An Efficacy and Safety Study of Golimumab (CNTO 148) in Participants With Moderately to Severely Active Ulcerative Colitis

NCT ID: NCT00488631

Last Updated: 2016-04-26

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1228 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-09-30

Study Completion Date

2015-02-28

Brief Summary

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The purpose of this study is to assess the safety and efficacy of golimumab administered subcutaneously (under the skin) injections in maintenance therapy.

Detailed Description

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This was a Phase 3, multicenter (conducted in more than one center), placebo-controlled (an inactive substance that is compared with a drug to test whether the drug has a real effect in a clinical trial), double-blind (neither the Physician nor the participant know about the study medication), parallel-group (a medical research study comparing the response in 2 or more groups of participants receiving different interventions), randomized-withdrawal study. Participants who were in clinical response to golimumab at Week 6 in induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539) will be randomly assigned in a 1:1:1 ratio at Week 0 of this study to receive 1 of the following maintenance treatment regimens administered subcutaneously every 4 weeks through Week 52: placebo, golimumab 50 mg, or golimumab 100 mg. Participants who were in clinical response to placebo and participants who were not in clinical response to golimumab or placebo at Week 6 in induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539) will not be randomly assigned but will be eligible to be enrolled in the study (i.e., the nonrandomized group) and received the following treatment regimens: placebo, golimumab 100 mg and golimumab 100 mg. Dose adjustment will be done for participants who were in clinical response to golimumab or placebo during induction studies C0524T16 (NCT00488774) or C0524T17 (NCT00487539) but lose clinical response during maintenance study C0524T18 (NCT00488631). On completing this study, participant will have the opportunity to continue to receive study medication in a study extension that will last up to approximately 3 years. Efficacy will be primarily evaluated by assessing the clinical response using Mayo Score. Participants' safety will be monitored throughout the study.

Conditions

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Colitis, Ulcerative

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Golimumab induction responders (GLM-I-Rsp)-Placebo Maintenance

Participants in clinical response to golimumab at Week 6 of induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539) and randomized to placebo subcutaneous (under the skin) injection matching to golimumab administered every 4 weeks through Week 52 in maintenance study C0524T18 (NCT00488631). Participants with loss of clinical response will have their dose increased to golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type BIOLOGICAL

Participants receive placebo subcutaneous injection matching to golimumab administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631).

Golimumab 100 mg

Intervention Type BIOLOGICAL

Participants receive golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631) initially or after dose adjustment following loss of clinical response.

GLM-I-Rsp-Golimumab 50 mg Maintenance

Participants in clinical response to golimumab at Week 6 of induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539) and randomized to golimumab 50 mg subcutaneous injection administered every 4 weeks through Week 52 in maintenance study C0524T18 (NCT00488631). Participants with loss of clinical response will be re-randomized to receive golimumab 50 mg or 100 mg subcutaneous injections every 4 weeks through Week 52.

Group Type EXPERIMENTAL

Golimumab 50 mg

Intervention Type BIOLOGICAL

Participants receive golimumab 50 mg subcutaneous injection administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631).

Golimumab 100 mg

Intervention Type BIOLOGICAL

Participants receive golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631) initially or after dose adjustment following loss of clinical response.

GLM-I-Rsp-Golimumab 100 mg Maintenance

Participants in clinical response to golimumab at Week 6 of induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539) and randomized to golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52 in maintenance study C0524T18 (NCT00488631). Participants with loss of clinical response will be re-randomized to receive golimumab 100 mg or 200 mg subcutaneous injections every 4 weeks through Week 52.

Group Type EXPERIMENTAL

Golimumab 100 mg

Intervention Type BIOLOGICAL

Participants receive golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631) initially or after dose adjustment following loss of clinical response.

Golimumab 200 mg

Intervention Type BIOLOGICAL

Participants receiving golimumab 100 mg initially who on loss of clinical response receive golimumab 200 mg administered every 4 weeks through Week 52.

