Efficacy and Safety of Fingolimod (FTY720) in Patients With Relapsing-remitting Multiple Sclerosis

NCT ID: NCT00355134

Last Updated: 2012-08-07

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1083 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-06-30

Study Completion Date

2011-08-31

Brief Summary

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This study assessed the safety, tolerability and efficacy of two doses of oral fingolimod compared to placebo on efficacy parameters in patients with relapsing-remitting multiple sclerosis (RRMS).

Detailed Description

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This randomized, multicenter, parallel-group study consisted of 2 phases: a 24-month double-blind, randomized, multicenter, placebo-controlled, parallel-group study and an Extension phase which consisted of a dose-blinded period and an open-label period.

In the Core phase, patients were randomized to receive a fixed dose of fingolimod (0.5 mg/day), fingolimod (1.25 mg/day) or placebo for up to 24 months.

For the Extension phase, patients who were treated with fingolimod during the Core phase continued treatment at the assigned dose level, while those previously treated with placebo during the Core phase were re-randomized in a 1:1 ratio to receive one of the two doses of fingolimod (1.25 mg or 0.5 mg). All patients in the extension received blinded investigational drug: fingolimod 1.25 mg and 0.5 mg in capsules for oral administration once daily until the decision to discontinue the fingolimod 1.25 mg dose became effective and subsequently all patients were switched to open-label fingolimod 0.5 mg.

With the implementation of Amendment 11, the 1.25 mg dose was discontinued and all patients were switched to fingolimod 0.5 mg dose. With the implementation of Amendment 12, all patients treated with Placebo in the fingolimod Core phase were switched to treatment with 0.5 mg fingolimod per day. The Extension phase continued until all patients either discontinued or transferred to Study CFTY720D2399 (NCT01201356; initiated in September 2010).

Conditions

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Multiple Sclerosis

Keywords

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fingolimod FTY720 relapsing-remitting multiple sclerosis MS RRMS

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Fingolimod 1.25 mg

Participants received 1.25 mg fingolimod orally once a day for up to 24 months during the core phase. In the Extension phase participants continued to receive 1.25 mg fingolimod orally once a day.

Note: Upon implementation of a protocol amendment all patients taking 1.25 mg fingolimod were switched to 0.5 mg fingolimod orally once a day.

Group Type EXPERIMENTAL

Fingolimod

Intervention Type DRUG

Fingolimod capsules for oral administration

Fingolimod 0.5 mg

Participants received 0.5 mg fingolimod orally once a day for up to 24 months during the core phase. In the Extension phase participants continued to receive 0.5 mg fingolimod orally once a day.

Group Type EXPERIMENTAL

Fingolimod

Intervention Type DRUG

Fingolimod capsules for oral administration

Placebo

Participants received placebo capsules orally once a day for up to 24 months during the core phase. In the Extension phase participants received either 1.25 or 0.5 mg fingolimod orally once a day.

Note: Upon implementation of a protocol amendment all patients taking 1.25 mg fingolimod were switched to 0.5 mg fingolimod orally once a day. Upon implementation of a protocol amendment, all patients taking placebo were switched to 0.5 mg fingolimod orally once a day.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Matching placebo capsules for oral administration.

Interventions

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Fingolimod

Fingolimod capsules for oral administration

Intervention Type DRUG

Placebo

Matching placebo capsules for oral administration.

Intervention Type DRUG

Other Intervention Names

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FTY720 Gilenya®

Eligibility Criteria

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Inclusion Criteria

* Male and female patients between ages 18-55 with a diagnosis of multiple sclerosis
* Patients with a relapsing-remitting disease course
* Patients with expanded disability status scale (EDSS) score of 0-5.5

Exclusion Criteria

* Patients with other chronic disease of the immune system, malignancies, acute pulmonary disease, cardiac failure, etc.
* Pregnant or nursing women

For inclusion in the extension phase patients should complete the 24 month core study with or without 24 months on study drug. If a patient discontinued study drug during the core study due to an adverse event, serious adverse event, laboratory abnormality etc. they would be excluded from the Extension Phase.
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_CHAIR

Novartis Pharmaceuticals

Locations

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University of Alabama Birmingham

