Efficacy and Safety of Fingolimod in Patients With Relapsing-remitting Multiple Sclerosis

NCT ID: NCT00289978

Last Updated: 2012-04-11

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1272 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-01-31

Study Completion Date

2009-07-31

Brief Summary

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This study assessed the efficacy, safety, and tolerability of 2 doses of oral fingolimod (1.25 mg/day and 0.5 mg/day) compared to placebo in patients with relapsing-remitting multiple sclerosis (RRMS)

Detailed Description

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Conditions

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Relapsing-remitting Multiple Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Fingolimod 1.25 mg

Group Type EXPERIMENTAL

Fingolimod 1.25 mg

Intervention Type DRUG

Patients self-administered fingolimod 1.25 mg capsules orally once daily.

Fingolimod 0.5 mg

Group Type EXPERIMENTAL

Fingolimod 0.5 mg

Intervention Type DRUG

Patients self-administered fingolimod 0.5 mg capsules orally once daily.

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Patients self-administered a fingolimod placebo capsule orally once daily.

Interventions

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Fingolimod 1.25 mg

Patients self-administered fingolimod 1.25 mg capsules orally once daily.

Intervention Type DRUG

Fingolimod 0.5 mg

Patients self-administered fingolimod 0.5 mg capsules orally once daily.

Intervention Type DRUG

Placebo

Patients self-administered a fingolimod placebo capsule orally once daily.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Male and female patients between ages 18-55 with a diagnosis of multiple sclerosis
* Patients with a relapsing-remitting disease course
* Patients with EDSS score of 0-5.5

Exclusion Criteria

* Patients with other chronic disease of the immune system, malignancies, acute pulmonary disease, cardiac failure, etc.
* Pregnant or nursing women
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_CHAIR

Novartis Pharmaceuticals

Locations

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The Queen Elizabeth Hospital