Placebo induction responders (PBO-I-Rsp)-Placebo Maintenance

Participants in clinical response to placebo at Week 6 of induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539) and received placebo subcutaneous injection matching to golimumab administered every 4 weeks through Week 52 in maintenance study C0524T18 (NCT00488631); not randomized. Participants with loss of clinical response will have their dose increased to golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type BIOLOGICAL

Participants receive placebo subcutaneous injection matching to golimumab administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631).

Golimumab 100 mg

Intervention Type BIOLOGICAL

Participants receive golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631) initially or after dose adjustment following loss of clinical response.

PBO-I-nonRsp-Golimumab 100 mg Maintenance

Participants not in clinical response to placebo at Week 6 induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539) and received golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52 in maintenance study C0524T18 (NCT00488631); not randomized.

Group Type EXPERIMENTAL

Golimumab 100 mg

Intervention Type BIOLOGICAL

Participants receive golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631) initially or after dose adjustment following loss of clinical response.

GLM-I-nonRsp-Golimumab 100 mg Maintenance

Participants not in clinical response to golimumab at Week 6 of induction study and received golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52 in maintenance study C0524T18 (NCT00488631); not randomized.

Group Type EXPERIMENTAL

Golimumab 100 mg

Intervention Type BIOLOGICAL

Participants receive golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631) initially or after dose adjustment following loss of clinical response.

Interventions

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Placebo

Participants receive placebo subcutaneous injection matching to golimumab administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631).

Intervention Type BIOLOGICAL

Golimumab 50 mg

Participants receive golimumab 50 mg subcutaneous injection administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631).

Intervention Type BIOLOGICAL

Golimumab 100 mg

Participants receive golimumab 100 mg subcutaneous injection administered every 4 weeks through Week 52 in the maintenance study C0524T18 (NCT00488631) initially or after dose adjustment following loss of clinical response.

Intervention Type BIOLOGICAL

Golimumab 200 mg

Participants receiving golimumab 100 mg initially who on loss of clinical response receive golimumab 200 mg administered every 4 weeks through Week 52.

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Participants who received all study agent administrations and completed the Week 6 Mayo score evaluation in induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539)
* Participants who completed the Week 0 visit for this maintenance study C0524T18 (NCT00488631) on the same day as the Week 6 visit of the induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539)

Exclusion Criteria

* Participants who increased the dose of their concomitant (given at the same time) UC medications since Week 0 of induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539)
* Participants who initiated a concomitant UC medication since Week 0 of an induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539)
* Participants who had a partial or total colectomy (surgery to remove part or all of the colon) or an ostomy (surgical construction of an artificial opening (stoma) for external fistulization of a duct or vessel by insertion of a tube with or without a supportive stent) since Week 0 of an induction study C0524T16 (NCT00488774) or C0524T17 (NCT00487539)
* Participants with signs or symptoms of latent or active granulomatous infection (including TB); a nontuberculous mycobacterial infection or opportunistic infection; or infection with HIV (Human Immunodeficiency Virus), hepatitis B, or hepatitis C
* Participants with signs and symptoms of any malignancy or suggestive of a possible lymphoproliferative disease (disorders characterized by proliferation of lymphoid tissue, general or unspecified)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role collaborator

Janssen Research & Development, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Janssen Research & Development, LLC Clinical Trial

Role: STUDY_DIRECTOR

Janssen Research & Development, LLC

Locations

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Birmingham, Alabama, United States

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Little Rock, Arkansas, United States

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Anaheim, California, United States

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Merced, California, United States

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Orange, California, United States

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Roseville, California, United States

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San Diego, California, United States

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Lakewood, Colorado, United States

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Littleton, Colorado, United States

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Bristol, Connecticut, United States

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Newark, Delaware, United States

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Boca Raton, Florida, United States

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Gainesville, Florida, United States

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Hialeah, Florida, United States

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Hollywood, Florida, United States

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Jacksonville, Florida, United States

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Naples, Florida, United States

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New Port Richey, Florida, United States

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North Miami Beach, Florida, United States

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Port Orange, Florida, United States

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Tampa, Florida, United States

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Winter Park, Florida, United States

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Zephyrhills, Florida, United States

