Safety & Efficacy of Peginesatide for Maintenance Treatment of Anemia in Participants With Chronic Kidney Disease on Hemodialysis

NCT ID: NCT00597753

Last Updated: 2013-02-12

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

803 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-09-30

Study Completion Date

2010-01-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of the study was to evaluate the safety and efficacy of peginesatide in the maintenance treatment of anemia in participants on dialysis.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Anemia associated with chronic kidney disease is due to several factors, primarily the inability of the diseased kidneys to produce adequate amounts of endogenous erythropoietin. Ancillary factors include the shortened lifespan of red blood cells, iron and other nutritional deficiencies, infection, and inflammation. The presence and severity of anemia are related to the duration and extent of kidney failure. Anemia is associated with increased mortality, increased likelihood of hospitalization, reduced cognitive function, and increased left ventricular hypertrophy and heart failure.

Erythropoiesis stimulating agents (ESAs) have been established as a treatment for anemia in chronic renal failure subjects, and have improved the management of anemia over alternatives such as transfusion. Peginesatide is a parenteral formulation developed for the treatment of anemia in patients with chronic kidney disease. Peginesatide binds to and activates the human erythropoietin receptor, and stimulates erythropoiesis in human red cell precursors in a manner similar to other known erythropoiesis-stimulating agents.

Eligible participants were randomized in a 2:1 ratio to peginesatide administered once every 4 weeks or to continued treatment with epoetin alfa administered 1-3 times each week, respectively. Total commitment time for this study was 4 weeks of screening followed by a minimum of 52 weeks of study treatment.

To evaluate the cardiovascular safety of peginesatide, a cardiovascular composite safety endpoint (CSE) was defined for use in prospectively planned analyses which combined cardiovascular safety data from the four Phase 3 peginesatide studies (NCT00598273, NCT00597753, NCT00598442, and NCT00597584). The CSE consisted of six events: death, stroke, myocardial infarction, and serious adverse events of congestive heart failure, unstable angina, and arrhythmia. An independent Event Review Committee (ERC) was used to provide blinded adjudication of potential CSE events.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Chronic Renal Failure Chronic Kidney Disease Anemia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Peginesatide

Group Type EXPERIMENTAL

peginesatide

Intervention Type DRUG

Participants received peginesatide by intravenous injection once every 4 weeks. The starting dose was based on the participant's total weekly epoetin alfa dose during the last week of the Screening Period; the first dose was administered one week after the last epoetin alfa dose. The dose was adjusted to maintain hemoglobin levels in a target range of 10.0-12.0 grams per deciliter (g/dL) and ± 1.5 g/dL from baseline during the Titration and Evaluation Periods, and 10.0-12.0 g/dL during the Long-Term Safety and Efficacy Period.

Epoetin alfa

Group Type ACTIVE_COMPARATOR

Epoetin Alfa

Intervention Type DRUG

Participants continued to receive commercially available epoetin alfa by intravenous injection, at the same starting dose and frequency as received during the last week of the Screening Period, with the first study dose of epoetin alfa administered after randomization at Week 0. The dose was adjusted to maintain hemoglobin levels in a target range of 10.0-12.0 g/dL and ± 1.5 g/dL from baseline during the Titration and Evaluation Periods, and 10.0-12.0 g/dL during the Long-Term Safety and Efficacy Period.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

peginesatide

Participants received peginesatide by intravenous injection once every 4 weeks. The starting dose was based on the participant's total weekly epoetin alfa dose during the last week of the Screening Period; the first dose was administered one week after the last epoetin alfa dose. The dose was adjusted to maintain hemoglobin levels in a target range of 10.0-12.0 grams per deciliter (g/dL) and ± 1.5 g/dL from baseline during the Titration and Evaluation Periods, and 10.0-12.0 g/dL during the Long-Term Safety and Efficacy Period.

