A Phase III Study to Investigate the Impact of Diamyd in Patients Newly Diagnosed With Type 1 Diabetes (EU)

NCT ID: NCT00723411

Last Updated: 2011-10-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

334 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-07-31

Study Completion Date

2011-08-31

Brief Summary

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The purpose of this study is to determine whether Diamyd (rhGAD65 formulated in alum) is effective in preserving the body's own insulin producing capacity in patients recently diagnosed with type 1 diabetes.

Detailed Description

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Conditions

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Type 1 Diabetes Mellitus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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A

This arm will receive 2 subcutaneous injections with 20 µg Diamyd on Days 1 and 30, i.e., 1 prime and 1 booster dose, followed by 2 additional single doses with Diamyd 20 µg on Days 90 and 270.

Group Type ACTIVE_COMPARATOR

rhGAD65

Intervention Type DRUG

Diamyd (rhGAD65) 20 µg injected subcutaneously at days 1, 30, 90 and 270.

B

This arm will receive 2 subcutaneous injections with 20 µg Diamyd on Days 1 and 30, i.e., 1 prime and 1 booster dose, followed by 2 additional single doses with placebo on Days 90 and 270.

Group Type ACTIVE_COMPARATOR

rhGAD65

Intervention Type DRUG

Diamyd (rhGAD65) 20 µg injected subcutaneously at days 1 and 30, followed by placebo injections at days 90 and 270.

C

This arm will receive 4 injections of placebo, 1 each on Days 1, 30, 90, and 270.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo injected subcutaneously at days 1, 30, 90 and 270

Interventions

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rhGAD65

Diamyd (rhGAD65) 20 µg injected subcutaneously at days 1, 30, 90 and 270.

Intervention Type DRUG

rhGAD65

Diamyd (rhGAD65) 20 µg injected subcutaneously at days 1 and 30, followed by placebo injections at days 90 and 270.

Intervention Type DRUG

Placebo

Placebo injected subcutaneously at days 1, 30, 90 and 270

Intervention Type DRUG

Other Intervention Names

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Diamyd GAD65 GAD-Alum GAD Diamyd GAD GAD65 GAD-Alum

Eligibility Criteria

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Inclusion Criteria

* Male and female patients between 10 and 20 years of age
* Insulin dependent type 1 diabetes mellitus diagnosed within the previous 3 months at time of screening
* Fasting C-peptide level at time of screening above 0.1 nmol/L
* Elevated GAD65 antibodies (GADA) at time of screening

Exclusion Criteria

* Treatment with immunosuppressants or any anti-diabetic medications other than insulin
* A history of certain diseases or conditions (e.g. anemia, HIV, hepatitis, epilepsy, head trauma, neurological diseases or cerebrovascular accident, alcohol or drug abuse etc)
* Treatment with any vaccine within 1 month prior to planned first Diamyd dose or planned treatment with vaccine up to 2 months after the last injection with Diamyd, excluding the influenza vaccine
* Participation in other clinical trials with a new chemical entity within the previous 3 months
* Pregnancy or planned pregnancy within 1 year after the last Diamyd dose
* Presence of associated serious disease or condition which in the opinion of the investigator makes the patient non-eligible for the study
Minimum Eligible Age

10 Years

Maximum Eligible Age

20 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Diamyd Therapeutics AB

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Johnny Ludvigsson, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Linkoeping University

Locations

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Helsingin yliopistollinen keskussairaala, Lasten ja nuorten sairaala