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Atlanta, Georgia, United States

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Decatur, Georgia, United States

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Savannah, Georgia, United States

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Snellville, Georgia, United States

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Arlington Heights, Illinois, United States

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Chicago, Illinois, United States

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Clive, Iowa, United States

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Fort Dodge, Iowa, United States

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Pratt, Kansas, United States

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Topeka, Kansas, United States

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Lexington, Kentucky, United States

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Louisville, Kentucky, United States

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Monroe, Louisiana, United States

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Hagerstown, Maryland, United States

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Hollywood, Maryland, United States

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Laurel, Maryland, United States

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Worcester, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Dearborn, Michigan, United States

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Troy, Michigan, United States

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Plymouth, Minnesota, United States

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Rochester, Minnesota, United States

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Pascagoula, Mississippi, United States

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Tupelo, Mississippi, United States

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Urbana, Missouri, United States

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Las Vegas, Nevada, United States

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Lebanon, New Hampshire, United States

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Egg Harbor, New Jersey, United States

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Great Neck, New York, United States

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Huntington, New York, United States

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New York, New York, United States

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Rochester, New York, United States

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Asheville, North Carolina, United States

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Boone, North Carolina, United States

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Charlotte, North Carolina, United States

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Harrisburg, North Carolina, United States

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Kinston, North Carolina, United States

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Morganton, North Carolina, United States

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New Bern, North Carolina, United States

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Raleigh, North Carolina, United States

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Wilmington, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Fargo, North Dakota, United States

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Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Colombus, Ohio, United States

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Norman, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Portland, Oregon, United States

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Limerick, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Charleston, South Carolina, United States

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Columbia, South Carolina, United States

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Germantown, Tennessee, United States

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Nashville, Tennessee, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Galveston, Texas, United States

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Houston, Texas, United States

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Logan, Utah, United States

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Ogden, Utah, United States

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Burlington, Vermont, United States

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Chesapeake, Virginia, United States

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Christiansburg, Virginia, United States

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Fairfax, Virginia, United States

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Richmond, Virginia, United States

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Bellevue, Washington, United States

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Seattle, Washington, United States

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Spokane, Washington, United States

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Tacoma, Washington, United States

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Madison, Wisconsin, United States

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Milwaukee, Wisconsin, United States

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Adelaide, , Australia

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Bankstown, , Australia

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Box Hill, , Australia

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Brisbane, , Australia

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Cairns, , Australia

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Fitzroy, , Australia

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Fremantle, , Australia

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Herston, , Australia

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Launceston, , Australia

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Malvern, , Australia

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Parkville, , Australia

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Prahran, , Australia

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Westmead, , Australia

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Innsbruck, , Austria

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Vienna, , Austria

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Bonheiden, , Belgium

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Brussels, , Belgium

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Ghent, , Belgium

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Leuven, , Belgium

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Liège, , Belgium

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Roeselare, , Belgium

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Bulgaria, , Bulgaria

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Pleven, , Bulgaria

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Plovdiv, , Bulgaria

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Rousse, , Bulgaria

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Sofia, , Bulgaria

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Calgary, Alberta, Canada

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Vancouver, British Columbia, Canada

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Victoria, British Columbia, Canada

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Winnipeg, Manitoba, Canada

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Barrie, Ontario, Canada

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Chatham, Ontario, Canada

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Hamilton, Ontario, Canada

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Kingston, Ontario, Canada

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London, Ontario, Canada

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Vaughan, Ontario, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Saskatoon, Saskatchewan, Canada

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Toronto, , Canada

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Windsor, , Canada

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Èeské Budìjovice 1, , Czechia

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Hradec Králové, , Czechia

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Litoměřice, , Czechia

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Ostrava, , Czechia

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Aalborg, , Denmark

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Aarhus C, , Denmark

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Hvidovre, , Denmark

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Odense C, , Denmark

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Amiens Cedex 1 80, , France

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Bordeaux, , France

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Clichy, , France

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Lille, , France

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Marseille, , France

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Nice, , France

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Paris, , France

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Rouen, , France

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Aachen, , Germany

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Berlin, , Germany

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Berlin Be, , Germany

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Bochum, , Germany

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Frankfurt, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Heidelberg, , Germany

