Kyiv, , Ukraine

Site Status

National Research Centre for Radiation Medicine of The National Academy of Medical Sciences of UKR

Kyiv, , Ukraine

Site Status

Ternopil Municipal City Hosipital 2

Ternopil, , Ukraine

Site Status

Medical Centre Pulse

Vinnytsia, , Ukraine

Site Status

Papworth Hospital NHS Foundation Trust

Cambridge, Cambridgeshire, United Kingdom

Site Status

Royal Devon and Exeter Hospital

Exeter, Devon, United Kingdom

Site Status

Royal Brompton Hospital

London, Greater London, United Kingdom

Site Status

Wythenshawe Hospital

Manchester, Greater Manchester, United Kingdom

Site Status

University Hospital Southampton NHS Foundation Trust

Southampton, Hampshire, United Kingdom

Site Status

Glenfield Hospital

Leicester, Leicestershire, United Kingdom

Site Status

Aintree Unversity Hospital NHS Foundation Trust

Liverpool, Merseyside, United Kingdom

Site Status

Newcastle Royal Victoria Infirmary

Newcastle upon Tyne, Newcastle, United Kingdom

Site Status

Nottingham City Hospital

Nottingham, Nottinghamshire, United Kingdom

Site Status

Sheffield Teaching Hospitals NHS Foundation Trust - Royal Hallamshire Hospital (RHH)

Sheffield, South Yorkshire, United Kingdom

Site Status

Birmingham Heartlands Hospital

Birmingham, West Midlands, United Kingdom

Site Status

Clinical Research Centre - Respiratory North Bristol NHS Trust Southmead Hospital

Bristol, , United Kingdom

Site Status

Royal Infirmary of Edinburgh

Edinburgh, , United Kingdom

Site Status

Countries

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United States Australia Belgium Canada France Georgia Germany Ireland Israel Italy Poland Russia Spain Ukraine United Kingdom

References

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Rebelo AL, Chevalier MT, Russo L, Pandit A. Role and therapeutic implications of protein glycosylation in neuroinflammation. Trends Mol Med. 2022 Apr;28(4):270-289. doi: 10.1016/j.molmed.2022.01.004. Epub 2022 Feb 1.

Reference Type DERIVED
PMID: 35120836 (View on PubMed)

Park AM, Khadka S, Sato F, Omura S, Fujita M, Hsu DK, Liu FT, Tsunoda I. Galectin-3 as a Therapeutic Target for NSAID-Induced Intestinal Ulcers. Front Immunol. 2020 Sep 23;11:550366. doi: 10.3389/fimmu.2020.550366. eCollection 2020.

Reference Type DERIVED
PMID: 33072090 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2018-002664-73

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GALACTIC-1

Identifier Type: -

Identifier Source: org_study_id

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