Intervention Type DRUG

Epoetin Alfa

Participants continued to receive commercially available epoetin alfa by intravenous injection, at the same starting dose and frequency as received during the last week of the Screening Period, with the first study dose of epoetin alfa administered after randomization at Week 0. The dose was adjusted to maintain hemoglobin levels in a target range of 10.0-12.0 g/dL and ± 1.5 g/dL from baseline during the Titration and Evaluation Periods, and 10.0-12.0 g/dL during the Long-Term Safety and Efficacy Period.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Omontys Hematide AF37702 Injection Epogen

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Participants with chronic renal failure on hemodialysis for ≥ 3 months prior to randomization.
2. On intravenous epoetin alfa maintenance therapy continuously prescribed for a minimum of 8 weeks prior to randomization.
3. Four consecutive hemoglobin values with a mean ≥ 10.0 and ≤ 12.0 g/dL during the screening period

Exclusion Criteria

1. Females who are pregnant or breast-feeding.
2. Known intolerance to any erythropoiesis stimulating agent (ESA) or pegylated molecule or to all parenteral iron supplementation products.
3. Known bleeding or coagulation disorder.
4. Known hematologic disease or cause of anemia other than renal disease
5. Poorly controlled hypertension
6. Evidence of active malignancy within one year prior to randomization.
7. Temporary (untunneled) dialysis access catheter.
8. A scheduled kidney transplant
9. A scheduled surgery that may be expected to lead to significant blood loss.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Takeda

INDUSTRY

Sponsor Role collaborator

Affymax

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Vice President, Clinical Development

Role: STUDY_DIRECTOR

Affymax

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Research Facility

Paragould, Arkansas, United States

Site Status

Research Facility

Fairfield, California, United States

Site Status

Research Facility

Granada Hills, California, United States

Site Status

Research Facility

Los Alamitos, California, United States

Site Status

Research Facility

Los Angeles, California, United States

Site Status

Research Facility

Los Angeles, California, United States

Site Status

Research Facility

Los Angeles, California, United States

Site Status

Research Facility

Lynwood, California, United States

Site Status

Research Facility

Monterey Park, California, United States

Site Status

Research Facility

Mountain View, California, United States

Site Status

Research Facility

Paramount, California, United States

Site Status

Research Facilities (2)