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Herne, , Germany

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Jena, , Germany

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Kiel, , Germany

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Magdeburg, , Germany

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Minden, , Germany

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München, , Germany

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Münster, , Germany

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Neustadt, , Germany

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Stade, , Germany

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Balatonfüred, , Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Dunaújváros, , Hungary

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Gyõr, , Hungary

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Gyula, , Hungary

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Gyulai Ut 18, , Hungary

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Miskolc, , Hungary

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Mosonmagyaróvár, , Hungary

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Pécs, , Hungary

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Siófok, , Hungary

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Sopron, , Hungary

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Szeged, , Hungary

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Szekszárd, , Hungary

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Székesfehérvár, , Hungary

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Szombathely, , Hungary

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Veszprém, , Hungary

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Zalaegerszeg, , Hungary

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Bangalore, , India

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Chennai, , India

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Hyderabad, , India

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Hyderabad Andh Prad, , India

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Jaipur, , India

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Kārnād, , India

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Lucknow Gpo, , India

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Ludhiana, , India

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New Delhi, , India

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Pune, , India

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Vishakapatanam, , India

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Afula, , Israel

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Beer Yaakov, , Israel

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Beersheba, , Israel

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Haifa, , Israel

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Hedera, , Israel

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Jerusalem, , Israel

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Kfar Saba, , Israel

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Kiryat Bialik, , Israel

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Nazareth, , Israel

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Petah-Tikv, , Israel

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Rehovot, , Israel

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Tel Aviv, , Israel

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Tel Litwinsky, , Israel

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Bunkyō City, , Japan

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Chikushinoshi, , Japan

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Fukuoka, , Japan

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Hiroshima, , Japan

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Kagoshima, , Japan

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Kurashiki, , Japan

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Kurume, , Japan

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Nagoya, , Japan

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Nishinomiya, , Japan

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Okayama, , Japan

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Osaka, , Japan

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Sakura, , Japan

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Sapporo, , Japan

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Tokyo, , Japan

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Yokkaichi, , Japan

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Balvi, , Latvia

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Daugavpils, , Latvia

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Riga, , Latvia

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Kaunas, , Lithuania

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Klaipėda, , Lithuania

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Šiauliai, , Lithuania

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Vilnius, , Lithuania

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Vilnius Lt, , Lithuania

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Amsterdam, , Netherlands

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Ede Gld, , Netherlands

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Groningen, , Netherlands

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Leiden, , Netherlands

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Nieuwegein, , Netherlands

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Rotterdam, , Netherlands

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Auckland, , New Zealand

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Christchurch, , New Zealand

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Dunedin, , New Zealand

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Hamilton, , New Zealand

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Hastings, , New Zealand

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Bialystok, , Poland

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Bydgoszcz, , Poland

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Częstochowa, , Poland

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Elblag, , Poland

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Gdansk, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Opole, , Poland

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Skierniewice, , Poland

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Sopot, , Poland

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Szczecin, , Poland

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Torun, , Poland

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Warsaw, , Poland

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Bucharest, , Romania

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Cluj-Napoca, , Romania

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Iași, , Romania

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Târgu Mureş, , Romania

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Timișoara, , Romania

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Moscow, , Russia

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Novosibirsk, , Russia

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Omsk, , Russia

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Saint Petersburg, , Russia

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Smolensk, , Russia

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Yaroslavl, , Russia

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Belgrade, , Serbia

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Niš, , Serbia

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Zemun, , Serbia

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Bratislava, , Slovakia

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Martin, , Slovakia

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Nitra, , Slovakia

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Nové Mesto nad Váhom, , Slovakia

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Prešov, , Slovakia

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Trnava, , Slovakia

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Cape Town, , South Africa

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Cape Town West Cape, , South Africa

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Durban, , South Africa

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Plumstead West Cape, , South Africa

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Pretoria Gauteng, , South Africa

