A Study to Evaluate Safety and Efficacy of Ocrelizumab in Comparison With Fingolimod in Children and Adolescents With Relapsing-Remitting Multiple Sclerosis (RRMS)

NCT ID: NCT05123703

Last Updated: 2025-12-31

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

188 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-05-19

Study Completion Date

2029-09-17

Brief Summary

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This double-blind, double-dummy study will evaluate the safety and efficacy of ocrelizumab compared with fingolimod in children and adolescents with RRMS aged between 10 and \< 18 years over a flexible duration. The double-blind period will last until after the last participant randomized has completed 24 weeks.

Detailed Description

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This Phase III randomized, double-blind, double-dummy, multicenter study will evaluate the safety and efficacy of ocrelizumab administered by IV infusion every 24 weeks compared with fingolimod taken orally daily, in children and adolescents with RRMS aged between 10 and \< 18 years. The study plans to enroll 171 participants in a 1:1 randomization (ocrelizumab:fingolimod), globally. This study consists of a double-blind, double dummy period in which participants will be treated with either active ocrelizumab or active fingolimod for a flexible duration. Participants who complete the double-blind period will be offered the possibility to enter an optional open-label extension (OLE) treatment period of at least 144 weeks with ocrelizumab.

Conditions

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Relapsing-Remitting Multiple Sclerosis

Keywords

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pediatric Multiple Sclerosis pediatric MS children MS children Multiple Sclerosis pediatric ocrelizumab

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Ocrelizumab

Participants will receive ocrelizumab by intravenous (IV) infusion every 24 weeks (Q24W). The first dose is given as dual infusions of half the dose of ocrelizumab on Days 1 and 15 and subsequent doses are given as single infusions of ocrelizumab Q24W. Participants will also receive a placebo of fingolimod administered as once a day (QD) capsule.

Group Type EXPERIMENTAL

Ocrelizumab

Intervention Type DRUG

Ocrelizumab 300 milligrams (mg) will be administered by IV infusion to participants who weigh \< 35 kilograms (kg) and ocrelizumab 600 mg IV will be administered to participants who weigh ≥ 35 kg on Days 1 and 15 (half the dose, 2 weeks apart) and Q24W thereafter.

Fingolimod Placebo

Intervention Type OTHER

Fingolimod matching placebo will be administered daily as a capsule.

Fingolimod

Participants will receive fingolimod orally (PO) QD as per the prescribing information provided with fingolimod. Participants will also receive a placebo of ocrelizumab administered as IV infusion on Days 1 and 15, and Q24W thereafter.

Group Type ACTIVE_COMPARATOR

Ocrelizumab Placebo

Intervention Type OTHER

Ocrelizumab matching placebo will be administered by IV infusion on Day 1 and Day 15 and Q24W thereafter.

Fingolimod

Intervention Type DRUG

Fingolimod will be administered daily as a capsule per the prescribing information (0.25 mg to participants who weigh ≤ 40 kg and 0.5 mg to participants who weigh \> 40 kg).

Interventions

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Ocrelizumab

Ocrelizumab 300 milligrams (mg) will be administered by IV infusion to participants who weigh \< 35 kilograms (kg) and ocrelizumab 600 mg IV will be administered to participants who weigh ≥ 35 kg on Days 1 and 15 (half the dose, 2 weeks apart) and Q24W thereafter.

Intervention Type DRUG

Ocrelizumab Placebo

Ocrelizumab matching placebo will be administered by IV infusion on Day 1 and Day 15 and Q24W thereafter.

Intervention Type OTHER

Fingolimod

Fingolimod will be administered daily as a capsule per the prescribing information (0.25 mg to participants who weigh ≤ 40 kg and 0.5 mg to participants who weigh \> 40 kg).

Intervention Type DRUG

Fingolimod Placebo

Fingolimod matching placebo will be administered daily as a capsule.

