Observation of Young Patients Who Are Undergoing Surgery for Craniopharyngioma

NCT ID: NCT00258453

Last Updated: 2013-08-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

NA

Total Enrollment

120 participants

Study Classification

INTERVENTIONAL

Study Start Date

2001-05-31

Study Completion Date

2009-09-30

Brief Summary

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RATIONALE: Collecting information on how craniopharyngioma is diagnosed and treated may help doctors predict a patient's response to treatment and help plan the best treatment. It may also help identify the intermediate- and long-term effects of treatment.

PURPOSE: This clinical trial is collecting information on diagnosis, treatment, and quality of life of young patients who are undergoing surgery for craniopharyngioma.

Detailed Description

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OBJECTIVES:

Primary

* Identify all applied therapy strategies in pediatric patients with craniopharyngioma.
* Correlate relapse status with different therapy strategies/modality in these patients.
* Determine the health status (i.e., ophthalmologic, neuropediatric, and endocrine findings) and the health-related quality of life of these patients after treatment.

Secondary

* Determine the incidence of craniopharyngioma in pediatric patients.
* Identify quality control measures for diagnosis and therapy in these patients.
* Improve long-term care through a standardized follow-up program in these patients.
* Determine the efficacy of endocrine substitution for postoperative hypopituitarism in these patients.
* Identify risk factors for developing obesity and correlate the neurotransmitter concentration of leptin and neuropeptide Y in cerebral spinal fluid, serum, and craniopharyngioma cystic fluid with the likelihood of developing obesity in these patients.
* Determine the incidence and extent of eating disorders in these patients.

OUTLINE: This is a multicenter study.

Patients undergo neurologic, endocrine, and ophthalmologic tests and anthropometric diagnostic measurements. Patients then undergo 1 of the following surgical procedures: total resection; incomplete, subtotal, or partial resection; biopsy; or cyst pressure release. Patients whose tumor relapses may undergo a second resection and/or radiotherapy.

Quality of life is assessed at baseline and then periodically thereafter.

After surgery, patients are followed periodically.

PROJECTED ACCRUAL: A total of 120 patients will be accrued for this study.

Conditions

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Brain and Central Nervous System Tumors Long-term Effects Secondary to Cancer Therapy in Children Perioperative/Postoperative Complications Psychosocial Effects of Cancer and Its Treatment Weight Changes

Keywords

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psychosocial effects of cancer and its treatment long-term effects secondary to cancer therapy in children perioperative/postoperative complications weight changes childhood craniopharyngioma

Study Design

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Primary Study Purpose

DIAGNOSTIC

Blinding Strategy

NONE

Interventions

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metabolic assessment

Intervention Type OTHER

physiologic testing

Intervention Type OTHER

biopsy

Intervention Type PROCEDURE

computed tomography

Intervention Type PROCEDURE

conventional surgery

Intervention Type PROCEDURE

magnetic resonance imaging

Intervention Type PROCEDURE

management of therapy complications

Intervention Type PROCEDURE

psychosocial assessment and care

Intervention Type PROCEDURE

quality-of-life assessment

Intervention Type PROCEDURE

radiation therapy

Intervention Type RADIATION

Eligibility Criteria

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Inclusion Criteria

DISEASE CHARACTERISTICS:

* Diagnosis of primary craniopharyngioma by MRI and CT scan (initial diagnosis)

* Patients with only cystic sellar or parasellar malformation (e.g., Rathke pouch cysts or suprasellar cysts) are allowed but will undergo observation only

PATIENT CHARACTERISTICS:

Performance status

* Not specified

Life expectancy

* Not specified

Hematopoietic

* Not specified

Hepatic

* Not specified

Renal

* Not specified

PRIOR CONCURRENT THERAPY: Not specified
Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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German Society for Pediatric Oncology and Hematology GPOH gGmbH

