Study of Acamprosate in Fragile x Syndrome

NCT ID: NCT01911455

Last Updated: 2021-02-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

46 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-08-27

Study Completion Date

2018-11-08

Brief Summary

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In this research study we want to understand the effectiveness of a drug treatment, acamprosate, for interfering symptoms (i.e., inattention/hyperactivity, social impairment) associated with Fragile X Syndrome (FXS).

Detailed Description

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Each subject with FXS will receive 10 weeks of blinded treatment with acamprosate or matching placebo. After completion of the double-blind phase, all subjects will have an opportunity to receive acamprosate as part of the study procedures for 16 weeks.

Conditions

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Fragile X Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

BASIC_SCIENCE

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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acamprosate

The maximum dose of acamprosate to be used in this study is 666 mg three times daily (total 1998 mg/day) for subjects weight ≥ 50 kg and 1332mg for subjects that weigh \< 50 kg.

Group Type ACTIVE_COMPARATOR

acamprosate

Intervention Type DRUG

Placebo

Placebo will be prescribed with the same frequency and duration as the acamprosate group.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Interventions

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acamprosate

Intervention Type DRUG

Placebo

Intervention Type DRUG

Other Intervention Names

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Campral

Eligibility Criteria

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Inclusion Criteria

* Diagnostic confirmation of full mutation FXS
* Age ≥5 years and \<23 years
* General good health as determined by physical exam, medical history and laboratory work up.

Exclusion Criteria

* Use of more than two psychotropic medications (medications affecting behavior).
* Unstable dosing of any psychotropic medication (medication affecting behavior)
* Problems with kidney functioning
* Unstable seizure disorder
* Change in any anti-convulsant drug dosing in the 60 days prior to study entry
* Prior adequate treatment trial with acamprosate as determined by the study doctor
* Pregnant or lactating females
Minimum Eligible Age

5 Years

Maximum Eligible Age

23 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Rush University Medical Center

OTHER

Sponsor Role collaborator

Children's Hospital Medical Center, Cincinnati

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Craig Erickson, MD

Role: PRINCIPAL_INVESTIGATOR

Children's Hospital Medical Center, Cincinnati

Elizabeth Berry-Kravis, MD

Role: PRINCIPAL_INVESTIGATOR

Rush University Medical Center

Locations

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Rush University Medical Center

Chicago, Illinois, United States

Site Status

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status

Countries

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United States

Other Identifiers

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CIN001- Acamprosate in FX

Identifier Type: -

Identifier Source: org_study_id

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