A Phase III Study to Investigate the Impact of Diamyd in Patients Newly Diagnosed With Type 1 Diabetes (USA)- DIAPREVENT

NCT ID: NCT00751842

Last Updated: 2012-10-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

331 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-09-30

Study Completion Date

2012-07-31

Brief Summary

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The intended purpose of this study was to determine whether Diamyd (rhGAD65 formulated in alum) is effective in preserving the body's own insulin producing capacity in patients recently diagnosed with type 1 diabetes.

Based on results from other clinical trials with the study drug it was judged unlikely this study would meet the intended primary or secondary efficacy endpoints. Therefore the primary focus of this study was changed to ensure that safety data was available for at least 6 months following the last dose of active study drug. Thereafter the study was terminated.

Detailed Description

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Conditions

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Type 1 Diabetes Mellitus

Keywords

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Diabetes Juvenile Diabetes Diabetes type 1 Autoimmune Diabetes Insulin dependent Diabetes Type 1 diabetes Type 1 diabetes mellitus Diamyd rhGAD65 GAD GAD-alum

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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A

This arm will receive 2 subcutaneous injections with 20 µg Diamyd on days 1 and 30, i.e., 1 prime and 1 booster dose, followed by 2 additional single doses with Diamyd 20 µg on days 90 and 270.

Group Type ACTIVE_COMPARATOR

rhGAD65

Intervention Type DRUG

Diamyd (rhGAD65) 20 µg injected subcutaneously at days 1, 30, 90 and 270.

B

This arm will receive 2 subcutaneous injections with 20 µg Diamyd on days 1 and 30, i.e., 1 prime and 1 booster dose, followed by 2 additional single doses with placebo on days 90 and 270.

Group Type ACTIVE_COMPARATOR

rhGAD65

Intervention Type DRUG

Diamyd (rhGAD65) 20 µg injected subcutaneously at days 1 and 30, followed by placebo injections at days 90 and 270.

C

This arm will receive 4 injections of placebo, 1 each on days 1, 30, 90 and 270.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo injected subcutaneously at days 1, 30, 90 and 270.

Interventions

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rhGAD65

Diamyd (rhGAD65) 20 µg injected subcutaneously at days 1, 30, 90 and 270.

Intervention Type DRUG

rhGAD65

Diamyd (rhGAD65) 20 µg injected subcutaneously at days 1 and 30, followed by placebo injections at days 90 and 270.

Intervention Type DRUG

Placebo

Placebo injected subcutaneously at days 1, 30, 90 and 270.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Insulin dependent type 1 diabetes mellitus diagnosed within the previous 3 months at time of screening
* Fasting C-peptide level at time of screening above 0.1 nmol/L
* Elevated GAD65 antibodies (GADA) at time of screening
* Male and female patients between 10 and 20 years of age

Exclusion Criteria

* Treatment with immunosuppressants or any anti-diabetic medications other than insulin
* A history of certain diseases or conditions (e.g. anemia, HIV, hepatitis, epilepsy, head trauma, neurological diseases or cerebrovascular accident, alcohol or drug abuse etc)
* Treatment with any vaccine within 1 month prior to planned first Diamyd dose or planned treatment with vaccine up to 2 months after the last injection with Diamyd, excluding the influenza vaccine
* Participation in other clinical trials with a new chemical entity within the previous 3 months
* Pregnancy or planned pregnancy within 1 year after the last Diamyd dose
* Presence of associated serious disease or condition which in the opinion of the investigator makes the patient non-eligible for the study
Minimum Eligible Age

10 Years

Maximum Eligible Age

20 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Diamyd Therapeutics AB

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Jerry Palmer, Professor

Role: PRINCIPAL_INVESTIGATOR

University of Washington

Locations

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University of Arizona

Tucson, Arizona, United States

Site Status

Arkansas Children's Hospital Research Institute

Little Rock, Arkansas, United States

Site Status

Alex Endocrine Associates

Rogers, Arkansas, United States

Site Status

Children's Hospital Orange County

Orange, California, United States

Site Status

Rady Children's Hospital

San Diego, California, United States

Site Status

Stanford University Medical Center

Stanford, California, United States

Site Status

Barbara Davis Center for Childhood Diabetes

Aurora, Colorado, United States

Site Status

Christina Care Research institute

Newark, Delaware, United States

Site Status

University of Florida

Gainsville, Florida, United States

Site Status

Nemours Children's Clinic

Jacksonville, Florida, United States

Site Status

Miami Children's Hospital Research Institute

Miami, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Atlanta Diabetes Associates