OTHER

Sponsor Role lead

Principal Investigators

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Hermann Mueller, MD

Role: STUDY_CHAIR

Klinikum Oldenburg

Locations

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Krankenhaus Dornbirn

Dornbirn, , Austria

Site Status

Landeskrankenhaus Feldkirch

Feldkirch-Tisis, , Austria

Site Status

Universitaet Kinderklinik

Graz, , Austria

Site Status

Innsbruck Universitaetsklinik

Innsbruck, , Austria

Site Status

Landeskrankenhaus Klagenfurt

Klagenfurt, , Austria

Site Status

LKH Leoben

Leoben, , Austria

Site Status

A. oe. Krankenhaus der Barmherzigen Schwestern Kinderabteilung

Linz, , Austria

Site Status

Landes-Kinderkrankenhaus

Linz, , Austria

Site Status

St. Johanns-Spital

Salzburg, , Austria

Site Status

Kardinal Schwarzenbersches Krankenhaus Betriebsgesellschraft mbH Kinderspital

Schwarzach, , Austria

Site Status

A. oe. Landeskrankenhaus Abt. fuer Kinderkrankheiten

Steyr, , Austria

Site Status

Allg. Krankenhaus der Stadt Wien Universitaets-Kinderklinik

Vienna, , Austria

Site Status

St. Anna Children's Hospital

Vienna, , Austria

Site Status

Kinderklinik - Universitaetsklinikum Aachen

Aachen, , Germany

Site Status

Klinikum Augsburg

Augsburg, , Germany

Site Status

Caritas-Krankenhaus Bad Mergentheim

Bad Mergentheim, , Germany

Site Status

Klinikum am Bamberg

Bamberg, , Germany

Site Status

Klinikum Bayreuth

Bayreuth, , Germany

Site Status

Helios Klinikum Berlin

Berlin, , Germany

Site Status

Charite - Campus Charite Mitte

Berlin, , Germany

Site Status

Charite University Hospital - Campus Virchow Klinikum

Berlin, , Germany

Site Status

Evangelisches Krankenhauus Bielfeld

Biefeld, , Germany

Site Status

Kinderklinik der Universitaet Bonn

Bonn, , Germany

Site Status

Klinikum Bremen-Mitte

Bremen, , Germany

Site Status

Allgemeinen Krankenhaus Celle Kinderklinik

Celle, , Germany

Site Status

Klinikum Chemnitz gGmbH

Chemnitz, , Germany

Site Status

Klinikum Coburg

Coburg, , Germany

Site Status

Kliniken der Stadt Koeln gGmbH - Kinderkrankenhaus Riehl

Cologne, , Germany

Site Status

Children's Hospital

Cologne, , Germany

Site Status

Carl - Thiem - Klinkum Cottbus

Cottbus, , Germany

Site Status

Vestische Kinderklinik Universitaetsklinik Witten/Herdecke

Datteln, , Germany

Site Status

Klinikum Lippe - Detmold

Detmold, , Germany

Site Status

Staedtisches Krankenhaus Dresden - Neustadt

Dresden, , Germany

Site Status

Universitatsklinikum Carl Gustav Carus

Dresden, , Germany

Site Status

Klinikum Duisburg

Duisburg, , Germany

Site Status

Klinikum Erfurt

Erfurt, , Germany

Site Status

Universitaets - Kinderklinik

Erlangen, , Germany

Site Status

Klinikum der J.W. Goethe Universitaet

Frankfurt, , Germany

Site Status

Universitaetskinderklinik - Universitaetsklinikum Freiburg

Freiburg im Breisgau, , Germany

Site Status

Kinderklinik

Giessen, , Germany

Site Status

Universitaetsklinikum Goettingen

Göttingen, , Germany

Site Status

Universitats - Kinderklinik

Greiswald, , Germany

Site Status

Kreiskrankenhaus Gummersbach GMBH

Gummersbach, , Germany

Site Status

Universitaetsklinikum Halle

Halle, , Germany

Site Status

University Medical Center Hamburg - Eppendorf

Hamburg, , Germany

Site Status

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Kreskrankenhaus Kinderabteilung

