Inhibition of Aggressive Behavior in Participants With Fragile X Syndrome

NCT ID: NCT07328529

Last Updated: 2026-01-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

NOT_YET_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

80 participants

Study Classification

INTERVENTIONAL

Study Start Date

2026-03-31

Study Completion Date

2028-03-31

Brief Summary

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The goal of this clinical trial is to learn if drug SRX246 works to treat irritability, agitation, aggression and self-injury (IAAS) behaviors in adult males with Fragile X Syndrome (FXS). It will also learn about the safety of drug SRX246. The main questions it aims to answer are:

* Does drug SRX246 lower the number of times participants experience IAAS behaviors?
* What medical problems do participants have when taking drug SRX246? Researchers will compare drug SRX246 to a placebo (a look-alike substance that contains no drug) to see if drug SRX246 works to treat IAAS behaviors.

Participants will:

* Take drug SRX246 or a placebo every day for up to 8 months
* Have weekly checkups by phone or video to answer study questions
* Have periodically scheduled home visits by nurses to conduct medical check-ups and tests
* Keep a diary of their symptoms

Detailed Description

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Conditions

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Aggressive Behavior in Fragile X Syndome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

CROSSOVER

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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SRX246

SRX246 will be provided as 120mg capsule to be taken orally, twice per day, once in the morning and once in the evening.

Group Type EXPERIMENTAL

SRX246

Intervention Type DRUG

SRX246 120mg capsules for oral administration

Placebo

Placebo will be provided as a matching capsule to be taken orally, twice per day, once in the morning and once in the evening.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo capsules for oral administration

Interventions

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SRX246

SRX246 120mg capsules for oral administration

Intervention Type DRUG

Placebo

Placebo capsules for oral administration

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Biological male, age 18 to 45 years inclusive
* Molecular genetic confirmation of the full Fragile X messenger ribonucleoprotein mutation (≥200 CGG repetitions)
* IAAS symptoms leading to a CGI-S score for Disruptive Behavior of 5 or more
* Reported history of aggression based on the CMAI-Agg subscale (average score \>22) and an average associated disruptiveness scale of at least 3.
* IQ \< 70
* Stable medication doses for the last month
* Has a caregiver who lives with or spends extensive time with the participant most days and can report behavioral symptoms
* Must be able to swallow study drug capsules whole

Exclusion Criteria

* Medical condition contraindicating study participation
* SGPT and SGOT values 2 or more times the upper limit of normal
* History of psychosis
* Suicidal behavior
Minimum Eligible Age

18 Years

Maximum Eligible Age

45 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Congressionally Directed Medical Research Programs

FED

Sponsor Role collaborator

Azevan Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of California, Davis, MIND Institute

Sacramento, California, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Cincinnati Children's Hospital

Cincinnati, Ohio, United States

Site Status

Countries

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United States

Central Contacts

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Neal G Simon, PhD

Role: CONTACT

610-610-0100

Facility Contacts

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David R Hessl, PhD

Role: primary

916-703-0249

Elizabeth M Berry-Kravis, MD, PhD

Role: primary

312-942-4036

Craig A Erickson, MD

Role: primary

513-636-6553

Other Identifiers

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CDMRP-PR240390

Identifier Type: OTHER_GRANT

Identifier Source: secondary_id

AVN014

Identifier Type: -

Identifier Source: org_study_id

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