Birmingham, Alabama, United States

Site Status

North Central Neurology Associates, PC

Cullman, Alabama, United States

Site Status

University of South Alabama - Dept of Neurology

Mobile, Alabama, United States

Site Status

Barrow Neurology Clinic

Phoenix, Arizona, United States

Site Status

Research and Education Institute of Alta Bates Summit Medical Center

Berkeley, California, United States

Site Status

University of California - Irvine, Deptarment of Neurology

Irvine, California, United States

Site Status

Cedars Sinai Medical Center

Los Angeles, California, United States

Site Status

The Neurology Center

Oceanside, California, United States

Site Status

Neuro-Therapeutics, Inc.

Pasadena, California, United States

Site Status

UC Davis Medical Center

Sacramento, California, United States

Site Status

Multiple Sclerosis Center at UCSF

San Francisco, California, United States

Site Status

University of Colorado

Denver, Colorado, United States

Site Status

Associated Neurologists, PC

Danbury, Connecticut, United States

Site Status

Associated Neurologists of Southern CT, P.C.

Fairfield, Connecticut, United States

Site Status

Yale University - Yale Multiple Sclerosis Center

New Haven, Connecticut, United States

Site Status

Georgetown University Hospital - Dept of Neurology

Washington D.C., District of Columbia, United States

Site Status

Sunrise Clinical Research, Inc.

Hollywood, Florida, United States

Site Status

University of Florida Health Sciences Center/Shands Jacksonville

Jacksonville, Florida, United States

Site Status

Neurology Associates, PA

Maitland, Florida, United States

Site Status

University of Miami, Department of Neurology

Miami, Florida, United States

Site Status

Neurological Associates

Pompano Beach, Florida, United States

Site Status

Roskamp Institute, Clinical Trials Division

Sarasota, Florida, United States

Site Status

Neurology Clinical Research, Inc

Sunrise, Florida, United States

Site Status

AMO Corporation

Tallahassee, Florida, United States

Site Status

Axiom Clinical Research of Florida

Tampa, Florida, United States

Site Status

The MS Center of Vero Beach

Vero Beach, Florida, United States

Site Status

MS Center of Atlanta

Atlanta, Georgia, United States

Site Status

Medical College of Georgia

Augusta, Georgia, United States

Site Status

Northwestern University Medical School - Dept of Neurology

Chicago, Illinois, United States

Site Status

Rush University Medical Center Department of Neurological Sciences

Chicago, Illinois, United States

Site Status

University of Chicago - Dept of Neurology

Chicago, Illinois, United States

Site Status

Alexian Brothers Neurosciences Research

Elk Grove Village, Illinois, United States

Site Status

South Suburban Neurology

Flossmoor, Illinois, United States

Site Status

Neurologic Associates, Ltd.

Palos Heights, Illinois, United States

Site Status

Fort Wayne Neurological Center

Fort Wayne, Indiana, United States

Site Status

Indiana University Medical Center

Indianapolis, Indiana, United States

Site Status

Ruan Neurology Clinical Research Center

Des Moines, Iowa, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Mid America Neuroscience Institute

Lenexa, Kansas, United States

Site Status

Kentucky Research Associates

Louisville, Kentucky, United States

Site Status

University of Maryland

Baltimore, Maryland, United States

Site Status

Johns Hopkins MS Center

Baltimore, Maryland, United States

Site Status

Caritas St. Elizabeth's Medical Center

Brighton, Massachusetts, United States

Site Status

Newton Wesley Hospital

Newton, Massachusetts, United States

Site Status

Springfield Neurology

Springfield, Massachusetts, United States

Site Status

UMass Memorial Medical Center

Worchester, Massachusetts, United States

Site Status

University of Michigan Mulitiple Sclerosis Clinic

Ann Arbor, Michigan, United States

Site Status

Wayne State University MS Clinic

Detroit, Michigan, United States

Site Status

Henry Ford Hospital, Department of Neurology

Detroit, Michigan, United States

Site Status

Michigan State University MS Clinic

East Lansing, Michigan, United States

Site Status

Michigan Medical, P.C.