Helsinki, , Finland

Site Status

Kuopion yliopistollinen sairaala, Lasten klinikka

Kuopio, , Finland

Site Status

Oulun yliopistollinen sairaala, Lasten ja nuorten klinikka

Oulu, , Finland

Site Status

Seinäjoen keskussairaala, Lastentautien poliklinikka

Seinäjoki, , Finland

Site Status

Tampereen yliopistollinen sairaala, Lasten klinikka

Tampere, , Finland

Site Status

Turun yliopistollinen keskussairaala, Lastentautien Klinikka

Turku, , Finland

Site Status

Medecine B

Angers, , France

Site Status

Centre Hospitalier Universitaire de Besançon

Besançon, , France

Site Status

Hôpital Pellegrin Enfants, Service d'endocrinologie pédiatrique

Bordeaux, , France

Site Status

Hôpital Jeanne de Flandre Sce Pédiatrie

Lille, , France

Site Status

CHU Timone Enfants, Service de pédiatrie multidisciplinaire

Marseille, , France

Site Status

CHU Montpellier Hôpital Arnaud de Villeneuve, Service de Pédiatrie 1

Montpellier, , France

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C.H.U.Serv.Pediatrie

Nantes, , France

Site Status

Hopital Robert Debré, Service d'Endocrinologie

Paris, , France

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Hôpital Necker, Clinique Robert Debré, Diabète de l'Enfant et de l'Adolescent,

Paris, , France

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CHU Rennes

Rennes, , France

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Hôpital des Enfants, Gastroentero-nutrition-diabétologie pédiatrique

Toulouse, , France

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Charité Campus Virchow Childrens Hospital

Berlin, , Germany

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DRK Kliniken Westend

Berlin, , Germany

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Hannover Kinderkrankenhaus auf der Bult

Hanover, , Germany

Site Status

Klinik und Poliklinik fȕr Kinder und Jugendliche der Universität Leipzig

Leipzig, , Germany

Site Status

Klinik fȕr Kinder- und Jugendmedizin

Mȕnchen, , Germany

Site Status

KHK Wilhelmstift

Rahlstedt, , Germany

Site Status

Universitätsklinik fȕr Kinder- und Jugendmedizin, Tȕbingen

Tȕbingen, , Germany

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Unità Operativa di Pediatria, Policlinico

Bologna, , Italy

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Struttura Complessa di Diabetologia, Ospedale S. Michele

Cagliari, , Italy

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S.S. Annunziata, Clinica Pediatrica

Chieti, , Italy

Site Status

Clinica Pediatrica, Università di Genova

Genova, , Italy

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Reparto di Pediatria, Ospedale S. Raffaele

Milan, , Italy

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Diabetologia - Dipartimento Clinica Pediatrica, Ospedale Luigi Sacco

Milan, , Italy

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Azienda Ospedaliero, Universitaria di Parma, Pediatria

Parma, , Italy

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Campus Bio-Medico, Dipartimento di Diabetologia e Endocrinologia

Roma, , Italy

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Diabetologia - Dipartimento Scienze Pediatriche, Ospedale Infantile, Regina Margherita

Torino, , Italy

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Meander Medisch Centrum, Lokatie Elisabeth

Amersfoort, , Netherlands

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Diabeter

Rotterdam, , Netherlands

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Orbis Medisch Centrum

Sittard-Geleen, , Netherlands

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Haga Ziekenhuis, Lokatie Juliana Kinderziekenhuis

The Hague, , Netherlands

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University Medical Centre Ljubljana, Department of Pediatric Endocrinology

Ljubljana, , Slovenia

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Hospital Materno-Infantil Vall Hebrón

Barcelona, , Spain

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Hospital Materno-Infantil de Cruces

Cruces / Barakaldo, , Spain

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Hospital Materno-Infantil Ramón y Cajal

Madrid, , Spain

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Hospital Materno-Infantil La Paz

Madrid, , Spain

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Hospital Materno-Infantil Carlos Haya

Málaga, , Spain

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Hospital Materno-Infantil Vírgen del Camino

Pamplona, , Spain

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Hospital Materno-Infantil Vírgen del Rocío

Seville, , Spain

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Hospital Materno-Infantil Clínico de Valencia

Valencia, , Spain

Site Status

Hospital Materno-Infantil Miguel Servet

Zaragoza, , Spain

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Barn- och ungdomskliniken, Lasarettet

Borås, , Sweden

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Barn- och ungdomskliniken, Länssjukhuset

Gävle, , Sweden

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Drottning Silvias Barnsjukhus, Barn- och ungdomssjukvården

Gothenburg, , Sweden

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Barn- och ungdomskliniken, Länssjukhuset

Halmstad, , Sweden

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Barn- och ungdomsmedicin, Lasarettet

Helsingborg, , Sweden

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Barnkliniken, Hudiksvalls Sjukhus

Hudiksvall, , Sweden

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Barn- och ungdomskliniken, Länssjukhuset Ryhov

