A 6-month, Randomized, Open-label, Patient OutComes, Safety and Tolerability Study of Fingolimod (FTY720) 0.5 mg/Day vs. Comparator in Patients With Relapsing Forms of Multiple Sclerosis

NCT ID: NCT01216072

Last Updated: 2014-02-10

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE4

Total Enrollment

1053 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-08-31

Study Completion Date

2012-08-31

Brief Summary

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The purpose of this study is to evaluate the change in patient-reported outcomes, physician assessment of a change as well as safety and tolerability in patients with Relapsing Forms of Multiple Sclerosis on previous Disease Modifying Therapy (DMT) who are randomized to one of two treatment arms: fingolimod vs. standard of care DMT.

Detailed Description

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Conditions

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Relapsing Forms of Multiple Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Fingolimod

Patients randomized in this arm received Fingolimod 0.5 mg/day oral capsule for 6 months core period .

Group Type EXPERIMENTAL

Fingolimod

Intervention Type DRUG

0.5 mg/day oral capsule

Multiple Sclerosis Disease Modifying Treatments (MS DMTs)

Patients randomized in this arm received selected Standard MS DMT such as Interferon beta-1b or Interferon beta-1a or Glatiramer acetate for 6 months. An open-label extension of up to 3 months of treatment with fingolimod was to be available for patients in the DMT arm who successfully completed all study visits.

Group Type ACTIVE_COMPARATOR

Standard MS DMTs

Intervention Type DRUG

Interventions

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Fingolimod

0.5 mg/day oral capsule

Intervention Type DRUG

Standard MS DMTs

Intervention Type DRUG

Other Intervention Names

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GILENYA™ Avonex®, Copaxone®, Rebif®, Betaseron®, Extavia®

Eligibility Criteria

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Inclusion Criteria

* Relapsing forms of MS
* Expanded Disability Status Scale (EDSS) 0-5.5
* Continuous treatment with MS DMT for a minimum of 6 months
* Fingolimod naive

Exclusion Criteria

* Immune system diseases other than MS
* Active macular edema
* History of selected prior infections and criteria for immunizations
* History of selected immune system treatments and/or medications
* Selected cardiovascular, pulmonary, or hepatic conditions
* Selected abnormal laboratory values
* Pregnant or nursing women
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Novartis Investigative Site

Birmingham, Alabama, United States

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Cullman, Alabama, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Anaheim, California, United States

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Berkeley, California, United States

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Fresno, California, United States

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Fullerton, California, United States

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La Habra, California, United States

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Loma Linda, California, United States

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Newport Beach, California, United States

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Oceanside, California, United States

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Sacramento, California, United States

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Walnut Creek, California, United States

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Boulder, Colorado, United States

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Colorado Springs, Colorado, United States

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Fort Collins, Colorado, United States

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Fairfield, Connecticut, United States

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New London, Connecticut, United States

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Stratford, Connecticut, United States

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Dover, Delaware, United States

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Newark, Delaware, United States

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Atlantis, Florida, United States

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Bradenton, Florida, United States

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Doral, Florida, United States

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Fort Lauderdale, Florida, United States

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Hollywood, Florida, United States

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Jacksonville, Florida, United States

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Montreal, Quebec, Canada

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Guaynabo, , Puerto Rico

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Countries

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United States Canada Puerto Rico

References

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Hughes B, Cascione M, Freedman MS, Agius M, Kantor D, Gudesblatt M, Goldstick LP, Agashivala N, Schofield L, McCague K, Hashmonay R, Barbato L; EPOC study investigators. First-dose effects of fingolimod after switching from injectable therapies in the randomized, open-label, multicenter, Evaluate Patient OutComes (EPOC) study in relapsing multiple sclerosis. Mult Scler Relat Disord. 2014 Sep;3(5):620-8. doi: 10.1016/j.msard.2014.06.006. Epub 2014 Jul 3.

Reference Type DERIVED
PMID: 26265274 (View on PubMed)

Fox E, Edwards K, Burch G, Wynn DR, LaGanke C, Crayton H, Hunter SF, Huffman C, Kim E, Pestreich L, McCague K, Barbato L; EPOC study investigators. Outcomes of switching directly to oral fingolimod from injectable therapies: Results of the randomized, open-label, multicenter, Evaluate Patient OutComes (EPOC) study in relapsing multiple sclerosis. Mult Scler Relat Disord. 2014 Sep;3(5):607-19. doi: 10.1016/j.msard.2014.06.005. Epub 2014 Jul 4.

Reference Type DERIVED
PMID: 26265273 (View on PubMed)

Calkwood J, Cree B, Crayton H, Kantor D, Steingo B, Barbato L, Hashmonay R, Agashivala N, McCague K, Tenenbaum N, Edwards K. Impact of a switch to fingolimod versus staying on glatiramer acetate or beta interferons on patient- and physician-reported outcomes in relapsing multiple sclerosis: post hoc analyses of the EPOC trial. BMC Neurol. 2014 Nov 26;14:220. doi: 10.1186/s12883-014-0220-1.

Reference Type DERIVED
PMID: 25424122 (View on PubMed)

Cascione M, Wynn D, Barbato LM, Pestreich L, Schofield L, McCague K. Randomized, open-label study to evaluate patient-reported outcomes with fingolimod after changing from prior disease-modifying therapy for relapsing multiple sclerosis: EPOC study rationale and design. J Med Econ. 2013 Jul;16(7):859-65. doi: 10.3111/13696998.2013.802239. Epub 2013 May 20.

Reference Type DERIVED
PMID: 23647445 (View on PubMed)

Related Links

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http://www.NovartisClinicalTrials.com

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Other Identifiers

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CFTY720DUS01

Identifier Type: -

Identifier Source: org_study_id

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