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Body weight ≥ 25 kilograms (kg)
* Diagnosis of RRMS in accordance with the International Pediatric Multiple Sclerosis Study Group (IPMSSG) criteria for pediatric Multiple Sclerosis (MS), Version 2012, or McDonald criteria 2017
* Expanded Disability Status Scale (EDSS) at screening: 0-5.5, inclusive
* For all countries except Germany, at least one MS relapse during the previous year or two MS relapses in the previous 2 years or evidence of at least one Gd enhancing lesion on MRI within 6 months


-Participants in Group A (ocrelizumab in the double-blind period \[DBP\]) and Group B (fingolimod in the DBP) who, in the opinion of the investigator, may benefit from switching to ocrelizumab and who have completed the DBP with study treatment (ocrelizumab/fingolimod), may participate in the OLE period

Exclusion Criteria

* Known presence or suspicion of other neurologic disorders that may mimic MS
* Significant uncontrolled somatic diseases, known active infection or any other significant condition that may preclude participant from participating in the study
* Participants with severe cardiac disease or significant findings on the screening Electrocardiograph (ECG)


-Participants who have discontinued the study during the DBP
Minimum Eligible Age

10 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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PPD Development, LP

INDUSTRY

Sponsor Role collaborator

Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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UC San Diego

La Jolla, California, United States

Site Status

University of California San Francisco

San Francisco, California, United States

Site Status

Children's Hospital Colorado

Aurora, Colorado, United States

Site Status

Children's National Hospital

Washington D.C., District of Columbia, United States

Site Status

Johns Hopkins Medicine

Baltimore, Maryland, United States

Site Status

Boston Children's Hospital Central Pharmacy

Boston, Massachusetts, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Robert Wood Johnson Medical School

New Brunswick, New Jersey, United States

Site Status

Cleveland Clinic, Mellen Center for Multiple Sclerosis

Cleveland, Ohio, United States

Site Status

The Boster Center for Multiple Sclerosis a Singlepoint Healthcare Company

Columbus, Ohio, United States

Site Status

The Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Baylor College of Medicine/Texas Children's Hospital