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Gothenburg, , Sweden

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Stockholm, , Sweden

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Donetsk, , Ukraine

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Ivano, , Ukraine

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Kharkiv, , Ukraine

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Kiev, , Ukraine

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Kyiv, , Ukraine

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Lviv, , Ukraine

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Poltava, , Ukraine

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Simferopol, , Ukraine

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Vinnitsa, , Ukraine

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Zhaporozhia 69104, , Ukraine

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Countries

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United States Australia Austria Belgium Bulgaria Canada Czechia Denmark France Germany Hungary India Israel Japan Latvia Lithuania Netherlands New Zealand Poland Romania Russia Serbia Slovakia South Africa Sweden Ukraine

References

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Weinstein CLJ, Meehan AG, Govoni M, Lin J, Reinisch W. Low Occurrence of Colectomy With Long-Term (up to 4 Years) Golimumab Treatment in Patients With Moderate-to-Severe Active Ulcerative Colitis: Data From the PURSUIT Maintenance and Long-Term Extension Studies. Crohns Colitis 360. 2023 Aug 26;5(3):otad044. doi: 10.1093/crocol/otad044. eCollection 2023 Jul.

Reference Type DERIVED
PMID: 37691729 (View on PubMed)

Perrig K, Krupka N, Jordi SBU, Rossel JB, Biedermann L, Greuter T, Schreiner P, Vavricka SR, Juillerat P, Burri E, Zimmermann D, Maillard MH, Sulz MC, Brand S, Rogler G, Misselwitz B. Effectiveness of golimumab in patients with ulcerative colitis: results of a real-life study in Switzerland. Therap Adv Gastroenterol. 2022 Feb 9;15:17562848221074188. doi: 10.1177/17562848221074188. eCollection 2022.

Reference Type DERIVED
PMID: 35154389 (View on PubMed)

Adedokun OJ, Xu Z, Liao S, Strauss R, Reinisch W, Feagan BG, Sandborn WJ. Population Pharmacokinetics and Exposure-Response Modeling of Golimumab in Adults With Moderately to Severely Active Ulcerative Colitis. Clin Ther. 2020 Jan;42(1):157-174.e4. doi: 10.1016/j.clinthera.2019.11.010. Epub 2020 Jan 22.

Reference Type DERIVED
PMID: 31982148 (View on PubMed)

Philip G, Cornillie F, Adedokun JO, Melsheimer R, Rutgeerts P, Colombel JF, Marano C. Early Dose Optimisation of Golimumab in Nonresponders to Induction Treatment for Ulcerative Colitis Is Effective and Supported by Pharmacokinetic Data. J Crohns Colitis. 2019 Sep 27;13(10):1257-1264. doi: 10.1093/ecco-jcc/jjz052.

Reference Type DERIVED
PMID: 30847474 (View on PubMed)

Reinisch W, Gibson PR, Sandborn WJ, Feagan BG, Strauss R, Johanns J, Padgett L, Adedokun OJ, Colombel JF, Collins J, Rutgeerts P, Tarabar D, Marano C. Long-Term Benefit of Golimumab for Patients with Moderately to Severely Active Ulcerative Colitis: Results from the PURSUIT-Maintenance Extension. J Crohns Colitis. 2018 Aug 29;12(9):1053-1066. doi: 10.1093/ecco-jcc/jjy079.

Reference Type DERIVED
PMID: 29917070 (View on PubMed)

Sandborn WJ, Feagan BG, Marano C, Zhang H, Strauss R, Johanns J, Adedokun OJ, Guzzo C, Colombel JF, Reinisch W, Gibson PR, Collins J, Jarnerot G, Rutgeerts P; PURSUIT-Maintenance Study Group. Subcutaneous golimumab maintains clinical response in patients with moderate-to-severe ulcerative colitis. Gastroenterology. 2014 Jan;146(1):96-109.e1. doi: 10.1053/j.gastro.2013.06.010. Epub 2013 Jun 14.

Reference Type DERIVED
PMID: 23770005 (View on PubMed)

Other Identifiers

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2006-003399-37

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

C0524T18

Identifier Type: OTHER

Identifier Source: secondary_id

CR014179

Identifier Type: -

Identifier Source: org_study_id

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