Heide, , Germany

Site Status

Universitaets-Kinderklinik Heidelberg

Heidelberg, , Germany

Site Status

SLK - Kliniken Heilbronn GmbH - Klinikum am Gesundbrunnen

Heilbronn, , Germany

Site Status

Gemeinschaftskrankenhaus

Herdecke, , Germany

Site Status

Staedtisches Krankenhaus Hildesheim

Hildesheim, , Germany

Site Status

Universitaetsklinikum des Saarlandes

Homburg, , Germany

Site Status

Clinic for Bone Marrow Transplantation and Hematology and Oncology

Idar-Oberstein, , Germany

Site Status

Universitaets - Kinderklinik

Jena, , Germany

Site Status

Municipal Hospital Complex of the University

Kaiserslautern, , Germany

Site Status

Staedtisches Klinikum Karlsruhe gGmbH

Karlsruhe, , Germany

Site Status

Klinikum Kassel

Kassel, , Germany

Site Status

Staedtisches Krankenhaus Kiel

Kiel, , Germany

Site Status

University Hospital Schleswig-Holstein - Kiel Campus

Kiel, , Germany

Site Status

Klinikum Kemperhof Koblenz

Koblenz, , Germany

Site Status

Klinik Konstanz

Konstanz, , Germany

Site Status

Klinikum Krefeld GmbH

Krefeld, , Germany

Site Status

Kinderkrankenhaus St. Marien

Landshut, , Germany

Site Status

Universitaets - Kinderklinik

Leipzig, , Germany

Site Status

St. Annastift Krankenhaus

Ludwigshafen, , Germany

Site Status

Universitaets - Kinderklinik - Luebeck

Lübeck, , Germany

Site Status

Universitatsklinikum der MA

Magdeburg, , Germany

Site Status

Johannes Gutenberg University

Mainz, , Germany

Site Status

Staedtisches Klinik - Kinderklinik

Mannheim, , Germany

Site Status

Universitaets - Kinderklinik

Marburg, , Germany

Site Status

Klinikum Minden

Minden, , Germany

Site Status

Krankenhaus Neuwerk Klinik fuer Kinder und Jugendmedizin

Mönchengladbach, , Germany

Site Status

Krankenhaus Muenchen Schwabing

Munich, , Germany

Site Status

Dr. von Haunersches Kinderspital der Universitaet Muenchen

Munich, , Germany

Site Status

Staedtisches Krankenhaus Muenchen - Harlaching

Munich, , Germany

Site Status

Klinik und Poliklinik fuer Kinder und Jugendmedizin - Universitaetsklinikum Muenster

Münster, , Germany

Site Status

Klinikum Neubrandenburg

Neubrandenburg, , Germany

Site Status

Lukaskrankenhaus Neuss

Neuss, , Germany

Site Status

Marienhaus Klinikum St. Elisabeth Neuwied

Neuwied, , Germany

Site Status

Cnopf'sche Kinderklinik

Nuremberg, , Germany

Site Status

Klinikum Nuernberg - Klinikum Sued

Nuremberg, , Germany

Site Status

Klinikum Oldenburg

Oldenburg, , Germany

Site Status

Marien Hospital

Osnabrück, , Germany

Site Status

Paracelsus - Klinik Osnabrueck

Osnabrück, , Germany

Site Status

Klinik St. Hedwig-Kinderklinik

Regensburg, , Germany

Site Status

Kinderklinik - Universitaetsklinikum Rostock

Rostock, , Germany

Site Status

Saarbrucker Winterbergkliniken

Saarbrücken, , Germany

Site Status

Johanniter-Kinderklinik

Sankt Augustin, , Germany

Site Status

Klinikum Schwerin

Schwerin, , Germany

Site Status

Kinderklink Siegen Deutsches Rotes Kreuz

Siegen, , Germany

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Olgahospital

Stuttgart, , Germany

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Krankenanstalt Mutterhaus der Borromaerinnen

Trier, , Germany

Site Status

Universitaetsklinikum Tuebingen

Tübingen, , Germany

Site Status

Comprehensive Cancer Center Ulm at Universitaetsklinikum Ulm

Ulm, , Germany

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St. Marienhospital - Vechta

Vechta, , Germany

Site Status

Staedtisches Klinikum - Howedestrase

Vechta, , Germany

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Dr. Horst-Schmidt-Kliniken

Wiesbaden, , Germany

Site Status

Reinhard-Nieter-Krankenhaus

Wilhelmshaven, , Germany

Site Status

Klinikum der Stadt Wolfsburg

Wolfsburg, , Germany

Site Status

Helios Kliniken Wuppertal University Hospital

Wuppertal, , Germany

Site Status

Universitaets - Kinderklinik Wuerzburg

Würzburg, , Germany

Site Status

Lanssjukhuset Ryhov

Jönköping, , Sweden

Site Status

Kantonspital Aarau

Aarau, , Switzerland

Site Status

Universitaets-Kinderspital beider Basel

Basel, , Switzerland

Site Status

Ospedale "la Carita", Locarno

Locarno, , Switzerland

Site Status

Kinderspital Luzern

Lucerne, , Switzerland

Site Status

Ostschweizer Kinderspital

Sankt Gallen, , Switzerland

Site Status

Kantonsspital Winterthur

Winterthur, , Switzerland

Site Status

University Children's Hospital

Zurich, , Switzerland

Site Status

Countries

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Austria Germany Sweden Switzerland

References

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Roth CL, Gebhardt U, Muller HL. Appetite-regulating hormone changes in patients with craniopharyngioma. Obesity (Silver Spring). 2011 Jan;19(1):36-42. doi: 10.1038/oby.2010.80. Epub 2010 Apr 8.

Reference Type RESULT
PMID: 20379145 (View on PubMed)

Muller HL, Gebhardt U, Schroder S, Pohl F, Kortmann RD, Faldum A, Zwiener I, Warmuth-Metz M, Pietsch T, Calaminus G, Kolb R, Wiegand C, Sorensen N; study committee of KRANIOPHARYNGEOM 2000/2007. Analyses of treatment variables for patients with childhood craniopharyngioma--results of the multicenter prospective trial KRANIOPHARYNGEOM 2000 after three years of follow-up. Horm Res Paediatr. 2010;73(3):175-80. doi: 10.1159/000284358. Epub 2010 Mar 3.