Woodville South, South Australia, Australia

Site Status

North Gosford Private Hospital

Burrabil Avenue, Suite 17, Gosford, , Australia

Site Status

Strategic Health Evaluators

Chatswood, , Australia

Site Status

St Vincent's Hospital Melbourne, Department of Clinical Neurosciences

Fitzroy, , Australia

Site Status

Austin Health, Department of Neurology

Heidelberg, , Australia

Site Status

Algemeen Ziekenhuis St. Jan, Department of Neurology

Ruddershove, Brugge, Belgium

Site Status

Erasme Hospital

Route de Lennik 808, Brussels Capital, Belgium

Site Status

CHU Charleroi, Hôpital Civil

Boulevard Paul Janson 92, Charleroi, Belgium

Site Status

University Hospital Gasthuisberg

Department Neurology, Herestraat 49, Leuven, Belgium

Site Status

AZ Alma

Department of Neurology & Rehab-Umit, Gentsesteenweg 132, Sijsele, Belgium

Site Status

Regionaal Ziekenhuis

St.Trudo, Diestersteenweg 100,, St.Truiden, Belgium

Site Status

MS Klinik

Boemerangstraat 2, Overpelt, , Belgium

Site Status

National Multiple Sclerose Centrum v.z.w

Vanheylenstraat 16, Melsbroek, , Belgium

Site Status

University of British Columbia

Me498 2211 Wesbrook Mall, Vancouver, British Columbia, Canada

Site Status

DMSRU - Capital Health

Halifax, Nova Scotia, Canada

Site Status

Kingston General Hospital, MS Clinic

Connell 7, 76 Stuart Street, Kingston, Ontario, Canada

Site Status

Nepean Medical Center

Ottawa, Ontario, Canada

Site Status

St. Michael's Hospital

Toronto, Ontario, Canada

Site Status

Clinical Trials Office,

Trillium Health Center, 00 Queesway West, Mississauga, Ontario, Canada

Site Status

Hopital Maisonneuve-Rosemont, Recherche Clinique de Neurologie

Montreal, Quebec, Canada

Site Status

University of Saskatchewan

Regina, Saskatchewan, Canada

Site Status

Military Hospital of Brno

Department of Neurology, Zabrdovicka 3, Brno, Czechia

Site Status

Faculty Hospital St. Anne

First Department of Neurology, Pekarska 53, Brno, Czechia

Site Status

Faculty Hospital

Department of Neurology, I.P. Paulova 6, Olomouc, Czechia

Site Status

Hospital of Pardubice

Department of Neurology, Kyjevska 44, Pardubice, Czechia

Site Status

Faculty Hospital

Department of Neurology, Alej Svobody 80, Plzeň, Czechia

Site Status

Neurologicka klinika, Fakultni nemocnice

Kralovske Vinohrady, Srobarova 50, Prague, Czechia

Site Status

Faculty Hospital Motol, MS Center

Department of Neurology, V Uvalu 84, Prague 5, Czechia

Site Status

Vseobecna fakultni nemocnice

MS Centrum, Neurologicka Klinika, Karlovo Namesti 32, Praha 2, Czechia

Site Status

MS Centrum

Neurology Department of Hospital Teplice, Duchcovska 53, Teplice, Czechia

Site Status

Centrum neurologicke pece

Jiraskova 1389, Rychnov Nad Kneznou, , Czechia

Site Status

Facultní Nemocnice Spoliklinikou Ostrava, Neurology Department

Ostrava, , Czechia

Site Status

Helsinki Headache Center Postitalon Lääkäriasema

Mannnerheiminaukio 1 B 2 Floor, Helsinki, Finland

Site Status

Finnish Special Neurology Center Ltd.

Brahenkatu 11 D,, Turku, Finland

Site Status

Suomen Terveystalo/ Päänsärkykeskus, Tampere

Hämeenkatu 18, 6th Fl., Tampere, , Finland

Site Status

Turku University Hospital, Neurology Department 799

Kiinanmyllynkatu 11- 14, Turku, , Finland

Site Status

Hyvinkään sairaala

Neurologian Poliklinikka, Sairaalankatu 1, Hyvinkää, , Finland

Site Status

CHU La Timone

Service Neurologie, Boulevard Jean Moulin, Marsielle Cedex 5, , France

Site Status

Investigational Site

Berlin, , Germany

Site Status

Investigational Site

Berlin, , Germany

Site Status

Investigational Site

Düsseldorf, , Germany

Site Status

Investigational Site

Giessen, , Germany

Site Status

Investigational Site

Hamburg, , Germany

Site Status

Investigational Site

Hamburg, , Germany

Site Status

Investigational Site

Leipzig, , Germany

Site Status

Investigational Site

Magdeburg, , Germany

Site Status

Investigational Site

München, , Germany

Site Status

Investigational Site

München, , Germany

Site Status

Investigational Site

Münster, , Germany

Site Status

Investigational Site

Regensburg, , Germany

Site Status

Investigational Site

Seesen/Harz, , Germany

Site Status

Investigational Site

Stuttgart, , Germany

Site Status

Investigational Site

Tübingen, , Germany

Site Status

Investigational Site

Würzburg, , Germany

Site Status

Athens Naval Hospital, Neurology Department

Athens, , Greece

Site Status

Neurology Department Athens General Hospital, G. Gennimatas

Mesogeion 154 Ave., Athens, , Greece

Site Status

1st IKA Papadimitriou Neurology Dept

Terma Zaimi, Melissia-Athens, , Greece

Site Status

University General Hospital of Thessaloniki "AHEPA", B' University Department of Neurology