Houston, Texas, United States

Site Status

University of Virginia Health System

Charlottesville, Virginia, United States

Site Status

Hospital de Pediatría S.A.M.I.C.- Prof. Dr. Juan P. Garrahan

Ciudad de Buenos Aires, , Argentina

Site Status

Clinica Universitaria Reina Fabiola

Córdoba, , Argentina

Site Status

Centro de Investigaciones Médicas Tucuman

San Miguel de Tucumán, , Argentina

Site Status

Royal Children's Hospital Melbourne - PIN

Parkville, Victoria, Australia

Site Status

Medizinische Universität Wien

Vienna, , Austria

Site Status

Hôpital Universitaire des Enfants Reine Fabiola

Brussels, , Belgium

Site Status

Cliniques Universitaires St-Luc

Brussels, , Belgium

Site Status

UZ Gent

Ghent, , Belgium

Site Status

L2 Ip - Instituto de Pesquisas Clinicas Ltda - ME

Brasília, Federal District, Brazil

Site Status

Instituto de Neurologia de Curitiba

Curitiba, Paraná, Brazil

Site Status

Universidade de Caxias do Sul - Rio Grande do Sul

Caxias do Sul, Rio Grande do Sul, Brazil

Site Status

Nucleo de Pesquisa Clinica do Rio Grande do Sul NPCR

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Hospital Sao Lucas - PUCRS

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

CPQuali Pesquisa Clínica Sao Paulo

São Paulo, São Paulo, Brazil

Site Status

Inst. Da Criança- Faculdade de Medicina Usp

São Paulo, , Brazil

Site Status

University of Alberta Hospital

Edmonton, Alberta, Canada

Site Status

Children's Hospital of Eastern Ontario

Ottawa, Ontario, Canada

Site Status

The Hospital for Sick Children

Toronto, Ontario, Canada

Site Status

Astra Kliinik

Tallinn, , Estonia

Site Status

Tartu University Hospital

Tartu, , Estonia

Site Status

Hospices Civils de Lyon - Hôpital Pierre Wertheimer

Bron, Rhône, France

Site Status

Centre Hospitalier Universitaire de Bicêtre

Le Kremlin-Bicêtre, , France

Site Status

CHRU de Montpellier, Hopital Gui de Chauliac

Montpellier, , France

Site Status

Hopital de Hautepierre

Strasbourg, , France

Site Status

Vestische Kinder- und Jugendklinik Datteln

Datteln, , Germany

Site Status

Universitaetsklinikum Carl Gustav Carus an der TU Dresden

Dresden, , Germany

Site Status

Universitätsmedizin Göttingen Georg-August-Universität

Göttingen, , Germany

Site Status

Universitätsklinikum Münster

Münster, , Germany

Site Status

Eginitio University General Hospital of Athens

Athens, Attica, Greece

Site Status

University General Hospital ''ATTIKON'' - General Hospital of West Attica H AGIA VARVARA

Chaïdári, Attica, Greece

Site Status

St. Luke's Hospital

Thessaloniki, , Greece

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

Debreceni Egyetem Klinikai Kozpont

Debrecen, , Hungary

Site Status

Zydus Hospital

Ahmedabad, Gujarat, India

Site Status

Artemis Hospital

Gurugram, Haryana, India

Site Status

Sparsh Super Speciality Hospital

Bangalore North, Karnataka, India

Site Status

Amrita Institute of Medical Sciences and Research Centre

Kochi, Kerala, India

Site Status

Deenanath Mangeshkar Hospital & Research Centre

Pune, Maharashtra, India

Site Status

All India Institute Of Medical Sciences (AIIMS)

New Delhi, National Capital Territory of Delhi, India

Site Status

Fortis Flight Lieutenant Rajan Dhall Hospital

New Delhi, National Capital Territory of Delhi, India

Site Status

Seth G.S Medical College K.E.M Hospital

Mumbai, , India

Site Status

Universita? G. D'Annunzio

Chieti, Abruzzo, Italy

Site Status

Azienda Ospedaliero-Universitaria Consorziale Pol. di Bari

Bari, Apulia, Italy

Site Status

IRCCS Materno Infantile Burlo Garofolo - INCIPIT - PIN

Trieste, Friuli Venezia Giulia, Italy

Site Status

Ospedale Pediatrico Bambino Gesù

Rome, Lazio, Italy

Site Status

Azienda Ospedaliera Sant'Andrea

Rome, Lazio, Italy

Site Status

Fondazione IRCCS Istituto Neurologico Carlo Besta

Milan, Lombardy, Italy

Site Status

Azienda Ospedaliero Universitaria Policlinico Vittorio Emanuele

Catania, Sicily, Italy

Site Status

Children's Clinical University Hospital

Riga, , Latvia

Site Status

Hospital Civil Fray Antonio Alcalde

Guadalajara, Jalisco, Mexico

Site Status

Clinstile S.A de C.V.

Mexico City, Mexico CITY (federal District), Mexico

Site Status

Grupo Médico Camino S.C.

Mexico City, Mexico CITY (federal District), Mexico

Site Status

Centro de Investigacion Clinica Chapultepec S. A. de C. V.

Morelia, Michoacán, Mexico

Site Status

Iecsi S.C.

Monterrey, Nuevo León, Mexico

Site Status

Neurociencias Estudios Clinicos S.C.