Atlanta, Georgia, United States

Site Status

Rocky Mountain Diabetes and Osteoporosis Center

Idaho Falls, Idaho, United States

Site Status

University of Iowa Hospitals and Clinicals

Iowa City, Iowa, United States

Site Status

Mid America Diabetes Associates

Wichita, Kansas, United States

Site Status

University of Kentucky College of Medicine

Lexington, Kentucky, United States

Site Status

University of Louisville Research Foundation

Louisville, Kentucky, United States

Site Status

Children's Hospital

New Orleans, Louisiana, United States

Site Status

University of Maryland Medical Center

Baltimore, Maryland, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

UMass Memorial Medical Center

Worcester, Massachusetts, United States

Site Status

University of Michigan Health System

Ann Arbor, Michigan, United States

Site Status

Alzohaili Medical Consultants

Dearborn, Michigan, United States

Site Status

The Children's Mercy Hospital

Kansas City, Missouri, United States

Site Status

St. Louis Children's Hospital

St Louis, Missouri, United States

Site Status

Creighton Diabetes Center

Omaha, Nebraska, United States

Site Status

Kathryn Eckert

Reno, Nevada, United States

Site Status

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Morristown Memorial Hospital

Morristown, New Jersey, United States

Site Status

Winthrop University Hospital

Mineola, New York, United States

Site Status

Naomi Berrie Diabetes Center of Columbia University

New York, New York, United States

Site Status

University of Rochester

Rochester, New York, United States

Site Status

SUNY Institute for Human Performance

Syracuse, New York, United States

Site Status

Children's Hospital Medical Center of Akron

Akron, Ohio, United States

Site Status

University of Oklahoma, Schustermann Center Clinic

Tulsa, Oklahoma, United States

Site Status

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, United States

Site Status

Regional Medical Clinic - Endocrinology

Rapid City, South Dakota, United States

Site Status

LeBonheur Children's Medical Center

Memphis, Tennessee, United States

Site Status

Cook Children's Medical Center

Fort Worth, Texas, United States

Site Status

CHRISTUS Santa Rosa Children's Hospital

San Antonio, Texas, United States

Site Status

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status

Benaroya Research Institute

Seattle, Washington, United States

Site Status

Countries

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United States

References

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Ludvigsson J, Faresjo M, Hjorth M, Axelsson S, Cheramy M, Pihl M, Vaarala O, Forsander G, Ivarsson S, Johansson C, Lindh A, Nilsson NO, Aman J, Ortqvist E, Zerhouni P, Casas R. GAD treatment and insulin secretion in recent-onset type 1 diabetes. N Engl J Med. 2008 Oct 30;359(18):1909-20. doi: 10.1056/NEJMoa0804328. Epub 2008 Oct 8.

Reference Type BACKGROUND
PMID: 18843118 (View on PubMed)

Ludvigsson J, Krisky D, Casas R, Battelino T, Castano L, Greening J, Kordonouri O, Otonkoski T, Pozzilli P, Robert JJ, Veeze HJ, Palmer J, Samuelsson U, Elding Larsson H, Aman J, Kardell G, Neiderud Helsingborg J, Lundstrom G, Albinsson E, Carlsson A, Nordvall M, Fors H, Arvidsson CG, Edvardson S, Hanas R, Larsson K, Rathsman B, Forsgren H, Desaix H, Forsander G, Nilsson NO, Akesson CG, Keskinen P, Veijola R, Talvitie T, Raile K, Kapellen T, Burger W, Neu A, Engelsberger I, Heidtmann B, Bechtold S, Leslie D, Chiarelli F, Cicognani A, Chiumello G, Cerutti F, Zuccotti GV, Gomez Gila A, Rica I, Barrio R, Clemente M, Lopez Garcia MJ, Rodriguez M, Gonzalez I, Lopez JP, Oyarzabal M, Reeser HM, Nuboer R, Stouthart P, Bratina N, Bratanic N, de Kerdanet M, Weill J, Ser N, Barat P, Bertrand AM, Carel JC, Reynaud R, Coutant R, Baron S. GAD65 antigen therapy in recently diagnosed type 1 diabetes mellitus. N Engl J Med. 2012 Feb 2;366(5):433-42. doi: 10.1056/NEJMoa1107096.

Reference Type BACKGROUND
PMID: 22296077 (View on PubMed)

Wherrett DK, Bundy B, Becker DJ, DiMeglio LA, Gitelman SE, Goland R, Gottlieb PA, Greenbaum CJ, Herold KC, Marks JB, Monzavi R, Moran A, Orban T, Palmer JP, Raskin P, Rodriguez H, Schatz D, Wilson DM, Krischer JP, Skyler JS; Type 1 Diabetes TrialNet GAD Study Group. Antigen-based therapy with glutamic acid decarboxylase (GAD) vaccine in patients with recent-onset type 1 diabetes: a randomised double-blind trial. Lancet. 2011 Jul 23;378(9788):319-27. doi: 10.1016/S0140-6736(11)60895-7. Epub 2011 Jun 27.

Reference Type BACKGROUND
PMID: 21714999 (View on PubMed)

Other Identifiers

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D/P3/07/5

Identifier Type: -

Identifier Source: org_study_id