Thessaloniki, , Greece

Site Status

Barzilai Medical Center

Ashkelon, , Israel

Site Status

Carmel Medical Center

Haifa, , Israel

Site Status

Sieff Medical Center

Safed, , Israel

Site Status

Sheba - Medical Center

Tel Hashomer, Ramat-Gan,, , Israel

Site Status

Kaunas University Hospital Department of Neurology

Eiveniu 2, Kaunas, , Lithuania

Site Status

Academisch Ziekenhuis VU

De Boelelaan 1118, Amsterdam, Netherlands

Site Status

St. Antonius Ziekenhuis

Postbus 2500, Nieuwegein, Netherlands

Site Status

Multiple Clerosis Center Nijmegen

Heiweg 97, Nyimegen, Netherlands

Site Status

Erasmus MC

Dr. Molewaterplein 40, Rotterdam, Netherlands

Site Status

Sint Elisabeth Ziekenhuis

Hilvarenbeekse Weg 60, Tilburg, Netherlands

Site Status

Maaslandziekenhuis Sittard

Walramstraat 23, BK Sittard, , Netherlands

Site Status

Samodzielny Publiczny Szpital Kliniczny

Klinika Neurologii, Ul. Marii Skłodowskiej-Curie 24 A, Bialystok, Poland

Site Status

Niezalezny Zespol Opieki Zdrowotnej Kendron

Ul. Swietego Mikolaja 1/8, Bialystok, Poland

Site Status

Oddzial Neurologiczny i Leczenia Udarow

Mozgu, Nowe Ogrody 1/6, Gdańsk, Poland

Site Status

Katedra i Klinika Neurologii Slaskiej Akademii Medycznej

Ul. Medykow 14, Katowice, Poland

Site Status

Univ. Med. Sci. Poznan, Katedra i Klinika Neurologii,

Department of Neurology, Ul. Przybyszewskiego 49, Poznan, Poland

Site Status

CSK MSWiA Hospital

Department of Neurology, Wołoska 137, Warsaw, Poland

Site Status

Jadwiga Kruszewska-Ozimska, Instytut Psychiatrii i Neurologii

II Klinika Neurologii, Ul. Sobieskiego 1/9, Warsaw, Poland

Site Status

Centralny Szpital Kliniczny, Klinika Neurologii

MSWiAw Warszawie, Woloska 137, Warszawa, Poland

Site Status

Katedra i Klinika Neurologii Centralny Szpital Kliniczny AM w Warszawie

Ul. Banacha 1A, Warszawa, Poland

Site Status

Medical University of Lodz

Lodz, , Poland

Site Status

Interregional Clinical Diagnistic Center, Neurology Department

Kazan', , Russia

Site Status

Central Clinical Hospital of Medical Center of Administration of President of Russian Federation

Moscow, , Russia

Site Status

Moscow Regional Research Clinical Institue

Moscow, , Russia

Site Status

Military Medical Academy, Neurology Department

Saint Petersburg, , Russia

Site Status

GUZ "Central Medical Sanitary Department #122 of Federal Medical-Biological agency", Neurology department

