MS Study Evaluating Safety and Efficacy of Two Doses of Fingolimod Versus Copaxone

NCT ID: NCT01633112

Last Updated: 2019-05-28

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

1064 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-08-09

Study Completion Date

2018-04-30

Brief Summary

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The purpose of this study was to demonstrate that at least one dose (0.5 mg followed by 0.25 mg) of fingolimod is superior to glatiramer acetate 20 mg SC in reducing the ARR up to 12 months in patients with relapsing-remitting MS

Detailed Description

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This was a multicenter, randomized, rater- and dose-blinded, study to compare the efficacy and safety of 0.25 mg and 0.5 mg of fingolimod with glatimer acetate 20 mg s.c. in patients with RRMS.

This study consisted of 3 periods:

* Screening Period: up to 45 days for all patients
* Treatment Period: 12 months of glatiramer acetate 20 mg, fingolimod 0.25 mg, or fingolimod 0.5 mg
* Follow-up occurred 3 months (12 weeks) after the last dose of study drug for all patients The informed consent form was signed prior to any study related activities at the screening visit. Randomization to either treatment group was preformed at visit 1 after a diligent check of applicable in- and exclusion criteria in a 1:1:1 ratio (changed to 5:3:2 after implementation of Amendment 2 in 2015).

Treatment groups:

* fingolimod 0.5 mg/day orally for up to 12 months
* fingolimod 0.25 mg/day orally for up to 12 months
* glatiramer acetate 20 mg/day subcutaneously for up to 12 months

Conditions

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Relapsing-remitting Multiple Sclerosis (RRMS)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Outcome Assessors
Fingolimod patients were dose blind.

Study Groups

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fingolimod 0.5 mg

orally once daily

Group Type EXPERIMENTAL

fingolimod

Intervention Type DRUG

capsule

fingolimod 0.25mg

orally once daily

Group Type EXPERIMENTAL

fingolimod

Intervention Type DRUG

capsule

glatiramer acetate 20 mg

subcutaneous once daily

Group Type ACTIVE_COMPARATOR

glatiramer acetate

Intervention Type DRUG

subcutaneous injection

Interventions

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fingolimod

capsule

Intervention Type DRUG

glatiramer acetate

subcutaneous injection

Intervention Type DRUG

Other Intervention Names

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FTY720, fingolimod hydrochloride, Gilenya Copaxone, Glatopa

Eligibility Criteria

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Inclusion Criteria

* Written informed consent must be obtained before any assessment is performed
* Male and female patients 18 to 65 years of age, inclusive.
* Patients with RRMS, as defined by 2010 revised McDonald criteria.
* Patients must be neurologically stable with no onset of relapse within 30 days of randomization
* Patients with at least 1 documented relapse during the previous year or 2 documented relapses during the previous 2 years before randomization.
* Patients with an EDSS score of 0 to 6, inclusive, at Screening. A score of 6.0 indicates unilateral assistance (cane or crutch) required to walk at least 100 meters with or without resting.

Exclusion Criteria

* Patients with a history of malignancy of any organ system (other than cutaneous basal cell carcinoma) in the last 5 years that do not have confirmation of absence of a malignancy prior to randomization
* Patients with an active chronic disease (or stable but treated with immune therapy) of the immune system other than MS (e.g., rheumatoid arthritis, scleroderma, Sjogren's syndrome, Crohn's disease, ulcerative colitis) or with a known immunodeficiency syndrome (HIV-antibody positive, AIDS, hereditary immune deficiency, drug-induced immune deficiency).
* Patients who have been treated with:
* High-dose intravenous (IV) immunoglobulin (Ig) within 4 weeks before randomization
* Immunosuppressive/chemotherapeutic medications (e.g., azathioprine, cyclophosphamide, methotrexate) within 6 months before randomization
* Natalizumab within 2 months before randomization
* Previous treatment with lymphocyte-depleting therapies (e.g., rituximab, alemtuzumab, ofatumumab, ocrelizumab, or cladribine) within 1 year before randomization Previous treatment with mitoxantrone within 6 months before randomization
* Use of teriflunomide within 3.5 months prior to randomization, except if active washout (with either cholestyramine or activated charcoal) was done. In that case, plasma levels are required to be measured and be below 0.02 mg/L before randomization.

No washout period is necessary for patients treated with dimethyl fumarate, interferon (IFN) beta, or glatiramer acetate.

Patients being treated with dimethyl fumarate, glatiramer acetate, or IFN beta at the Screening visit can continue drug intake up to the day before Day 1 of this study (i.e., there is no need for a washout period).