Reference Type RESULT
PMID: 20197669 (View on PubMed)

Sowithayasakul P, Beckhaus J, Ozyurt J, Bison B, Friedrich C, Muller HL. Prolactin serum concentrations in childhood-onset craniopharyngioma patients. J Endocrinol Invest. 2025 Sep;48(9):2041-2051. doi: 10.1007/s40618-025-02622-4. Epub 2025 Jun 7.

Reference Type DERIVED
PMID: 40481916 (View on PubMed)

Mann-Markutzyk LV, Beckhaus J, Ozyurt J, Mehren A, Friedrich C, Muller HL. Daytime sleepiness and health-related quality of life in patients with childhood-onset craniopharyngioma. Sci Rep. 2025 Mar 19;15(1):9407. doi: 10.1038/s41598-025-94384-5.

Reference Type DERIVED
PMID: 40108339 (View on PubMed)

Wagener K, Beckhaus J, Boekhoff S, Friedrich C, Muller HL. Sporadic and neurofibromatosis type 2-associated meningioma in children and adolescents. J Neurooncol. 2023 Jul;163(3):555-563. doi: 10.1007/s11060-023-04344-0. Epub 2023 Jul 4.

Reference Type DERIVED
PMID: 37402092 (View on PubMed)

Beckhaus J, Friedrich C, Boekhoff S, Calaminus G, Bison B, Eveslage M, Timmermann B, Flitsch J, Muller HL. Outcome after pediatric craniopharyngioma: the role of age at diagnosis and hypothalamic damage. Eur J Endocrinol. 2023 Mar 2;188(3):lvad027. doi: 10.1093/ejendo/lvad027.

Reference Type DERIVED
PMID: 36857103 (View on PubMed)

Mehren A, Ozyurt J, Zu Klampen P, Boekhoff S, Thiel CM, Muller HL. Self- and informant-rated apathy in patients with childhood-onset craniopharyngioma. J Neurooncol. 2018 Oct;140(1):27-35. doi: 10.1007/s11060-018-2936-z. Epub 2018 Jul 3.

Reference Type DERIVED
PMID: 29971569 (View on PubMed)

Ozyurt J, Muller HL, Warmuth-Metz M, Thiel CM. Hypothalamic tumors impact gray and white matter volumes in fronto-limbic brain areas. Cortex. 2017 Apr;89:98-110. doi: 10.1016/j.cortex.2017.01.017. Epub 2017 Feb 3.

Reference Type DERIVED
PMID: 28259055 (View on PubMed)

Daubenbuchel AM, Hoffmann A, Eveslage M, Ozyurt J, Lohle K, Reichel J, Thiel CM, Martens H, Geenen V, Muller HL. Oxytocin in survivors of childhood-onset craniopharyngioma. Endocrine. 2016 Nov;54(2):524-531. doi: 10.1007/s12020-016-1084-5. Epub 2016 Sep 1.

Reference Type DERIVED
PMID: 27585663 (View on PubMed)

Hoffmann A, Warmuth-Metz M, Lohle K, Reichel J, Daubenbuchel AM, Sterkenburg AS, Muller HL. Fusiform dilatation of the internal carotid artery in childhood-onset craniopharyngioma: multicenter study on incidence and long-term outcome. Pituitary. 2016 Aug;19(4):422-8. doi: 10.1007/s11102-016-0722-5.

Reference Type DERIVED
PMID: 27125511 (View on PubMed)

Ozyurt J, Thiel CM, Lorenzen A, Gebhardt U, Calaminus G, Warmuth-Metz M, Muller HL. Neuropsychological outcome in patients with childhood craniopharyngioma and hypothalamic involvement. J Pediatr. 2014 Apr;164(4):876-881.e4. doi: 10.1016/j.jpeds.2013.12.010. Epub 2014 Feb 6.

Reference Type DERIVED
PMID: 24507865 (View on PubMed)

Roth CL, Enriori PJ, Gebhardt U, Hinney A, Muller HL, Hebebrand J, Reinehr T, Cowley MA. Changes of peripheral alpha-melanocyte-stimulating hormone in childhood obesity. Metabolism. 2010 Feb;59(2):186-94. doi: 10.1016/j.metabol.2009.06.031. Epub 2009 Sep 18.

Reference Type DERIVED
PMID: 19766264 (View on PubMed)

Other Identifiers

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CDR0000450768

Identifier Type: REGISTRY

Identifier Source: secondary_id

EU-20537

Identifier Type: -

Identifier Source: secondary_id

GPOH-CRANIOPHARYNGIOMA-2000

Identifier Type: -

Identifier Source: org_study_id