Saint Petersburg, , Russia

Site Status

II. Neurologická klinika Fakultná nemocnica s poliklinikou Bratislava pracovisko Kramáre

Limbová 5, Bratislava Region, Slovakia

Site Status

Neurologická klinika, Martinská fakultná nemocnica

Kollárova 2, Martin, , Slovakia

Site Status

I. Neurologická klinika, Fakultná nemocnica s poliklinikou Bratislava pracovisko Staré mesto

Mickiewiczova 13, Bratislava, , Slovakia

Site Status

Neurologické oddelenie, Nemocnica s poliklinikou Žilina

ul.V. Spanyola 43, Žilina, , Slovakia

Site Status

Umhlanga Hospital

Umhlanga, KwaZulu-Natal, South Africa

Site Status

Division of Neurology, Groote Schuur Hospital

E 8-74, Groote Schuur Hospital, Observatory Cape Town, , South Africa

Site Status

Private Neurologist (Morningside Medi-Clinic), Suite C, Block C, Rochester Place

Sandton, , South Africa

Site Status

MS Centrum

Forskningsenhet, SU/Östra CKÖ Plan 0, Gothenburg, Sweden

Site Status

Karolinska University Hospital Huddinge

Department of Neurology R54, Stockholm, , Sweden

Site Status

Karolinska University Hospital, Department of Medicine

Neuroimmunology Unit, CMM L8:04, Stockholm, , Sweden

Site Status

Kantonsspital Basel, Policlinic

Neurology-Neurosurgical, Petersgraben 4, Basel, Switzerland

Site Status

Centre Hospitalier, Universitaire Vaudois Policlinique de Neurologie

Rue Du Bugnon, Lausanne, Switzerland

Site Status

UniversitätsSpital Zürich, Neurologische Klinik

Frauenklinikstr. 26, Zurich, , Switzerland

Site Status

Hacettepe Universiti Hospitals

Department of Neurology, Ankara, Turkey (Türkiye)

Site Status

Gazi University

Medical Faculty Neurology Department, Besevler Ankara, Turkey (Türkiye)

Site Status

EGE University

Medical Faculty Hospital Neurolgy Department, Bornova Izmir, Turkey (Türkiye)

Site Status

Istanbul University, Istanbul Faculty of Medicine

Departement of Neurology, Capa Istanbul, Turkey (Türkiye)

Site Status

Istanbul University, Cerrahpasa School of Medicine

Department of Neurology, Cerrahpasa Istanbul, Turkey (Türkiye)

Site Status

Gaziantep University School of Medicine

Neurology Department, Gaziantep, Turkey (Türkiye)

Site Status

Uludag University Faculty of Medche

Tip Fakultesi, Noroloji ABD, Görükle / Bursa, Turkey (Türkiye)

Site Status

Tepecik Training and Research

Hospital Neurology Service, 35120 Gaziler Cad. Izmir, , Turkey (Türkiye)

Site Status

Dokuz University Medical Faculty, Neurology Department

Inciralti, Izmir, , Turkey (Türkiye)

Site Status

Bakirkoy Ruh ve Sinir Hastaliklari Hastanesi

Istanbul, , Turkey (Türkiye)

Site Status

Mersin Universitesi Tip Fakultesi Hastanesi

Noroloji ABD, Mersin, , Turkey (Türkiye)

Site Status

T.C. Saglik Bakanligi Goztepe Egitim ve Arastirma Hastanesi

Noroloji Klinigi, Göztepe Istanbul, , Turkey (Türkiye)

Site Status

King's College Hospital, Trials office Academie Neuroscience Center

P041 Institute of Psychiatry, Denmark Hill, London, United Kingdom

Site Status

Queens Medical Centre

Division of Clinical Neurology Medical School, Nottingham, United Kingdom

Site Status

Royal Hallamshire Hospital

Glossop Road, Sheffield, United Kingdom

Site Status

St. George's Hospital, Neurology Dept. Atkinson Morley Wing

Backshaw Road, London, , United Kingdom

Site Status

Frenchay Hospital, Department of Neurology

Beckspool Road, Bristol, , United Kingdom

Site Status

Royal Victoria Infirmary

Queen Victoria Road, Newcastle-upon-Tyne, , United Kingdom

Site Status

Countries

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Australia Belgium Canada Czechia Finland France Germany Greece Israel Lithuania Netherlands Poland Russia Slovakia South Africa Sweden Switzerland Turkey (Türkiye) United Kingdom

References

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Nowak CP, Mutze T, Konietschke F. Group sequential methods for the Mann-Whitney parameter. Stat Methods Med Res. 2022 Oct;31(10):2004-2020. doi: 10.1177/09622802221107103. Epub 2022 Jun 13.

Reference Type DERIVED
PMID: 35698787 (View on PubMed)

Fox RJ, Chan A, Zhang A, Xiao J, Levison D, Lewin JB, Edwards MR, Marantz JL. Comparative effectiveness using a matching-adjusted indirect comparison between delayed-release dimethyl fumarate and fingolimod for the treatment of multiple sclerosis. Curr Med Res Opin. 2017 Feb;33(2):175-183. doi: 10.1080/03007995.2016.1248380. Epub 2016 Nov 10.