Grand Rapids, Michigan, United States

Site Status

Michigan Neurology Associates, PC

Saint Clair Shores, Michigan, United States

Site Status

St. Luke's Hospital - Mid-America Brain and Stroke Institute

Kansas City, Missouri, United States

Site Status

The MS Center for Innovation in Care

St Louis, Missouri, United States

Site Status

Institute for Neurosciences

Reno, Nevada, United States

Site Status

Multiple Sclerosis Center

Lebanon, New Hampshire, United States

Site Status

Gimbel Multiple Sclerosis Center at Holy Name Hospital

Teaneck, New Jersey, United States

Site Status

University of New Mexico Health Science Center

Albuquerque, New Mexico, United States

Site Status

Empire Neurology, PC

Latham, New York, United States

Site Status

NYU Hospital for Joint Diseases

New York, New York, United States

Site Status

Cornell University - NY Presbyterian Hospital

New York, New York, United States

Site Status

Mount Sinai School of Medicine

New York, New York, United States

Site Status

Island Neurological Associates, PC

Plainview, New York, United States

Site Status

University of Rochester Medical Center

Rochester, New York, United States

Site Status

Alpha Neurology

Staten Island, New York, United States

Site Status

SUNY Stony Brook

Stony Brook, New York, United States

Site Status

SUNY Upstate Medical University

Syracuse, New York, United States

Site Status

UNC - Chapel Hill Neuroscience Hospital

Chapel Hill, North Carolina, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Raleigh Neurology Associates

Raleigh, North Carolina, United States

Site Status

Wake Forest University Baptist Medical Center

Winston-Salem, North Carolina, United States

Site Status

Neurology & Neuroscience Associates, Inc.

Akron, Ohio, United States

Site Status

Northern Ohio Neuroscience, LLC.

Bellevue, Ohio, United States

Site Status

NeuroCare Center, Inc

Canton, Ohio, United States

Site Status

River Hills Health Care

Cincinnati, Ohio, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

University of Toledo Health Science Campus

Toledo, Ohio, United States

Site Status

Oak Clinic

Uniontown, Ohio, United States

Site Status

MS Center of Oklahoma, Mercy Neuroscience Institute

Oklahoma City, Oklahoma, United States

Site Status

Neurologial Associates of Tulsa

Tulsa, Oklahoma, United States

Site Status

Oregon Neurology

Tualatin, Oregon, United States

Site Status

University of Pennsylvania, Department of Neurology

Philadelphia, Pennsylvania, United States

Site Status

Thomas Jefferson University Hospital, Department of Neurology

Philadelphia, Pennsylvania, United States

Site Status

Allegheny Neurological Associates

Pittsburgh, Pennsylvania, United States

Site Status

University of Pittsburgh - Dept of Neurology

Pittsburgh, Pennsylvania, United States

Site Status

Absher Neurology

Greenville, South Carolina, United States

Site Status

Mountain Empire Neurological Associates, PC

Bristol, Tennessee, United States

Site Status

Advanced Neurosciences Institute

Nashville, Tennessee, United States

Site Status

Vanderbilt Stallworth Rehabilitation Hospital

Nashville, Tennessee, United States

Site Status

University of Texas - Houston Medical School

Houston, Texas, United States

Site Status

Investigational Site - Private Practice

Lubbock, Texas, United States

Site Status

Integra Clinical Research, LLC

San Antonio, Texas, United States

Site Status

Neurology Health Care Service - Fletcher Allen Hospital

Burlington, Vermont, United States

Site Status

University of Virginia - Fontaine Adult Neurology

Charlottesville, Virginia, United States

Site Status

Virginia Mason Multiple Sclerosis Center

Seattle, Washington, United States

Site Status

Seattle Neuroscience Institute at Swedish Medical Center

Seattle, Washington, United States

Site Status

University Health Associates - West Virgina University

Morgantown, West Virginia, United States

Site Status

Dean Foundation

Madison, Wisconsin, United States

Site Status

University of Wisconsin Medical School

Madison, Wisconsin, United States

Site Status

St. Luke's Medical Center

Milwaukee, Wisconsin, United States

Site Status

Novartis Investigative Site

North Gosford, New South Wales, Australia

Site Status

Novartis Investigative Site

Vienna, , Austria

Site Status

Novartis Investigative Site

Ottawa, Ontario, Canada

Site Status

Novartis Investigative Site

Greenfield Park, Quebec, Canada

Site Status

Novartis Investigative Site

Bialystok, , Poland

Site Status

Novartis Investigative Site

Warsaw, , Poland

Site Status

Novartis Investigative Site

Bucharest, , Romania

Site Status

Novartis Investigative Site

Târgu Mureş, , Romania

Site Status

Novartis Investigative Site

Istanbul, , Turkey (Türkiye)