* Patients who have been treated with systemic corticosteroids or adrenocorticotropic hormones in the past 30 days prior to the screening magnetic resonance imaging (MRI) procedure.
* Patients with uncontrolled diabetes mellitus (glycosylated hemoglobin \>9%) or with diabetic neuropathy.
* Patients with a diagnosis of macular edema during Screening (patients with a history of macular edema will be allowed to enter the study provided that they do not have macular edema at Screening).
* Patients with severe active bacterial, viral, or fungal infections.
* Patients without acceptable evidence of immunity to varicella zoster virus (VZV) at randomization.
* Patients who have received any live or live-attenuated vaccines (including VZV, herpes simplex, or measles) within 1 month before randomization.
* Patients who have received total lymphoid irradiation or bone marrow transplantation.
* Patients with any unstable medical/psychiatric condition, as assessed by the primary treating physician at each site.
* Patients who in the last 6 months experienced any of the following cardiovascular conditions or findings in the screening electrocardiogram (ECG): myocardial infarction, unstable angina, stroke, transient ischemic attack or decompensated heart failure requiring hospitalization or Class III/IV heart failure.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Novartis Investigative Site

Cullman, Alabama, United States

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Los Angeles, California, United States

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Sacramento, California, United States

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Aurora, Colorado, United States

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Boulder, Colorado, United States

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Denver, Colorado, United States

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Fort Collins, Colorado, United States

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Loveland, Colorado, United States

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Fairfield, Connecticut, United States

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Newark, Delaware, United States

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Washington D.C., District of Columbia, United States

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Jacksonville, Florida, United States

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Maitland, Florida, United States

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Naples, Florida, United States

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New Port Richey, Florida, United States

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Orlando, Florida, United States

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Ormond Beach, Florida, United States

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Pompano Beach, Florida, United States

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Ponte Vedra Beach, Florida, United States

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Port Charlotte, Florida, United States

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Sarasota, Florida, United States

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Tallahassee, Florida, United States

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Tampa, Florida, United States

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Vero Beach, Florida, United States

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West Palm Beach, Florida, United States

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Atlanta, Georgia, United States

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Elk Grove Village, Illinois, United States

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Evanston, Illinois, United States

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Flossmoor, Illinois, United States

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Northbrook, Illinois, United States

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Indianapolis, Indiana, United States

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Indianapolis, Indiana, United States

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West Des Moines, Iowa, United States

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Kansas City, Kansas, United States

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Lenexa, Kansas, United States

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Louisville, Kentucky, United States

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Hammond, Louisiana, United States

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New Orleans, Louisiana, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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Springfield, Massachusetts, United States

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Detroit, Michigan, United States

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Detroit, Michigan, United States

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Farmington Hills, Michigan, United States

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Grand Rapids, Michigan, United States

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Traverse City, Michigan, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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Great Falls, Montana, United States

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Las Vegas, Nevada, United States

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Freehold, New Jersey, United States

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Newark, New Jersey, United States

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Teaneck, New Jersey, United States

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Albuquerque, New Mexico, United States

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Albany, New York, United States

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Amherst, New York, United States

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Buffalo, New York, United States

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Patchogue, New York, United States

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Rochester, New York, United States

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Stony Brook, New York, United States

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Syracuse, New York, United States

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Chapel Hill, North Carolina, United States

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Charlotte, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Akron, Ohio, United States

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Bellevue, Ohio, United States

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Dayton, Ohio, United States

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Toledo, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Portland, Oregon, United States

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Philadelphia, Pennsylvania, United States

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Spartanburg, South Carolina, United States

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Cordova, Tennessee, United States

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Knoxville, Tennessee, United States

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Nashville, Tennessee, United States

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Nashville, Tennessee, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Round Rock, Texas, United States

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San Antonio, Texas, United States

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Sherman, Texas, United States

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Salt Lake City, Utah, United States

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Alexandria, Virginia, United States

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Charlottesville, Virginia, United States

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Norfolk, Virginia, United States

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Roanoke, Virginia, United States

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Issaquah, Washington, United States

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Seattle, Washington, United States

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Milwaukee, Wisconsin, United States

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CABA, Buenos Aires, Argentina

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Buenos Aires, , Argentina

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Belo Horizonte, Minas Gerais, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Joinville, Santa Catarina, Brazil

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Goiânia, , Brazil

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Passo Fundo, , Brazil

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Rio de Janeiro, , Brazil

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Edmonton, Alberta, Canada

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Burnaby, British Columbia, Canada

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Halifax, Nova Scotia, Canada

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Ottawa, Ontario, Canada

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Chicoutimi, Quebec, Canada

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Montreal, Quebec, Canada

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Montreal, Quebec, Canada

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Santiago, , Chile

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Santiago, , Chile

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Tlalnepantla, Edo de Mexico, Mexico

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Mexico City, Mexico City, Mexico

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Monterrey, Nuevo León, Mexico

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San Luis Potosí City, San Luis Potosí, Mexico

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Aguascalientes, , Mexico

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Chihuahua City, , Mexico

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Chihuahua City, , Mexico

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Monterrey, , Mexico

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Guaynabo, , Puerto Rico

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Countries

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United States Argentina Brazil Canada Chile Mexico Puerto Rico

References

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Cree BAC, Goldman MD, Corboy JR, Singer BA, Fox EJ, Arnold DL, Ford C, Weinstock-Guttman B, Bar-Or A, Mientus S, Sienkiewicz D, Zhang Y, Karan R, Tenenbaum N; ASSESS Trial Investigators. Efficacy and Safety of 2 Fingolimod Doses vs Glatiramer Acetate for the Treatment of Patients With Relapsing-Remitting Multiple Sclerosis: A Randomized Clinical Trial. JAMA Neurol. 2020 Aug 24;78(1):1-13. doi: 10.1001/jamaneurol.2020.2950. Online ahead of print.

Reference Type DERIVED
PMID: 32852530 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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CFTY720D2312

Identifier Type: -

Identifier Source: org_study_id

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