Culiacán, Sinaloa, Mexico

Site Status

Centro para el Desarrollo de la Medicina y de Asistencia

Culiacán, Sinaloa, Mexico

Site Status

FAICIC S de R.L. de C.V

Veracruz, , Mexico

Site Status

Hassan II University Hospital

Fes, , Morocco

Site Status

CHU Mohammed VI

Marrakesh, , Morocco

Site Status

Centre Hospitalier Ibn Sina CHIS - Hopital des Specialites

Rabat, , Morocco

Site Status

Hospital Militaire Dinstruction Mohammed V de Rabat

Rabat, , Morocco

Site Status

Instytut Centrum Zdrowia Matki Polki

?ód?, , Poland

Site Status

Uniwersyteckie Centrum Kliniczne

Gda?sk, , Poland

Site Status

Uniwersytecki Szpital Kliniczny w Poznaniu

Późna, , Poland

Site Status

Dzieci?cy Szpital Kliniczny im. Józefa Polikarpa Brudzi?skiego

Warsaw, , Poland

Site Status

Instytut Pomnik Centrum Zdrowia Dziecka

Warsaw, , Poland

Site Status

Hospital de Braga

Braga, , Portugal

Site Status

ULS de Coimbra, EPE - Hospitais da Universidade de Coimbra

Coimbra, , Portugal

Site Status

Hospital Santo Antonio dos Capuchos

Lisbon, , Portugal

Site Status

Centro Hospitalar Lisboa Norte, E.P.E. ? Hospital de Santa Maria

Lisbon, , Portugal

Site Status

Victor Gomoiu Clinical Hospital for Children

Bucharest, , Romania

Site Status

Prof Dr Alexandru Obregia Clinical Psychiatric Hospital

Bucharest, , Romania

Site Status

Childrens University Hospital

Belgrade, , Serbia

Site Status

Clinic for Neurology and Psychiatry for Children and Youth

Belgrade, , Serbia

Site Status

Mother and Child Health Care Institute of Serbia Dr Vukan Cupic

Belgrade, , Serbia

Site Status

University Clinical Centre of Nis

Niš, , Serbia

Site Status

Hospital Sant Joan De Deu

Esplugues de Llobregas, Barcelona, Spain

Site Status

Hospital de Cruces

Barakaldo, Vizcaya, Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario de la Princesa

Madrid, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Hospital Regional Universitario Carlos Haya

Málaga, , Spain

Site Status

Hospital Universitario Virgen Macarena

Seville, , Spain

Site Status

Universitäts-Kinderspital Zürich - Eleonorenstiftung

Zurich, , Switzerland

Site Status

Communal noncommercial enterprise of Lviv Regional Council Lviv Regional Clinical Hospital

Lviv, Kharkiv Governorate, Ukraine

Site Status

Ukrainian medical rehabilitation center for children with organic lesions of the nervous system

Kyiv, KIEV Governorate, Ukraine

Site Status

KZ "Dnipropetrovska oblasna dytiacha klinichna likarnia" DOR

Dnipropetrovsk, Tavria Okruha, Ukraine

Site Status

State Institution Institute of Neurology, Psychiatry and Narcology of NAMS of Ukraine

Kharkiv, , Ukraine

Site Status

Addenbrookes Hospital

Cambridge, , United Kingdom

Site Status

Royal Hospital for Children and Young People

Edinburgh, , United Kingdom

Site Status

Great Ormond Street Hospital For Children

London, , United Kingdom

Site Status

Countries

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Bulgaria Croatia Denmark Netherlands Russia Turkey (Türkiye) United States Argentina Australia Austria Belgium Brazil Canada Estonia France Germany Greece Hungary India Italy Latvia Mexico Morocco Poland Portugal Romania Serbia Spain Switzerland Ukraine United Kingdom

References

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Mar S, Valeriani M, Steinborn B, Schreiner T, Waubant E, Filippi M, Kotulska K, Mazurkiewicz-Beldzinska M, El Azzouzi B, Lin CJ, Shen YA, Kletzl H, Evershed J, Hogea A, Manlius C, Bonati U, Banwell B. Ocrelizumab dose selection for treatment of pediatric relapsing-remitting multiple sclerosis: results of the OPERETTA I study. J Neurol. 2025 Jan 15;272(2):137. doi: 10.1007/s00415-024-12879-z.

Reference Type DERIVED
PMID: 39812825 (View on PubMed)

Other Identifiers

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2020-004128-41

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-506516-40-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

WN42086

Identifier Type: -

Identifier Source: org_study_id