Site Status

Novartis Investigative Site

Izmir, , Turkey (Türkiye)

Site Status

Novartis Investigative Site

Yenisehir/Izmir, , Turkey (Türkiye)

Site Status

Novartis Investigative Site

Bristol, , United Kingdom

Site Status

Countries

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Lithuania United States Australia Austria Canada Poland Romania Turkey (Türkiye) United Kingdom

References

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Wang L, Tan H, Yu J, ZhangBao J, Huang W, Chang X, Zhou L, Lu C, Xiao Y, Lu J, Zhao C, Wang M, Wu X, Wu M, Dong Q, Ngew KY, Quan C. Baseline retinal nerve fiber layer thickness as a predictor of multiple sclerosis progression: New insights from the FREEDOMS II study. Eur J Neurol. 2023 Feb;30(2):443-452. doi: 10.1111/ene.15612. Epub 2022 Nov 15.

Reference Type DERIVED
PMID: 36286605 (View on PubMed)

Fox RJ, Chan A, Zhang A, Xiao J, Levison D, Lewin JB, Edwards MR, Marantz JL. Comparative effectiveness using a matching-adjusted indirect comparison between delayed-release dimethyl fumarate and fingolimod for the treatment of multiple sclerosis. Curr Med Res Opin. 2017 Feb;33(2):175-183. doi: 10.1080/03007995.2016.1248380. Epub 2016 Nov 10.

Reference Type DERIVED
PMID: 27733070 (View on PubMed)

Derfuss T, Bergvall NK, Sfikas N, Tomic DL. Efficacy of fingolimod in patients with highly active relapsing-remitting multiple sclerosis. Curr Med Res Opin. 2015;31(9):1687-91. doi: 10.1185/03007995.2015.1067191. Epub 2015 Aug 20.

Reference Type DERIVED
PMID: 26121423 (View on PubMed)

Chinea Martinez AR, Correale J, Coyle PK, Meng X, Tenenbaum N. Efficacy and safety of fingolimod in Hispanic patients with multiple sclerosis: pooled clinical trial analyses. Adv Ther. 2014 Oct;31(10):1072-81. doi: 10.1007/s12325-014-0154-4. Epub 2014 Sep 23.

Reference Type DERIVED
PMID: 25245812 (View on PubMed)

Calabresi PA, Radue EW, Goodin D, Jeffery D, Rammohan KW, Reder AT, Vollmer T, Agius MA, Kappos L, Stites T, Li B, Cappiello L, von Rosenstiel P, Lublin FD. Safety and efficacy of fingolimod in patients with relapsing-remitting multiple sclerosis (FREEDOMS II): a double-blind, randomised, placebo-controlled, phase 3 trial. Lancet Neurol. 2014 Jun;13(6):545-56. doi: 10.1016/S1474-4422(14)70049-3. Epub 2014 Mar 28.

Reference Type DERIVED
PMID: 24685276 (View on PubMed)

Winges KM, Werner JS, Harvey DJ, Cello KE, Durbin MK, Balcer LJ, Calabresi PA, Keltner JL. Baseline retinal nerve fiber layer thickness and macular volume quantified by OCT in the North American phase 3 fingolimod trial for relapsing-remitting multiple sclerosis. J Neuroophthalmol. 2013 Dec;33(4):322-9. doi: 10.1097/WNO.0b013e31829c51f7.

Reference Type DERIVED
PMID: 24051419 (View on PubMed)

Related Links

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http://www.msclinicaltrials.com

Fingolimod clinical trials information website

Other Identifiers

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CFTY720D2309

Identifier Type: -

Identifier Source: org_study_id

NCT00774670

Identifier Type: -

Identifier Source: nct_alias