San Diego, California, United States

Site Status

Research Facility

San Dimas, California, United States

Site Status

Research Facility

Whittier, California, United States

Site Status

Research Facility

Denver, Colorado, United States

Site Status

Research Facility

Middlebury, Connecticut, United States

Site Status

Research Facility

Hudson, Florida, United States

Site Status

Research Facility

Ocala, Florida, United States

Site Status

Research Facility

Orlando, Florida, United States

Site Status

Research Facility

Orlando, Florida, United States

Site Status

Research Facility

Pembroke Pines, Florida, United States

Site Status

Research Facility

Augusta, Georgia, United States

Site Status

Research Facility

Augusta, Georgia, United States

Site Status

Research Facility

Decatur, Georgia, United States

Site Status

Research Facility

Marietta, Georgia, United States

Site Status

Research Facility

Honolulu, Hawaii, United States

Site Status

Research Facility

Boise, Idaho, United States

Site Status

Research Facility

Chicago, Illinois, United States

Site Status

Research Facility

Evergreen Park, Illinois, United States

Site Status

Research Facility

Gurnee, Illinois, United States

Site Status

Research Facility

Peoria, Illinois, United States

Site Status

Research Facility

Evansville, Indiana, United States

Site Status

Research Facility

Wichita, Kansas, United States

Site Status

Research Facility

Lexington, Kentucky, United States

Site Status

Research Facility

Baton Rouge, Louisiana, United States

Site Status

Research Facility

Lafayette, Louisiana, United States

Site Status

Research Facility

New Orleans, Louisiana, United States

Site Status

Research Facility

Shreveport, Louisiana, United States

Site Status

Research Facility

Bethesda, Maryland, United States

Site Status

Research Facility

Rockville, Maryland, United States

Site Status

Research Facility

Fall River, Massachusetts, United States

Site Status

Research Facility

Worcester, Massachusetts, United States

Site Status

Research Facility

Dearborn, Michigan, United States

Site Status

Research Facility

Kalamazoo, Michigan, United States

Site Status

Research Facility

Columbus, Mississippi, United States

Site Status

Research Facility

Tupelo, Mississippi, United States

Site Status

Research Facility

St Louis, Missouri, United States

Site Status

Research Facility

Las Vegas, Nevada, United States

Site Status

Research Facility

Eatontown, New Jersey, United States

Site Status

Research Facility

Brooklyn, New York, United States

Site Status

Research Facility

New York, New York, United States

Site Status

Research Facility

The Bronx, New York, United States

Site Status

Research Facility

The Bronx, New York, United States

Site Status

Research Facility

Williamsville, New York, United States

Site Status

Research Facility

Yonkers, New York, United States

Site Status

Research Facility

Durham, North Carolina, United States

Site Status

Research Facility

Raleigh, North Carolina, United States

Site Status

Research Facility

Canton, Ohio, United States

Site Status

Research Facility

Cincinnati, Ohio, United States

Site Status

Research Facility

Columbus, Ohio, United States

Site Status

Research Facility

Roseburg, Oregon, United States

Site Status

Research Facility

Allentown, Pennsylvania, United States

Site Status

Research Facility

Philadelphia, Pennsylvania, United States

Site Status

Research Facility

Philadelphia, Pennsylvania, United States

Site Status

Research Facility

Pittsburgh, Pennsylvania, United States

Site Status

Research Facilities (2)

Greenville, South Carolina, United States

Site Status

Research Facility

Sumter, South Carolina, United States

Site Status

Research Facility

Dyersburg, Tennessee, United States

Site Status

Research Facility

Knoxville, Tennessee, United States

Site Status

Research Facility

Nashville, Tennessee, United States

Site Status

Research Facility

Arlington, Texas, United States

Site Status

Research Facility

Fort Worth, Texas, United States

Site Status

Research Facility

Fort Worth, Texas, United States

Site Status

Research Facility

Fort Worth, Texas, United States

Site Status

Research Facility

Grand Prairie, Texas, United States

Site Status

Research Facilities (2)

Houston, Texas, United States

Site Status

Research Facility

Houston, Texas, United States

Site Status

Research Facility

McAllen, Texas, United States

Site Status

Research Facility

San Antonio, Texas, United States

Site Status

Research Facility

San Antonio, Texas, United States

Site Status

Research Facility

Tyler, Texas, United States

Site Status

Research Facility

Alexandria, Virginia, United States

Site Status

Research Facility

Chesapeake, Virginia, United States

Site Status

Research Facility

Fairfax, Virginia, United States

Site Status

Research Facility

Mechanicsville, Virginia, United States

Site Status

Research Facilities (2)

Norfolk, Virginia, United States

Site Status

Research Facility

Morgantown, West Virginia, United States

Site Status

Research Facility

Appleton, Wisconsin, United States

Site Status

Research Facility

Oshkosh, Wisconsin, United States

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States

References

Explore related publications, articles, or registry entries linked to this study.

Fishbane S, Schiller B, Locatelli F, Covic AC, Provenzano R, Wiecek A, Levin NW, Kaplan M, Macdougall IC, Francisco C, Mayo MR, Polu KR, Duliege AM, Besarab A; EMERALD Study Groups. Peginesatide in patients with anemia undergoing hemodialysis. N Engl J Med. 2013 Jan 24;368(4):307-19. doi: 10.1056/NEJMoa1203165.

Reference Type RESULT
PMID: 23343061 (View on PubMed)

Macdougall IC, Provenzano R, Sharma A, Spinowitz BS, Schmidt RJ, Pergola PE, Zabaneh RI, Tong-Starksen S, Mayo MR, Tang H, Polu KR, Duliege AM, Fishbane S; PEARL Study Groups. Peginesatide for anemia in patients with chronic kidney disease not receiving dialysis. N Engl J Med. 2013 Jan 24;368(4):320-32. doi: 10.1056/NEJMoa1203166.

Reference Type DERIVED
PMID: 23343062 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

AFX01-12

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.