Reference Type DERIVED
PMID: 27733070 (View on PubMed)

Derfuss T, Bergvall NK, Sfikas N, Tomic DL. Efficacy of fingolimod in patients with highly active relapsing-remitting multiple sclerosis. Curr Med Res Opin. 2015;31(9):1687-91. doi: 10.1185/03007995.2015.1067191. Epub 2015 Aug 20.

Reference Type DERIVED
PMID: 26121423 (View on PubMed)

Kremenchutzky M, O'Connor P, Hohlfeld R, Zhang-Auberson L, von Rosenstiel P, Meng X, Grinspan A, Hashmonay R, Kappos L. Impact of prior treatment status and reasons for discontinuation on the efficacy and safety of fingolimod: Subgroup analyses of the Fingolimod Research Evaluating Effects of Daily Oral Therapy in Multiple Sclerosis (FREEDOMS) study. Mult Scler Relat Disord. 2014 May;3(3):341-9. doi: 10.1016/j.msard.2013.10.006. Epub 2013 Nov 5.

Reference Type DERIVED
PMID: 25876471 (View on PubMed)

Chinea Martinez AR, Correale J, Coyle PK, Meng X, Tenenbaum N. Efficacy and safety of fingolimod in Hispanic patients with multiple sclerosis: pooled clinical trial analyses. Adv Ther. 2014 Oct;31(10):1072-81. doi: 10.1007/s12325-014-0154-4. Epub 2014 Sep 23.

Reference Type DERIVED
PMID: 25245812 (View on PubMed)

Zarbin MA, Jampol LM, Jager RD, Reder AT, Francis G, Collins W, Tang D, Zhang X. Ophthalmic evaluations in clinical studies of fingolimod (FTY720) in multiple sclerosis. Ophthalmology. 2013 Jul;120(7):1432-9. doi: 10.1016/j.ophtha.2012.12.040. Epub 2013 Mar 24.

Reference Type DERIVED
PMID: 23531349 (View on PubMed)

Radue EW, O'Connor P, Polman CH, Hohlfeld R, Calabresi P, Selmaj K, Mueller-Lenke N, Agoropoulou C, Holdbrook F, de Vera A, Zhang-Auberson L, Francis G, Burtin P, Kappos L; FTY720 Research Evaluating Effects of Daily Oral Therapy in Multiple Sclerosis (FREEDOMS) Study Group. Impact of fingolimod therapy on magnetic resonance imaging outcomes in patients with multiple sclerosis. Arch Neurol. 2012 Oct;69(10):1259-69. doi: 10.1001/archneurol.2012.1051.

Reference Type DERIVED
PMID: 22751847 (View on PubMed)

Devonshire V, Havrdova E, Radue EW, O'Connor P, Zhang-Auberson L, Agoropoulou C, Haring DA, Francis G, Kappos L; FREEDOMS study group. Relapse and disability outcomes in patients with multiple sclerosis treated with fingolimod: subgroup analyses of the double-blind, randomised, placebo-controlled FREEDOMS study. Lancet Neurol. 2012 May;11(5):420-8. doi: 10.1016/S1474-4422(12)70056-X. Epub 2012 Apr 10.

Reference Type DERIVED
PMID: 22494956 (View on PubMed)

Kappos L, Radue EW, O'Connor P, Polman C, Hohlfeld R, Calabresi P, Selmaj K, Agoropoulou C, Leyk M, Zhang-Auberson L, Burtin P; FREEDOMS Study Group. A placebo-controlled trial of oral fingolimod in relapsing multiple sclerosis. N Engl J Med. 2010 Feb 4;362(5):387-401. doi: 10.1056/NEJMoa0909494. Epub 2010 Jan 20.

Reference Type DERIVED
PMID: 20089952 (View on PubMed)

Related Links

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http://www.msclinicaltrials.com

Fingolimod clinical trials information website

Other Identifiers

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CFTY720D2301

Identifier Type: -

Identifier Source: org_study_id

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