Jönköping, , Sweden

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Barn- och ungdomskliniken, Lasarettet

Kalmar, , Sweden

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Barn- och ungdomskliniken, Centralsjukhuset

Karlstad, , Sweden

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Barn och ungdomsmedicinska kliniken, Centralsjukhuset

Kristianstad, , Sweden

Site Status

Barn- och ungdomskliniken, Universitetssjukhuset

Linköping, , Sweden

Site Status

Barn- och ungdomskliniken, Universitetssjukhuset

Lund, , Sweden

Site Status

Barn- och ungdomscentrum, Universitetssjukhuset MAS

Malmo, , Sweden

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Barn- och ungdomskliniken, Vrinnevi sjukhus

Norrköping, , Sweden

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Barn- och ungdomskliniken, Universitetssjukhuset

Örebro, , Sweden

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Sachsska Barnsjukhuset, Södersjukhuset

Stockholm, , Sweden

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Barn- och ungdomskliniken, NU-sjukvården/NÄL

Trollhättan, , Sweden

Site Status

Barn- och ungdomskliniken, Uddevalla Sjukhus

Uddevalla, , Sweden

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Barn- och ungdomskliniken, Centrallasarettet

Vaxjo, , Sweden

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Barn- och ungdomskliniken, Centrallasarettet

Västerås, , Sweden

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Maternal & Child Health Sciences, University of Dundee

Dundee, , United Kingdom

Site Status

Children's Admin Centre

Leicester, , United Kingdom

Site Status

Centre for Diabetes and Metabolic Medicine (DMM), Barts and The London School of Medicine and Dentistry

London, , United Kingdom

Site Status

Countries

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Finland France Germany Italy Netherlands Slovenia Spain Sweden United Kingdom

References

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Tavira B, Cheramy M, Axelsson S, Akerman L, Ludvigsson J, Casas R. Effect of simultaneous vaccination with H1N1 and GAD-alum on GAD65-induced immune response. Diabetologia. 2017 Jul;60(7):1276-1283. doi: 10.1007/s00125-017-4263-x. Epub 2017 Mar 29.

Reference Type DERIVED
PMID: 28357504 (View on PubMed)

Ludvigsson J, Cheramy M, Axelsson S, Pihl M, Akerman L, Casas R; Clinical GAD-Study Group in Sweden. GAD-treatment of children and adolescents with recent-onset type 1 diabetes preserves residual insulin secretion after 30 months. Diabetes Metab Res Rev. 2014 Jul;30(5):405-14. doi: 10.1002/dmrr.2503.

Reference Type DERIVED
PMID: 24302596 (View on PubMed)

Ludvigsson J, Krisky D, Casas R, Battelino T, Castano L, Greening J, Kordonouri O, Otonkoski T, Pozzilli P, Robert JJ, Veeze HJ, Palmer J, Samuelsson U, Elding Larsson H, Aman J, Kardell G, Neiderud Helsingborg J, Lundstrom G, Albinsson E, Carlsson A, Nordvall M, Fors H, Arvidsson CG, Edvardson S, Hanas R, Larsson K, Rathsman B, Forsgren H, Desaix H, Forsander G, Nilsson NO, Akesson CG, Keskinen P, Veijola R, Talvitie T, Raile K, Kapellen T, Burger W, Neu A, Engelsberger I, Heidtmann B, Bechtold S, Leslie D, Chiarelli F, Cicognani A, Chiumello G, Cerutti F, Zuccotti GV, Gomez Gila A, Rica I, Barrio R, Clemente M, Lopez Garcia MJ, Rodriguez M, Gonzalez I, Lopez JP, Oyarzabal M, Reeser HM, Nuboer R, Stouthart P, Bratina N, Bratanic N, de Kerdanet M, Weill J, Ser N, Barat P, Bertrand AM, Carel JC, Reynaud R, Coutant R, Baron S. GAD65 antigen therapy in recently diagnosed type 1 diabetes mellitus. N Engl J Med. 2012 Feb 2;366(5):433-42. doi: 10.1056/NEJMoa1107096.

Reference Type DERIVED
PMID: 22296077 (View on PubMed)

Other Identifiers

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D/P3/07/4

Identifier Type: -

Identifier Source: org_study_id